An Investigational Immuno-therapy Study of Nivolumab Compared to Temozolomide, Each Given With Radiation Therapy, for Newly-diagnosed Patients With Glioblastoma (GBM, a Malignant Brain Cancer)

NCT ID: NCT02617589

Last Updated: 2023-03-28

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

560 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-03-01

Study Completion Date

2022-03-04

Brief Summary

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The purpose of this study is to evaluate patients with glioblastoma that is MGMT-unmethylated (the MGMT gene is not altered by a chemical change). Patients will receive Nivolumab every two weeks in addition to radiation therapy, and then every four weeks. They will be compared to patients receiving standard therapy with temozolomide in addition to radiation therapy.

Detailed Description

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Conditions

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Brain Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Nivolumab + Radiotherapy Arm

Nivolumab IV infusion + Radiotherapy dose as specified

Group Type EXPERIMENTAL

Nivolumab

Intervention Type DRUG

Radiotherapy

Intervention Type RADIATION

Temozolomide + Radiotherapy Arm

Temozolomide + Radiotherapy dose as specified

Group Type ACTIVE_COMPARATOR

Temozolomide

Intervention Type DRUG

Radiotherapy

Intervention Type RADIATION

Interventions

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Nivolumab

Intervention Type DRUG

Temozolomide

Intervention Type DRUG

Radiotherapy

Intervention Type RADIATION

Eligibility Criteria

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Inclusion Criteria

* Males and Females, age ≥ 18 years old
* Newly-diagnosed brain cancer or tumor called glioblastoma or GBM
* Tumor test result shows MGMT unmethylated type
* Karnofsky performance status of ≥ 70 (able to care for self)

Exclusion Criteria

* Prior treatment for GBM (other than surgical resection)
* Any known tumor outside of the brain
* Recurrent or secondary GBM
* Active known or suspected autoimmune disease
* Biopsy with less than 20% of tumor removed
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ono Pharmaceutical Co. Ltd

INDUSTRY

Sponsor Role collaborator

Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Local Institution - 0083

Phoenix, Arizona, United States

Site Status

Cedars Sinai Medical Center

Los Angeles, California, United States

Site Status

Local Institution - 0019

Los Angeles, California, United States

Site Status

Sutter Institute For Medical Research

Sacramento, California, United States

Site Status

Sharp Memorial Hospital

San Diego, California, United States

Site Status

The Regents of the University of California, San Francisco

San Francisco, California, United States

Site Status

Yale Cancer Center

New Haven, Connecticut, United States

Site Status

Georgetown University Medical Center

Washington D.C., District of Columbia, United States

Site Status

University Of Miami Sylvester Comprehensive Cancer Center

Miami, Florida, United States

Site Status

Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Emory University - Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

The University Of Chicago

Chicago, Illinois, United States

Site Status

University Of Kansas Medical Center

Westwood, Kansas, United States

Site Status

Norton Cancer Institute

Louisville, Kentucky, United States

Site Status

Johns Hopkins University School Of Medicine

Baltimore, Maryland, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Local Institution - 0006

Detroit, Michigan, United States

Site Status

Washington University School OF Medicine-Siteman Cancer Center

St Louis, Missouri, United States

Site Status

JFK Medical Center

Edison, New Jersey, United States

Site Status

Local Institution - 0064

Hackensack, New Jersey, United States

Site Status

Columbia University Medical Center (Cumc)

