A Study to Assess the Efficacy and Safety of Empasiprubart Versus IVIg in Adults With Multifocal Motor Neuropathy

NCT ID: NCT06742190

Last Updated: 2026-01-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

115 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-12-18

Study Completion Date

2029-12-31

Brief Summary

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The main purpose of this study is to compare empasiprubart and IVIg in adult patients with MMN. The study consists of a double-blinded part A (empasiprubart, IVIg) and an open-label part B (empasiprubart). The maximum study duration for participants is up to 49 months.

Detailed Description

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Conditions

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Multifocal Motor Neuropathy (MMN) MMN

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Part A - empasiprubart + IVIg-placebo

During the double blinded - double dummy part A, participants receive empasiprubart and a placebo resembling the IVIg treatment in this arm

Group Type EXPERIMENTAL

Empasiprubart

Intervention Type BIOLOGICAL

Intravenous infusion of empasiprubart

IVIg-placebo

Intervention Type OTHER

A placebo resembling the IVIg treatment

Part A - IVIg + empasiprubart-placebo

During the double blinded - double dummy part A, participants receive IVIg and a placebo resembling the empasiprubart treatment in this arm

Group Type ACTIVE_COMPARATOR

IVIG (Intravenous Immunoglobulin)

Intervention Type BIOLOGICAL

Intravenous infusion of IVIg

Empasiprubart-placebo

Intervention Type OTHER

A placebo resembling the empasiprubart treatment

Part B - empasiprubart

After completion of part A, participants can proceed to part B where they receive empasiprubart (no IVIg)

Group Type EXPERIMENTAL

Empasiprubart

Intervention Type BIOLOGICAL

Intravenous infusion of empasiprubart

Interventions

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Empasiprubart

Intravenous infusion of empasiprubart

Intervention Type BIOLOGICAL

IVIG (Intravenous Immunoglobulin)

Intravenous infusion of IVIg

Intervention Type BIOLOGICAL

Empasiprubart-placebo

A placebo resembling the empasiprubart treatment

Intervention Type OTHER

IVIg-placebo

A placebo resembling the IVIg treatment

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Is at least 18 years of age and the local legal age of consent for clinical studies
* Has a confirmed diagnosis of definite or probable MMN at screening according to the EFNS/PNS 2010 guidelines
* Has responded to IVIg in the past 5 years.
* Is receiving IVIg at a treatment interval of once every 2, 3, 4, or 5 weeks, and a dose of 0.4 to 2.0 g/kg body weight per cycle
* Is receiving a maintenance regimen (no change in frequency, and no change in dose \>10%) of IVIg for at least 8 weeks before screening (or at least 10 weeks for participants receiving IVIg once every 5 weeks)
* Minimum converted weekly IVIg dose of ≥0.125 g/kg
* Has documented immunization against encapsulated bacterial pathogens (N meningitidis and S pneumoniae) within 5 years of screening or is willing to receive immunization at least 14 days before first study drug administration

Exclusion Criteria

* Besides the indication under study, known autoimmune disease (eg, SLE) or any other medical condition that would confound the study results or put the participant at undue risk
* Clinical signs or symptoms suggestive of neuropathies other than MMN, such as motor neuron disease (eg, bulbar signs, brisk reflexes) or other inflammatory neuropathies (eg, sensory neuropathy)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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argenx

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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HonorHealth Neurology - Bob Bove Neuroscience Institute - Neurology

Scottsdale, Arizona, United States

Site Status RECRUITING

The Neurology Group

Pomona, California, United States

Site Status RECRUITING

Samir Macwan, M.D., Inc.

