A Study of BGB-16673 Compared to Investigator's Choice in Participants With Chronic Lymphocytic Leukemia or Small Lymphocytic Lymphoma Previously Exposed to Both Bruton Tyrosine Kinase (BTK) and B-cell Leukemia/Lymphoma 2 Protein (BCL2) Inhibitors

NCT ID: NCT06846671

Last Updated: 2025-11-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

250 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-04-10

Study Completion Date

2030-02-14

Brief Summary

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The purpose of this study is to investigate the efficacy and safety of BGB-16673 compared with investigator's choice (idelalisib plus rituximab \[for CLL only\] or bendamustine plus rituximab or venetoclax plus rituximab retreatment) in participants with chronic lymphocytic leukemia (CLL) or small lymphocytic lymphoma (SLL) previously exposed to both BTK inhibitors (BTKi) and BCL2 inhibitors (BCL2i).

Detailed Description

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Chronic lymphocytic leukemia is a type of blood cancer that affects people around the world. People with CLL suffer from enlarged lymph nodes, spleen, or liver, or have symptoms like night sweats, weight loss and fever. They have shorter life expectancy compared to healthy people. There is an urgent need for new treatment to prolong life and control disease-related symptoms.

In this study, participants with relapsed/refractory (R/R) CLL who were previously exposed to a BTKi and a BCL2i will receive BGB-16673 or the investigator's choice of idelalisib plus rituximab (for CLL only) or bendamustine plus rituximab or venetoclax plus rituximab retreatment. The main purpose of this study is to compare the length of time that participants live without their CLL or SLL worsening between those participants who receive BGB-16673 versus the investigator's choice of treatment (idelalisib plus rituximab or bendamustine plus rituximab, or venetoclax plus rituximab).

Approximately 250 participants will be included in this study around the world. Participants will be randomly allocated to receive either BGB-16673 or the investigator's choice of treatment.

Conditions

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CLL Chronic Lymphocytic Leukemia

Keywords

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CLL

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A: BGB-16673 monotherapy

Participants will receive BGB-16673 once daily until any of the treatment discontinuation criteria are met

Group Type EXPERIMENTAL

BGB-16673

Intervention Type DRUG

Administered orally

Arm B: Investigator's Choice

Participants will receive investigator's choice of idelalisib plus rituximab for CLL only or bendamustine plus rituximab, or venetoclax plus rituximab retreatment.

Group Type ACTIVE_COMPARATOR

Bendamustine

Intervention Type DRUG

Administered intravenously

Idelalisib

Intervention Type DRUG

Administered orally

Rituximab

Intervention Type DRUG

Administered intravenously

Venetoclax

Intervention Type DRUG

Administered orally

Interventions

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BGB-16673

Administered orally

Intervention Type DRUG

Bendamustine

Administered intravenously

Intervention Type DRUG

Idelalisib

Administered orally

Intervention Type DRUG

Rituximab

Administered intravenously

Intervention Type DRUG

Venetoclax

Administered orally

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Confirmed diagnosis of CLL or SLL, requiring treatment, based on 2018 international workshop on chronic lymphocytic leukemia (iwCLL) criteria.
2. Previously received treatment for CLL/SLL with both a BTKi and a BCL2i.
3. Participants with SLL must have measurable disease by computer tomography (CT)/magnetic resonance imaging (MRI)
4. Eastern Cooperative Oncology Group (ECOG) score 0, 1, or 2
5. Adequate liver function
6. Adequate blood clotting function

Exclusion Criteria

1. Known prolymphocytic leukemia or history of, or currently suspected, Richter's transformation
2. Prior autologous stem cell transplant or chimeric antigen receptor-T cell therapy in the last 3 months
3. Known central nervous system involvement
4. Prior exposure to any BTK protein degraders
5. Active fungal, bacterial and/or viral infection requiring parenteral systemic therapy
6. Clinically significant cardiovascular disease
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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BeOne Medicines

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

BeOne Medicines

Locations

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Florida Oncology and Hematology

Fort Myers, Florida, United States

Site Status RECRUITING

Oncology Hematology Associates

Springfield, Missouri, United States

Site Status RECRUITING

Oncology Hematology West, Pc Dba Nebraska Cancer Specialists

Omaha, Nebraska, United States

Site Status RECRUITING

Clinical Research Alliance, Inc

Westbury, New York, United States

Site Status RECRUITING

Cancer Care Associates of York

York, Pennsylvania, United States

Site Status RECRUITING

FUNDALEU

Caba, , Argentina

Site Status RECRUITING

Concord Repatriation General Hospital

Concord, New South Wales, Australia

Site Status RECRUITING

Toowoomba Hospital

Toowoomba, Queensland, Australia

Site Status RECRUITING

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status RECRUITING

Perth Blood Institute

West Perth, Western Australia, Australia

Site Status RECRUITING

CETUS

Belo Horizonte, , Brazil

Site Status RECRUITING

Hospital Sirio Libanes Brasilia

Brasília, , Brazil

Site Status RECRUITING

Hospital Erasto Gaertner

Curitiba, , Brazil

Site Status RECRUITING

Centro de Ensino E Pesquisa Em Oncologia de Santa Catarina (Cepen)

