Efficacy and Safety Study of CC-5013 Monotherapy in Subjects With Myelodysplastic Syndromes

NCT ID: NCT00064974

Last Updated: 2013-04-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

215 participants

Study Classification

INTERVENTIONAL

Study Start Date

2003-06-30

Study Completion Date

2007-02-28

Brief Summary

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This study is a multi-center, single-arm, open-label study of oral CC-5013 monotherapy administered at a dose of 10 mg daily on Days 1-21 every 28 days (28-day cycles) to red blood cell (RBC) transfusion-dependent subjects with low- or intermediate-1-risk MDS who do not have a del (5q31-33) cytogenetic abnormality. Screening procedures will take place within 28 days of first day of study drug treatment. Subjects will receive study drug (CC-5013) in 28-day cycles for up to 6 cycles, or until bone marrow disease progression or progression/relapse following erythroid hematologic improvement (Appendix I) is documented. Study visits will occur every cycle (every 28 days) and laboratory monitoring to assess hematological parameters will occur every 14 days. Safety and efficacy assessments to be performed during the study are outlined in the Schedule of Study Assessments.

Detailed Description

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Conditions

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Myelodysplastic Syndromes

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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CC-5013

CC-5013 10 mg (two 5 mg capsules) daily on days 1-28 every 28 days (28 day cycles)

Group Type EXPERIMENTAL

CC-5013

Intervention Type DRUG

CC-5013 10 mg (two 5 mg capsules) daily on days 1-28 every 28 days (28 day cycles)

Interventions

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CC-5013

CC-5013 10 mg (two 5 mg capsules) daily on days 1-28 every 28 days (28 day cycles)

Intervention Type DRUG

Other Intervention Names

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lenalidomide

Eligibility Criteria

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Inclusion Criteria

* Must understand and voluntarily sign an informed consent form.
* Age ≥ 18 years at the time of signing the informed consent form.
* Must be able to adhere to the study visit schedule and other protocol requirements.
* Diagnosis of low - or intermediate-1-risk IPSS (Appendix III) MDS without an abnormality of chromosome 5 involving a deletion between bands q31 and q33.
* Red blood cell (RBC) transfusion-dependent anemia defined as having received ≥ to 2 units of RBCs within 8 weeks of the first day of study drug treatment.
* Eastern Cooperative Oncology Group (ECOG) (Appendix IV) performance status score of 0, 1, or 2.
* Women of childbearing potential (WCBP) must have a negative serum or urine pregnancy test within 7 days of starting study drug.
* Sexually active WCBP must agree to use adequate contraceptive methods (oral, injectable, or implantable hormonal contraceptive; tubal ligation; intra-uterine device; barrier contraceptive with spermicide; or vasectomized partner) while on study drug.
* WCBP must agree to have pregnancy tests every 4 weeks while on study drug.

Exclusion Criteria

* Pregnant or lactating females.
* Prior therapy with lenalidomide.
* An abnormality of chromosome 5 involving a deletion between bands q31 and q33.
* Lab Abnormality: Absolute neutrophil count (ANC) \<500 cells/mm3 (0.5 x 109/L)
* Lab Abnormality: Platelet count \<50,000/mm3 (50 x 109/L)
* Lab Abnormality: Serum creatinine \>2.5 mg/dL (221 mmol/L)
* Lab Abnormality: Serum glutamic oxaloacetic transaminase/Aspartate transaminase (SGOT/AST) or Serum glutamic pyruvic transaminase/Alanine transaminase (SGPT/ALT) \>3.0 x upper limit of normal (ULN)
* Lab Abnormality: Serum total bilirubin \>2.0 mg/dL (34 mmol/L)
* Prior ≥ grade 3 National Cancer Institute (NCI) Common Toxicity Criteria (CTC) (Appendix VI) allergic reaction/hypersensitivity to thalidomide.
* Prior ≥ grade 3 NCI CTC (Appendix VI) rash or any desquamation (blistering) while taking thalidomide.
* Clinically significant anemia due to factors such as iron, B12 or folate deficiencies, autoimmune or hereditary hemolysis or gastrointestinal bleeding
* If a marrow aspirate is not evaluable for storage iron, transferrin saturation must be \> 20 % and serum ferritin not less than 50 ng/mL.
* Use of hematopoietic growth factors within 7 days of the first day of study drug treatment.
* Chronic use (\>2 weeks) of greater than physiologic doses of a corticosteroid agent (dose equivalent to \>10 mg/day of prednisone) within 28 days of the first day of study drug treatment.
* Use of experimental or standard drugs (i.e. chemotherapeutic, immunosuppressive, and cytoprotective agents) for the treatment of MDS within 28 days of the first day of study drug treatment.
* Prior history of malignancy other than MDS (except basal cell or squamous cell carcinoma or carcinoma in situ of the cervix or breast) unless the subject has been free of disease for greater than or equal to 3 years.
* Use of any other experimental therapy within 28 days of the first day of study drug treatment.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Celgene Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Robert Knight, MD

