Ivosidenib in Locally Advanced or Metastatic Cholangiocarcinoma With IDH1 R132 Mutation After at Least One Prior Systemic Treatment - an Observational Study

NCT ID: NCT06607302

Last Updated: 2025-11-26

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Total Enrollment

100 participants

Study Classification

OBSERVATIONAL

Study Start Date

2024-10-08

Study Completion Date

2027-12-31

Brief Summary

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Cholangiocarcinoma is a rare and aggressive tumor of the bile duct associated with a poor prognosis and very limited treatment options. The IDH1 inhibitor ivosidenib provides a new, targeted treatment option for this disease. Ivosidenib was approved by European Medicines Agency (EMA) in May 2023 as monotherapy in adult patients with locally advanced or metastatic cholangiocarcinoma with an IDH1 R132 mutation who were previously treated by at least one prior line of systemic therapy.

The prospective, multicenter, observational study IDHIRA will collect first real-world data on ivosidenib treatment in a broad patient population in Germany. Ivosidenib will be administered according to the current SmPC. Thus, IDHIRA will generate real-world evidence on effectiveness, quality of life (QoL) and safety of ivosidenib.

Detailed Description

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Conditions

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Cholangiocarcinoma

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Eligibility Criteria

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Inclusion Criteria

* Age 18 years or older.
* Histologically confirmed locally advanced or metastatic CCC with a documented IDH1 R132 mutation diagnosed by an appropriate diagnostic test
* Patients must have at least one prior systemic therapy
* Decision for treatment with ivosidenib according to current SmPC.
* Signed written informed consent before or within 6 weeks of first ivosidenib dose (inclusion of patients up to 6 weeks after first ivosidenib intake is allowed for patients not participating in the PRO module)
* For patients participating in the PRO module (optional):

* Dated signature of informed consent form before start of study treatment.
* Willingness and capability to participate in PRO assessment in German language.
* Other criteria according to current SmPC.

Exclusion Criteria

* Participation in an interventional clinical trial within 30 days prior to enrolment or concurrent participation in an interventional clinical trial except for the follow-up period.
* Other contraindications according to current SmPC.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Servier Deutschland GmbH

INDUSTRY

Sponsor Role collaborator

iOMEDICO AG

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Hämatologisch-Onkologische Schwerpunktpraxis in Bad Liebenwerda

Bad Liebenwerda, , Germany

Site Status RECRUITING

Caritas Krankenhaus Bad Mergentheim

Bad Mergentheim, , Germany

Site Status RECRUITING

Onkologisches Versorgungszentrum Berlin MVZ

Berlin, , Germany

Site Status RECRUITING

Onkologie Hannover

Hanover, , Germany

Site Status RECRUITING

Onkologie Hof

Hof, , Germany

Site Status RECRUITING

Medizinisches Versorgungszentrum Mönchengladbach

Mönchengladbach, , Germany

Site Status RECRUITING

ze:roPRAXEN MVZ für Innere Medizin

Weinheim, , Germany

Site Status RECRUITING

Countries

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Germany

Central Contacts

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Sina Grebhardt, PhD

Role: CONTACT

+49 761 15 242 31

Facility Contacts

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Stephan Kreher, PD Dr. med.

Role: primary

Matthias Raab, Dr.

Role: primary

Reinhard Musch

Role: primary

Haytham Kamal, Dr. med.

Role: primary

Markus Kapp, Dr. med.

Role: primary

Ludger Sellmann, PD Dr. med.

Role: primary

Manuel Zink, Dr. med.

Role: primary

References

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Michl M, Hagemeyer N, Looss M, Grebhardt S, Ringwald K, Potthoff K. IDHIRA: a prospective, observational study on ivosidenib in patients with IDH1 R132-mutated advanced cholangiocarcinoma. Future Oncol. 2025 Apr;21(9):1057-1064. doi: 10.1080/14796694.2025.2470609. Epub 2025 Mar 3.

Reference Type DERIVED
PMID: 40028796 (View on PubMed)

Other Identifiers

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iOM-040498

Identifier Type: -

Identifier Source: org_study_id

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