A Study to Evaluate the Efficacy and Safety of Autogene Cevumeran With Nivolumab Versus Nivolumab Alone in Participants With High-risk Muscle-invasive Urothelial Carcinoma (MIUC)

NCT ID: NCT06534983

Last Updated: 2026-02-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

362 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-12-09

Study Completion Date

2034-01-06

Brief Summary

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The main purpose of the study is to evaluate the efficacy of adjuvant treatment with autogene cevumeran plus nivolumab compared with nivolumab in participants with high risk MIUC.

In this study participants will be enrolled in a safety run-in phase to receive autogene cevumeran + nivolumab. This phase will be conducted to monitor and ensure the safety of study participants. After all participants in the safety run-in have been enrolled to receive autogene cevumeran + nivolumab, further participants will be randomized in either autogene cevumeran + nivolumab or the saline + nivolumab arm.

Detailed Description

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Conditions

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Muscle-invasive Urothelial Carcinoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Autogene Cevumeran + Nivolumab

Participants will receive autogene cevumeran along with nivolumab intravenously (IV) at a recommended dose at specified timepoints.

Group Type EXPERIMENTAL

Autogene Cevumeran

Intervention Type DRUG

Autogene cevumeran will be administered as an IV infusion per the schedule specified in the arm.

Nivolumab

Intervention Type DRUG

Nivolumab will be administered as an IV infusion per the schedule specified in the arm.

Saline + Nivolumab

Participants will receive saline solution along with 480 milligrams (mg) of nivolumab, IV, once every 4 weeks (Q4W) for 1 year.

Group Type ACTIVE_COMPARATOR

Nivolumab

Intervention Type DRUG

Nivolumab will be administered as an IV infusion per the schedule specified in the arm.

Saline

Intervention Type DRUG

Saline solution for IV infusion.

Interventions

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Autogene Cevumeran

Autogene cevumeran will be administered as an IV infusion per the schedule specified in the arm.

Intervention Type DRUG

Nivolumab

Nivolumab will be administered as an IV infusion per the schedule specified in the arm.

Intervention Type DRUG

Saline

Saline solution for IV infusion.

Intervention Type DRUG

Other Intervention Names

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RO7198457 Opdivo

Eligibility Criteria

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Inclusion Criteria

* Participants must have the capacity to participate/enroll in the study and to provide informed consent
* Histologically confirmed muscle-invasive UC (also termed transitional cell carcinoma \[TCC\]) of the bladder or upper urinary tract
* Tumor-node-metastasis (TNM ) classification (Union for International Cancer Control \[UICC\]/American Joint Committee on Cancer \[AJCC\] 7th edition) at pathological examination of surgical resection specimen of (y)pT3-4 or (y)pN+ and M0
* Surgical resection of MIUC of the bladder or upper tract
* Participants who have received neoadjuvant chemotherapy (NAC), including antibody drug-conjugate, either alone or in combination with a checkpoint inhibitor (CPI), are eligible
* Participants who have not received any prior NAC are also eligible, provided they meet one of the following criteria, which would make them ineligible to receive adjuvant cisplatin-based therapy: participant refusal, cisplatin ineligibility or investigator decision
* Tumor tissue must be provided for biomarker analysis
* Absence of residual disease and absence of metastasis, as confirmed by a negative baseline computed tomography (CT) or magnetic resonance imaging (MRI) scan of the pelvis, abdomen, and chest no more than 28 days prior to randomization
* Full recovery from cystectomy or nephroureterectomy within 120 days following surgery
* Eastern cooperative oncology group (ECOG) performance status of 0 or 1
* Negative human immunodeficiency virus (HIV) test at screening
* Negative hepatitis B surface antigen (HbsAg) test at screening
* Positive hepatitis B surface antibody (HBsAb), or a negative HBsAb at screening accompanied by either of the following: negative total hepatitis B core antibody (HBcAb) or positive total HBcAb test followed by quantitative hepatitis B virus (HBV) deoxyribonucleic acid (DNA) \< 500 international units/milliliter (IU/mL)
* Negative hepatitis C virus (HCV) antibody test at screening, or a positive HCV antibody test followed by a negative HCV ribonucleic acid (RNA) test at screening

Exclusion Criteria

* Partial cystectomy in the setting of bladder cancer primary tumor or partial nephroureterectomy in the setting of renal pelvis primary tumor
* Any approved anti-cancer therapy, including chemotherapy, or hormonal therapy within 3 weeks prior to initiation of study treatment
* Adjuvant chemotherapy, immunotherapy, or radiation therapy for UC following surgical resection
* Prior active malignancies within 3 years prior to randomization
* Treatment with a live, attenuated vaccine within 4 weeks prior to initiation of study treatment
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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BioNTech SE

INDUSTRY

Sponsor Role collaborator

Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Highlands Oncology Group.

