A Master Protocol (LY900023) That Includes Several Clinical Trials of Drugs for Children and Young Adults With Cancer

NCT ID: NCT05999994

Last Updated: 2025-12-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

105 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-01-22

Study Completion Date

2027-05-31

Brief Summary

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The main purpose of the master is to help the research sites and sponsor carry out several clinical trials more efficiently by providing a common research protocol. Individual clinical trials under this master protocol define drug/disease-specific research goals and activities to test them. New studies will be added as new drugs emerge against different cancers. Participation in the trial will depend on how long the benefit lasts.

Detailed Description

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Conditions

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Neoplasms Child Adolescent

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Ramucirumab + Cyclophosphamide + Vinorelbine (DSRCT ISA)

Ramucirumab given intravenously (IV), cyclophosphamide given orally and vinorelbine given IV in 28-day cycles for desmoplastic small round cell tumor (DSRCT) intervention-specific appendix (ISA).

Group Type EXPERIMENTAL

Ramucirumab

Intervention Type DRUG

Administered IV

Cyclophosphamide

Intervention Type DRUG

Administered orally

Vinorelbine

Intervention Type DRUG

Administered IV

Cyclophosphamide + Vinorelbine (DSRCT ISA)

Cyclophosphamide given orally and vinorelbine given IV in 28-day cycles for DSRCT ISA.

Group Type ACTIVE_COMPARATOR

Cyclophosphamide

Intervention Type DRUG

Administered orally

Vinorelbine

Intervention Type DRUG

Administered IV

Ramucirumab + Gemcitabine + Docetaxel (SS ISA)

Ramucirumab and gemcitabine given IV in 21-day cycles for synovial sarcoma (SS) ISA.

Group Type EXPERIMENTAL

Ramucirumab

Intervention Type DRUG

Administered IV

Gemcitabine

Intervention Type DRUG

Administered IV

Docetaxel

Intervention Type DRUG

Administered IV

Gemcitabine + Docetaxel (SS ISA)

Gemcitabine and docetaxel given IV in 21-day cycles for SS ISA.

Group Type ACTIVE_COMPARATOR

Gemcitabine

Intervention Type DRUG

Administered IV

Docetaxel

Intervention Type DRUG

Administered IV

Abemaciclib + Irinotecan + Temozolomide (ES ISA)

Abemaciclib given orally, irinotecan given IV, and temozolomide given orally in 21-day cycles for Ewing's sarcoma (ES) ISA.

Group Type EXPERIMENTAL

Abemaciclib

Intervention Type DRUG

Administered orally

Irinotecan

Intervention Type DRUG

Administered IV

Temozolomide

Intervention Type DRUG

Administered orally

Irinotecan + Temozolomide (ES ISA)

Irinotecan given IV and temozolomide given orally in 21-day cycles for ES ISA.

Group Type ACTIVE_COMPARATOR

Irinotecan

Intervention Type DRUG

Administered IV

Temozolomide

Intervention Type DRUG

Administered orally

Interventions

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Ramucirumab

Administered IV

Intervention Type DRUG

Cyclophosphamide

Administered orally

Intervention Type DRUG

Vinorelbine

Administered IV

Intervention Type DRUG

Gemcitabine

Administered IV

Intervention Type DRUG

Docetaxel

Administered IV

Intervention Type DRUG

Abemaciclib

Administered orally

Intervention Type DRUG

Irinotecan

Administered IV

Intervention Type DRUG

Temozolomide

Administered orally

Intervention Type DRUG

Other Intervention Names

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LY3009806 LY188011 LY2835219

Eligibility Criteria

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Inclusion Criteria

* Have either measurable or evaluable disease using standard techniques by the Response Evaluation Criteria in Solid Tumors, Version 1.1 (RECIST 1.1).
* The participant has a Lansky (\<16 years of age) or Karnofsky (≥16 years of age) performance score of at least 50.
* Participants must have discontinued all previous treatments for cancer or investigational agents greater than or equal to (≥)7 days after the last dose and must have recovered from clinically significant side effects.
* The participant has adequate hematologic and organ function.
* Female participants of childbearing potential must have a negative urine or serum pregnancy test within 7 days prior to first dose.
* Both female and male participants of childbearing potential must agree to use highly effective contraceptive precautions during the trial and for at least 3 months following the last dose of study drug.