Role: STUDY_DIRECTOR

Celgene Corporation

Locations

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Arizona Cancer Center

Scottsdale, Arizona, United States

Site Status

Mayo Clinic

Scottsdale, Arizona, United States

Site Status

Arizona Cancer Center

Tucson, Arizona, United States

Site Status

Alta Bates Cancer Center

Berkeley, California, United States

Site Status

Desert Hematology Oncology Medical Group, Inc.

Rancho Mirage, California, United States

Site Status

Stanford University Medical Center

Stanford, California, United States

Site Status

Florida Cancer Specialists

Fort Myers, Florida, United States

Site Status

Mayo Clinic

Jacksonville, Florida, United States

Site Status

Cancer & Blood Disease Center

Lecanto, Florida, United States

Site Status

University of Miami- Sylvester Comp Cancer Center

Miami, Florida, United States

Site Status

H. Lee Moffitt Cancer Center and Research Institute

Tampa, Florida, United States

Site Status

Northwest Georgia Oncology - Wellstar Cancer Research

Marietta, Georgia, United States

Site Status

Rush Presbyterian-St. Luke's Medical Center

Chicago, Illinois, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Midwest Cancer Research Group

Skokie, Illinois, United States

Site Status

Indiana University Medical Center

Indianapolis, Indiana, United States

Site Status

Johns Hopkins Oncology Center

Baltimore, Maryland, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Wayne State University School of Medicine

