A Study to Assess the Efficacy and Safety of ITI-1284 in the Treatment of Agitation Associated With Alzheimer's Dementia

NCT ID: NCT06651567

Last Updated: 2026-01-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

320 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-10-22

Study Completion Date

2027-11-30

Brief Summary

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This is a multicenter, randomized, double-blind, placebo-controlled, flexible-dose study of the efficacy, safety, and tolerability of ITI-1284 in patients with agitation associated with Alzheimer's dementia

Detailed Description

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The study will be conducted in 3 periods:

* Screening Period (up to 4 weeks) during which patient eligibility will be assessed;
* Double-blind Treatment Period (12 weeks) during which all patients will be randomized in a 1:1 ratio to receive either ITI-1284 or placebo;
* Safety Follow-up Period (30 days) during which all patients will return for a safety follow-up visit approximately 30 days after the last dose of study drug.

Conditions

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Agitation Associated With Alzheimer's Dementia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ITI-1284

ITI-1284 10 mg or 20 mg rapidly disintegrating tablet, taken once daily, sublingual administration

Group Type EXPERIMENTAL

ITI-1284

Intervention Type DRUG

ITI-1284 10 mg or 20 mg rapidly disintegrating tablet, taken once daily, sublingual administration

Placebo

Placebo rapidly disintegrating tablet, taken once daily, sublingual administration

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo rapidly disintegrating tablet, taken once daily, sublingual administration

Interventions

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ITI-1284

ITI-1284 10 mg or 20 mg rapidly disintegrating tablet, taken once daily, sublingual administration

Intervention Type DRUG

Placebo

Placebo rapidly disintegrating tablet, taken once daily, sublingual administration

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Can understand the nature of the trial and protocol requirements and provide signed informed consent, if in the judgement of the Investigator is deemed competent to provide consent or if patient is deemed not competent to provide informed consent, with the patient's assent (if capable), consent may be provided by an appropriate person (eg, patient's Legally Authorized Representative \[LAR\]) before the initiation of any study-specific procedures in accordance with local regulations;
* Meets clinical criteria for Alzheimer's disease based on 2011 National Institute of Aging-Alzheimer's Association (NIA-AA) dementia criteria and biomarker criteria and either:

* Has a high likelihood for amyloid pathology consistent with Alzheimer's disease, as confirmed by blood-based biomarker at Screening; or
* Has historical documentation of cerebrospinal fluid (CSF) biomarker or amyloid positron emission tomography (PET) brain scan;
* Meets all criteria for agitation according to the International Psychogeriatric Association (IPA) consensus definition
* Has clinically meaningful agitation defined as a Neuropsychiatric Inventory-Agitation/Aggression (NPI-AA) domain total score of ≥ 4 at both Screening and Baseline;
* CGI-S score ≥ 4 at Screening and Baseline;
* Has Mini-Mental State Examination, 2nd Edition™: Standard Version (MMSE-2®:SV) score of 6 to 24 at Screening;

Exclusion Criteria

* Agitation symptoms are attributable to concomitant medications, adverse environmental conditions, substance abuse, or active medical or psychiatric conditions as per Investigator's judgment;
* Has been diagnosed with one or more of the following psychiatric conditions:

* Schizophrenia, schizoaffective disorder, or other psychotic disorder that is not related to Alzheimer's dementia;
* Bipolar disorder;
* Major depressive disorder, unless it is considered stable and treated for at least 8 weeks prior to Screening;
* Has a significant risk for suicidal behavior during the course of their participation in the study, or is considered to be an imminent danger to themselves or others, in the opinion of the investigator, and/or as assessed by Columbia Suicide Severity Rating Scale (C-SSRS); or the patient has had 1 or more suicide attempts within the 2 years prior to Screening;
* The patient has known hypersensitivity or intolerance to ITI-1284 or lumateperone, or to any of their excipients.
Minimum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Intra-Cellular Therapies, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Clinical Site

