Observational Study to Assess Endpoint Operational Feasibility & Measurement Properties in Patients with Retinal Degeneration

NCT ID: NCT06375239

Last Updated: 2025-01-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Total Enrollment

120 participants

Study Classification

OBSERVATIONAL

Study Start Date

2024-04-05

Study Completion Date

2026-04-30

Brief Summary

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The Vision Research and Assessment Institute (VRAI) was established with the purpose of serving as a testing facility for efficacy endpoints for patients with Low Vision.

The mission of the VRAI is to enable the highest quality, standardized efficacy testing of patients with visual impairment.

The VRAI facilitates the development and refinement of existing endpoints specifically for testing patients with Low Vision.

Detailed Description

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The VRAI is a state-of-the-art research institute specifically for patients with low or very low vision due to diseases of the retina of the eye. The Institute is staffed by highly experienced Low Vision specialists and provides a comfortable, familiar environment for patient testing.

The study is a non-interventional prospective cohort study of up to 40 patients for each disease condition (Retinitis Pigmentosa, Choroideremia, Stargardt Macular Dystrophy, Geographic Atrophy from Age-related Macular Degeneration, X-linked Retinoschisis or other retinal dystrophies ).

Patients are scheduled for an initial visit where they are tested on a series of efficacy tests. Thereafter, patients will be invited to attend for a further visit up to two weeks and then periodically for up to one year. The objectives of the study are to evaluate how well patients use their vision, how the tests relate to activities of daily living, establish clinical meaningfulness, assess the impact of disease progression and the precision and accuracy of each test in the context of their eye condition.

Conditions

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Retinitis Pigmentosa Choroideremia Stargardt Macular Dystrophy Stargardt Disease Geographic Atrophy from Age-related Macular Degeneration X-lined Retinoschisis Retinal Dystrophies

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Retinitis Pigmentosa

Up to 40 patients with Retinitis Pigmentosa

No interventions assigned to this group

Choroideremia

Up to 40 patients with Choroideremia

No interventions assigned to this group

Stargardt Macular Dystrophy (Stargardt Disease)

Up to 40 patients with Stargardt Macular Dystrophy also known as Stargardt Disease

No interventions assigned to this group

Geographic Atrophy from Age-related Macular Degeneration

Up to 40 patients with Geographic Atrophy from Age-related Macular Degeneration

No interventions assigned to this group

X-linked Retinoschisis

Up to 40 patients with X-linked Retinoschisis

No interventions assigned to this group

Other Retinal Dystrophies

Up to 40 patients with other retinal dystrophies

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of bilateral retinitis pigmentosa, choroideremia, Stargardt macular dystrophy, geographic atrophy from age-related macular degeneration, X-linked retinoschisis or other retinal dystrophies confirmed from previous eye examination records
* Best-corrected visual acuity between 20/70 and HM in at least one eye as tested with clinic-based visual acuity method
* Reasonably fluent in English

Exclusion Criteria

* Cognitive impairment, memory loss or dementia sufficient in severity to preclude informed consent or in the opinion of the investigator would prevent satisfactory completion of some or all of the testing.
* Any circumstance that in the opinion of the investigator, would interfere with participation in, or compliance with the study protocol
* Current pregnancy as reported by patient
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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The Vision Research and Assessment Institute (VRAI)

UNKNOWN

Sponsor Role collaborator

Ray Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Vision Research and Assessment Institute

Irvine, California, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Shawn Yu, OD

Role: CONTACT

949-264-3793

Facility Contacts

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Shawn Yu, OD

Role: primary

949-264-3793

Other Identifiers

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RTx-VRAI-NHS01

Identifier Type: -

Identifier Source: org_study_id

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