New York, New York, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

Levine Cancer Institute

Charlotte, North Carolina, United States

Site Status

Preston Robert Tisch Brain Tumor Center at Duke University

Durham, North Carolina, United States

Site Status

Local Institution - 0010

Cleveland, Ohio, United States

Site Status

Local Institution - 0095

Columbus, Ohio, United States

Site Status

Local Institution - 0132

Allentown, Pennsylvania, United States

Site Status

Local Institution - 0007

Philadelphia, Pennsylvania, United States

Site Status

Medical University Of South Carolina

Charleston, South Carolina, United States

Site Status

Local Institution - 0090

Chattanooga, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

University Of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

University Of Texas Md Anderson Cancer Ctr

Houston, Texas, United States

Site Status

Local Institution - 0068

Salt Lake City, Utah, United States

Site Status

Swedish Neuroscience Institute

Seattle, Washington, United States

Site Status

Royal North Shore Hospital

St Leonards, New South Wales, Australia

Site Status

Local Institution - 0003

Heidelberg, Victoria, Australia

Site Status

Local Institution - 0004

Prahran, Victoria, Australia

Site Status

Local Institution - 0001

Nedlands, Western Australia, Australia

Site Status

Local Institution - 0002

New South Wales, , Australia

Site Status

Local Institution - 0061

Linz, , Austria

Site Status

Local Institution - 0060

Vienna, , Austria

Site Status

Universitair Ziekenhuis Brussel

Brussels, , Belgium

Site Status

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

Uz Leuven

Leuven, , Belgium

Site Status

BC Cancer - Vancouver

Vancouver, British Columbia, Canada

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Princess Margaret Cancer Centre

