A Study of Nivolumab Plus Bempegaldesleukin (Bempeg/NKTR-214) vs Nivolumab Alone vs Standard of Care in Participants With Bladder Cancer That May Have Invaded The Muscle Wall of the Bladder and Who Cannot Get Cisplatin, A Type of Medicine Given To Treat Bladder Cancer

NCT ID: NCT04209114

Last Updated: 2024-06-27

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

114 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-02-05

Study Completion Date

2023-06-07

Brief Summary

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The purpose of the study is to see if treatment with nivolumab plus bempegaldesleukin or nivolumab alone, before and after surgery to remove the bladder, is more effective than surgery alone in participants with high-risk urothelial cancer, including muscle-invasive bladder cancer who are not able to receive cisplatin chemotherapy.

Detailed Description

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Conditions

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Bladder Cancer Bladder Tumor Muscle-Invasive Bladder Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A: Combination Therapy

Neoadjuvant (pre-surgical treatment) nivolumab + bempeg, followed by radical cystectomy (RC), followed by adjuvant (post-surgical treatment) nivolumab + bempeg

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

Radical cystectomy (RC)

Intervention Type PROCEDURE

Surgical removal of the bladder

Bempegaldesleukin

Intervention Type BIOLOGICAL

Specified dose on specified days

Arm B: Monotherapy

Neoadjuvant nivolumab, followed by RC, followed by adjuvant nivolumab

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

Radical cystectomy (RC)

Intervention Type PROCEDURE

Surgical removal of the bladder

Arm C: Standard-of-care

RC alone, without neoadjuvant or adjuvant therapy

Group Type OTHER

Radical cystectomy (RC)

Intervention Type PROCEDURE

Surgical removal of the bladder

Interventions

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Nivolumab

Specified dose on specified days

Intervention Type BIOLOGICAL

Radical cystectomy (RC)

Surgical removal of the bladder

Intervention Type PROCEDURE

Bempegaldesleukin

Specified dose on specified days

Intervention Type BIOLOGICAL

Other Intervention Names

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Opdivo BMS-936558 BMS-986321 NKTR-214 Bempeg

Eligibility Criteria

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Inclusion Criteria

* Urothelial carcinoma (UC) of the bladder, clinical stage T2-T4aN0, M0 or T1-T4aN1, M0, diagnosed at transurethral resection of bladder tumor (TURBT)
* Must be deemed eligible for Radical Cystectomy (RC) by urologist, and must agree to undergo RC. For arms A and B, participants must agree to undergo RC after completion of neoadjuvant therapy.
* Eastern Cooperative Oncology Group (ECOG) performance status 0 or 1
* Cisplatin-ineligible participants will be defined by any one of the following criteria:

i) Impaired renal function (glomerular filtration rate \[GFR\] ≥ 30 but \< 60 mL/min) ii) GFR should be assessed by direct measurement (ie, creatinine clearance) or, if not available, by calculation from serum/plasma creatinine (Cockcroft-Gault formula) iii) Common Terminology Criteria for Adverse Events (CTCAE) version 5, ≥ Grade 2 hearing loss (assessed per local SOC).

iv) CTCAE version 5, ≥ Grade 2 peripheral neuropathy.

* Documented Left Ventricular Ejection Fraction (LVEF) more than 45%

Exclusion Criteria

* Clinical evidence of ≥ N2 or metastatic bladder cancer
* Prior systemic therapy, radiation therapy, or surgery for bladder cancer other than TURBT or biopsies is not permitted. Prior Bacillus Calmette-Guerin (BCG) or other intravesicular treatment of non-muscle invasive bladder cancer (NMIBC) is permitted if completed at least 6 weeks prior to initiating study treatment.
* Evidence of urothelial carcinoma (UC) in upper urinary tracts (ureters or renal pelvis) or history of previous MIBC
* History of pulmonary embolism (PE), deep vein thrombosis (DVT), or prior clinically significant venous or non-CVA(cerebrovascular accident)/TIA (Transient ischemic attack) arterial thromboembolic event
* Known cardiovascular history, including unstable or deteriorating cardiac disease within the previous 12 months (including unstable angina or myocardial infarction, congestive heart failure or uncontrolled clinically significant arrhythmias)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Nektar Therapeutics

INDUSTRY

Sponsor Role collaborator

Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Local Institution - 0080

Gilbert, Arizona, United States

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Local Institution - 0136

Tucson, Arizona, United States

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Local Institution - 0029

La Jolla, California, United States

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Local Institution - 0015

Orange, California, United States

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Local Institution - 0002

Iowa City, Iowa, United States

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Rochester, Minnesota, United States