Springdale, Arkansas, United States

Site Status RECRUITING

Kaiser Permanente - Baldwin Park

Baldwin Park, California, United States

Site Status SUSPENDED

City of Hope Cancer Center

Duarte, California, United States

Site Status SUSPENDED

Kaiser Permanente - Los Angeles (N. Vermont)

Los Angeles, California, United States

Site Status SUSPENDED

Kaiser Permanente - Riverside

Riverside, California, United States

Site Status SUSPENDED

University of California San Francisco

San Francisco, California, United States

Site Status SUSPENDED

Yale Cancer Center

New Haven, Connecticut, United States

Site Status RECRUITING

Georgetown University Medical Center Lombardi Cancer Center

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Norton Cancer Institute

Louisville, Kentucky, United States

Site Status RECRUITING

Henry Ford Health System

Detroit, Michigan, United States

Site Status RECRUITING

Memorial Sloan Kettering Cancer Center Basking Ridge

Basking Ridge, New Jersey, United States

Site Status RECRUITING

MSK Monmouth

Middletown, New Jersey, United States

Site Status RECRUITING

MSK Bergen

Montvale, New Jersey, United States

Site Status RECRUITING

MSK Commack

Commack, New York, United States

Site Status RECRUITING

MSK Westchester

Harrison, New York, United States

Site Status RECRUITING

Columbia University Irving Medical Center

New York, New York, United States

Site Status SUSPENDED

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status RECRUITING

MSK Nassau

Uniondale, New York, United States

Site Status RECRUITING

Providence Portland Medical Ctr

Portland, Oregon, United States

Site Status SUSPENDED

AHN Cancer Institute ? Allegheny General Hospital

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status SUSPENDED

Bon Secours - St. Francis Hospital

Greenville, South Carolina, United States

Site Status RECRUITING

MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Inova Schar Cancer Institute