Rancho Mirage, California, United States

Site Status RECRUITING

University of California San Francisco

San Francisco, California, United States

Site Status RECRUITING

University of Colorado - Anschutz Cancer Pavilion (Neuro Onc Clinic)

Aurora, Colorado, United States

Site Status RECRUITING

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status RECRUITING

Medstar Health Research Institute

Washington D.C., District of Columbia, United States

Site Status RECRUITING

EZR Research LLC

Boca Raton, Florida, United States

Site Status RECRUITING

Healthcare Innovations Institute, LLC

Coral Springs, Florida, United States

Site Status RECRUITING

University of Miami Miller School of Medicine

Miami, Florida, United States

Site Status RECRUITING

University of South Florida

Tampa, Florida, United States

Site Status RECRUITING

Northwestern University

Chicago, Illinois, United States

Site Status RECRUITING

Indiana University Health Neuroscience Center

Indianapolis, Indiana, United States

Site Status RECRUITING

University of Kansas Medical Center

Fairway, Kansas, United States

Site Status RECRUITING

Perelman Center for Advanced Medicine

Columbia, Maryland, United States

Site Status RECRUITING

UC Irvine - MDA ALS and Neuromuscular Center

Columbia, Maryland, United States

Site Status RECRUITING

University of Minnesota

Minneapolis, Minnesota, United States

Site Status RECRUITING

Dent Neurologic Institute Amherst

Amherst, New York, United States

Site Status RECRUITING

Columbia University Medical Center

New York, New York, United States

Site Status RECRUITING

University of North Carolina at Chapel Hill

Morrisville, North Carolina, United States

Site Status RECRUITING

The Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status RECRUITING

Oregon Health and Science University

Portland, Oregon, United States

Site Status RECRUITING

National Neuromuscular Research Institute

Austin, Texas, United States

Site Status RECRUITING

NeuroCarePlus

Houston, Texas, United States

Site Status RECRUITING

Royal Melbourne Hospital

Parkville, , Australia

Site Status RECRUITING

Gold Coast University Hospital

Southport, , Australia

Site Status RECRUITING

Brain and Mind Center

Sydney, , Australia

Site Status RECRUITING

Princess Alexandra Hospital

Woolloongabba, , Australia

Site Status RECRUITING

Universitätsklinikum AKH Wien

Vienna, , Austria

Site Status RECRUITING

UZ Antwerpen

Edegem, , Belgium

Site Status RECRUITING

UZ Leuven

Leuven, , Belgium

Site Status RECRUITING

Hôpital de la Citadelle

Liège, , Belgium

Site Status RECRUITING

Hospital Das Clinicas da Faculdade de Medicina de Ribeirão Preto

Ribeirão Preto, , Brazil

Site Status RECRUITING

PSEG Centro de Pesquisa Clínica

São Paulo, , Brazil

Site Status RECRUITING

Neuro-Outaouais Clinic

Gatineau, , Canada

Site Status RECRUITING

London Health Sciences Centre

London, , Canada

Site Status RECRUITING

Huashan Hospital Fudan University

Shanghai, , China

Site Status RECRUITING

Fakultni nemocnice Brno

Brno, , Czechia

Site Status RECRUITING

Fakultni nemocnice Hradec Kralove

Hradec Králové, , Czechia

Site Status RECRUITING

Vseobecna Fakultni Nemocnice V Praze

Prague, , Czechia

Site Status RECRUITING

Aarhus Universitetshospital

Aarhus, , Denmark

Site Status RECRUITING

Rigshospitalet-Inge Lehmanns Vej 8

Copenhagen, , Denmark

Site Status RECRUITING

CHU de Bordeaux - Hôpital Pellegrin

Bordeaux, , France

Site Status RECRUITING

CHU de Brest - Hôpital La Cavale Blanche

Brest, , France

Site Status RECRUITING

Hospices Civils de Lyon - Hôpital Pierre Wertheimer

Bron, , France

Site Status RECRUITING

AP-HP - Hôpital Bicêtre

Le Kremlin-Bicêtre, , France

Site Status RECRUITING

Hôpital Roger Salengro

Lille, , France

Site Status RECRUITING

CHU Limoges - Dupuytren 1

Limoges, , France

Site Status RECRUITING

AP-HM- Hôpital de La Timone

Marseille, , France

Site Status RECRUITING

AP-HM- Hôpital de La Timone

Marseille, , France

Site Status RECRUITING

CHU de Nice-Hôpital Pasteur

Nice, , France

Site Status RECRUITING

AP-HP - Hôpital de la Pitié Salpétrière

Paris, , France

Site Status RECRUITING

CHU de Strasbourg - Hôpital de Hautepierre

Strasbourg, , France

Site Status RECRUITING

Universitätsklinikum Essen

Essen, , Germany

Site Status RECRUITING

Universität Georg August

Göttingen, , Germany

Site Status RECRUITING

Universitätsklinikum Schleswig-Holstein - Campus Lübeck

Lübeck, , Germany

Site Status RECRUITING

Universitätsklinikum Münster

Münster, , Germany

Site Status RECRUITING

Alexianer - MVZ St. Josefs-Krankenhaus Potsdam GmbH

Potsdam, , Germany

Site Status RECRUITING

Universitätsklinikum Würzburg

Würzburg, , Germany

Site Status RECRUITING

University General Hospital ''ATTIKON'' - General Hospital of West Attica H AGIA VARVARA

Chaïdári, , Greece

Site Status RECRUITING

AHEPA University General Hospital of Thessaloniki

Thessaloniki, , Greece

Site Status RECRUITING

Ospedale Policlinico San Martino IRCCS

Genova, , Italy

Site Status RECRUITING

Fondazione Serena Onlus - Centro Clinico NeMO Brescia

Gussago, , Italy

Site Status RECRUITING

Az. Ospedaliera Universitaria Policlinico G. Martino

Messina, , Italy

Site Status RECRUITING

Ospedale San Raffaele S.r.l.

