Lenalidomide in Subject With Low and Intermediate-1 Risk MDS and Without Chromosome 5 Abnormality.

NCT ID: NCT01718379

Last Updated: 2016-11-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

132 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-07-31

Study Completion Date

2016-06-30

Brief Summary

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The goal of the present study is to assess, through a randomized phase II trial, the efficacy and safety of Lenalidomide with or without Epoetin beta in transfusion-dependent, ESA-resistant, IPSS low and intermediate-1 risk MDS patients without chromosome 5 abnormality.

Patients will receive either Lenalidomide alone or Lenalidomide and Epoetin beta for 4 months. Responders will be eligible for maintenance treatment with cycles identical to the first cycles, until relapse occurs or until unacceptable toxicity.

Detailed Description

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This is a multi-center, open-label, randomized, Phase II study.

Patients will be treated either with arm A or B

* Arm A: Lenalidomide 10 mg/day for 21 days every 28 days for 4 courses.
* Arm B: Lenalidomide 10 mg/day for 21 days every 28 days for 4 courses combined with weekly subcutaneous injections of Epoetin beta (60,000 Units/w).

Evaluation of response at the end of 4 months according to IWG 2006 and IWG 2000 criteria.

Maintenance: responders will continue to follow the corresponding treatment arm until relapse occurs; non responders at Evaluation of response at the end of 4 months according to IWG 2006 and IWG 2000 criteria.

in arm A will be considered in failure of treatment and the introduction of Epoetin beta is at the discretion of the physician.

The patients will be followed every 3 months for 12 months

Conditions

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Myelodysplastic Syndromes

Keywords

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Myelodysplasia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A

Lenalidomide 10 mg/day for 21 days every 28 days for 4 courses.

Evaluation of response at the end of 4 months according to IWG 2006 and IWG 2000 criteria.

Maintenance: responders will continue to follow the corresponding treatment arm until relapse occurs; non responders at cycle 4 in arm A will be considered in failure of treatment and the introduction of Epoetin beta is at the discretion of the physician.

The patients will be followed every 3 months for 12 months

Group Type EXPERIMENTAL

Lenalidomide

Intervention Type DRUG

Lenalidomide:10 mg per day during 21 days

Arm B

Lenalidomide 10 mg/day for 21 days every 28 days for 4 courses combined with weekly subcutaneous injections of Epoetin beta (60,000 Units/w).

Evaluation of response at the end of 4 months according to IWG 2006 and IWG 2000 criteria.

Maintenance: responders will continue to follow the corresponding treatment arm until relapse occurs; non responders at cycle 4 in arm A will be considered in failure of treatment and the introduction of Epoetin beta is at the discretion of the physician.

The patients will be followed every 3 months for 12 months

Group Type EXPERIMENTAL

Epoetin beta

Intervention Type DRUG

Epoetin beta: 60,000 Units/week.

Interventions

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Lenalidomide

Lenalidomide:10 mg per day during 21 days

Intervention Type DRUG

Epoetin beta

Epoetin beta: 60,000 Units/week.

Intervention Type DRUG

Other Intervention Names

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Revlimid NEORECORMON

Eligibility Criteria

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Inclusion Criteria

MDS defined as

* Low or int-1 IPSS score
* Documented absence of chromosome 5 abnormality (del(5q) or -5 karyotype)
* De novo MDS, excluding therapy-related MDS AND
* Transfusion dependance (requirement of at least 4 units of RBC transfusions every 8 weeks )
* Resistance or loss of response to a previous treatment with Epoetin alpha/beta (at least 60,000 Units/w) or Darbepoetin (at least 250 µg/w), for at least 12 weeks
* Ineligibility for allogeneic stem cell transplantation or intensive chemotherapy during the next 12 months
* ECOG performance status ≤ 2
* Age ≥ 18 years
* Life expectancy ≥ 3 months
* Adequate liver function (transaminases serum levels ≤ 3N)
* Adequate renal function (calculate creatinine clearance \> 50 ml/min)
* Female subjects of chilbearing potential\* must :

Agree to use effective contraception without interruption throughout the study and for at least 4 weeks after the end of treatment

• Men must: Agree to not conceive during the treatment and to use effective contraception during the treatment period (including periods of dose reduction or temporary suspension) and during one week after end of treatment if their partner is of childbearing potential.

