Safety and Efficacy of CAR T Cell Therapy in Patients with R/r B-ALL

NCT ID: NCT06635330

Last Updated: 2024-10-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

5 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-05-20

Study Completion Date

2027-09-22

Brief Summary

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The goal of this clinical trial is to evaluate the safety and efficacy of CD19 CAR-T cells in pediatric patients of all genders, aged 2 to 18 years, with relapsing or refractory B cell acute lymphoblastic leukemia (r/r B-ALL). The main questions it aims to answer are as following:

1. What is the percentage of patients with overall remission rate (ORR) of complete response (CR) or complete remission with incomplete blood count recovery (CRi)?
2. What is the rate of Event-free survival at first month and 2-3 months after intervention?
3. What is the rate of Overall survival at first month and at 3 months after the intervention?

Detailed Description

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B-cell acute lymphoblastic leukemia (B-ALL), as the most common type of pediatric tumor, is identified by unregulated cell proliferation of immature lymphoid cells that can infiltrate the bone marrow and blood. Also, relapse and refractory B-ALL (R/R B-ALL) is the main reason of global mortality due to the constraints of combination chemotherapy.

Over the past few years, substantial advancements have been made in treatment of ALL, specifically in the R/R context. Chimeric antigen receptor T (CAR-T) cells are a type of cancer immunotherapy treatment that function through modification of patient T cells to express CAR antigen on their surface. CAR-T cells aimed at CD19 have demonstrated promising activity in treatment of r/r B-ALL. In this study we aim to evaluate safety and efficacy of Anti-CD19 CAR T cell therapy in children with R/R B-ALL.

Conditions

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Relapse/Refractory B-cell Acute Lymphoblastic Leukemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Anti-CD19 CAR-T treatment group

Group Type EXPERIMENTAL

anti-CD19 CAR T cell therapy

Intervention Type BIOLOGICAL

Anti-CD19 CAR-T cell therapy for R/R B-ALL pediatric patients. For patients 50 kg and less: 0.2 to 5 in ten to the power of six live CAR+ T cells per kilogram of body weight/ For patients over 50 kg: 0.1 to 2.5 in ten to the power of eight live CAR+ T cells (without considering weight).

Interventions

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anti-CD19 CAR T cell therapy

Anti-CD19 CAR-T cell therapy for R/R B-ALL pediatric patients. For patients 50 kg and less: 0.2 to 5 in ten to the power of six live CAR+ T cells per kilogram of body weight/ For patients over 50 kg: 0.1 to 2.5 in ten to the power of eight live CAR+ T cells (without considering weight).

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Ages 2 to 18 years with relapsed or refractory CD19+ B-ALL
* Presence of disease in the bone marrow
* Able to tolerate the apheresis process
* Life expectancy \> 12 weeks
* Lansky or Karnofsky score \> 50%
* At least 7 days passed since the last chemotherapy and the last treatment with corticosteroids
* Informed consent
* Having potential donor for stem cell transplantation

Exclusion Criteria

* Presence of active malignancy other than the disease under study
* Chloroma and leukemic infiltration on MRI or significant neurological symptoms
* Any CNS disorder
* Presence of active GVHD
* Radiation therapy within last 14 days
* History of Anti-CD19 or Anti-CD20 therapy
* Donor lymphocyte injection or other cell therapy methods within the last 30 days
* Presence of severe active infection
* Organ dysfunction
Minimum Eligible Age

2 Years

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Kara Yakhteh Tajhiz Azma Company

NETWORK

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Pediatric cell and gene therapy research center, Children medical center

Tehran, Tehran Province, Iran

Site Status RECRUITING

Countries

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Iran

Central Contacts

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Setayesh Sadeghi

Role: CONTACT

+989124779968

Facility Contacts

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Amir Ali Hamidieh

Role: primary

+989121593270

Other Identifiers

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IR.NREC.1403.003

Identifier Type: -

Identifier Source: org_study_id

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