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Local Institution - 0006

New Brunswick, New Jersey, United States

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Local Institution - 0004

Buffalo, New York, United States

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Local Institution - 0009

The Bronx, New York, United States

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Local Institution - 0005

Allentown, Pennsylvania, United States

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Local Institution - 0007

Charleston, South Carolina, United States

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Local Institution - 0139

Houston, Texas, United States

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Local Institution - 0023

Temple, Texas, United States

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Local Institution - 0122

Gig Harbor, Washington, United States

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Local Institution - 0102

Seattle, Washington, United States

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Local Institution - 0096

Capital Federal, Buenos Aires, Argentina

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Local Institution - 0028

Ciudad Autónoma de Buenos Aires, Buenos Aires, Argentina

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Local Institution - 0124

La Plata, Buenos Aires, Argentina

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Local Institution - 0027

Capital Federal, Distrito Federal, Argentina

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Local Institution - 0174

Rosario, Santa Fe Province, Argentina

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Local Institution - 0097

Córdoba, , Argentina

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Local Institution - 0137

Gosford, New South Wales, Australia

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Local Institution - 0158

Ballarat, Victoria, Australia

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Local Institution - 0157

Fitzroy, Victoria, Australia

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Local Institution - 0011

Heidelberg, Victoria, Australia

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Local Institution - 0013

Murdoch, Western Australia, Australia

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Local Institution - 0148

Graz, , Austria

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Local Institution - 0123

Vienna, , Austria

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Local Institution - 0150

Vienna, , Austria

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Local Institution - 0083

Wilrijk, Antwerpen, Belgium

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Local Institution - 0101

Brussels, Brussels Capital, Belgium

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Local Institution - 0098

Edegem, , Belgium

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Local Institution - 0068

Ghent, , Belgium

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Local Institution - 0100

Liège, , Belgium

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Local Institution - 0177

Porto Alegre, Rio Grande do Sul, Brazil

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Local Institution - 0039

Porto Alegre, Rio Grande do Sul, Brazil

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Local Institution - 0176

Barretos, São Paulo, Brazil

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Local Institution - 0037

Jaú, São Paulo, Brazil

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Local Institution - 0038

São Paulo, São Paulo, Brazil

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Local Institution - 0041

Rio de Janeiro, , Brazil

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Local Institution - 0040

São Paulo, , Brazil

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Local Institution - 0082

Oshawa, Ontario, Canada

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Local Institution - 0018

Québec, Quebec, Canada

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Local Institution - 0036

Sherbrooke, Quebec, Canada

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Local Institution - 0204

Chongqing, Chongqing Municipality, China

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Xiamen, Fujian, China

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Zhengzhou, Henan, China

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Wuhan, Hubei, China

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Changsha, Hunan, China

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Taiyuan, Shan1xi, China

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Jinan, Shandong, China

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Local Institution - 0022

Olomouc, , Czechia

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Local Institution - 0021

Prague, , Czechia

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Local Institution - 0020

Prague, , Czechia

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Local Institution - 0077

Avignon, , France

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Local Institution - 0091

Bordeaux, , France

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Local Institution - 0151

Clermont-Ferrand, , France

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Local Institution - 0059

La Roche-sur-Yon, , France

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Lyon, , France

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Marseille, , France

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Montpellier, , France

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Nice, , France

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Paris, , France

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Paris, , France

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Quimper, , France

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Local Institution - 0161

Reims, , France

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Strasbourg, , France

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Local Institution - 0056

Suresnes, , France

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Local Institution - 0074

Tours, , France

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Universitatsklinikum Carl Gustav Carus

Dresden, , Germany

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Local Institution - 0117

Düsseldorf, , Germany

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Erlangen, , Germany

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Essen, , Germany

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Hamburg, , Germany

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Hamburg, , Germany

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Herne, , Germany

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Jena, , Germany

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Lübeck, , Germany

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Münster, , Germany

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Nuremberg, , Germany

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Tübingen, , Germany

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Local Institution - 0178

Athens, , Greece

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Local Institution - 0088

Athens, , Greece

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Chaïdári, , Greece

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Thessaloniki, , Greece

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Local Institution - 0129

Haifa, , Israel

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Local Institution - 0131

Tel Aviv, , Israel

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Local Institution - 0130

Tel Litwinsky, , Israel

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Local Institution - 0149

Florence, , Italy

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Local Institution - 0162

Milan, , Italy

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Local Institution - 0025

Milan, , Italy

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Pavia, , Italy

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Pisa, , Italy

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Roma, , Italy

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Rozzano, , Italy

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Local Institution - 0154

La Paz, BAJA Californa SUR, Mexico

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Local Institution - 0132

Mexico City, Mexico City, Mexico

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Local Institution - 0160

Mexico City, Mexico City, Mexico

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Local Institution - 0133

Monterrey, Nuevo León, Mexico

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Local Institution - 0069

Amsterdam, , Netherlands

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Local Institution - 0167

Biała Podlaska, , Poland

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Local Institution - 0054

Warsaw, , Poland

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Omsk, , Russia

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Saint Petersburg, , Russia

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Local Institution - 0104

A Coruña, , Spain

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Local Institution - 0106

Badalona, , Spain

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Local Institution - 0110

Barcelona, , Spain

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Local Institution - 0109

Córdoba, , Spain

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Local Institution - 0105

Madrid, , Spain

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Local Institution - 0108

Madrid, , Spain

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Local Institution - 0103

Madrid, , Spain

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Local Institution - 0107

Santander, , Spain

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Local Institution - 0111

Seville, , Spain

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Stevenage, Hertfordshire, United Kingdom

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Local Institution - 0085

Leicester, , United Kingdom

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Local Institution - 0042

London, , United Kingdom

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Countries

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United States Argentina Australia Austria Belgium Brazil Canada China Czechia France Germany Greece Israel Italy Mexico Netherlands Poland Russia Spain United Kingdom

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2018-002676-40

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

18-214-13

Identifier Type: OTHER

Identifier Source: secondary_id

CA045-009

Identifier Type: -

Identifier Source: org_study_id

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