A Study of Two Vismodegib Regimens in Participants With Multiple Basal Cell Carcinomas

NCT ID: NCT01815840

Last Updated: 2017-09-28

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

229 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-04-30

Study Completion Date

2016-08-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This randomized, double-blind, regimen-controlled, phase II, multicenter study will assess the efficacy and safety of two different vismodegib regimens in participants with multiple basal cell carcinoma. Participants will receive vismodegib 150 mg orally once daily either in an intermittent schedule of 12 weeks vismodegib followed by 8 weeks placebo (Arm A) or as 24 weeks induction followed by an intermittent schedule of 8 weeks placebo followed by 8 weeks vismodegib (Arm B). Anticipated time on study treatment is 72 weeks.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Basal Cell Carcinoma

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Vismodegib Intermittent Schedule

Vismodegib intermittent schedule of 12 weeks vismodegib followed by 8 weeks placebo, repeated 3 times with a final course of vismodegib (total 72 weeks), followed by 52 weeks treatment-free follow up

Group Type EXPERIMENTAL

Vismodegib

Intervention Type DRUG

Vismodegib 150 mg hard gelatin capsule orally once daily

Placebo

Intervention Type DRUG

Vismodegib placebo orally once daily

Vismodegib Induction Followed by Intermittent Schedule

Vismodegib beginning with 24 weeks induction followed by intermittent schedule 8 weeks placebo, 8 weeks vismodegib (total 72 weeks), followed by 52 weeks treatment-free follow up

Group Type EXPERIMENTAL

Vismodegib

Intervention Type DRUG

Vismodegib 150 mg hard gelatin capsule orally once daily

Placebo

Intervention Type DRUG

Vismodegib placebo orally once daily

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Vismodegib

Vismodegib 150 mg hard gelatin capsule orally once daily

Intervention Type DRUG

Placebo

Vismodegib placebo orally once daily

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Erivedge®

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Adult participants, \>/= 18 years of age
* Participants with multiple basal cell carcinomas, including participants with Gorlin syndrome, with at least 6 clinically evident basal cell carcinomas at the time of randomization, of which 3 measure 5 mm or more in diameter and are considered target lesions. All other lesions are considered to be non-target lesions
* Histopathologic confirmation that at least one of the three target lesions is basal cell carcinoma
* Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1 or 2
* Adequate renal and hepatic function and hematopoietic capacity
* Women of childbearing potential must agree to use contraception as defined by protocol during treatment and for at least 9 months after completion of study treatment
* Male participants with female partners of childbearing potential must agree to use contraception as defined by protocol during treatment and for 2 months after completion of study treatment

Exclusion Criteria

* Inability or unwillingness to swallow capsules
* Pregnant or breastfeeding women
* Any metastatic basal cell carcinoma
* Locally advanced basal cell carcinoma lesion that is considered to be inoperable or to have medical contraindications to surgery
* Recent (i.e., within the past 28 days prior to randomization) or current participation in another experimental drug study
* Known or suspected alcohol abuse
* One of the following known rare hereditary conditions: galactose intolerance, primary hypolactasia or glucose-galactose malabsorption
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Dermatology Research Associate

Los Angeles, California, United States

Site Status

Stanford University

Palo Alto, California, United States

Site Status

Skin Surgery Med Group, Inc

San Diego, California, United States

Site Status

California Pacific Medical Center Research Institute

Santa Rosa, California, United States

Site Status

Advanced Derm & Cosmetic Surg

Ormond Beach, Florida, United States

Site Status

Skin and Cancer Associates and the Center for Cosmetic Enhancement

Plantation, Florida, United States

Site Status

Emory University Clinic

Atlanta, Georgia, United States

Site Status

Laser & Skin Surgery Center of Indiana

Carmel, Indiana, United States

Site Status

Beverly Hospital;Oncology Center Pharmacy

Beverly, Massachusetts, United States

Site Status

Saint Louis University School of Medicine; Department of Dermatology

St Louis, Missouri, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Long Island Skin Cancer and Dermatologic Surgery

Smithtown, New York, United States

Site Status

Mariwalla Dermatology

West Islip, New York, United States

Site Status

The Skin Surgery Center

Winston-Salem, North Carolina, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

Penn State Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Dermatology and Laser Center of Charleston PA

Charleston, South Carolina, United States

Site Status

LKH Innsbruck; Universitätsklinik für Dermatologie

Innsbruck, , Austria

Site Status

Medizinische Universität Wien; Univ.Klinik für Dermatologie

Vienna, , Austria

Site Status

UBC Department of Dermatology & Skin Sciences

Vancouver, British Columbia, Canada

Site Status

Dermetics

Burlington, Ontario, Canada

Site Status

Innovaderm Research Inc.

