EF-41/KEYNOTE D58: Phase 3 Study of Optune Concomitant With Temozolomide Plus Pembrolizumab in Newly Diagnosed Glioblastoma

NCT ID: NCT06556563

Last Updated: 2026-01-21

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

741 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-02-03

Study Completion Date

2029-04-30

Brief Summary

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This is a multicenter, two-arm, randomized, double-blind, placebo-controlled study of Optune® (Tumor Treating Fields at 200 kHz) together with maintenance Temozolomide (TMZ) chemotherapy agent and pembrolizumab compared to Optune® together with maintenance TMZ and placebo in newly diagnosed Glioblastoma (GBM) patients. The primary objective of the study is to evaluate the Overall Survival (OS).

Detailed Description

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Conditions

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Glioblastoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

The participants in the study will be randomized in a ratio of 2:1 in favor of the treatment group to one of the following groups:

Treatment Group - Optune concomitant with maintenance TMZ and pembrolizumab.

Control Group - Optune concomitant with maintenance TMZ and placebo.
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Treatment Group

Group Type EXPERIMENTAL

Optune® device

Intervention Type DEVICE

Optune® device delivering TTFields therapy at 200 kHz.

Temozolomide

Intervention Type DRUG

Temozolomide per approved labeling.

Pembrolizumab

Intervention Type DRUG

Pembrolizumab dose throughout this study is 200 mg IV Q3W for a maximum of 35 cycles.

Control Group

Group Type PLACEBO_COMPARATOR

Optune® device

Intervention Type DEVICE

Optune® device delivering TTFields therapy at 200 kHz.

Temozolomide

Intervention Type DRUG

Temozolomide per approved labeling.

Placebo

Intervention Type DRUG

Placebo (saline solution) dose throughout this study is 200 mg IV Q3W for a maximum of 35 cycles.

Interventions

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Optune® device

Optune® device delivering TTFields therapy at 200 kHz.

Intervention Type DEVICE

Temozolomide

Temozolomide per approved labeling.

Intervention Type DRUG

Pembrolizumab

Pembrolizumab dose throughout this study is 200 mg IV Q3W for a maximum of 35 cycles.

Intervention Type DRUG

Placebo

Placebo (saline solution) dose throughout this study is 200 mg IV Q3W for a maximum of 35 cycles.

Intervention Type DRUG

Other Intervention Names

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TTFields

Eligibility Criteria

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Inclusion Criteria

1. The participant (or legally acceptable representative) has provided documented informed consent for the study.
2. Be ≥ 18 years of age on day of providing informed consent.
3. Participant with new diagnosis of GBM according to World Health Organization (WHO) 2021 Classification.
4. Recovered from maximal debulking surgery (gross total resection, partial resection and biopsy-only patients are all acceptable), Gliadel wafers placement at the time of surgical resection is not allowed.
5. Have completed standard adjuvant chemoradiotherapy of radiotherapy (RT) according to local practice (56-64 Gy), and concomitant TMZ chemotherapy.
6. Amenable to treatment with Optune concomitant with maintenance TMZ (150-200 mg/m\^2 daily x 5, Q28 days).
7. Have an Eastern Cooperative Oncology Group (ECOG) Performance Status of 0 to 1 assessed within 7 days before randomization.
8. Stable or decreasing dose of corticosteroids (dexamethasone ≤ 2mg or equivalent) for the last 7 days prior to randomization, if applicable.

