To Assess the Safety and Efficacy of SP-002 with Vismodegib for the Treatment of Locally Advanced Basal Cell Carcinoma

NCT ID: NCT06344052

Last Updated: 2024-09-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

80 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-04-09

Study Completion Date

2029-03-30

Brief Summary

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The goal of this clinical trial is to evaluate the efficacy of using SP-002 in participants with locally advanced Basal cell carcinoma. The main question it aims to answer is what the objective response rate for a basal cell carcinoma tumor is following 1 or 3 cycles of SP-002 treatment given as an add-on to hedgehog pathway inhibitor therapy.

Researchers will compare the objective response rate for treated Basal cell carcinoma tumors between 3 treatment Arms.

* Arm 1 participants will receive daily hedgehog pathway inhibitor, and 3 cycles of SP-002 treatment.
* Arm 2 participants will receive daily hedgehog pathway inhibitor, and 1 cycle of SP-002 treatment.
* Arm 3 participants will receive daily hedgehog pathway inhibitor only.

Detailed Description

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This is a Phase 2, 3-arm, multi-center, open-label, randomized, clinical study to evaluate the efficacy of SP-002 in combination with vismodegib in subjects with locally advanced Basal cell carcinoma.

The study will be completed in 2 consecutive parts. Each part consists of a screening period, a treatment period, and a follow-up period.

* Part A: 20 participants who meet study entry criteria will be randomized in a 1:1 ratio into 2 treatment arms (Arm 2 and Arm 3) and will provide preliminary safety and performance in a population with target Basal cell carcinoma lesions.
* Part B: 60 participants who meet study entry criteria will be randomized in a 1:1:1 ratio into 3 treatment arms (Arm 1, Arm 2, and Arm 3) in a population with target Basal cell carcinoma lesions.

Conditions

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Basal Cell Carcinoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm 1

vismodegib, with 3 cycles SP-002

Group Type EXPERIMENTAL

SP-002

Intervention Type DRUG

SP-002 is a replication deficient adenovirus-5 encoding human interferon gamma (IFNγ), designed for intra-tumoral administration

Vismodegib

Intervention Type DRUG

The HHPI vismodegib is currently indicated for the treatment of adult patients with metastatic BCC, or with laBCC where surgery and/or radiation therapy are not appropriate.

Arm 2

vismodegib, with 1 cycles SP-002

Group Type EXPERIMENTAL

SP-002

Intervention Type DRUG

SP-002 is a replication deficient adenovirus-5 encoding human interferon gamma (IFNγ), designed for intra-tumoral administration

Vismodegib

Intervention Type DRUG

The HHPI vismodegib is currently indicated for the treatment of adult patients with metastatic BCC, or with laBCC where surgery and/or radiation therapy are not appropriate.

Arm 3

vismodegib monotherapy

Group Type PLACEBO_COMPARATOR

Vismodegib

Intervention Type DRUG

The HHPI vismodegib is currently indicated for the treatment of adult patients with metastatic BCC, or with laBCC where surgery and/or radiation therapy are not appropriate.

Interventions

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SP-002

SP-002 is a replication deficient adenovirus-5 encoding human interferon gamma (IFNγ), designed for intra-tumoral administration

Intervention Type DRUG

Vismodegib

The HHPI vismodegib is currently indicated for the treatment of adult patients with metastatic BCC, or with laBCC where surgery and/or radiation therapy are not appropriate.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Subject has provided written informed consent prior to initiation of study-specified procedures.
2. Subject is 18 years of age or older.
3. Eastern Cooperative Oncology Group performance status 0, 1 or 2.
4. Subject has a single lesion that is histologically confirmed as BCC. The externally visible component of the lesions should be at least 1 cm in one dimension to facilitate accurate and reproducible measurement, to 5 cm at longest diameter, that in the opinion of the investigator:

A. is considered not a good candidate for surgery or has recurred after definitive surgical treatment and curative surgical resection is unlikely. OR

B. subject has a medical contraindication to surgery where acceptable medical contraindications to surgery include:
* Anticipated substantial morbidity and/or deformity from surgery (e.g., removal of all or part of a vital facial structure, such as nose, ear, eyelid, eye; or requirement for limb amputation).
* Medical conditions predisposing to poor surgical outcome (e.g., diabetes with history of poor wound healing).
* Other conditions considered to be medically contraindicating must be discussed with the Medical Monitor before enrolling the subject.

A copy of the surgical consultation note must be provided. laBCC with prior history of or ongoing HPPI treatment are eligible under the following conditions:
* Achieved objective response with disease progression \>3 months after treatment discontinuation.