Montreal, Quebec, Canada

Site Status

CHU Amiens - Hopital Sud

Amiens, , France

Site Status

Hopital Saint Andre CHU De Bordeaux; Dermatologie

Bordeaux, , France

Site Status

Chu Site Du Bocage;Dermatologie

Dijon, , France

Site Status

Hopital Dupuytren; Dermatologie

Limoges, , France

Site Status

Hopital Timone Adultes; Dermatologie

Marseille, , France

Site Status

Hopital Saint Eloi; CHU de Montpellier; Svc de Dermatologie

Montpellier, , France

Site Status

Hopital Hotel Dieu Et Hme; Clinique Dermatologique

Nantes, , France

Site Status

Hôpital Saint-Louis

Paris, , France

Site Status

Ch Francois Mitterrand; Medecine Oncologie

Pau, , France

Site Status

Hopital Nord ; Dermatologie

Saint-Etienne, , France

Site Status

Universitätsklinik Essen; Klinik und Poliklinik für Dermatologie, Venerologie und Allergologie

Essen, , Germany

Site Status

Klinik Johann Wolfgang von Goethe Uni; Klinik für Dermatologie, Venerologie und Allergologie

Frankfurt, , Germany

Site Status

SRH Wald-Klinikum Gera; Klinik für Hautkrankheiten und Allergologie

Gera, , Germany

Site Status

Medizinische Hochschule Hannover; Klinik für Dermatologie, Allergologie und Venerologie

Hanover, , Germany

Site Status

UNI-Klinikum Campus Kiel Klinik f.Dermatologie Tagesklinik f.Dermatologie

Kiel, , Germany

Site Status

Klinikum der LMU München; Klinik und Poliklinik für Dermatologie und Allergologie

München, , Germany

Site Status

Fachklinik Hornheide; Dermatologie

Münster, , Germany

Site Status

Universitätsklinikum Tübingen Universitäts-Hautklinik

Tübingen, , Germany

Site Status

Ospedale San Salvatore (ASL-01); Dip. di Dermatologia U.O.S. di Dermatologia Oncol

L’Aquila, Abruzzo, Italy

Site Status

Arcispedale Santa Maria Nuova; Dermatologia

Reggio Emilia, Emilia-Romagna, Italy

Site Status

Università di Brescia; Dipartimento di Dermatologia

Brescia, Lombardy, Italy

Site Status

Azienda Ospedaliera Città della Salute e della Scienza di Torino

Turin, Piedmont, Italy

Site Status

Ospedale IOT- Palagi Dermatologia 2

Florence, Tuscany, Italy

Site Status

Hospital General de México

Mexico City, , Mexico

Site Status

Hospital General Dr. Manuel Gea Gonzalez; Dermatology

México, , Mexico

Site Status

VU MEDISCH CENTRUM;Afdeling Dermatologie

Amsterdam, , Netherlands

Site Status

Academ Ziekenhuis Groningen; Medical Oncology

Groningen, , Netherlands

Site Status

Maastricht University Medical Centre; Dermatologie

Maastricht, , Netherlands

Site Status

Blokhin Cancer Research Center; General Oncology Department

Moscow, , Russia

Site Status

FSBI "Russian Oncology Research Center n.a. N. N. Blokhin" of Ministry of Health of the Russian Fed

Moscow, , Russia

Site Status

City Clinical Oncology Dispensary

Saint Petersburg, , Russia

Site Status

Hospital Costa Del Sol; Servicio de Dermatologia

Málaga, Malaga, Spain

Site Status

Hospital Clinic i Provincial; Servicio de Farmacia

Barcelona, , Spain

Site Status

Hospital General Universitario de Guadalajara; Servicio de Dermatologia

Guadalajara, , Spain

Site Status

Hospital General Universitario de Valencia; Servicio de oncologia

Valencia, , Spain

Site Status

Instituto Valenciano Oncologia; Oncologia Medica

Valencia, , Spain

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Austria Canada France Germany Italy Mexico Netherlands Russia Spain

References

Explore related publications, articles, or registry entries linked to this study.

Jacobsen AA, Kydd AR, Strasswimmer J. Practical management of the adverse effects of Hedgehog pathway inhibitor therapy for basal cell carcinoma. J Am Acad Dermatol. 2017 Apr;76(4):767-768. doi: 10.1016/j.jaad.2016.04.063. No abstract available.

Reference Type DERIVED
PMID: 28325399 (View on PubMed)

Dreno B, Kunstfeld R, Hauschild A, Fosko S, Zloty D, Labeille B, Grob JJ, Puig S, Gilberg F, Bergstrom D, Page DR, Rogers G, Schadendorf D. Two intermittent vismodegib dosing regimens in patients with multiple basal-cell carcinomas (MIKIE): a randomised, regimen-controlled, double-blind, phase 2 trial. Lancet Oncol. 2017 Mar;18(3):404-412. doi: 10.1016/S1470-2045(17)30072-4. Epub 2017 Feb 8.

Reference Type DERIVED
PMID: 28188086 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2012-003305-10

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

MO28295

Identifier Type: -

Identifier Source: org_study_id