Milan, , Italy

Site Status RECRUITING

Azienda Ospedaliero-Universitaria San Luigi Gonzaga

Milan, , Italy

Site Status RECRUITING

Azienda Ospedaliero-Universitaria Sant'Andrea

Roma, , Italy

Site Status RECRUITING

Fondazione PTV Policlinico Tor Vergata

Roma, , Italy

Site Status RECRUITING

IRCCS Istituto Clinico Humanitas

Rozzano, , Italy

Site Status RECRUITING

Juntendo University Hospital

Bunkyō City, , Japan

Site Status RECRUITING

Institute of Science Tokyo Hospital

Bunkyō City, , Japan

Site Status RECRUITING

Chiba University Hospital

Chūōku, , Japan

Site Status RECRUITING

National Center of Neurology and Psychiatry

Kodaira, , Japan

Site Status RECRUITING

Nagoya University Hospital

Nagoya, , Japan

Site Status RECRUITING

Yamaguchi University Hospital

Ube, , Japan

Site Status RECRUITING

Pauls Stradins Clinical University Hospital

Riga, , Latvia

Site Status RECRUITING

Hospital of Lithuanian University of Health Sciences Kauno klinikos

Kaunas, , Lithuania

Site Status RECRUITING

Amsterdam UMC

Amsterdam, , Netherlands

Site Status RECRUITING

Oslo Universitetssykehus HF, Ullevål

Oslo, , Norway

Site Status RECRUITING

MICS Centrum Medyczne Bydgoszcz

Bydgoszcz, , Poland

Site Status RECRUITING

Centrum Medyczne Neurologia Slaska

Katowice, , Poland

Site Status RECRUITING

SP ZOZ Szpital Uniwersytecki w Krakowie

Krakow, , Poland

Site Status RECRUITING

Galen Clinic -- Lublin

Lublin, , Poland

Site Status RECRUITING

UCK WUM, Centralny Szpital Kliniczny

Warsaw, , Poland

Site Status RECRUITING

ULS de Santo António, EPE - Hospital de Santo António

Porto, , Portugal

Site Status RECRUITING

University Clinical Center of Serbia

Belgrade, , Serbia

Site Status RECRUITING

Univerzitna nemocnica Bratislava

Bratislava, , Slovakia

Site Status RECRUITING

Univerzitna nemocnica MARTIN

Martin, , Slovakia

Site Status RECRUITING

University Medical Centre Ljubljana

Ljubljana, , Slovenia

Site Status RECRUITING

Hospital General Universitario Dr. Balmis

Alicante, , Spain

Site Status RECRUITING

Hospital Universitario Germans Trias i Pujol

Badalona, , Spain

Site Status RECRUITING

Hospital Universitario Vall d'Hebron

Barcelona, , Spain

Site Status RECRUITING

Hospital de La Santa Creu i Sant Pau

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario de Bellvitge

Barcelona, , Spain

Site Status RECRUITING

Hospital Clinico San Carlos

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario de Basurto

Madrid, , Spain

Site Status RECRUITING

Hospital Quironsalud Malaga

Málaga, , Spain

Site Status RECRUITING

Hospital Universitario de Donostia

San Sebastián, , Spain

Site Status RECRUITING

Inselspital - Universitätsspital Bern

Bern, , Switzerland

Site Status RECRUITING

Queen Elizabeth University Hospital

Glasgow, , United Kingdom

Site Status RECRUITING

John Radcliffe Hospital

Oxford, , United Kingdom

Site Status RECRUITING

Salford Royal Hospital

Salford, , United Kingdom

Site Status RECRUITING

Musgrove Park Hospital

Taunton, , United Kingdom

Site Status RECRUITING

Countries

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United States Australia Austria Belgium Brazil Canada China Czechia Denmark France Germany Greece Italy Japan Latvia Lithuania Netherlands Norway Poland Portugal Serbia Slovakia Slovenia Spain Switzerland United Kingdom

