A Safety and Tolerability Study of VRDN-003 in Participants With Thyroid Eye Disease (TED)

NCT ID: NCT06812325

Last Updated: 2025-12-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

321 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-02-03

Study Completion Date

2026-10-31

Brief Summary

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This is a clinical trial assessing the safety and tolerability of an investigational drug, VRDN-003, in participants with Thyroid Eye Disease (TED).

Detailed Description

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This is a randomized (meaning participants will be assigned to study arms by chance), double-masked (meaning study doctor and participant will not know which study arm participant is assigned to), controlled study that will include participants with TED of any duration. The key objectives of this study are to determine if VRDN-003 is safe and tolerable when administered as a series of subcutaneous (SC) injections every 4 weeks or every 8 weeks in participants with TED.

Conditions

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Thyroid Eye Disease (TED)

Keywords

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Graves Thyroid Eye Disease Thyroid-Associated Ophthalmopathy Dysthyroid Ophthalmopathy Graves Eye Disease Graves Orbitopathy Myopathic Ophthalmopathy Congestive Ophthalmopathy Edematous Ophthalmopathy Infiltrative Ophthalmopathy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Participants will be randomized to one of the two study arms.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Participant, Site personnel (except pharmacy personnel preparing the injection), and Sponsor are masked.

Study Groups

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VRDN-003 every 4 weeks

6 subcutaneous administrations of VRDN-003

Group Type EXPERIMENTAL

VRDN-003

Intervention Type DRUG

VRDN-003 is an investigational, subcutaneously administered, humanized monoclonal antibody directed against the Insulin-like Growth Factor-1 receptor (IGF-1R).

VRDN-003 every 8 weeks

3 subcutaneous administrations of VRDN-003 and 3 subcutaneous administrations of placebo

Group Type EXPERIMENTAL

VRDN-003

Intervention Type DRUG

VRDN-003 is an investigational, subcutaneously administered, humanized monoclonal antibody directed against the Insulin-like Growth Factor-1 receptor (IGF-1R).

Placebo

Intervention Type DRUG

Placebo injections that appear identical to VRDN-003 injections but have no active drug.

Interventions

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VRDN-003

VRDN-003 is an investigational, subcutaneously administered, humanized monoclonal antibody directed against the Insulin-like Growth Factor-1 receptor (IGF-1R).

Intervention Type DRUG

Placebo

Placebo injections that appear identical to VRDN-003 injections but have no active drug.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Have a clinical diagnosis of TED with or without proptosis and with any CAS (0-7) and in the opinion of the Investigator may benefit from VRDN-003
* Not require immediate ophthalmological or orbital surgery in the study eye for any reason.
* Must agree to use highly effective contraception as specified in the protocol
* Female TED participants must have a negative serum pregnancy test at screening

Exclusion Criteria

* Must not have received prior treatment with another anti-IGF-1R therapy
* Must not have received systemic corticosteroids or steroid eye drops for any condition, including TED, or selenium within 2 weeks prior to first dose.
* Must not have received other immunosuppressive drugs for any condition, including TED, or any other therapy for TED within 12 weeks prior to first dose
* Must not have received an investigational agent for any condition, including TED, within 8 weeks or longer duration (depending on the type of investigational agent) prior to first dose
* Must not have received radioactive iodine (RAI) treatment within 8 weeks prior to first dose
* Must not have had previous orbital irradiation or decompression surgery for TED to the study eye's orbit
* Must not have a pre-existing ophthalmic condition in the study eye which in the study doctor's opinion, would interfere with interpretation of study results
* Must not have abnormal hearing test before first dose. Must also not have a history of ear conditions considered significant by study doctor
* Must not have a history of inflammatory bowel disease
* Female TED participants must not be pregnant or breastfeeding
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Viridian Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Catalina Eye Care

Tuscon, Arizona, United States

Site Status

United Medical Research Institute

Inglewood, California, United States

Site Status

Orbital Plastics

Newport Beach, California, United States

Site Status

California Eye Specialists Medical Group INC

Pasadena, California, United States

Site Status

FOMAT Medical Research

Pismo Beach, California, United States

Site Status

Pacific Neuroscience Institute

Santa Monica, California, United States

Site Status

Pacific Neuroscience Institute at Saint John's Physician Partners

Torrance, California, United States

Site Status

C A Clinical Trial Corp.