Note: where the subject has \>1 lesion, one lesion may be selected for treatment at the discretion of the investigator.
5. Radiotherapy is contraindicated or inappropriate in the opinion of the investigator, for example, hypersensitivity to radiation due to genetic syndrome such as Gorlin syndrome, limitations because of location of tumor, or anticipated significant morbidity, loss of function, or unacceptable cosmetic outcomes. Patients with Basal Cell Nevus Syndrome (Gorlin syndrome) may enroll in this study but must meet the criteria for locally advanced or listed above.
6. Subject is able and willing to comply with all study requirements including biopsies at baseline and during the study. Biopsy 3-4 mm preferred, biopsies must be \<25% of the area the tumor. Screening biopsies performed 1-12 weeks before Day 1.
7. Subject has adequate hematopoietic capacity, as defined by the following:

* Neutrophil count \>1,500/mm3
* Hemoglobin \>9 g/dL
* Platelet count \>100,000/ mm3
* Prothrombin international normalized ratio \<1.5
8. Subject has adequate hepatic function, as defined by the following:

* Total bilirubin \<1.5 × the upper limit of normal (ULN) or within 3 × the ULN for patients with Gilbert disease
* Aspartate aminotransferase, alanine aminotransferase or alkaline phosphate \<2 × the ULN
9. Adequate renal function, as defined by the following:

* Creatinine \<1.5 x ULN
10. For female subjects of childbearing potential\*, agreement to use two acceptable methods of contraception (including one barrier method), during the study and for at least (per United States Prescribing Information \[USPI\]) 24 months after discontinuation of vismodegib.

For male subjects with female partners of childbearing potential\*, agreement to use a latex condom, and to advise their female partner to use an additional method of contraception during the study and for at least (per USPI) 24 months after discontinuation of vismodegib.
11. Subjects agree not to donate blood or blood products during the study and for at least (per USPI) 24 months after discontinuation of vismodegib; male subjects agree not to donate sperm during the study and for at least 2 months after discontinuation of vismodegib.

* Childbearing potential is defined as any female who has experienced menarche and who has not undergone surgical sterilization (hysterectomy or bilateral oophorectomy) and is not postmenopausal. Menopause is defined as 12 months of amenorrhea in the absence of other biological causes. In addition, females under the age of 55 years must have a documented serum follicle stimulating hormone level \>40 mIU/mL to confirm menopause.

Exclusion Criteria

1. laBCC that has progressed on systemic HHPI therapy as defined below:

* Best response of progressive disease (primary progression).
* Objective response followed by disease progression while on HHPI treatment.
* laBCC with a best response of stable disease on systemic HHPI treatment.
2. laBCC that has recurred in the same location after two or more surgical procedures, or that has recurred following radiation therapy.
3. laBCC that has bone involvement (radiologically confirmed if clinically suspected).
4. laBCC with invasion of underlying soft tissue that is not accessible by standard syringe/needle.
5. Patients with evidence of metastatic BCC.
6. Female subjects who are lactating or pregnant.
7. Life expectancy of \<12 weeks.
8. Concurrent non-protocol-specified anti-tumor therapy (e.g., chemotherapy, other targeted therapy, or radiation therapy).
9. Recent (within 4 weeks of Day 1), current, or planned participation in an experimental drug study.
10. History of other malignancies within 3 years of Day 1, except for tumors with a negligible risk for metastasis or death, such as adequately treated basal and squamous-cell carcinoma of the skin, ductal carcinoma in situ of the breast, or carcinoma in situ of the cervix.
11. Uncontrolled medical illnesses such as infection requiring treatment with intravenous antibiotics.
12. History of other stable disease, metabolic dysfunction, physical examination finding, or clinical laboratory finding giving reasonable suspicion of a disease or condition that contraindicates use of an investigational drug or that might affect interpretation of the results of the study or renders the subject at high risk from treatment complications.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Stamford Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Stamford Pharmaceuticals

Role: STUDY_CHAIR

Stamford Pharmaceuticals

Locations

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Research Site

Phoenix, Arizona, United States

Site Status RECRUITING

Research Site

Boca Raton, Florida, United States

Site Status RECRUITING

Research Site

Coral Springs, Florida, United States

Site Status RECRUITING

Research Site

Cutler Bay, Florida, United States

Site Status RECRUITING

Research Site

Rockville, Maryland, United States

Site Status RECRUITING

Research Site

Lee's Summit, Missouri, United States

Site Status RECRUITING

Research Site

Rochester, New York, United States

Site Status RECRUITING

Research Site

Cedar Park, Texas, United States

Site Status RECRUITING

Research Site

Humble, Texas, United States

Site Status RECRUITING

Research Site

Longview, Texas, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Stamford Pharmaceuticals

Role: CONTACT

5126944241

Other Identifiers

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SP-002-004

Identifier Type: -

Identifier Source: org_study_id

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