Central Contacts

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Sabine Coppieters, MD

Role: CONTACT

857-350-4834

Facility Contacts

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Todd Levine, MD

Role: primary

857-350-4834

Sadiq Altamimi, MD

Role: primary

857-350-4834

Samir Macwan, MD

Role: primary

857-350-4834

Madina Tugizova, MD

Role: primary

857-350-4834

Varun Sreenivasan, MD

Role: primary

857-350-4834

Bhaskar Roy, MD

Role: primary

857-350-4834

Nicholas Samuel Streicher, MD

Role: primary

857-350-4834

Patricio Espinosa Prado, MD

Role: primary

857-350-4834

Sonia Kalirao, MD

Role: primary

857-350-4834

Khema Sharma, MD

Role: primary

857-350-4834

Kathleen Murray, MD

Role: primary

857-350-4834

Arjun Seth, MD

Role: primary

857-350-4834

Alexandru Barboi, MD

Role: primary

857-350-4834

Mamatha Pasnoor, MD

Role: primary

857-350-4834

Chafic Karam, MD

Role: primary

857-350-4834

Jeffrey Mullen, MD

Role: primary

857-350-4834

Georgios Manousakis, MD

Role: primary

857-350-4834

Luisa Rojas Estupinan, MD

Role: primary

857-350-4834

Thomas Brannagan, MD

Role: primary

857-350-4834

Rebecca Traub, MD

Role: primary

857-350-4834

Yuebing Li, MD

Role: primary

857-350-4834

Nizar Chahin, MD

Role: primary

857-350-4834

Yessar Hussain, MD

Role: primary

857-350-4834

Nicolas Nammour, MD

Role: primary

857-350-4834

Belinda Cruse, MD

Role: primary

857-350-4834

Arman Sabet, MD

Role: primary

857-350-4834

Judith Spies, MD

Role: primary

857-350-4834

Stefan Blum, MD

Role: primary

857-350-4834

Jakob Rath, MD

Role: primary

857-350-4834

Alicia Alonso-Jiménez, MD

Role: primary

857-350-4834

Kristl Claeys, MD

Role: primary

857-350-4834

Stephanie Delstanche, MD

Role: primary

857-350-4834

Wilson Marques, MD

Role: primary

857-350-4834

Paulo Sgobbi de Souza, MD

Role: primary

857-350-4834

Francois Jacques, MD

Role: primary

857-350-4834

Anita Florendo-Cumbermack, MD

Role: primary

857-350-4834

Jie Lin, MD

Role: primary

857-350-4834

Josef Bednarik, MD

Role: primary

857-350-4834

Zbysek Pavelek, MD

Role: primary

857-350-4834

Michaela Tyblova, MD

Role: primary

857-350-4834

Thomas Harbo, MD

Role: primary

857-350-4834

Tina Dysgaard, MD

Role: primary

857-350-4834

Gwendal Le Masson, MD

Role: primary

857-350-4834

Jean-Baptiste Noury, MD

Role: primary

857-350-4834

Francoise Bouhour, MD

Role: primary

857-350-4834

Andoni Echaniz-Laguna, MD

Role: primary

857-350-4834

Céline Tard, MD

Role: primary

857-350-4834

Laurent Magy, MD

Role: primary

857-350-4834

Shahram Attarian, MD

Role: primary

857-350-4834

Shahram Attarian, MD

Role: primary

857-350-4834

Sabrina Sacconi, MD

Role: primary

857-350-4834

Karine Viala Bosc, MD

Role: primary

857-350-4834

Jérôme De Seze, MD

Role: primary

857-350-4834