Exclusion Criteria

1. Has received prior therapy with an anti-Programmed Cell Death 1 (PD-1), anti- Programmed Cell Death-Ligand 1(PD-L1), or anti Programmed Cell Death-Ligand 2 (PD-L2) agent or with an agent directed to another stimulatory or co-inhibitory T-cell receptor (e.g.Cytotoxic T-Lymphocyte-Associated protein 4 (CTLA-4), OX 40, CD137).
2. Ongoing requirement for \>2 mg dexamethasone (or equivalent), due to intracranial mass effect.
3. Has received prior systemic anti-cancer therapy including investigational agents within 4 weeks prior to randomization.
4. Received a live or live-attenuated vaccine within 30 days before the first dose of study intervention. Administration of killed vaccines are allowed.
5. Is currently participating in or has participated in a study of an investigational agent or has used an investigational device within 4 weeks prior to the first study treatment.
6. Has a diagnosis of immunodeficiency or is receiving chronic systemic steroid therapy (in dosing exceeding 10 mg daily of prednisone equivalent) or any other form of immunosuppressive therapy within 7 days prior the first dose of study medication. Has a known additional malignancy that is progressing or has required active treatment within the past 3 years.
7. Has a history of (noninfectious) pneumonitis/interstitial lung disease that required steroids or has current pneumonitis/interstitial lung disease.
8. Early progressive disease after the end of TMZ/RT. If pseudo progression is suspected, additional imaging studies should be performed to rule out true progression.
9. Infratentorial or leptomeningeal disease.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role collaborator

NovoCure GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Mayo Clinic Hospital

Phoenix, Arizona, United States

Site Status RECRUITING

University of Southern California

Los Angeles, California, United States

Site Status RECRUITING

Hoag Memorial Hospital Presbyterian

Newport Beach, California, United States

Site Status RECRUITING

Stanford Cancer Institute

Palo Alto, California, United States

Site Status RECRUITING

UF Health Neuromedicine

Gainesville, Florida, United States

Site Status RECRUITING

Mayo Clinic - Florida

Jacksonville, Florida, United States

Site Status RECRUITING

Miami Cancer Institute

Miami, Florida, United States

Site Status RECRUITING

Moffitt Cancer Center

Tampa, Florida, United States

Site Status RECRUITING

Northwestern Memorial Hospital

Chicago, Illinois, United States

Site Status RECRUITING

University of Kentucky Medical Center

Lexington, Kentucky, United States

Site Status RECRUITING

University of Maryland

Baltimore, Maryland, United States

Site Status RECRUITING

Tufts Medical Center

Boston, Massachusetts, United States

Site Status RECRUITING

Masonic Cancer Center, University of Minnesota

Minneapolis, Minnesota, United States

Site Status RECRUITING

Mayo Clinic - Rochester

Rochester, Minnesota, United States

Site Status RECRUITING

Washington University

St Louis, Missouri, United States

Site Status RECRUITING

John Theurer Cancer Center/ Hackensack Meridian Health

Hackensack, New Jersey, United States

Site Status RECRUITING

Northwell Health

Lake Success, New York, United States

Site Status RECRUITING

Columbia University Irving Medical Center

New York, New York, United States

Site Status RECRUITING

Montefiore Medical Center- Montefiore Medical Park

The Bronx, New York, United States

Site Status RECRUITING

Duke University Medical Center

Durham, North Carolina, United States

Site Status RECRUITING

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status RECRUITING

The Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

Thomas Jefferson University, Sidney Kimmel Comprehensive Cancer Center, Clinical Trials Organization

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status RECRUITING

The University of Texas

Houston, Texas, United States

Site Status RECRUITING

University of Texas, MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Huntsman Cancer Institute, University of Utah