Exclusion Criteria

* Active serious infection not controlled by oral or intravenous antibiotics
* Platelets less than 50 G/L
* Prior history of deep vein thrombosis or pulmonary embolism
* Previous treatment by Thalidomide
* Treatment with any investigational antileukemic agent or chemotherapy at least 6 weeks prior to study entry and lack of full recovery from side effects due to prior therapy independent of when that therapy were given
* Rapidely progressive disease with copromised organ function judged to be life-threatening by the Investigator
* Pregnant or lactating female
* Known human immunodeficiency virus (HIV) infection
* Known active hepatitis B and/or C virus infection
* Hypersensitivity or intolerance to Lenalidomide or any of the excipients
* Hypersensitivity to Epoetin beta or any of the excipients
* Uncontrolled arterial hypertension
* Any history of malignancy (other than myelodysplastic syndrome) unless the patient has remained disease free for more than 5 years
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Celgene

INDUSTRY

Sponsor Role collaborator

Roche Pharma AG

INDUSTRY

Sponsor Role collaborator

Groupe Francophone des Myelodysplasies

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Andréa TOMA, MD

Role: PRINCIPAL_INVESTIGATOR

Groupe Francophone des Myelodysplasies

François Dreyfus, MD

Role: STUDY_DIRECTOR

Groupe Francophone des Myelodysplasies

Locations

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Hematology Dpt, Service d'Hématologie Clinique

CHU Albert Michallon, Grenoble, France

Site Status

Hematology Dpt, CHR La Source orléans

Orléans, Orléans, France

Site Status

Chu Amiens

Amiens, , France

Site Status

CHU Angers

Angers, , France

Site Status

Hematology Dpt, CH d'Avignon-305 rue Follereau-

Avignon, , France

Site Status

CH de la Cote Basque

Bayonne, , France

Site Status

centre de Blois

Blois, , France

Site Status

Hopital Avicenne

Bobigny, , France

Site Status

Hematology Dpt, CHU Haut-Lévèque

Bordeaux, , France

Site Status

Hôpital Boulogne Sur Mer

Boulogne-sur-Mer, , France

Site Status

hôpital Morvan

Brest, , France

Site Status

CHU Clémenceau

Caen, , France

Site Status

CH de Carcassonne

Carcassonne, , France

Site Status

Hematology Dpt, CH René Dubos

Cergy-Pontoise, , France

Site Status

CHU de Clermont-Ferrand

Clermont-Ferrand, , France

Site Status

CH de Compiègne

Compiègne, , France

Site Status

Hematology Dpt, Hôpital Sud Francilien

Corbeil-Essonnes, , France

Site Status

hopital Henri Mondor

Créteil, , France

Site Status

CHU de Dijon

Dijon, , France

Site Status

Hematology Dpt, Hôpital Versailles

Le Chesnay, , France

Site Status

Hematology Dpt,CH Le mans

Le Mans, , France

Site Status

CHRU Huriez

Lille, , France

Site Status

Hopital Saint-Vincent de Paul

Lille, , France

Site Status

CHRU de Limoges

Limoges, , France

Site Status

Hematology Dpt, Centre Hospitalier Lyon Sud

Lyon, , France

Site Status

CH de Mantes-la-jolie

Mantes-la-Jolie, , France

Site Status

Institut Paoli Calmettes

Marseille, , France

Site Status

Hematology Dpt, CHU Brabois

Nancy, , France

Site Status

Hematology Dpt, CHU de nantes

Nantes, , France

Site Status

Hematology Dpt, CHU Archet

Nice, , France

Site Status

Hematology Dpt, CHU Caremeau

Nîmes, , France

Site Status

Hematology Dpt, Hôpital la pitié-Salpétrière

Paris, , France

Site Status

Hematology Dpt, Hopital Saint Louis

Paris, , France

Site Status

Hopital Saint Antoine

Paris, , France

Site Status

centre René Huguenin

Paris Saint Cloud, , France

Site Status

Hematology Dpt, Hôpital Maréchal Joffre

Perpignan, , France

Site Status

Hôpital Jean Bernard

Poitiers, , France

Site Status

Hematology Dpt, Centre Hospitalier de la région d'Annecy

Pringy, , France

Site Status

CHRU de Reims

Reims, , France

Site Status

CHU Pontchaillou

Rennes, , France

Site Status

Centre Henri Becquerel

Rouen, , France

Site Status

CH de Saint Quentin

Sint Quentin, , France

Site Status

Chu Strasbourg

Strasbourg, , France

Site Status

Hematology Dpt, CHU PURPAN

Toulouse, , France

Site Status

Hematology Dpt, CH CHU Bretoneau

Tours, , France

Site Status

Hematology Dpt, CHU de Bicêtre

Le Kremlin-Bicêtre, Île-de-France Region, France

Site Status

Hematology Dpt, CHU Cochin

Paris, Île-de-France Region, France

Site Status

centre hopitalier princesse Grace

Monaco, , Monaco

Site Status

Countries

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France Monaco

References

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Chesnais V, Renneville A, Toma A, Lambert J, Passet M, Dumont F, Chevret S, Lejeune J, Raimbault A, Stamatoullas A, Rose C, Beyne-Rauzy O, Delaunay J, Solary E, Fenaux P, Dreyfus F, Preudhomme C, Kosmider O, Fontenay M; Groupe Francophone des Myelodysplasies. Effect of lenalidomide treatment on clonal architecture of myelodysplastic syndromes without 5q deletion. Blood. 2016 Feb 11;127(6):749-60. doi: 10.1182/blood-2015-04-640128. Epub 2015 Dec 1.

Reference Type DERIVED
PMID: 26626993 (View on PubMed)

Other Identifiers

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GFM-Len-Epo-08

Identifier Type: -

Identifier Source: org_study_id