A Study to Evaluate the Efficacy and Safety of Oral HRS-5965 in Adult Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients Who Are Naive to Complement Inhibitor Therapy

NCT ID: NCT06593938

Last Updated: 2025-09-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

76 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-10-25

Study Completion Date

2025-07-31

Brief Summary

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A study of the efficacy and safety of HRS-5965 capsules compared to eculizumab for 24 weeks in patients with PNH.

Detailed Description

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Conditions

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Paroxysmal Nocturnal Hemoglobinuria

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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HRS-5965 capsule

Group Type EXPERIMENTAL

HRS-5965 capsule

Intervention Type DRUG

HRS-5965 capsule for 24 weeks

Eculizumab Injection

Group Type EXPERIMENTAL

Eculizumab Injection

Intervention Type DRUG

Eculizumab Injection for 24 weeks

Interventions

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HRS-5965 capsule

HRS-5965 capsule for 24 weeks

Intervention Type DRUG

Eculizumab Injection

Eculizumab Injection for 24 weeks

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Diagnosis of PNH confirmed by flow cytometry with clone size \> 10%.
2. Have not received complement inhibitor therapy;
3. LDH \> 1.5\*ULN at screening.
4. Hemoglobin level \< 10 g/dL at screening.

Exclusion Criteria

1. Known or suspected hereditary or acquired complement deficiency;
2. Patients with laboratory evidence of bone marrow failure (reticulocytes \<100x109/L; platelets \<30x109/L; neutrophils \<0.5x109/L);
3. Presence or suspicion of a systemic active bacterial, viral, or fungal infection (based on judgment of the investigator) within 2 weeks prior to the first dose of HRS-5965;
4. History of infection with capsular bacteria (e.g., meningococcus, pneumococcus, etc.)
5. Positive of HIV, HBsAg or HCVAb.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Chengdu Suncadia Medicine Co., Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Peking Union Medical College Hospital, Chinese Academy of Medical Sciences

Beijing, Beijing Municipality, China

Site Status

The Blood Disease Hospital of the Chinese Academy of Medical Sciences

Tianjin, Tianjin Municipality, China

Site Status

Countries

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China

Other Identifiers

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HRS-5965-301

Identifier Type: -

Identifier Source: org_study_id

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