A Study of ANAVEX3-71 in Adults With Schizophrenia

NCT ID: NCT06245213

Last Updated: 2025-05-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

71 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-03-15

Study Completion Date

2025-06-30

Brief Summary

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A study to evaluate the safety, tolerability, efficacy, pharmacokinetics, and electrophysiology of ANAVEX3-71 in patients with Schizophrenia.

Detailed Description

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ANAVEX3-71-SZ-001 is a two-part study. The first part is Part A: Multiple Ascending Dose, PK, safety, and dose selection. The second part is Part B: Double Blind, Placebo Controlled for exploratory efficacy and continued repeat-dose safety. This study will investigate the effects of ANAVEX3-71 in patients with Schizophrenia for the first time. This is an in-patient study. In both parts, participants will undergo either 10 or 28 days of dosing (Part A and Part B, respectively). Standard clinical outcome measures used in the clinic and novel fluid and electrophysiological biomarkers will also be assessed.

Conditions

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Schizophrenia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Parallel Assignment in Part A and Part B. Part A: n = 16; Part B: n = 55;
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ANAVEX3-71 30 mg TID (Part A)

The first active treatment arm of the study during Part A (multiple ascending doses).

Group Type ACTIVE_COMPARATOR

ANAVEX3-71 oral capsules

Intervention Type DRUG

ANAVEX®3-71 (formerly AF710B) is a dual SIGMAR1 receptor agonist and M1 positive allosteric modulator with agonistic effects. This novel mechanism of action offers the potential to treat all symptom domains (positive, negative, and cognitive) of schizophrenia without the side effects of standard of care antipsychotics.

ANAVEX3-71 60 mg TID (Part A)

The second active treatment arm of the study during Part A (multiple ascending doses).

Group Type ACTIVE_COMPARATOR

ANAVEX3-71 oral capsules

Intervention Type DRUG

ANAVEX®3-71 (formerly AF710B) is a dual SIGMAR1 receptor agonist and M1 positive allosteric modulator with agonistic effects. This novel mechanism of action offers the potential to treat all symptom domains (positive, negative, and cognitive) of schizophrenia without the side effects of standard of care antipsychotics.

ANAVEX3-71 Placebo TID (Part A)

The placebo arm of Part A (multiple ascending doses).

Group Type PLACEBO_COMPARATOR

Placebo oral capsules

Intervention Type DRUG

The placebo comparator for the study.

ANAVEX3-71 TBD mg TID (Part B)

The active arm of Part B of the study. The dose will be determined based on data obtained in Part A.

Group Type ACTIVE_COMPARATOR

ANAVEX3-71 oral capsules

Intervention Type DRUG

ANAVEX®3-71 (formerly AF710B) is a dual SIGMAR1 receptor agonist and M1 positive allosteric modulator with agonistic effects. This novel mechanism of action offers the potential to treat all symptom domains (positive, negative, and cognitive) of schizophrenia without the side effects of standard of care antipsychotics.

ANAVEX3-71 Placebo TID (Part B)

The placebo arm of Part B of the study.

Group Type PLACEBO_COMPARATOR

Placebo oral capsules

Intervention Type DRUG

The placebo comparator for the study.

Interventions

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ANAVEX3-71 oral capsules

ANAVEX®3-71 (formerly AF710B) is a dual SIGMAR1 receptor agonist and M1 positive allosteric modulator with agonistic effects. This novel mechanism of action offers the potential to treat all symptom domains (positive, negative, and cognitive) of schizophrenia without the side effects of standard of care antipsychotics.

Intervention Type DRUG

Placebo oral capsules

The placebo comparator for the study.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Male and female volunteers 18-55 years of age, inclusive at screening.
2. Has a primary diagnosis of schizophrenia, for ≥ 1 year
3. Stable schizophrenia psychiatric symptoms for at least 6 weeks prior to screening.
4. Schizophrenia clinical symptom severity defined by meeting ALL of the following per the Positive and Negative Syndrome Scale (PANSS) item scores at screening:

1. Delusions (P1) ≤ 4
2. Hallucinatory behavior (P3) ≤ 4
3. Unusual thought content (G9) ≤ 4
4. Hostility (P7) ≤ 4
5. Patient has a PANSS total score ≤ 80 at screening and baseline visits and no worsening in PANSS total score between screening and baseline, of more than 20%.
6. Has a Brief Assessment of Cognition (BACS) T-score \< 50 at the screening visit.
7. On a stable regimen of at least one and up to a maximum of two second-generation ("atypical") antipsychotic medications for at least 6 weeks prior to screening and agree to stay on this regimen for their entire study participation, with the following exceptions:

1. Clozapine use is not permitted
2. Quetiapine for sleep at doses less than 300 mg are permitted.
3. Day time (including morning) quetiapine use as the background antipsychotic is not permitted.
8. Able to understand the requirements of the study and able and willing to provide written informed consent and to abide by the study procedures, in the judgment of the Investigator, including able and willing to remain in an in-patient setting during the study.
9. If of childbearing potential, using adequate contraceptive methods for the duration of the study.
10. Body mass index of 18.5 to 40.0 kg/m2 (inclusive) and total body weight \> 50 kg (110 lbs.) for males and \> 40 kg (88 lbs.) for females.
11. Has a negative urine screen for drugs of abuse and negative alcohol breath test at screening and check-in.
12. Patient resides in a stable living situation and is anticipated to return to that same stable living situation.

Exclusion Criteria

1. Participation in a schizophrenia study in which the patient has received any investigational medications within 60 days prior to the baseline visit.
2. History or presence of a clinically significant, poorly treated, or unstable conditions that would jeopardize the safety of the patient or the validity of the study results.
3. Clinically significant abnormal findings on the physical examination, medical history, ECG, or clinical laboratory results at screening.
4. Calgary Depression Scale for schizophrenia (CDSS) score ≥6 at the screening or baseline visits.
5. Simpson Angus Scale (SAS) total score ≥5 at the screening and baseline visits at the screening or baseline visits.
6. Abnormal Involuntary Movement (AIMS) score of 2 for two or more movements or a score of 3 or 4 for any single movement on this scale at the screening or baseline visits.
7. Any primary the DSM-5-TR (American Psychiatric Association 2022) disorder other than schizophrenia within 12 months before screening (confirmed using MINI version 7.0.2 at screening).
8. Pregnant, lactating, or less than 3 months postpartum. Sperm donation is not allowed for 90 days after the final dose of study drug.
9. Risk for suicidal behavior during the study.
10. Inability to detect a 1000 Hz tone at 40 dB in both ears at screening.
11. Has psychiatric hospitalization(s) for more than 30 days (cumulative) during the 90 days before screening.
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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COGNISION

UNKNOWN

Sponsor Role collaborator

Cognitive Research Corporation

INDUSTRY

Sponsor Role collaborator

Hassman Research Institute

UNKNOWN

Sponsor Role collaborator

Anavex Life Sciences Corp.

INDUSTRY

Sponsor Role lead

Responsible Party

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Kathy Skoff

Investigator

Responsibility Role PRINCIPAL_INVESTIGATOR

Locations

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CenExel Hassman Research Institute

Marlton, New Jersey, United States

Site Status

Countries

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United States

Other Identifiers

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ANAVEX3-71-SZ-001

Identifier Type: -

Identifier Source: org_study_id

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