Temozolomide in Treating Young Patients With Refractory or Recurrent Leukemia

NCT ID: NCT00083070

Last Updated: 2014-02-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

16 participants

Study Classification

INTERVENTIONAL

Study Start Date

2004-03-31

Study Completion Date

2008-06-30

Brief Summary

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RATIONALE: Drugs used in chemotherapy, such as temozolomide, work in different ways to stop cancer cells from dividing so they stop growing or die.

PURPOSE: This phase I trial is studying the side effects and best dose of temozolomide in treating young patients with refractory or recurrent leukemia.

Detailed Description

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OBJECTIVES:

Primary

* Determine the maximum tolerated dose and recommended phase II dose of temozolomide in pediatric patients with refractory or recurrent leukemia.
* Determine the toxic effects of this drug in these patients.
* Determine the pharmacokinetics of this drug in these patients.

Secondary

* Determine the antitumor activity of this drug in these patients.
* Determine the biologic activity and mechanism(s) of resistance to this drug in these patients.

OUTLINE: This is an open-label, dose-escalation, multicenter study.

Patients receive oral temozolomide once daily on days 1-5. Treatment repeats every 28 days for up to 12 courses in the absence of disease progression or unacceptable toxicity.

Cohorts of 3-6 patients receive escalating doses of temozolomide until the maximum tolerated dose (MTD) is determined. The MTD is defined as the dose preceding that at which 2 of 6 patients experience dose-limiting toxicity.

PROJECTED ACCRUAL: A total of 3-36 patients will be accrued for this study within 18-24 months.

Conditions

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Leukemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Temozolomide Therapy

Group Type EXPERIMENTAL

temozolomide

Intervention Type DRUG

Interventions

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temozolomide

Intervention Type DRUG

Other Intervention Names

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Temodar NSC # 362856

Eligibility Criteria

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Inclusion Criteria

DISEASE CHARACTERISTICS:

* Histologically confirmed leukemia of any of the following types:

* Acute lymphoblastic leukemia
* Acute myeloid leukemia
* Chronic myelogenous leukemia in blast crisis
* Refractory or recurrent disease
* Immunophenotypic confirmation of disease at initial diagnosis or recurrence
* More than 25% blasts in the bone marrow (M3)
* Active extramedullary disease allowed except for leptomeningeal disease
* No known curative therapy or therapy proven to prolong survival with an acceptable quality of life
* No active CNS disease

PATIENT CHARACTERISTICS:

Age

* 1 to 21

Performance status

* Karnofsky 50-100% (for patients \> 10 years of age)
* Lansky 50-100% (for patients ≤ 10 years of age)

Life expectancy

* Not specified

Hematopoietic

* WBC \< 30,000/mm\^3 (hydroxyurea or leukapheresis allowed at the discretion of the principal investigator)
* Platelet count ≥ 20,000/mm\^3 (platelet transfusions allowed)
* Hemoglobin ≥ 8.0 g/dL (red blood cell transfusions allowed)

Hepatic

* ALT ≤ 5 times upper limit of normal (ULN)
* Albumin ≥ 2 g/dL
* Bilirubin ≤ 1.5 times ULN

Renal

* Creatinine normal for age OR
* Creatinine clearance OR radioisotope glomerular filtration rate ≥ 70 mL/min/1.73 m\^2

Other

* Not pregnant or nursing
* Negative pregnancy test
* Fertile patients must use effective contraception
* No uncontrolled infection

PRIOR CONCURRENT THERAPY:

Biologic therapy

* At least 7 days since prior biologic therapy, including immunotherapy
* At least 3 months since prior stem cell transplantation

* No evidence of active graft-vs-host disease
* No concurrent biologic therapy
* No concurrent immunotherapy

Chemotherapy

* Recovered from prior chemotherapy
* At least 6 weeks since prior nitrosoureas
* Prior therapy with hydroxyurea allowed for up to 24 hours before initiation of study drug
* No other concurrent chemotherapy

Endocrine therapy

* Concurrent hydrocortisone or other corticosteroids allowed as premedications prior to blood product transfusions in patients with prior severe allergic reactions

Radiotherapy

* Recovered from prior radiotherapy
* No concurrent radiotherapy

Surgery

* Not specified

Other

* No other concurrent anticancer agents
* No other concurrent investigational drugs
Minimum Eligible Age

1 Year

Maximum Eligible Age

21 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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National Cancer Institute (NCI)

NIH

Sponsor Role collaborator

Children's Oncology Group

NETWORK

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Terzah M. Horton, MD, PhD

Role: STUDY_CHAIR

Texas Children's Cancer Center

Locations

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Stanford Cancer Center at Stanford University Medical Center

Stanford, California, United States

Site Status

Indiana University Cancer Center

Indianapolis, Indiana, United States

Site Status

Fairview University Medical Center - University Campus

Minneapolis, Minnesota, United States

Site Status

Mayo Clinic Cancer Center

Rochester, Minnesota, United States

Site Status

University of Mississippi Medical Center

Jackson, Mississippi, United States

Site Status

Herbert Irving Comprehensive Cancer Center at Columbia University

New York, New York, United States

Site Status

SUNY Upstate Medical University Hospital

Syracuse, New York, United States

Site Status

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

St. Jude Children's Research Hospital

Memphis, Tennessee, United States

Site Status

Simmons Comprehensive Cancer Center at University of Texas Southwestern Medical Center - Dallas

Dallas, Texas, United States

Site Status

Baylor University Medical Center - Houston

Houston, Texas, United States

Site Status

Children's Hospital and Regional Medical Center - Seattle

Seattle, Washington, United States

Site Status

Hospital for Sick Children

Toronto, Ontario, Canada

Site Status

Hopital Sainte Justine

Montreal, Quebec, Canada

Site Status

Countries

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United States Canada

References

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Horton TM, Thompson PA, Berg SL, Adamson PC, Ingle AM, Dolan ME, Delaney SM, Hedge M, Weiss HL, Wu MF, Blaney SM; Children's Oncology Group Study. Phase I pharmacokinetic and pharmacodynamic study of temozolomide in pediatric patients with refractory or recurrent leukemia: a Children's Oncology Group Study. J Clin Oncol. 2007 Nov 1;25(31):4922-8. doi: 10.1200/JCO.2007.12.0667.

Reference Type RESULT
PMID: 17971589 (View on PubMed)

Horton TM, Dolan E, Hegde M, et al.: A phase I study of temozolomide (Temodar®) in pediatric patients with relapsed or refractory leukemia: a Children's Oncology Group study. [Abstract] Blood 106 (11): A-4455, 2005.

Reference Type RESULT

Other Identifiers

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CDR0000362059

Identifier Type: OTHER

Identifier Source: secondary_id

COG-ADVL0411

Identifier Type: OTHER

Identifier Source: secondary_id

ADVL0411

Identifier Type: -

Identifier Source: org_study_id

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