Phase 2 Trial of RGX-314 in Adults With Center Involved - Diabetic Macular Edema (CI - DME)

NCT ID: NCT06942520

Last Updated: 2025-04-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

18 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-03-18

Study Completion Date

2027-12-31

Brief Summary

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Phase 2 open label, randomized, active controlled, dose-ranging trial in adults with Center Involved - Diabetic Macular Edema (CI - DME)

Detailed Description

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This Phase 2 trial is an open label, randomized, active controlled, dose-ranging trial to allow for preliminary safety and efficacy data on subretinal (SR) delivery of RGX-314 in participants with CI - DME

Conditions

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Diabetic Macular Edema

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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RGX-314 Treatment Arm (Dose 1)

Genetic: RGX-314 Dose 1

\- AAV8 vector containing a transgene for anti-VEGF fab (Dose 1)

Group Type EXPERIMENTAL

RGX-314 Dose 1

Intervention Type GENETIC

AAV8 vector containing a transgene for anti-VEGF fab (Dose 1)

Treatment Arm (Dose 2)

Genetic: RGX-314 Dose 2

-AAV8 vector containing a transgene for anti-VEGF fab (Dose 2)

Group Type EXPERIMENTAL

RGX-314 Dose 2

Intervention Type GENETIC

AAV8 vector containing a transgene for anti-VEGF fab (Dose 2)

Aflibercept Treatment Arm

Biological: Aflibercept IVT

* Commercially available Active Comparator
* Other Names: Eylea

Group Type ACTIVE_COMPARATOR

Aflibercept (2.0 mg)

Intervention Type BIOLOGICAL

Commercially available Active Comparator

Interventions

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RGX-314 Dose 1

AAV8 vector containing a transgene for anti-VEGF fab (Dose 1)

Intervention Type GENETIC

RGX-314 Dose 2

AAV8 vector containing a transgene for anti-VEGF fab (Dose 2)

Intervention Type GENETIC

Aflibercept (2.0 mg)

Commercially available Active Comparator

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Type I or Type II diabetes mellitus with center involving diabetic macular edema with previous treatment
* HbA1c ≤12%
* BCVA in study eye 78 to 25 ETDRS letters (\~20/32 to 20/320) at screening
* Decreased visual acuity attributable primarily due to CI - DME
* Demonstrate clinical response to aflibercept injection in the study eye
* Provide written informed consent

Exclusion Criteria

* Women of childbearing potential
* Neovascularization in the study eye from a cause other than DR
* Evidence in the study eye of optic nerve pallor on clinical examination
* History of pan retinal photocoagulation in the study eye
* Any concurrent ocular condition in the study eye other than CI-DME that could require surgical intervention within 6 months or any condition in the study eye that may increase the risk to the participant, require either medical or surgical intervention during the study to prevent or treat vision loss, or interfere with the study procedures or assessments
* Presence of an implant in the study eye at screening (excluding intraocular lens)
* Any condition in the investigator's opinion that could limit VA improvement in the study eye
* Active or history of glaucoma, steroid response, or ocular hypertension
* Any prior intravitreal steroid injection in the study eye within 6 months prior to screening, administration in the study eye of Ozudrex® within 12 months prior to screening, or administration in the study eye if Iluven® within 36 months prior to screening
* Diabetic macular edema diagnosis ≥ 7 years
* History of chronic renal failure requiring dialysis or kidney transplant
* Participation in any other gene therapy study or receipt of any investigational product within 30 days prior to enrollment or 5 half-lives of the investigational product, whichever is longer, or any plans to use an investigational product within 6 months following enrollment
Minimum Eligible Age

25 Years

Maximum Eligible Age

89 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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REGENXBIO Inc.

INDUSTRY

Sponsor Role collaborator

Sierra Eye Associates

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Sierra Eye Associates

Reno, Nevada, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Clinical Research Study Coordinator

Role: CONTACT

775-329-0286

Facility Contacts

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Clinical Research Study Coordinator

Role: primary

775-329-0286

Other Identifiers

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SEA1979

Identifier Type: -

Identifier Source: org_study_id

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