Salt Lake City, Utah, United States

Site Status RECRUITING

Inova Schar Cancer Institute

Fairfax, Virginia, United States

Site Status RECRUITING

Swedish Medical Center

Seattle, Washington, United States

Site Status RECRUITING

Nemocnice Na Homolce

Prague, , Czechia

Site Status RECRUITING

Centre Hospitalier Universitaire de Lyon

Bron, , France

Site Status RECRUITING

Hopital de la Timone

Marseille, , France

Site Status RECRUITING

Hopital Saint-Louis

Paris, , France

Site Status RECRUITING

Groupe Hospitalier Pitie - Salpetriere

Paris, , France

Site Status RECRUITING

Institut Claudius Regaud

Toulouse, , France

Site Status RECRUITING

Charité Campus Virchow-Klinikum

Berlin, , Germany

Site Status RECRUITING

Universitätsklinikum Essen

Essen, , Germany

Site Status RECRUITING

University Hospital Frankfurt

Frankfurt, , Germany

Site Status RECRUITING

Rambam Medical Center

Haifa, , Israel

Site Status RECRUITING

Rabin Medical Center- Beilinson Hospital

Petah Tikva, , Israel

Site Status RECRUITING

Chaim Sheba Medical Center

Ramat Gan, , Israel

Site Status RECRUITING

Tel-Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status RECRUITING

Ospedale Bellaria

Bologna, , Italy

Site Status RECRUITING

Fondazione IRCCS Istituto Neurologico Carlo Besta

Milan, , Italy

Site Status RECRUITING

Ospedale del Mare

Napoli, , Italy

Site Status RECRUITING

UOC Oncologia Medica 1 Istituto Oncologico Veneto IOV-IRCCS

Padua, , Italy

Site Status RECRUITING

IRCCS Istituto Clinico Humanitas

Rozzano, , Italy

Site Status RECRUITING

Kyushu University Hospital

Fukuoka, , Japan

Site Status RECRUITING

Hokkaido University Hospital

Hokkaido, , Japan

Site Status RECRUITING

Kanazawa University Hospital

Ishikawa, , Japan

Site Status RECRUITING

Kumamoto University Hospital

Kumamoto, , Japan

Site Status RECRUITING

Kyoto University Hospital

Kyoto, , Japan

Site Status RECRUITING

Kyorin University Hospital

Mitaka, , Japan

Site Status RECRUITING

Nagoya University Hospital

Nagoya, , Japan

Site Status RECRUITING

Saitama Medical University International Medical Center

Saitama, , Japan

Site Status RECRUITING

Tohoku University Hospital

Sendai, , Japan

Site Status RECRUITING

National Cancer Center Hospital

Tokyo, , Japan

Site Status RECRUITING

Centrum Onkologii

Bydgoszcz, , Poland

Site Status RECRUITING

Narodowy Instytut Onkologii

Gliwice, , Poland

Site Status RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status RECRUITING

Institut Català d'Oncologia de L'Hospitalet (ICO L'Hospitalet)

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status RECRUITING

Hospital Universitario Virgen de las Nieves

Granada, , Spain

Site Status RECRUITING

Hospital Universitario Ramón y Cajal

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status RECRUITING

Hospital Universitari i Politécnic La Fe

Valencia, , Spain

Site Status RECRUITING

University Hospital Basel Medical Oncology

Basel, , Switzerland

Site Status RECRUITING

Centre Hospitalier Universitaire Vaudois (CHUV)

Lausanne, , Switzerland

Site Status RECRUITING

University Hospital Zurich

Zurich, , Switzerland

Site Status RECRUITING

Queen Elizabeth

Birmingham, , United Kingdom

Site Status RECRUITING

Addenbrooke's Hospital (Cambridge University Hospitals NHS Foundation Trust)

Cambridge, , United Kingdom

Site Status RECRUITING

Velindre Cancer Centre

Cardiff, , United Kingdom

Site Status RECRUITING

Western General Hospital

Edinburgh, , United Kingdom

Site Status RECRUITING

The Christie Hospital

Manchester, , United Kingdom

Site Status RECRUITING

Weston Park Hospital

Sheffield, , United Kingdom

Site Status RECRUITING

Southampton General Hospital

Southampton, , United Kingdom

Site Status RECRUITING

Royal Marsden

Sutton, , United Kingdom

Site Status RECRUITING

Countries

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United States Czechia France Germany Israel Italy Japan Poland Spain Switzerland United Kingdom

