A Multicenter Multinational Observational Study of Children With Hypochondroplasia
NCT ID: NCT06212947
Last Updated: 2025-04-03
Study Results
The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.
Basic Information
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RECRUITING
400 participants
OBSERVATIONAL
2023-11-27
2043-12-31
Brief Summary
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Detailed Description
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Conditions
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Study Design
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COHORT
PROSPECTIVE
Study Groups
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Children with Hypochondroplasia
Children with Hypochondroplasia
No interventions assigned to this group
Eligibility Criteria
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Inclusion Criteria
* Participants must have genetic confirmation of Hypochondroplasia diagnosis
Exclusion Criteria
* Received an investigational product or medical device within 6 months before the Screening visit
15 Years
ALL
No
Sponsors
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BioMarin Pharmaceutical
INDUSTRY
Responsible Party
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Principal Investigators
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Medical Director, MD
Role: STUDY_DIRECTOR
BioMarin Pharmaceutical
Locations
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Phoenix Children's Hospital
Phoenix, Arizona, United States
Cedars-Sinai Medical Center
Los Angeles, California, United States
UCSF Benioff Children's Hospital
Oakland, California, United States
Nemours Alfred I. Dupont Hospital for Children
Wilmington, Delaware, United States
Children's National Health System
Washington D.C., District of Columbia, United States
Ann & Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, United States
The Johns Hopkins University School of Medicine
Baltimore, Maryland, United States
Boston Children's Hospital
Boston, Massachusetts, United States
University of Minnesota Masonic Children's Hospital
Minneapolis, Minnesota, United States
University of Missouri
Columbia, Missouri, United States
Washington University School of Medicine in St. Louis
St Louis, Missouri, United States
Mount Sinai Kravis Children's Hospital
New York, New York, United States
Akron Children's Hospital
Akron, Ohio, United States
Nationwide Children's Hospital
Columbus, Ohio, United States
Cook Children's Endocrinology
Fort Worth, Texas, United States
Medical College of Wisconsin, Children's Hospital
Milwaukee, Wisconsin, United States
Hospital de Pediatria SAMIC Prof. Dr. Juan P Garrahan
Buenos Aires, , Argentina
Royal Children's Hospital Melbourne
Parkville, Victoria, Australia
Hospital de Clinicas de Porto Algre
Porto Alegre, Rio Grande Do Sol, Brazil
Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto
Ribeirão Preto, São Paulo, Brazil
Stollery Children's Hospital
Edmonton, Alberta, Canada
SickKids - The Hospital for Sick Children
Toronto, Ontario, Canada
Centre Hospitalier Universitaire Sainte-Justine
Montreal, Quebec, Canada
Hospices Civils de Lyon - Hôpital Femme Mère Enfant
Lyon, , France
Hopital de la Timone
Marseille, , France
Hôpital Necker-Enfants Malades
Paris, , France
CHU de Toulouse - Hopital des Efants
Toulouse, , France
Uniklinik Koln
Cologne, , Germany
Universitatskinderklinik Magdeburg
Magdeburg, , Germany
Istituto Giannina Gaslini
Genoa, Liguria, Italy
Ospedale Pediatrico Bambino Gesù
Roma, Rome, Italy
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico
Milan, , Italy
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Rome, , Italy
Kumamoto University Hospital
Kumamoto, Kumamoto, Japan
Osaka University Hospital
Suita, Osaka, Japan
Tottori University Hospital
Yonago, Tottori, Japan
Tokushima University Hospital
Tokushima, , Japan
Institute of Science Tokyo Hospital
Tokyo, , Japan
Hospital Universitario La Paz
Madrid, , Spain
Vithas Hospital San Jose
Vitoria-Gasteiz, , Spain
Great Ormond Street Hospital for Children NHS Foundation Trust
London, England, United Kingdom
Myriad Trials Ltd
London, England, United Kingdom
NHS Greater Glasgow and Clyde
Glasgow, Scottland, United Kingdom
Countries
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Central Contacts
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Other Identifiers
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111-902
Identifier Type: -
Identifier Source: org_study_id
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