Exclusion Criteria

* Participants with severe and/or uncontrolled concurrent medical disease or psychiatric illness/social situation that, in the opinion of the investigator, could cause unacceptable safety risks or compromise compliance with the protocol.
* Participants who have active infections requiring therapy.
* Participants who have had allogeneic bone marrow or solid organ transplant.
* Participants who have had, or are planning to have, certain invasive procedures.
* Female participants who are pregnant or breastfeeding.
Minimum Eligible Age

1 Year

Maximum Eligible Age

39 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eli Lilly and Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 8 AM - 8 PM Eastern time (UTC/GMT - 5 hours, EST)

Role: STUDY_DIRECTOR

Eli Lilly and Company

Locations

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Childrens Hospital of Alabama

Birmingham, Alabama, United States

Site Status NOT_YET_RECRUITING

Phoenix Children's Hospital

Phoenix, Arizona, United States

Site Status RECRUITING

Phoenix Children's Hospital

Phoenix, Arizona, United States

Site Status RECRUITING

Childrens Hospital of Los Angeles

Los Angeles, California, United States

Site Status COMPLETED

UCLA Medical Center

Los Angeles, California, United States

Site Status NOT_YET_RECRUITING

Children's Hospital of Orange County

Orange, California, United States

Site Status RECRUITING

Children's Hospital of Colorado

Denver, Colorado, United States

Site Status RECRUITING

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Golisano Children's Hospital of Southwest Florida

Fort Myers, Florida, United States

Site Status RECRUITING

Mayo Clinic in Florida

Jacksonville, Florida, United States

Site Status RECRUITING

Children's Healthcare of Atlanta, Inc. at Egleston

Atlanta, Georgia, United States

Site Status NOT_YET_RECRUITING

Ann & Robert H Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

Site Status RECRUITING

Riley Hospital for Children

Indianapolis, Indiana, United States

Site Status ACTIVE_NOT_RECRUITING

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status NOT_YET_RECRUITING

C.S. Mott Children's Hospital

Ann Arbor, Michigan, United States

Site Status NOT_YET_RECRUITING

University of Minnesota Hospital

Minneapolis, Minnesota, United States

Site Status NOT_YET_RECRUITING

Children's Mercy Hospital

Kansas City, Missouri, United States

Site Status RECRUITING

Washington University Medical School

St Louis, Missouri, United States

Site Status COMPLETED

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status RECRUITING

Nationwide Children's Hosp

Columbus, Ohio, United States

Site Status RECRUITING

Oregon Health and Science University

Portland, Oregon, United States

Site Status NOT_YET_RECRUITING

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status COMPLETED

UPMC Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Lifespan Cancer Institute

Providence, Rhode Island, United States

Site Status RECRUITING

University of Texas Southwestern Medical Center at Dallas

Dallas, Texas, United States

Site Status RECRUITING

Cook Children's Hospital

Fort Worth, Texas, United States

Site Status ACTIVE_NOT_RECRUITING

Texas Childrens Hospital

Houston, Texas, United States

Site Status NOT_YET_RECRUITING

University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Seattle Children's Hospital Research Foundation

Seattle, Washington, United States

Site Status RECRUITING

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status NOT_YET_RECRUITING

Chris O'Brien Lifehouse

Camperdown, , Australia

Site Status RECRUITING

Peter MacCallum Cancer Centre

Melbourne, , Australia

Site Status RECRUITING

Royal Children's Hospital

Melbourne, , Australia

Site Status RECRUITING

The Sydney Children's Hospitals Network

Westmead, , Australia

Site Status NOT_YET_RECRUITING

UCL- Saint Luc

Brussels, , Belgium

Site Status RECRUITING

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status COMPLETED

Institut Bergonié - Centre Régional de Lutte Contre Le Cancer de Bordeaux et Sud Ouest

Bordeaux, , France

Site Status RECRUITING

Centre Leon Berard

Lyon, , France

Site Status NOT_YET_RECRUITING

Centre Leon Berard

Lyon, , France

Site Status RECRUITING

Institut Curie

Paris, , France

Site Status NOT_YET_RECRUITING

Universitaetsklinikum Essen

Essen, , Germany

Site Status RECRUITING

Universitaetsklinikum Freiburg

Freiburg im Breisgau, , Germany

Site Status RECRUITING

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status RECRUITING

IRCCS Istituto Ortopedico Rizzoli

Bologna, , Italy

Site Status RECRUITING

Istituto di Candiolo IRCCS - Fondazione del Piemonte per l'Oncologia

Candiolo, , Italy

Site Status RECRUITING

Istituto Nazionale dei Tumori

Milan, , Italy

Site Status RECRUITING

Azienda Ospedaliera Di Padova

Padua, , Italy

Site Status RECRUITING

Ospedale Bambino Gesu

Roma, , Italy

Site Status RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS - Università Cattolica del Sacro Cuore

