First-In-Human Study of STX-721/PFL-721 in Participants With Locally Advanced or Metastatic Non-Small Cell Lung Cancer Harboring EGFR or HER2 Exon 20 Insertion Mutations

NCT ID: NCT06043817

Last Updated: 2026-01-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

251 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-09-26

Study Completion Date

2029-12-01

Brief Summary

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Study STX-721-101/PFL-721CI101 is an open label, Phase 1/2 study evaluating the safety, tolerability, pharmacokinetic (PK) exposure, and preliminary antitumor activity of STX-721/PFL-721 in participants with non-small cell lung cancer (NSCLC) carrying EGFR or HER2 exon 20 insertion (ex20ins) mutations.

Detailed Description

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Conditions

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Non-Small Cell Lung Cancer NSCLC EGFR/HER2 Exon 20 Insertion Mutation

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Part 1: Dose Escalation

Group Type EXPERIMENTAL

STX-721/PFL-721 (Escalated)

Intervention Type DRUG

STX-721/PFL-721 dose will be escalated per cBLRM-design.

Part 2: RP2D Selection

Group Type EXPERIMENTAL

STX-721/PFL-721 (3 dose levels)

Intervention Type DRUG

Participants will receive STX-721/PFL-721 at one of three dose levels.

Part 3: Dose Expansion

Group Type EXPERIMENTAL

STX-721/PFL-721 (RP2D)

Intervention Type DRUG

Participants will receive the RP2D of STX-721/PFL-721.

Interventions

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STX-721/PFL-721 (Escalated)

STX-721/PFL-721 dose will be escalated per cBLRM-design.

Intervention Type DRUG

STX-721/PFL-721 (3 dose levels)

Participants will receive STX-721/PFL-721 at one of three dose levels.

Intervention Type DRUG

STX-721/PFL-721 (RP2D)

Participants will receive the RP2D of STX-721/PFL-721.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Has histologically- or cytologically confirmed diagnosis of NSCLC Stage IIIB/C or IV not eligible for curative intent surgery or chemoradiation
2. Part 1: Tumor tissue EGFR or HER2 exon 20 insertion mutations confirmed by qualified local laboratories. Parts 2 and 3: EGFR/HER2 exon 20 insertion mutations confirmed by qualified local laboratories
3. Part 1: Has received all approved therapies for advanced or metastatic NSCLC or is ineligible. Part 2 and Part 3: Has received at least 1, but not more than 2, prior lines of treatment for advanced or metastatic NSCLC, 1 of which must be platinum-based chemotherapy unless contraindicated
4. Has documented tumor progression (based on radiological imaging)
5. Has new or recent tumor biopsy (collected at screening, if feasible) or archival tumor specimen collected in the past 10 years available for genomic profiling
6. Has at least one measurable tumor lesion per RECIST v1.1
7. Is ≥18 years of age at the time of signing the ICF
8. Has Eastern Cooperative Oncology Group (ECOG) performance status score of 0 or 1

Exclusion Criteria

1. Has a tumor that is known to harbor EGFR ex20ins p.H773\_V774insH variant, or any EGFR kinase domain activating mutation concurrent with either a T790M and/or C797S resistance mutations
2. Has history (within ≤2 years before screening) of solid tumor or hematological malignancy that is histologically distinct from NSCLC
3. Has symptomatic brain or spinal metastases
4. Has toxicities from previous anticancer therapies that have not resolved to baseline levels or to CTCAE Grade ≤1, except for alopecia and peripheral neuropathy
5. Has any condition for which, in the opinion of the investigator, participation would not be in the best interest of the participant (e.g., could compromise the participant's well-being) or would prevent, limit, or confound the protocol-specified assessments
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pierre Fabre Medicament

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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City of Hope

Duarte, California, United States

Site Status RECRUITING

City of Hope

Huntington Beach, California, United States

Site Status RECRUITING

City of Hope

Irvine, California, United States

Site Status RECRUITING

Levine Cancer Institute - Charlotte

Charlotte, North Carolina, United States

Site Status RECRUITING

Thomas Jefferson University Research Facility

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

SCRI Oncology Partners - PPDS

Nashville, Tennessee, United States

Site Status RECRUITING

University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

University of Utah - Huntsman Cancer Institute - PPDS

Salt Lake City, Utah, United States

Site Status RECRUITING

NEXT Virginia

Fairfax, Virginia, United States

Site Status RECRUITING

EDOG Institut de Cancerologie de l'Ouest - PPDS

Saint-Herblain, Loire-Atlantique, France

Site Status RECRUITING

Institut Claudius Regaud - PPDS

Toulouse, , France

Site Status RECRUITING

Gustave Roussy

Villejuif, , France

Site Status RECRUITING

Charité - Universitätsmedizin Berlin (CBF) - Hindenburgdamm 30

Berlin, , Germany

Site Status RECRUITING

Universitätsklinikum Carl Gustav Carus an der TU Dresden

Dresden, , Germany

Site Status RECRUITING

Nederlands Kanker Instituut-Antoni van Leeuwenhoek Ziekenhuis

Amsterdam, , Netherlands

Site Status RECRUITING

Chungbuk National University Hospital

Cheongju-si, , South Korea

Site Status RECRUITING

CHA Bundang Medical Center, CHA University

Seongnam-si, , South Korea

Site Status RECRUITING

Hospital Regional Universitario de Malaga - Hospital General

Málaga, Malaga, Spain

Site Status RECRUITING

Instituto de Investigacion Oncologica Vall dHebron (VHIO) - EPON

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status RECRUITING

National Taiwan University Hospital

Taipei, , Taiwan

Site Status RECRUITING

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status RECRUITING

Countries

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United States France Germany Netherlands South Korea Spain Taiwan

Central Contacts

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Claire FABRE, Head of clinical development, MD, PhD

Role: CONTACT

+33 6 42 04 84 76

Other Identifiers

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STX-721-101/PFL-721CI101

Identifier Type: -

Identifier Source: org_study_id

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