Fairfax, Virginia, United States

Site Status RECRUITING

Fred Hutchinson Cancer Research Center

Seattle, Washington, United States

Site Status RECRUITING

University of Washington Medical Center

Seattle, Washington, United States

Site Status RECRUITING

Instituto Alexander Fleming

Buenos Aires, , Argentina

Site Status RECRUITING

Hospital Britanico

Buenos Aires, , Argentina

Site Status RECRUITING

Hospital Italiano

Ciudad Autonoma Buenos Aires, , Argentina

Site Status RECRUITING

Lyell McEwin Hospital

Elizabeth Vale, South Australia, Australia

Site Status RECRUITING

Box Hill Hospital

Box Hill, Victoria, Australia

Site Status RECRUITING

Sunshine Hospital

St Albans, Victoria, Australia

Site Status RECRUITING

UZ Gent

Ghent, , Belgium

Site Status RECRUITING

AZ Groeninge

Kortrijk, , Belgium

Site Status RECRUITING

UZ Leuven Gasthuisberg

Leuven, , Belgium

Site Status RECRUITING

Clinique Ste-Elisabeth

Namur, , Belgium

Site Status RECRUITING

Cross Cancer Institute

Edmonton, Alberta, Canada

Site Status RECRUITING

Princess Margaret Cancer Center

Toronto, Ontario, Canada

Site Status RECRUITING

Jewish General Hospital

Montreal, Quebec, Canada

Site Status RECRUITING

McGill University Health Center

Montreal, Quebec, Canada

Site Status SUSPENDED

Aalborg Universitetshospital

Aalborg, , Denmark

Site Status RECRUITING

Aarhus Universitetshospital

Aarhus N, , Denmark

Site Status RECRUITING

Herlev Hospital

Herlev, , Denmark

Site Status RECRUITING

Hopital Claude Huriez

Lille, , France

Site Status RECRUITING

Institut Paoli Calmettes

Marseille, , France

Site Status RECRUITING

Centre Eugene Marquis

Rennes, , France

Site Status SUSPENDED

Institut Gustave Roussy

Villejuif, , France

Site Status RECRUITING

Vivantes Klinikum Am Urban

Berlin, , Germany

Site Status SUSPENDED

Universitätsklinikum Düsseldorf;Urologische Klinik

Düsseldorf, , Germany

Site Status RECRUITING

Uniklinik Essen

Essen, , Germany

Site Status RECRUITING

Uniklinik-Eppendorf

Hamburg, , Germany

Site Status SUSPENDED

Uniklinikum Heidelberg

Heidelberg, , Germany

Site Status RECRUITING

Marien Hospital Herne

Herne, , Germany

Site Status RECRUITING

Universitätsklinikum Jena, Urologische Klinik und Poliklinik

Jena, , Germany

Site Status RECRUITING

Klinikum rechts der Isar der TU München

München, , Germany

Site Status SUSPENDED

Klinikum Stuttgart - Katharinenhospital

Stuttgart, , Germany

Site Status RECRUITING

Universitätsklinikum Ulm

Ulm, , Germany

Site Status RECRUITING

Alexandras Hospital

Athens, , Greece

Site Status SUSPENDED

Attikon University General Hospital

Athens, , Greece

Site Status RECRUITING

Theageneio Hospital

Thessaloniki, , Greece

Site Status RECRUITING

A.O. Universitaria Ospedale Consorziale Policlinico Di Bari

Bari, Apulia, Italy

Site Status RECRUITING

Istituto Nazionale Tumori Irccs Fondazione G. Pascale

Napoli, Campania, Italy

Site Status RECRUITING

AZ.Osp S. Orsola ? Malpighi-Reparto di Oncologia Medica

Bologna, Emilia-Romagna, Italy

Site Status RECRUITING

IFO - Istituto Regina Elena

Rome, Lazio, Italy

Site Status RECRUITING

Asst Papa Giovanni XXIII

Bergamo, Lombardy, Italy

Site Status SUSPENDED

Istituto Clinico Humanitas

Rozzano, Lombardy, Italy

Site Status SUSPENDED

A.O. Universitaria S. Luigi Gonzaga

Orbassano, Piedmont, Italy

Site Status RECRUITING

IOV - Istituto Oncologico Veneto - IRCCS

Padua, Veneto, Italy

Site Status RECRUITING

A.O.U di Verona Policlinico G.B. Rossi

Verona, Veneto, Italy

Site Status RECRUITING

Hospital Civil de Guadalajara Fray Antonio Alcalde

Guadalajara, Jalisco, Mexico

Site Status SUSPENDED

Erasmus MC

Rotterdam, , Netherlands

Site Status RECRUITING

St. Antonius locatie Leidsche Rijn

Utrecht, , Netherlands

Site Status SUSPENDED

Akershus universitetssykehus

Lørenskog, , Norway

Site Status SUSPENDED

Centrum Onkologii im. Prof. Franciszka ?ukaszczyka

Bydgoszcz, , Poland

Site Status RECRUITING

Szpital Wojewodzki im. M. Kopernika w Koszalinie

Koszalin, , Poland

Site Status RECRUITING

Centrum Onkologii Ziemi Lubelskiej im. sw. Jana z Dukli

Lublin, , Poland

Site Status RECRUITING

Szpital Kliniczny Ministerstwa Spraw Wewn?trznych i Administracji z Warmi?sko-Mazurskim Centrum Onkologii w Olsztynie

Olsztyn, , Poland

Site Status RECRUITING

Radomskie Centrum Onkologii

Radom, , Poland

Site Status RECRUITING

AIDPORT Sp. z o. o.

Skórzewo, , Poland

Site Status RECRUITING

Narodowy Instytut Onkologii im. M. Sklodowskiej-Curie

Warsaw, , Poland

Site Status RECRUITING

Seoul National University Bundang Hospital

Seongnam-si, , South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, , South Korea

Site Status RECRUITING

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status RECRUITING

Asan Medical Center

Seoul, , South Korea

Site Status RECRUITING

Samsung Medical Center

Seoul, , South Korea

Site Status RECRUITING

Hospital Universitario Son Espases

Palma de Mallorca, Balearic Islands, Spain

Site Status RECRUITING

ICO L'Hospitalet

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status SUSPENDED

Vall d'Hebron Institute of Oncology (VHIO), Barcelona

Sant Andreu de la Barca, Barcelona, Spain

Site Status RECRUITING

Complejo Hospitalario Universitario de Santiago (CHUS)

Santiago de Compostela, LA Coruna, Spain

Site Status RECRUITING

Hospital Clinico San Carlos

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status RECRUITING

Instituto Valenciano Oncologia

Valencia, , Spain

Site Status RECRUITING

Hospital General Universitario de Valencia

Valencia, , Spain

Site Status RECRUITING

Hospital Clinico Universitario Lozano Blesa

Zaragoza, , Spain

Site Status RECRUITING

Sahlgrenska University Hospital

Gothenburg, , Sweden

Site Status RECRUITING

Skånes Onkologiska Klinik, Universitetssjukhuset

Lund, , Sweden

Site Status RECRUITING

Chang Gung Medical Foundation - Kaohsiung

Kaohsiung City, , Taiwan

Site Status RECRUITING

National Taiwan Uni Hospital

Taipei, , Taiwan

Site Status RECRUITING

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status RECRUITING

Clatterbridge Cancer Centre

Bebington, , United Kingdom

Site Status RECRUITING

Royal Devon and Exeter Hospital

Exeter, , United Kingdom

Site Status RECRUITING

Barts & London School of Med;Medical Oncology

London, , United Kingdom

Site Status SUSPENDED

Royal Preston Hosptial

Preston, , United Kingdom

Site Status RECRUITING

Southampton General Hospital

Southampton, , United Kingdom

Site Status RECRUITING

Countries

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United States Argentina Australia Belgium Canada Denmark France Germany Greece Italy Mexico Netherlands Norway Poland South Korea Spain Sweden Taiwan United Kingdom

Central Contacts

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Reference Study ID Number: BO45230 https://forpatients.roche.com/

Role: CONTACT

888-662-6728 (U.S. Only)

Other Identifiers

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BO45230

Identifier Type: -

Identifier Source: org_study_id

2023-509023-40-00

Identifier Type: CTIS

Identifier Source: secondary_id

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