Cape Coral, Florida, United States

Site Status

Herco Medical and Research Center

Coral Gables, Florida, United States

Site Status

Alfa Medical Research

Davie, Florida, United States

Site Status

D H Doral Research Center

Doral, Florida, United States

Site Status

Eye Centers of Florida

Fort Myers, Florida, United States

Site Status

Sina Medical Center

Homestead, Florida, United States

Site Status

East Coast Institute for Research, LLC

Jacksonville, Florida, United States

Site Status

Southern Clinical Research LLC

Miami, Florida, United States

Site Status

Retreat Medical Research

Miami, Florida, United States

Site Status

Continental Clinical Research

Miami, Florida, United States

Site Status

Edward Jenner Research Group LLC

Plantation, Florida, United States

Site Status

Sarasota Retina Institute

Sarasota, Florida, United States

Site Status

Advanced Quality Medical Research

Orland Park, Illinois, United States

Site Status

Ophthalmic Consultants of Boston

East Weymouth, Massachusetts, United States

Site Status

Fraser Eye Care Center

Fraser, Michigan, United States

Site Status

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status

University of Missouri Kansas City

Kansas City, Missouri, United States

Site Status

Rutgers New Jersey Medical School

Newark, New Jersey, United States

Site Status

Jackson Clinic

Jackson, Tennessee, United States

Site Status

DFW Clinical Trials

Carrollton, Texas, United States

Site Status

Neuro Eye Clinical Trials

Houston, Texas, United States

Site Status

Pioneer Research Solutions Inc.

Houston, Texas, United States

Site Status

San Antonio Clinical Trials

San Antonio, Texas, United States

Site Status

Eyeplastx

San Antonio, Texas, United States

Site Status

Elevate Clinical Research

Seabrook, Texas, United States

Site Status

Servicde d'Endocrinologie, Diabetologieet Nutrition Centre Hospitalier Universitaire d'Angers

Angers, , France

Site Status

Abeillon du Payrat

Bron, , France

Site Status

Hôpital La Pitiélsalpêtrière

Paris, , France

Site Status

Charite Universitatsmeizin Berlin KoR Campus Virchow Klinikum

Berlin, , Germany

Site Status

Universitatsklinikum Essen

Essen, , Germany

Site Status

Universitaetsmedizin Goettingen

Göttingen, , Germany

Site Status

Johannes Gutenberg University Medical Center Department of Medicine 1

Mainz, , Germany

Site Status

Uniwersytecki Szpital Kliniczny w Białymstoku, Klinika Okulistyki, Centrum Badań Klinicznych

Bialystok, , Poland

Site Status

Optimum Profesorskie Centrum Okulistyki Sp. z o. o.

Gdansk, , Poland

Site Status

Centrum Medyczne Pratia Gdynia

Gdynia, , Poland

Site Status

Santa Familia PTG Lodz

Lodz, , Poland

Site Status

ETG Lublin

Lublin, , Poland

Site Status

Centrum Medyczne Pulawska Sp. z o.o.

Piaseczno, , Poland

Site Status

Warszawski Szpital Okulistyczny

Warsaw, , Poland

Site Status

Polimedica PTG

Warsaw, , Poland

Site Status

Hospital Provincial de Conxo

A Coruña, , Spain

Site Status

Institut Català de Retina

Barcelona, , Spain

Site Status

Hospital La Arruzafa

Córdoba, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Clinica Universidad de Navarre

Navarrés, , Spain

Site Status

Hospital Universitario Virgen Macarena

Seville, , Spain

Site Status

Hospital Universitario Miguel Servet Consultas de Oftalmologia

Zaragoza, , Spain

Site Status

Gazi University Medical Faculty Hospital

Ankara, , Turkey (Türkiye)

Site Status

Hacettepe Univeristy Medical Fculty Hospital

Ankara, , Turkey (Türkiye)

Site Status

Akdeniz Üniversitesi Tıp Fakültesi Göz Hastalıkları Anabilim Dalı

Antalya, , Turkey (Türkiye)

Site Status

Marmara Üniversitesi Pendik Eğitim ve Araştırma Hastanesi Göz Hastalıkları Kliniği

Istanbul, , Turkey (Türkiye)

Site Status

University Hospitals Bristol and Weston NHS Foundation Trust Clinical Research Unit

Bristol, , United Kingdom

Site Status

Addenbrookes Hospital

Cambridge, , United Kingdom

Site Status

Imperial College Healthcare NHS Trust

London, , United Kingdom

Site Status

Guy's and St Thomas' NHS Foundation Trust

London, , United Kingdom

Site Status

Moorefields Eye Hospital NHS Foundation Trust

London, , United Kingdom

Site Status

The Newcastle Upon Tyne Hospitals NHS Foundation Trust

Newcastle, , United Kingdom

Site Status

Countries

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United States France Germany Poland Spain Turkey (Türkiye) United Kingdom

Other Identifiers

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VRDN-003-303

Identifier Type: -

Identifier Source: org_study_id