Florianópolis, , Brazil

Site Status RECRUITING

Instituto Joinvilense de Hematologia E Oncologia

Joinville, , Brazil

Site Status RECRUITING

Complexo Hospitalar de Niteroi

Niterói, , Brazil

Site Status RECRUITING

Hospital Sao Lucas Dasa Oncologia

Rio de Janeiro, , Brazil

Site Status RECRUITING

Oncoclinicas Rio de Janeiro Sa

Rio de Janeiro, , Brazil

Site Status RECRUITING

Instituto Brasileiro de Controle Do Cancer

São Paulo, , Brazil

Site Status RECRUITING

Instituto Dor de Pesquisa E Ensino Sao Paulo

São Paulo, , Brazil

Site Status RECRUITING

Sociedade Beneficente Israelita Brasileira Hospital Albert Einstein

São Paulo, , Brazil

Site Status RECRUITING

Hospital Santa Rita de Cassia Afecc

Vitória, , Brazil

Site Status RECRUITING

Fakultni Nemocnice Brno

Brno, , Czechia

Site Status RECRUITING

Fakultni Nemocnice Hradec Kralove

Hradec Králové, , Czechia

Site Status RECRUITING

Vseobecna Fakultni Nemocnice V Praze

Prague, , Czechia

Site Status RECRUITING

Invo Institut Fur Versorgungsforschung in Der Onkologie

Koblenz, , Germany

Site Status RECRUITING

Irccs Istituto Tumori Giovanni Paolo Ii

Bari, , Italy

Site Status RECRUITING

Aou Careggi, Servizio Sanitario Toscana

Florence, , Italy

Site Status RECRUITING

Ospedale San Raffaele

Milan, , Italy

Site Status RECRUITING

Aou Maggiore Della Carita

Novara, , Italy

Site Status RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli

Roma, , Italy

Site Status RECRUITING

Hiroshima Red Cross Hospital and Atomic Bomb Survivors Hospital

Hiroshima, Hiroshima, Japan

Site Status RECRUITING

Aiiku Hospital

Sapporo, Hokkaido, Japan

Site Status RECRUITING

Hyogo Prefectural Amagasaki General Medical Center

AmagasakiCity, Hyōgo, Japan

Site Status RECRUITING

Kagoshima University Hospital

Kagoshima, Kagoshima-ken, Japan

Site Status RECRUITING

University Hospital, Kyoto Prefectural Univ of Medicine

KyotoShi, Kyoto, Japan

Site Status RECRUITING

Tohoku University Hospital

Sendai, Miyagi, Japan

Site Status RECRUITING

Niigata University Medical and Dental Hospital

Niigata, Niigata, Japan

Site Status RECRUITING

Kansai Medical University Hospital

Hirakata, Osaka, Japan

Site Status RECRUITING

Kindai University Hospital

Sayama, Osaka, Japan

Site Status RECRUITING

Saitama Medical Center

Kawagoeshi, Saitama, Japan

Site Status RECRUITING

Ntt Medical Center Tokyo

Shinagawaku, Tokyo, Japan

Site Status RECRUITING

Kumamoto University Hospital

Kumamoto, , Japan

Site Status RECRUITING

National Hospital Organization Okayama Medical Center

Okayama, , Japan

Site Status RECRUITING

Osaka Metropolitan University Hospital

Osaka, , Japan

Site Status RECRUITING

Szpital Specjalist W Brzozowie,Podkarpacki Osrodek Onkologiczny

Brzozów, , Poland

Site Status RECRUITING

Pratia Onkologia Katowice

Katowice, , Poland

Site Status RECRUITING

Pratia McM Krakow

Krakow, , Poland

Site Status RECRUITING

Wielospecjalistyczne Centrum Onkologii I Traumatologii Im M Kopernika W Lodzi

Lodz, , Poland

Site Status RECRUITING

Uniwersytecki Szpital Kliniczny Nr W Lublinie

Lublin, , Poland

Site Status RECRUITING

Uniwersytecki Szpital Kliniczny Im Jana Mikulicza Radeckiego We Wroclawiu

Wroclaw, , Poland

Site Status RECRUITING

Dong A University Hospital

Seogu, Busan Gwang'yeogsi, South Korea

Site Status RECRUITING

Kyungpook National University Hospital

Junggu, Daegu Gwang'yeogsi, South Korea

Site Status RECRUITING

National Cancer Center (Korea)

IlsandongGu GoyangSi, Gyeonggi-do, South Korea

Site Status RECRUITING

Chonnam National University Hwasun Hospital

HwasunGun, Jeollanam-do, South Korea

Site Status RECRUITING

Samsung Medical Center

GangnamGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

The Catholic University of Korea, Seoul St Marys Hospital

SeochoGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Antalya Memorial Hospital

Dokuma, , Turkey (Türkiye)

Site Status RECRUITING

Aberdeen Royal Infirmary

Aberdeen, , United Kingdom

Site Status RECRUITING

Birmingham Heartlands Hospital

Birmingham, , United Kingdom

Site Status RECRUITING

The Royal Bournemouth and Christchurch Hospitals Nhs Foundation

Bournemouth, , United Kingdom

Site Status RECRUITING

University College Hospital

London, , United Kingdom

Site Status RECRUITING

Royal Marsden Hospital

London, , United Kingdom

Site Status RECRUITING

Countries

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Canada Mexico Netherlands New Zealand Sweden United States Argentina Australia Brazil Czechia Germany Italy Japan Poland South Korea Turkey (Türkiye) United Kingdom

Central Contacts

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Study Director

Role: CONTACT

Phone: 1.877.828.5568

Email: [email protected]

Other Identifiers

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2024-518893-15-00

Identifier Type: CTIS

Identifier Source: secondary_id

BGB-16673-302

Identifier Type: -

Identifier Source: org_study_id