Mark Stettner, MD

Role: primary

857-350-4834

Jana Zschuentzsch, MD

Role: primary

857-350-4834

Julian Grosskreutz, MD

Role: primary

857-350-4834

Gerd Meyer zu Hoerste, MD

Role: primary

857-350-4834

Olaf Hoffmann, MD

Role: primary

857-350-4834

Claudia Sommer, MD

Role: primary

857-350-4834

Georgios Tsivgoulis, MD

Role: primary

857-350-4834

Vasilios Kimiskidis, MD

Role: primary

857-350-4834

Chiara Gemelli, MD

Role: primary

857-350-4834

Massimiliano Filosto, MD

Role: primary

857-350-4834

Luca Gentile, MD

Role: primary

857-350-4834

Stefano Previtali, MD

Role: primary

857-350-4834

Marinella Clerico, MD

Role: primary

857-350-4834

Stefania Morino, MD

Role: primary

857-350-4834

Girolama Alessandra Marfia, MD

Role: primary

857-350-4834

Claudia Cutellè, MD

Role: primary

857-350-4834

Yuji Tomizawa, MD

Role: primary

857-350-4834

Sonoko Misawa, MD

Role: primary

857-350-4834

Kazumoto Shibuya, MD

Role: primary

857-350-4834

Tomoko Okamoto, MD

Role: primary

857-350-4834

Yuki Fukami, MD

Role: primary

857-350-4834

Masayuki Nakamori, MD

Role: primary

857-350-4834

Viktorija Kenina, MD

Role: primary

857-350-4834

Kestutis Petrikonis, MD

Role: primary

857-350-4834

Filip Eftimov, MD

Role: primary

857-350-4834

Angelina Maniaol, MD

Role: primary

857-350-4834

Lukasz Rzepinski, MD

Role: primary

857-350-4834

Marek Smilowski, MD

Role: primary

857-350-4834

Agnieszka Slowik, MD

Role: primary

857-350-4834

Urszula Chyrchel-Paszkiewicz, MD

Role: primary

857-350-4834

Anna Kostera-Pruszczyk, MD

Role: primary

857-350-4834

Ernestina Santos, MD

Role: primary

857-350-4834

Stojan Peric, MD

Role: primary

857-350-4834

Ivan Martinka, MD

Role: primary

857-350-4834

Monika Turcanova Koprusakova, MD

Role: primary

857-350-4834

Blaz Koritnik, MD

Role: primary

857-350-4834

Carmen Diaz Marin, MD

Role: primary

857-350-4834

Giuseppe Lucente, MD

Role: primary

857-350-4834

Raúl Juntas Morales, MD

Role: primary

857-350-4834

Luis Querol, MD

Role: primary

857-350-4834

Carlos Casasnovas Pons, MD

Role: primary

857-350-4834

Lucia Galan Davila, MD

Role: primary

857-350-4834

Solange Kapetanovic, MD

Role: primary

857-350-4834

Jesus Romero Imbroda, MD

Role: primary

857-350-4834

Roberto Fernandez Torron, MD

Role: primary

857-350-4834

Robert Hoepner, MD

Role: primary

857-350-4834

Kathryn Brennan, MD

Role: primary

857-350-4834

Simon Rinaldi, MD

Role: primary

857-350-4834

Ryan Keh, MD

Role: primary

857-350-4834

Simon Shields, MD

Role: primary

857-350-4834

Other Identifiers

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2024-516473-72-00

Identifier Type: CTIS

Identifier Source: secondary_id

ARGX-117-2302

Identifier Type: -

Identifier Source: org_study_id

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