A Prospective, Multicenter, Open-Label, Observational Phase 4 Study to Evaluate Real-World Safety, Tolerability, and Treatment Patterns of Pegcetacoplan (Syfovre) in Patients With Geographic Atrophy Secondary to Age-Related Macular Degeneration

NCT ID: NCT06161584

Last Updated: 2025-11-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Total Enrollment

300 participants

Study Classification

OBSERVATIONAL

Study Start Date

2023-09-28

Study Completion Date

2028-06-30

Brief Summary

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A Prospective, Multicenter, Open-Label, Observational Phase 4 Study to Evaluate Real-World Safety, Tolerability, and Treatment Patterns of Pegcetacoplan (Syfovre) in Patients with Geographic Atrophy Secondary to Age-Related Macular Degeneration

Detailed Description

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Conditions

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Geographic Atrophy

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Observation

Pegcetacoplan

Intervention Type DRUG

Administered intravitreally (IVT) in eyes with geographic atrophy (GA)

Interventions

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Pegcetacoplan

Administered intravitreally (IVT) in eyes with geographic atrophy (GA)

Intervention Type DRUG

Other Intervention Names

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Syfovre

Eligibility Criteria

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Inclusion Criteria

* Eyes that are naive to treatment with pegcetacoplan that are prescribed pegcetacoplan per routine clinical practice according to approved pegcetacoplan prescribing information (ie, the clinical decision to treat with pegcetacoplan must be made before study participation is discussed with the patient)
* Patient age ≥60 years
* Visual acuity better than 20/200 on Snellen chart
* Clinical diagnosis of GA of the macula secondary to AMD in one or both eyes as determined by the investigator using OCT and/or FAF imaging
* GA lesion meeting the following criteria as determined by the investigator's assessment of Spectralis OCT and/or FAF images at screening:

1. Nonsubfoveal lesion(s)
2. GA lesion visualized in its entirety on the macula-centered OCT image and not contiguous with any areas of peripapillary atrophy
3. Presence of any pattern of hyperautofluorescence in the junctional zone of GA; absence of hyperautofluorescence (ie, pattern = none) exclusionary
* Adequate clarity of ocular media and adequate pupillary dilation and fixation to permit the collection of good quality images as determined by the investigator
* Patient willing and able to give informed consent and to comply with the study procedures and assessments

Exclusion Criteria

* GA secondary to a condition other than AMD such as Stargardt disease, cone rod dystrophy, or toxic maculopathies like Plaquenil maculopathy in either eye
* Active, suspected, or history of intraocular inflammation in either eye at screening or on day 1
* Any history of or active choroidal neovascularization associated with AMD or any other cause, including any evidence of retinal pigment epithelial tears or rips in SD OCT imaging
* Presence of an active ocular disease that in the opinion of the investigator compromises or confounds visual function, including but not limited to uveitis and other macular diseases (eg, clinically significant epiretinal membrane, full thickness macular hole, uncontrolled glaucoma/ocular hypertension). Conditions that in the opinion of the investigator are benign, such as peripheral retina dystrophy, are not exclusionary
* Any prior treatment with anti-VEGF agents
* Intraocular surgery (including lens replacement surgery) within 3 months prior to screening
* History of laser therapy in the macular region
* Aphakia or absence of the posterior capsule. Note: Yttrium aluminum garnet laser posterior capsulotomy for posterior capsule opacification done at least 60 days prior to screening is not exclusionary.
* Any ocular condition other than GA secondary to AMD that may require surgery or medical intervention during the study period or, in the opinion of the investigator, could compromise visual function during the study period
* Any contraindication to IVT injection
* Current ocular or periocular infection in either eye
* Intravitreal medical device placement
* Participation in any prior or current systemic experimental treatment within 6 weeks or 5 half lives of the active ingredient (whichever is longer) prior to the start of study treatment or in any other investigational treatments specific to GA. Clinical trials solely involving observation, over-the-counter vitamins, supplements, or diets are not exclusionary
* Medical or psychiatric conditions that, in the opinion of the investigator, make consistent follow-up unlikely or would make the patient an unsafe study candidate
* Known hypersensitivity to fluorescein sodium for injection or hypersensitivity to pegcetacoplan or any of the excipients in pegcetacoplan solution
* History or current use of brolucizumab and/or pharmacological treatments that gain approval for the treatment of GA
Minimum Eligible Age

60 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Apellis Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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California Retina Consultants (01-026)

Bakersfield, California, United States

Site Status

Retina-Vitreous Associates Medical Group (01-020)

Beverly Hills, California, United States

Site Status

Illinois Retina Associates (01-035)

Fullerton, California, United States

Site Status

Retinal Consultants Medical Group Inc (01-008)

Modesto, California, United States

Site Status

Retina Consultants San Diego Inc. (01-018)

Poway, California, United States

Site Status

California Retina Consultants (01-027)

Santa Barbara, California, United States

Site Status

Bay Area Retina Associates (01-005)

Walnut Creek, California, United States

Site Status

Colorado Retina Associates, PLLC (01-011)

Lakewood, Colorado, United States

Site Status

Retina Specialty Institute (01-019)

Pensacola, Florida, United States

Site Status

South East Retina Center, PC (01-030)

Augusta, Georgia, United States

Site Status

Georgia Retina (01-032)

Marietta, Georgia, United States

Site Status

Illinois Retina Associates (01-037)

Oak Park, Illinois, United States

Site Status

The Retina Care Center (01-023)

Baltimore, Maryland, United States

Site Status

Cumberland Valley Retina Consultants, P.C. (01-002)

Hagerstown, Maryland, United States

Site Status

Mid Atlantic Retina Specialist (01-029)

Hagerstown, Maryland, United States

Site Status

Retina Consultants of Minnesota, PLLC (01-025)

Edina, Minnesota, United States

Site Status

Mid Atlantic Retina Research (01-014)

Cherry Hill, New Jersey, United States

Site Status

Mid Atlantic Retina (01-031)

Cherry Hill, New Jersey, United States

Site Status

OCLI Research Department (01-007)

Oceanside, New York, United States

Site Status

Long Island Vitreoretinal Consultants (01-013)

Westbury, New York, United States

Site Status

Western Carolina Retinal Associates, PA (01-009)

Asheville, North Carolina, United States

Site Status

Retina Associates of Cleveland, Inc. (01-017)

Cleveland, Ohio, United States

Site Status

Retina Associates of Cleveland, Inc. (01-022)

Cleveland, Ohio, United States

Site Status

Retina Associates of Cleveland, Inc. (01-016)

Youngstown, Ohio, United States

Site Status

Mid Atlantic Retina (01-001)

Bethlehem, Pennsylvania, United States

Site Status

The Retina Care Center (01-034) - Satellite Site

York, Pennsylvania, United States

Site Status

Black Hills Regional Eye Institute (01-010)

Rapid City, South Dakota, United States

Site Status

Tennessee Retina (01-033)

Nashville, Tennessee, United States

Site Status

Integrated Clinical Research (01-024)

Abilene, Texas, United States

Site Status

Retina Consultants of Texas (01-004)

Bellaire, Texas, United States

Site Status

Texas Retina Associates (01-028)

Dallas, Texas, United States

Site Status

Retina Consultants of Texas (01-003)

The Woodlands, Texas, United States

Site Status

The Retina Group of Washington (01-021)

Fairfax, Virginia, United States

Site Status

Pacific Northwest Retina (01-036)

Bellevue, Washington, United States

Site Status

Countries

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United States

Other Identifiers

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APL2-GA-411

Identifier Type: -

Identifier Source: org_study_id

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