Toronto, Ontario, Canada

Site Status

Montreal Neurological Institute and Hospital

Montreal, Quebec, Canada

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Local Institution

Copenhagen, , Denmark

Site Status

Local Institution

Odense, , Denmark

Site Status

Local Institution - 0032

Bron, , France

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Local Institution

Lille, , France

Site Status

Local Institution - 0024

Marseille, , France

Site Status

Local Institution - 0101

Nancy, , France

Site Status

Local Institution - 0023

Paris, , France

Site Status

Local Institution - 0038

Paris, , France

Site Status

Centre Eugene Marquis

Rennes, , France

Site Status

Local Institution - 0106

Toulouse, , France

Site Status

Local Institution - 0051

Bonn, , Germany

Site Status

Local Institution - 0139

Cologne, , Germany

Site Status

Local Institution - 0072

Erlangen, , Germany

Site Status

Local Institution - 0049

Frankfurt am Main, , Germany

Site Status

Local Institution - 0073

Freiburg im Breisgau, , Germany

Site Status

Local Institution - 0054

Hamburg, , Germany

Site Status

Local Institution - 0052

Heidelberg, , Germany

Site Status

Local Institution - 0138

Munich, , Germany

Site Status

Local Institution - 0050

Münster, , Germany

Site Status

Local Institution - 0055

Regensburg, , Germany

Site Status

Local Institution - 0056

Tübingen, , Germany

Site Status

Local Institution - 0096

Petah Tikva, , Israel

Site Status

Local Institution - 0097

Tel Aviv, , Israel

Site Status

Local Institution - 0076

Bologna, , Italy

Site Status

Local Institution - 0079

Milan, , Italy

Site Status

Local Institution - 0126

Padua, , Italy

Site Status

Local Institution - 0135

Rozzano (milano), , Italy

Site Status

Local Institution - 0078

Siena, , Italy

Site Status

Local Institution - 0077

Torino, , Italy

Site Status

Local Institution - 0115

Nagoya, Aichi-ken, Japan

Site Status

Local Institution - 0125

Chiba, Chiba, Japan

Site Status

Local Institution - 0123

Hiroshima, Hiroshima, Japan

Site Status

Local Institution - 0122

Sapporo, Hokkaido, Japan

Site Status

Local Institution - 0129

Kobe, Hyōgo, Japan

Site Status

Local Institution - 0111

Tsukuba, Ibaraki, Japan

Site Status

Local Institution - 0121

Kanazawa, Ishikawa-ken, Japan

Site Status

Local Institution - 0131

Kagoshima, Kagoshima-ken, Japan

Site Status

Local Institution - 0133

Sagamihara-shi, Kanagawa, Japan

Site Status

Local Institution - 0119

Kumamoto, Kumamoto, Japan

Site Status

Local Institution - 0117

Kyoto, Kyoto, Japan

Site Status

Local Institution - 0116

Kyoto, Kyoto, Japan

Site Status

Local Institution - 0134

Okayama, Okayama-ken, Japan

Site Status

Local Institution

Hirakata-shi, Osaka, Japan

Site Status

Local Institution - 0130

Suita-shi, Osaka, Japan

Site Status

Local Institution - 0113

Hidaka, Saitama, Japan

Site Status

Local Institution - 0128

Bunkyo-ku, Tokyo, Japan

Site Status

Local Institution - 0114

Chuo-ku, Tokyo, Japan

Site Status

Local Institution - 0118

Mitaka-shi, Tokyo, Japan

Site Status

Local Institution - 0110

Yamagata, Yamagata, Japan

Site Status

Local Institution - 0112

Tokyo, , Japan

Site Status

NKI AVL

Amsterdam, , Netherlands

Site Status

Universitair Medisch Centrum Groningen

Groningen, , Netherlands

Site Status

Erasmus Mc

Rotterdam, , Netherlands

Site Status

Local Institution - 0063

Utrecht, , Netherlands

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Local Institution

Oslo, , Norway

Site Status

Local Institution - 0080

Gdansk, , Poland

Site Status

Local Institution - 0081

Warsaw, , Poland

Site Status

Local Institution - 0070

Moscow, , Russia

Site Status

Local Institution - 0105

Moscow, , Russia

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Badalona-Barcelona, , Spain

Site Status

Local Institution

Barcelona, , Spain

Site Status

Local Institution - 0028

Barcelona, , Spain

Site Status

Local Institution - 0029

Madrid, , Spain

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Madrid, , Spain

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Santiago de Compostela, , Spain

Site Status

Local Institution - 0025

Valencia, , Spain

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Lund, , Sweden

Site Status

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Solna, , Sweden

Site Status

Local Institution - 0059

Geneva, , Switzerland

Site Status

Local Institution - 0057

Lausanne, , Switzerland

Site Status

Local Institution - 0053

Zurich, , Switzerland

Site Status

University College Hospital

London, Greater London, United Kingdom

Site Status

Christie Hospital Nhs Found. Trust

Manchester, Greater Manchester, United Kingdom

Site Status

Royal Marsden Hospital

Sutton, Surrey, United Kingdom

Site Status

Beaston West of Scotland Cancer Centre

Glasgow, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Canada Denmark France Germany Israel Italy Japan Netherlands Norway Poland Russia Spain Sweden Switzerland United Kingdom

References

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Grkovski M, Daras M, Bale T, Lyashchenko S, Reiner AS, Mellinghoff IK, Schoder H, Dunphy MPS. 18F-BMS-986229 PET imaging of tumor PD-L1 expression in glioblastoma patients. EJNMMI Res. 2025 Sep 26;15(1):124. doi: 10.1186/s13550-025-01283-x.

Reference Type DERIVED
PMID: 41003913 (View on PubMed)

Omuro A, Brandes AA, Carpentier AF, Idbaih A, Reardon DA, Cloughesy T, Sumrall A, Baehring J, van den Bent M, Bahr O, Lombardi G, Mulholland P, Tabatabai G, Lassen U, Sepulveda JM, Khasraw M, Vauleon E, Muragaki Y, Di Giacomo AM, Butowski N, Roth P, Qian X, Fu AZ, Liu Y, Potter V, Chalamandaris AG, Tatsuoka K, Lim M, Weller M. Radiotherapy combined with nivolumab or temozolomide for newly diagnosed glioblastoma with unmethylated MGMT promoter: An international randomized phase III trial. Neuro Oncol. 2023 Jan 5;25(1):123-134. doi: 10.1093/neuonc/noac099.

Reference Type DERIVED
PMID: 35419607 (View on PubMed)

Woroniecka K, Fecci PE. Immuno-synergy? Neoantigen vaccines and checkpoint blockade in glioblastoma. Neuro Oncol. 2020 Sep 29;22(9):1233-1234. doi: 10.1093/neuonc/noaa170. No abstract available.

Reference Type DERIVED
PMID: 32691060 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2015-003739-37

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CA209-498

Identifier Type: -

Identifier Source: org_study_id

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