An Efficacy, Safety, and Tolerability Study of VRDN-003 in Participants With Active Thyroid Eye Disease (TED)

NCT ID: NCT06625411

Last Updated: 2025-09-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

117 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-08-27

Study Completion Date

2026-11-15

Brief Summary

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This is a clinical trial assessing the efficacy, safety, and tolerability of an investigational drug, VRDN-003, in participants with active Thyroid Eye Disease (TED).

Detailed Description

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This is a randomized (meaning participants will be assigned to study arms by chance), double-masked (meaning study doctor and participant will not know which study arm participant is assigned to), placebo-controlled study that will include participants with active TED. The key objectives of this study are to determine if VRDN-003 is efficacious, safe and tolerable when administered as a series of subcutaneous/SC injections given every 4 weeks or every 8 weeks compared to placebo in participants with active TED.

Participants who do not have a meaningful response at Week 24 (irrespective of the initial treatment arm) may be eligible to receive additional subcutaneous injections of VRDN-003.

Conditions

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Thyroid Eye Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Participants will be randomized to one of the three study arms.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Participants, Investigator, Outcomes Assessor and Sponsor will be masked.

Study Groups

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VRDN-003 every 4 weeks

6 subcutaneous administrations of VRDN-003

Group Type EXPERIMENTAL

VRDN-003

Intervention Type DRUG

VRDN-003 is an investigational, subcutaneously administered, humanized monoclonal antibody directed against the Insulin-like Growth Factor-1 receptor (IGF-1R).

VRDN-003 every 8 weeks

3 subcutaneous administrations of VRDN-003 and 3 subcutaneous administrations of placebo

Group Type EXPERIMENTAL

VRDN-003

Intervention Type DRUG

VRDN-003 is an investigational, subcutaneously administered, humanized monoclonal antibody directed against the Insulin-like Growth Factor-1 receptor (IGF-1R).

Placebo

Intervention Type DRUG

All participants will receive the same number of injections to maintain masking. Masking will be maintained by the use of placebo injections that appear identical to VRDN-003 injections.

Placebo every 4 weeks

6 subcutaneous administrations of placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

All participants will receive the same number of injections to maintain masking. Masking will be maintained by the use of placebo injections that appear identical to VRDN-003 injections.

Interventions

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VRDN-003

VRDN-003 is an investigational, subcutaneously administered, humanized monoclonal antibody directed against the Insulin-like Growth Factor-1 receptor (IGF-1R).

Intervention Type DRUG

Placebo

All participants will receive the same number of injections to maintain masking. Masking will be maintained by the use of placebo injections that appear identical to VRDN-003 injections.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Must have moderate to severe active TED with documented evidence of ocular symptoms or signs that began within 15 months prior to screening
* Must have a Clinical Activity Score (CAS) of ≥ 3 on the 7-item scale for the study eye
* Must agree to use highly effective contraception as specified in the protocol
* Female TED participants must have a negative serum pregnancy test at screening

Exclusion Criteria

* Must not have received prior treatment with another anti-IGF-1R therapy
* Must not have received systemic corticosteroids or steroid eye drops for any condition, including TED, or selenium within 2 weeks prior to first dose
* Must not have received other immunosuppressive drugs for any condition, including TED, or any other therapy for TED within 12 weeks prior to first dose.
* Must not have received an investigational agent for any condition, including TED, within 8 weeks or longer duration (depending on the type of investigational agent) prior to first dose
* Must not have received radioactive iodine (RAI) treatment within 8 weeks prior to first dose
* Must not have had previous orbital irradiation or decompression surgery for TED to the study eye's orbit
* Must not have a pre-existing ophthalmic condition in the study eye which in the study doctor's opinion, would interfere with interpretation of study results
* Must not have abnormal hearing test before first dose. Must also not have a history of ear conditions considered significant by study doctor
* Must not have a history of inflammatory bowel disease
* Female TED participants who must not be pregnant or breastfeeding

NOTE: There are additional eligibility criteria for participants who do not have a meaningful response at Week 24 (irrespective of initial treatment arm) who may receive additional injections of VRDN-003. These are described in the protocol.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Viridian Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Scottsdale Clinical Trials

Scottsdale, Arizona, United States

Site Status

Alliance Research Institute - Canoga Park

Canoga Park, California, United States

Site Status

Marvel Clinical Research

Huntington Beach, California, United States

Site Status

United Medical Research Institute

Inglewood, California, United States

Site Status

Advancing Research International, LLC

Los Angeles, California, United States

Site Status

Roski Eye Institute, Keck School of Medicine, USC

Los Angeles, California, United States

Site Status

Alliance Research Institute - Lynwood

Lynwood, California, United States

Site Status

A.P.J. Office

Newport Beach, California, United States

Site Status

Byers Eye Institute at Stanford University

Palo Alto, California, United States

Site Status

Pasadena Clinical Trials

Pasadena, California, United States

Site Status

Senta Clinic

San Diego, California, United States

Site Status

C&A Clinical Trials Corp

Cape Coral, Florida, United States

Site Status

Ilumina Medical Research

Kissimmee, Florida, United States

Site Status

Med-Care Research

Miami, Florida, United States

Site Status

Continental Clinical Research

Miami, Florida, United States

Site Status

Hype Clinical Research LLC

Miami, Florida, United States

Site Status

Anmed Health Services LLC

Miami, Florida, United States

Site Status

Sarasota Retina Institute

Sarasota, Florida, United States

Site Status

Agile Clinical Research Trials, LLC

Atlanta, Georgia, United States

Site Status

Vision Medical Research

Orland Park, Illinois, United States

Site Status

Opthalmic Consultants of Boston

East Weymouth, Massachusetts, United States

Site Status

Fraser Eye Care Center

Fraser, Michigan, United States

Site Status

Kahana Oculoplastic & Orbital Surgery

Livonia, Michigan, United States

Site Status

University Health

Kansas City, Missouri, United States

Site Status

S.L. Office

Las Vegas, Nevada, United States

Site Status

Vector Clinical Trials

Sparks, Nevada, United States

Site Status

Rutgers New Jersey Medical School

Newark, New Jersey, United States

Site Status

Asheville Clinical Research

Asheville, North Carolina, United States

Site Status

Duke Eye Center

Durham, North Carolina, United States

Site Status

Baylor College of Medicine/Alkek Eye Center

Houston, Texas, United States

Site Status

Gulf Coast Clinical Trials

Houston, Texas, United States

Site Status

Neuro-Eye Clinical Trials

Houston, Texas, United States

Site Status

University of Washington, Eye institute

Seattle, Washington, United States

Site Status

West Virginia University Eye Institute

Morgantown, West Virginia, United States

Site Status

Countries

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United States

Other Identifiers

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VRDN-003-301

Identifier Type: -

Identifier Source: org_study_id

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