Roma, , Italy

Site Status RECRUITING

Istituto Clinico Humanitas

Rozzano, , Italy

Site Status RECRUITING

National Cancer Center Hospital

Chūōku, , Japan

Site Status RECRUITING

Kyushu University Hospital

Fukuoka, , Japan

Site Status RECRUITING

Hyogo Prefectural Kobe Children's Hospital

Kobe, , Japan

Site Status RECRUITING

Leids Universitair Medisch Centrum

Leiden, , Netherlands

Site Status RECRUITING

Prinses Maxima Centrum

Utrecht, , Netherlands

Site Status RECRUITING

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status RECRUITING

Hospital Sant Joan de Déu

Esplugues de Llobregat, , Spain

Site Status RECRUITING

Hospital General Universitario Gregorio Marañon

Madrid, , Spain

Site Status RECRUITING

Hospital General Universitario Gregorio Marañon

Madrid, , Spain

Site Status RECRUITING

Hospital Infantil Universitario Niño Jesús

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario de Canarias

San Cristóbal de La Laguna, , Spain

Site Status RECRUITING

Hospital Universitario Virgen Del Rocio

Seville, , Spain

Site Status RECRUITING

Hospital Universitario Virgen Del Rocio

Seville, , Spain

Site Status RECRUITING

Hospital Universitari i Politecnic La Fe

Valencia, , Spain

Site Status RECRUITING

University College Hospital - London

London, , United Kingdom

Site Status RECRUITING

Royal Marsden Hospital

London, , United Kingdom

Site Status RECRUITING

Royal Marsden Hospital

London, , United Kingdom

Site Status RECRUITING

Royal Manchester Children's Hospital

Manchester, , United Kingdom

Site Status RECRUITING

The Christie NHS Foundation Trust

Manchester, , United Kingdom

Site Status RECRUITING

Countries

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United States Australia Belgium France Germany Italy Japan Netherlands Spain United Kingdom

Central Contacts

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Trial questions or participation questions: 1-877-CTLILLY (1-877-285-4559) or

Role: CONTACT

1-317-615-4559

Physicians interested in becoming principal investigators please contact

Role: CONTACT

Facility Contacts

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Role: primary

602-546-0990

Role: primary

720-777-6740

Role: primary

202-476-4744

Role: primary

239-343-5437

Role: primary

904-953-2000

Role: primary

404-785-0910

Role: primary

312-227-4834

Role: primary

617-632-5869

Role: primary

734-615-7790

Role: primary

612-626-3593

Role: primary

816-302-6808

Role: primary

212-639-8856

Role: primary

614-355-1202

Role: primary

503-494-4671

Role: primary

401-829-6552

Role: primary

832-824-4632

Role: primary

713-745-6754

Role: primary

206-987-2114

Role: primary

414-456-4170

Role: primary

61290365375

Role: primary

61385598339

Role: primary

61298452138

Role: primary

3227642376

Role: primary

33547306088

Role: primary

33478785126

Role: primary

+33478782642

Role: primary

33144324068

Role: primary

492017232255

Role: primary

4976127043010

Role: primary

4940741020622

Role: primary

390516366411

Role: primary

390119933278

Role: primary

39022393062

Role: primary

390668592444

Role: primary

81120023812

Role: primary

81120023812

Role: primary

81120023812

Role: primary

31715263459

Role: primary

31650006353

Role: primary

0034934894695

Role: primary

34932532100

Role: primary

34917277516

Role: primary

34955923113

Role: primary

34955012593

Role: primary

00442034479346

Role: primary

00442073528171

Role: primary

00441617018430

Role: primary

01614463000

Provided Documents

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Document Type: Study Protocol

View Document

Other Identifiers

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J1S-MC-JAAA

Identifier Type: OTHER

Identifier Source: secondary_id

17304

Identifier Type: -

Identifier Source: org_study_id

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