Detroit, Michigan, United States

Site Status

St. Luke's Oncology and Hematology Associates

Duluth, Minnesota, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

University of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status

Roswell Park Cancer Institute

Buffalo, New York, United States

Site Status

Winthrop University Hospital

Mineola, New York, United States

Site Status

St. Vincents Comprehensive Cancer Center

New York, New York, United States

Site Status

New York Hospital- Cornell

New York, New York, United States

Site Status

Memorial Sloan-Kettering Cancer Center

New York, New York, United States

Site Status

Mt. Sinai Medical Center

New York, New York, United States

Site Status

University of Rochester-James P. Wilmot Cancer Center

Rochester, New York, United States

Site Status

Wake Forest University School of Medicine

Winston-Salem, North Carolina, United States

Site Status

The Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

Kaiser Permanente Northwest Region

Portland, Oregon, United States

Site Status

Drexel University College of Medicine

Philadelphia, Pennsylvania, United States

Site Status

Western Pennsylvania Cancer Institute

Pittsburgh, Pennsylvania, United States

Site Status

MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Swedish Cancer Institute

Seattle, Washington, United States

Site Status

Fred Hutchinson Cancer Research Center

Seattle, Washington, United States

Site Status

Royal Adelaide Hospital - SA Pathology Haematology

Adelaide, South Australia, Australia

Site Status

Princess Alexandra Hospital - Haematology

Brisbane, , Australia

Site Status

Royal Prince Alfred Hospital - Institute of Haematology

Camperdown, , Australia

Site Status

Peter McCallum Cancer Institute - Directorate of Cancer Medecine

East Melbourne, , Australia

Site Status

Frankston Hospital-peninsula Health - Oncology Day Unit

Frankston, , Australia

Site Status

The Alfred Hospital - malignant haematology & stem cell transplantation

Melbourne, , Australia

Site Status

Calvary Mater Newcastle - Haematology

Waratah, , Australia

Site Status

Border Medical Oncology

Wodonga, , Australia

Site Status

Wollongong Hospital - Haematology

Wollongong, , Australia

Site Status

UZ Gent - Hematology

Ghent, , Belgium

Site Status

University Hospital Leuven - Hematology

Leuven, , Belgium

Site Status

Cliniques Universitaires ULC de Mont-Godinne - Hematology

Yvoir, , Belgium

Site Status

Fakultní nemocnice Hradec Králové - Hematology

Hradec Králové, , Czechia

Site Status

Charles university Hospital - Internal Medicine

Prague, , Czechia

Site Status

Aalborg Sygemus - Haematology

Aalborg, , Denmark

Site Status

Aarhus University Hospital

Aarhus, , Denmark

Site Status

Odense University Hospital

Odense, , Denmark

Site Status

Vejle Hospital - Hematology

Vejle, , Denmark

Site Status

CHU Angers - Service des maladies du sang

Angers, , France

Site Status

Centre Hospitalier de la côte basque - Hematologie

Bayonne, , France

Site Status

Centre Hospitalier Départemental Vendée - Onco-hematologie

La Roche-sur-Yon, , France

Site Status

CHRU de Lille - Service des maladies du sang

Lille, , France

Site Status

Institut Paoli Calmette - Hematology 1

Marseille, , France

Site Status

CHU Hôtel-Dieu - Hematologie

Nantes, , France

Site Status

Hôpital Saint Louis - Immuno-hematologie

Paris, , France

Site Status

CHU Saint Antoine - Service des maladies du sang

Paris, , France

Site Status

CHRU - Hôpital du Haut Lévêque - Centre François Magendie

Pessac, , France

Site Status

Centre Hospitalier Lyon sud - Hematologie

Pierre-Bénite, , France

Site Status

CHRU Hôpital Purpan - Hematologie

Toulouse, , France

Site Status

Hôpital Bretonneau - Hématologie & Thérapie cellulaire

Tours, , France

Site Status

CHU Nancy - Hematologie

Vandœuvre-lès-Nancy, , France

Site Status

Universitätsklinikum Essen, Klinik für Hämatologie

Essen, , Germany

Site Status

Universitätsklinikum Heidelberg - Medizinische Klinik und Poliklinik V

Heidelberg, , Germany

Site Status

Universitätsklinikum Jena - Klinik fur Innere Medizin II-Hamatologie/Onkologie

Jena, , Germany

Site Status

Universitätsklinikum Leipzig - Medizinische Klinik und Poliklinik II

Leipzig, , Germany

Site Status

Universitätsklinikum Münster - Medizinische Klinik und Poliklinik A

Münster, , Germany

Site Status

Universitätsklinikum Tübingen - Medizinische Klinik und Poliklinik - Abteilung II

Tübingen, , Germany

Site Status

Universitätsklinikum Ulm - Klinik fur Innere Medizin III

Ulm, , Germany

Site Status

Universitätsklinikum Würzburg - Medizinische Klinik und Poliklinik II

Würzburg, , Germany

Site Status

University of Athens - Alexandra Hospital; Clinical Therapeutics

Athens, , Greece

Site Status

Università degli Studi di Bologna - Policlinico S. Orsola - Hematology

Bologna, , Italy

Site Status

AO Universitaria San Martino - hematooncology

Genova, , Italy

Site Status

Fondazione "G. Pascale" - Hematology

Napoli, , Italy

Site Status

Ospedale San Luigi AO Luigi Gonzaga - Hematology

Orbassano, , Italy

Site Status

Universita degli Studi di Padova - Clinical & Experimental Medicine

Padua, , Italy

Site Status

Ospedale Guglielmo da Saliceto - hematooncology

Piacenza, , Italy

Site Status

Unità di Ematologia Arcispedale S. Maria Nuova - Haematology

Reggio Emilia, , Italy

Site Status

Policlinico Umberto I, Università "La Sapienza" di Roma - Hematology

Roma, , Italy

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A.O.U. San Giovanni Battista - Hematology