Anaheim, California, United States

Site Status RECRUITING

Clinical Site

Costa Mesa, California, United States

Site Status RECRUITING

Clinical Site

Garden Grove, California, United States

Site Status RECRUITING

Clinical Site

Boca Raton, Florida, United States

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Clinical Site

Bonita Springs, Florida, United States

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Clinical Site

Brandon, Florida, United States

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Clinical Site

Delray Beach, Florida, United States

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Clinical Site

Doral, Florida, United States

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Clinical Site

Hialeah, Florida, United States

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Clinical Site

Homestead, Florida, United States

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Clinical Site_2

Maitland, Florida, United States

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Clinical Site

Maitland, Florida, United States

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Clinical Site

Miami, Florida, United States

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Clinical Site_2

Miami, Florida, United States

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Clinical Site_3

Miami, Florida, United States

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Clinical Site

Miami, Florida, United States

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Clinical Site

Miami, Florida, United States

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Clinical Site

Miami, Florida, United States

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Clinical Site

Miami, Florida, United States

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Clinical Site

Miami, Florida, United States

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Clinical Site

Orlando, Florida, United States

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Clinical Site

Orlando, Florida, United States

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Clinical Site_2

Tampa, Florida, United States

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Clinical Site

Tampa, Florida, United States

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Clinical Site

West Palm Beach, Florida, United States

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Clinical Site

Boston, Massachusetts, United States

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Clinical Site

Las Vegas, Nevada, United States

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Clinical Site

Toms River, New Jersey, United States

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Clinical Site

Raleigh, North Carolina, United States

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Clinical Site

San Antonio, Texas, United States

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Clinical Site

Lovech, , Bulgaria

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Clinical Site

Pleven, , Bulgaria

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Clinical Site

Sofia, , Bulgaria

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Clinical Site

Sofia, , Bulgaria

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Clinical Site

Sofia, , Bulgaria

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Clinical Site

Sofia, , Bulgaria

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Clinical Site

Stara Zagora, , Bulgaria

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Clinical Site_2

Zagreb, , Croatia

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Clinical Site_3

Zagreb, , Croatia

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Clinical Site

Zagreb, , Croatia

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Clinical Site

Zagreb, , Croatia

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Clinical Site

Brno, , Czechia

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Clinical Site

Choceň, , Czechia

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Clinical Site

Kutná Hora, , Czechia

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Clinical Site

Pilsen, , Czechia

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Clinical Site

Prague, , Czechia

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Prague, , Czechia

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Clinical Site

Bucharest, , Romania

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Bucharest, , Romania

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Bucharest, , Romania

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Bucharest, , Romania

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Clinical Site

Sânpetru, , Romania

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Clinical Site

Sibiu, , Romania

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Clinical Site_2

Belgrade, , Serbia

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Clinical Site

Belgrade, , Serbia

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Clinical Site

Kovin, , Serbia

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Clinical Site

Niš, , Serbia

Site Status RECRUITING

Clinical Site

Novi Kneževac, , Serbia

Site Status RECRUITING

Clinical Site

Banská Bystrica, , Slovakia

Site Status RECRUITING

Clinical Site

Bratislava, , Slovakia

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Clinical Site

Košice, , Slovakia

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Clinical Site

Krompachy, , Slovakia

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Clinical Site

Svidník, , Slovakia

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Clinical Site

Vranov nad Topľou, , Slovakia

Site Status RECRUITING

Clinical Site

Albacete, , Spain

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Clinical Site

Barcelona, , Spain

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Clinical Site

Málaga, , Spain

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Clinical Site

Zamora, , Spain

Site Status RECRUITING

Clinical Site

Zaragoza, , Spain

Site Status RECRUITING

Countries

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United States Bulgaria Croatia Czechia Romania Serbia Slovakia Spain

Central Contacts

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ITI Clinical Trials

Role: CONTACT

646-440-9333

Other Identifiers

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ITI-1284-101

Identifier Type: -

Identifier Source: org_study_id

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