Central Contacts

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Uz Stammberger

Role: CONTACT

1-877-678-8611

Facility Contacts

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Alyx Porter

Role: primary

480-342-2000

Frances Chow

Role: primary

323-865-3300

Simon Khagi

Role: primary

Role: backup

9199664786

Lawrence Recht

Role: primary

650-498-4686

Ashley Ghiaseddin

Role: primary

Wendy Sherman

Role: primary

904-953-2000

Yazmin Odia

Role: primary

305-595-2141

Patrick Grogan

Role: primary

507-250-5032

Roger Stupp

Role: primary

312-926-9268

John Villano

Role: primary

312-996-6651

Haroon Ahmad

Role: primary

410-706-5875

Suriya Jeyapalan

Role: primary

617-636-2694

Elizabeth Neil

Role: primary

612-625-5317

Ugur Sener

Role: primary

507-284-2511

Omar Butt

Role: primary

314-747-4241

Deric Park

Role: primary

551-996-5230

Samuel Singer

Role: primary

516-941-1260

Fabio Iwamoto

Role: primary

212-342-0571

Adilia Hormigo

Role: primary

718-430-2399

Katherine Peters

Role: primary

919-684-3914

Herbert Newton

Role: primary

216-368-5693

Mark Malkin

Role: primary

216-445-8380

Iyad Alnahhas

Role: primary

215-955-7000

Jan Drappatz

Role: primary

412-864-7791

Eric Wong

Role: primary

401-444-4184

Jay Jiguang Zhu

Role: primary

713-486-8000

Chirag Patel

Role: primary

713-792-0778

Howard Colman

Role: primary

801-585-0255

Adam Cohen

Role: primary

571-472-4724

Mark Loreen

Role: primary

206-320-7121

Josef Vymazal

Role: primary

+420257273200

Francois Ducray

Role: primary

+ 33 4 72 68 13 21

Emeline Tabouret

Role: primary

+33 4 91 38 46 44

Stefania Cuzzubbo

Role: primary

33-(0)1-71-20-74-66 ext. 7467

Khe Hoang-Xuan

Role: primary

(33)1 42 16 0381

Elizabeth Moyal

Role: primary

(+33) 5 31 15 54 45

Martin Misch

Role: primary

49 30 450 660 097

Sied Kebir

Role: primary

004920172383133

Michael Burger

Role: primary

0049-(0)69-6301-87711

Rachel Grossman

Role: primary

+972527360004

Shlomit Yust-Katz

Role: primary

+972587454567

Alisa Talianski

Role: primary

+97235305261

Deborah Blumenthal

Role: primary

(972) 36973494

Enrico Franceschi

Role: primary

05162225697

Antonio Silvani

Role: primary

+0223942440

Bruno Daniele

Role: primary

+39-081-18775340

Giuseppe Lombardi

Role: primary

0498215888

Matteo Simonelli

Role: primary

+39 02 8224 4559

Uz Stammberger

Role: primary

1-877-678-8611

Uz Stammberger

Role: primary

1-877-678-8611

Uz Stammberger

Role: primary

1-877-678-8611

Uz Stammberger

Role: primary

1-877-678-8611

Uz Stammberger

Role: primary

1-877-678-8611

Uz Stammberger

Role: primary

1-877-678-8611

Uz Stammberger

Role: primary

1-877-678-8611

Uz Stammberger

Role: primary

1-877-678-8611

Uz Stammberger

Role: primary

1-877-678-8611

Uz Stammberger

Role: primary

1-877-678-8611

Maciej Harat

Role: primary

+48 600 411 874

Elżbieta Nowicka

Role: primary

+48 32 278 86 01

Maria Vieito Villar

Role: primary

+34 93 274 60 85

Jordi Bruna Escuer

Role: primary

+34932607744

Raquel Serrano Blanch

Role: primary

+34 957011456

Raquel Luque Caro

Role: primary

+34 958020234

María Ángeles Vaz Salgado

Role: primary

(+34) 91 336 82 63

Juan Manuel Sepulveda Sanchez

Role: primary

0034913908339

Virginia Martinez Marín

Role: primary

00 34 91 727 75 16

Miriam Alonso Garcia

Role: primary

+34955013068

Regina Gironés Sarrio

Role: primary

003496 1244188

Benjamin Thiele

Role: primary

061 328 49 53

Andreas Hottinger

Role: primary

+41213146541

Michael Weller

Role: primary

+41 44 2555500

Helen Benghiat

Role: primary

+441216272000

Fiona Harris

Role: primary

01223-586705

James Powell

Role: primary

+447870199969

Faye Robertson

Role: primary

+447970835542

Gerben Borst

Role: primary

+441614463362

Olamide Rominiy

Role: primary

+441142265394

Sean Main

Role: primary

Liam Welsh

Role: primary

+442078082271

Other Identifiers

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EF-41

Identifier Type: -

Identifier Source: org_study_id

2024-513550-30-00

Identifier Type: CTIS

Identifier Source: secondary_id

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