Torino, , Italy

Site Status

VUMC - Hematology

Amsterdam, , Netherlands

Site Status

Erasmus Medical Center - Hematology

Rotterdam, , Netherlands

Site Status

University Medical Center - Hematology

Utrecht, , Netherlands

Site Status

Medical Sciences - Hematology & BMT

Moscow, , Russia

Site Status

Moscow State Medical Institution Municipal Clinical Hospital n.a. S.P. Botkin - Hematology

Moscow, , Russia

Site Status

Russian Research Institute of Hematology and Blood Transfusion - Hematology

Saint Petersburg, , Russia

Site Status

State Higher Educational Institution St. Petersburg State Medical University - Onco-hematology

Saint Petersburg, , Russia

Site Status

Hospital Germans Trias i Pujol - Hematology

Badalona, , Spain

Site Status

Hospital Clinic i Provincial de Barcelona - Hematology

Barcelona, , Spain

Site Status

Hospital de Donostia - Hematology

Guipúzcoa, , Spain

Site Status

Hospital de La Princesa - Hematology

Madrid, , Spain

Site Status

Hospital 12 de Octubre - Hematology

Madrid, , Spain

Site Status

Hospital de Salamanca - Hematology

Salamanca, , Spain

Site Status

Hospital Universitario Marqués de Valdecilla - Hematology

Santander, , Spain

Site Status

Hospital La Fe - Hematology

Valencia, , Spain

Site Status

Sahlgrenska Hospital, University of Goteborg - Hematology

Gothenburg, , Sweden

Site Status

Karolinska University Hospital Huddinge - Center of hematology

Stockholm, , Sweden

Site Status

Karolinska University Hospital Solna- medicine

Stockholm, , Sweden

Site Status

Overlakare Medocomcentrum - Hematology

Uppsala, , Sweden

Site Status

Inselspital, Institut für Medizinische Onkologie

Bern, , Switzerland

Site Status

Hôpitaux Universitaire de Genève - Oncologie

Geneva, , Switzerland

Site Status

Klinik und Poliklinik für Onkologie - UniversitätsSpital Zürich

Zurich, , Switzerland

Site Status

Royal Bournemouth Hospital - Haematology

Bournemouth, , United Kingdom

Site Status

St James's University Hospital - Haematology

Leeds, , United Kingdom

Site Status

St Bartholomew's Hospital - Medical Oncology

London, , United Kingdom

Site Status

King's College Hospital - Haematology Clinical Trials

London, , United Kingdom

Site Status

Freeman Hospital - Northern Centre for Cancer Care

Newcastle upon Tyne, , United Kingdom

Site Status

Nottingham City Hospital - Centre for Clinical Haematology

Nottingham, , United Kingdom

Site Status

Derriford Hospital - Haematology

Plymouth, , United Kingdom

Site Status

Royal hallamshire Hospital - Haematology

Sheffield, , United Kingdom

Site Status

Royal Marsden NHS Foundation Trust - Haematology

Surrey, , United Kingdom

Site Status

Royal Wolverhampton hospitals trust - Research and development

Wolverhampton, , United Kingdom

Site Status

Countries

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United States Australia Belgium Czechia Denmark France Germany Greece Italy Netherlands Russia Spain Sweden Switzerland United Kingdom

References

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Raza A, Reeves JA, Feldman EJ, Dewald GW, Bennett JM, Deeg HJ, Dreisbach L, Schiffer CA, Stone RM, Greenberg PL, Curtin PT, Klimek VM, Shammo JM, Thomas D, Knight RD, Schmidt M, Wride K, Zeldis JB, List AF. Phase 2 study of lenalidomide in transfusion-dependent, low-risk, and intermediate-1 risk myelodysplastic syndromes with karyotypes other than deletion 5q. Blood. 2008 Jan 1;111(1):86-93. doi: 10.1182/blood-2007-01-068833. Epub 2007 Sep 24.

Reference Type DERIVED
PMID: 17893227 (View on PubMed)

Other Identifiers

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CC-5013-MDS-002

Identifier Type: -

Identifier Source: org_study_id

NCT00077506

Identifier Type: -

Identifier Source: nct_alias

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