Dose Optimization of Caffeine for HIE

NCT ID: NCT06448780

Last Updated: 2025-08-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1

Total Enrollment

16 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-07-26

Study Completion Date

2028-11-30

Brief Summary

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This is a phase Ib, open-label, dose-validating and safety study of caffeine in neonates with hypoxic-ischemic encephalopathy (HIE) undergoing therapeutic hypothermia.

Detailed Description

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In a previous phase I trial (NCT03913221), the investigators characterized the pharmacokinetics (PK) of caffeine in the setting of HIE and therapeutic hypothermia using a population PK model. This is an open-label study of caffeine citrate in neonates with HIE to validate the population PK model and determine optimal dosing for HIE.

Conditions

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Hypoxic-Ischemic Encephalopathy

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

The first cohort of 8 infants will receive a lower loading dose of caffeine. Following a safety review, an additional 8 infants will receive a higher loading dose.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Lower loading dose (20 mg/kg)

Within 24 hours after delivery, participants will receive a loading dose of 20 mg/kg caffeine citrate IV.

Group Type ACTIVE_COMPARATOR

Caffeine citrate 20 mg/kg

Intervention Type DRUG

Following loading dose of 20 mg/kg of caffeine citrate IV, participants will receive 2 daily doses of 10 mg/kg caffeine citrate IV.

Higher loading dose (30 mg/kg)

Within 24 hours after delivery, participants will receive a loading dose of 30 mg/kg caffeine citrate IV.

Group Type ACTIVE_COMPARATOR

Caffeine citrate 30 mg/kg

Intervention Type DRUG

Following loading dose of 30 mg/kg of caffeine citrate IV, participants will receive 2 daily doses of 10 mg/kg caffeine citrate IV.

Interventions

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Caffeine citrate 20 mg/kg

Following loading dose of 20 mg/kg of caffeine citrate IV, participants will receive 2 daily doses of 10 mg/kg caffeine citrate IV.

Intervention Type DRUG

Caffeine citrate 30 mg/kg

Following loading dose of 30 mg/kg of caffeine citrate IV, participants will receive 2 daily doses of 10 mg/kg caffeine citrate IV.

Intervention Type DRUG

Other Intervention Names

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Cafcit Cafcit

Eligibility Criteria

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Inclusion Criteria

* Documented informed consent from parent or guardian
* ≥ 36 weeks gestational age at birth
* Receiving therapeutic hypothermia for a diagnosis of HIE
* Intravenous (IV) access
* Postnatal age \< 24 hours

Exclusion Criteria

* Receiving \> 1 anti-epileptic drug for seizures
* Sustained (\>4 hours) heart rate \> 180 beats per minute
* Known major congenital anomaly
Maximum Eligible Age

24 Hours

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)

NIH

Sponsor Role collaborator

University of North Carolina, Chapel Hill

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Wesley M Jackson, MD, MPH

Role: PRINCIPAL_INVESTIGATOR

University of North Carolina, Chapel Hill

Locations

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The University of North Carolina at Chapel Hill Newborn Critical Care Center

Chapel Hill, North Carolina, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Wesley M Jackson, MD, MPH

Role: CONTACT

984-215-3449

Facility Contacts

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Wesley M Jackson, MD, MPH

Role: primary

984-215-3449

References

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Shankaran S, McDonald SA, Laptook AR, Hintz SR, Barnes PD, Das A, Pappas A, Higgins RD; Eunice Kennedy Shriver National Institute of Child Health and Human Development Neonatal Research Network. Neonatal Magnetic Resonance Imaging Pattern of Brain Injury as a Biomarker of Childhood Outcomes following a Trial of Hypothermia for Neonatal Hypoxic-Ischemic Encephalopathy. J Pediatr. 2015 Nov;167(5):987-93.e3. doi: 10.1016/j.jpeds.2015.08.013. Epub 2015 Sep 16.

Reference Type BACKGROUND
PMID: 26387012 (View on PubMed)

Selewski DT, Charlton JR, Jetton JG, Guillet R, Mhanna MJ, Askenazi DJ, Kent AL. Neonatal Acute Kidney Injury. Pediatrics. 2015 Aug;136(2):e463-73. doi: 10.1542/peds.2014-3819. Epub 2015 Jul 13.

Reference Type BACKGROUND
PMID: 26169430 (View on PubMed)

Jackson W, Gonzalez D, Greenberg RG, Lee YZ, Laughon MM. A phase I trial of caffeine to evaluate safety in infants with hypoxic-ischemic encephalopathy. J Perinatol. 2024 Apr;44(4):508-512. doi: 10.1038/s41372-023-01752-y. Epub 2023 Aug 16.

Reference Type BACKGROUND
PMID: 37587184 (View on PubMed)

Other Identifiers

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1K23HD111623-01

Identifier Type: NIH

Identifier Source: secondary_id

View Link

24-0654

Identifier Type: -

Identifier Source: org_study_id

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