A Study of AK117 in Combination With Azacitidine in Patients With Myelodysplastic Syndromes

NCT ID: NCT06196203

Last Updated: 2025-02-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

90 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-02-07

Study Completion Date

2026-06-30

Brief Summary

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This is a Phase 2 randomized, double-blind, placebo-controlled, multicenter study evaluating the efficacy and safety of AK117 or placebo, combined with azacitidine in patients with newly diagnosed higher-risk myelodysplastic syndromes (HR-MDS).

Detailed Description

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Conditions

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Higher-risk Myelodysplastic Syndromes

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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AK117 (dose 1) in combination with azacitidine

Subjects receive AK117 (dose 1) intravenously, in combination with azacitidine (75 mg/m2, D1-7, Q4W) subcutaneously

Group Type EXPERIMENTAL

AK117

Intervention Type DRUG

AK117 IV injection

Azacitidine

Intervention Type DRUG

Azacitidine SC injection

AK117 (dose 2) in combination with azacitidine

Subjects receive AK117 (dose 2) intravenously, in combination with azacitidine (75 mg/m2, D1-7, Q4W) subcutaneously

Group Type EXPERIMENTAL

AK117

Intervention Type DRUG

AK117 IV injection

Azacitidine

Intervention Type DRUG

Azacitidine SC injection

Placebo in combination with azacitidine

Subjects receive placebo intravenously, in combination with azacitidine (75 mg/m2, D1-7, Q4W) subcutaneously

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo IV injection

Azacitidine

Intervention Type DRUG

Azacitidine SC injection

Interventions

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AK117

AK117 IV injection

Intervention Type DRUG

Placebo

Placebo IV injection

Intervention Type DRUG

Azacitidine

Azacitidine SC injection

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Age ≥ 18 years old at the time of enrolment.
* Eastern Cooperative Oncology Group (ECOG) performance status score of 0 to 2.
* Expected life expectancy ≥ 3 months.
* Newly diagnosed HR-MDS, according to the 2016 World Health Organization (WHO) classification with the presence of \< 20% blasts in bone marrow or peripheral blood; Overall IPSS-R score ≥ 3.5.
* Ability to undergo the study-required bone marrow sample collection procedures.
* Suitable venous access for the study-required blood sampling (i.e., including PK and immunogenicity).
* Female patients of childbearing age must have negative serum pregnancy test results before randomization or per region-specific guidance documented in the informed consent and a negative urine pregnancy test on the day of first dose prior to dosing.
* Female patients of childbearing potential having sex with an unsterilized male partner must agree to use a highly effective method of contraception from the beginning of screening until 180 days after the last dose of the study treatment.
* Unsterilized male patients having sex with a female partner of childbearing potential must agree to use an effective method of contraception from the beginning of screening until 180 days after the last dose of study treatment.

Exclusion Criteria

* MDS evolving from a pre-existing myeloproliferative neoplasm (MPN), myelodysplastic/myeloproliferative neoplasms (MDS/MPN).
* Prior treatment with Cluster of Differentiation (CD) 47 or Signal-regulatory protein alpha (SIRPα)-targeting agents.
* Concurrently participating in another interventional clinical study, unless it is an observational (non-interventional) clinical study or during the follow-up period of an interventional study.
* Patients who previously diagnosed with another malignancy and have any evidence of residual disease.
* Known allergy to any component of any study drug; known history of severe hypersensitivity to other monoclonal antibodies.
* Patients with any psychiatric or social factor which the investigator deems may interfere with the patient's ability to comply with the requirements of the study.
* Patients with current hypertension with systolic blood pressure ≥ 160 mmHg or diastolic blood pressure ≥ 100 mmHg after oral antihypertensive therapy.
* Patients with known cardiopulmonary disease defined as unstable angina, clinically significant arrhythmia, congestive heart failure (New York Heart Association Class III or IV), decompensated cirrhosis, nephrotic syndrome, uncontrolled metabolic disorders.
* Patients who are breastfeeding or plans to breastfeed during the study.
* Other conditions where the investigator considers the patient inappropriate for enrollment.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Akeso

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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UCLA Ronald Reagan Medical Center

Los Angeles, California, United States

Site Status RECRUITING

Rocky Mountain Cancer Centers

Aurora, Colorado, United States

Site Status RECRUITING

Yale Cancer Center

New Haven, Connecticut, United States

Site Status RECRUITING

Mid Florida Hematology and Oncology Center

Orange City, Florida, United States

Site Status RECRUITING

American Oncology Partners, PA (The Center for Cancer and Blood Disorders-Bethesda)

Bethesda, Maryland, United States

Site Status RECRUITING

Maryland Oncology-Columbia

Columbia, Maryland, United States

Site Status RECRUITING

Washington University School of Medicine in St. Louis

St Louis, Missouri, United States

Site Status RECRUITING

Montefiore Einstein Comprehensive Cancer Center

The Bronx, New York, United States

Site Status RECRUITING

UNC Lineberger Comprehensive Cancer Center

Chapel Hill, North Carolina, United States

Site Status RECRUITING

Gabrail Cancer Center

Canton, Ohio, United States

Site Status RECRUITING

Ohio State University

Columbus, Ohio, United States

Site Status RECRUITING

Oncology Associates of Oregon

Eugene, Oregon, United States

Site Status RECRUITING

MUSC Hollings Cancer Center

Charleston, South Carolina, United States

Site Status RECRUITING

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status RECRUITING

Institute of hematolongy&blood diseases hospital, chinese academy of medical sciences&peking union medical college

Tianjin, , China

Site Status RECRUITING

Countries

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United States China

Central Contacts

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Wenting Li, MD

Role: CONTACT

(+86)18116403289

Facility Contacts

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Luke Fletcher

Role: primary

Yazan Madanat

Role: primary

Zhijian Xiao

Role: primary

Other Identifiers

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AK117-205

Identifier Type: -

Identifier Source: org_study_id

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