Determine Effectiveness of Anifrolumab In SYstemic Sclerosis (DAISY)

NCT ID: NCT05925803

Last Updated: 2026-02-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

314 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-11-08

Study Completion Date

2027-12-31

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of treatment with subcutaneous anifrolumab versus placebo in adult participants with systemic sclerosis. The target population for this study includes patients who meet the 2013 American College of Rheumatology/European League Against Rheumatism (ACR/EULAR) classification for systemic sclerosis, either limited or diffuse cutaneous subsets, with a disease duration of less than 6 years from first non-Raynaud's phenomenon symptom.

Detailed Description

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This is a multicenter, randomized, double-blind, placebo-controlled, Phase III study to evaluate the efficacy and safety of anifrolumab in the treatment of adult participants with Systemic Sclerosis (SSc) who may be taking one or a combination of protocol-specified standard therapies. The use of one of the following standard immunosuppressant therapies is permitted at a stable dose, but not mandated: hydroxychloroquine, mycophenolate mofetil (MMF), mycophenolic acid or mycophenolate sodium (MPA/MPS), methotrexate, azathioprine, tacrolimus, and oral glucocorticoids. MMF or MPA/MPS, azathioprine, and methotrexate may be used in combination with hydroxychloroquine and/or low-dose oral glucocorticoids \[≤ 10 mg/day\].

Approximately 306 eligible participants will be randomized in a 1:1 ratio to receive either anifrolumab (or matching placebo) given subcutaneously once weekly for 52 weeks. The study will be stratified by the following factors:

* Interstitial lung disease (ILD) (yes, no) at Week 0 (Day1);
* MMF or MPA/MPS use (yes ,no) at Week 0 (Day 1); and
* Disease duration, defined as the time from the first non-Raynaud's symptom attributable to SSc (\<18 months, ≥ 18 months) at Week 0 (Day 1)

Study treatment will be administered subcutaneously via an accessorized prefilled syringe by study staff or by the participant or carer, either in the clinic or at home, with most doses being administered at home. The study consists of 4 periods: a 6-week screening period, a 52-week, double-blind, placebo-controlled period, a 52-week open-label active treatment period, and a 12-week safety follow-up period. There are a total of 16 study visits with most visits in the treatment period occurring every 8 to 12 weeks. The periods are described below:

* Screening Period: This may involve one or more visits to the study site.
* Double Blind Treatment Period: Treatment Period when participants will receive once weekly injections of anifrolumab or matching placebo. Participation will involve in-clinic study visits at Weeks 0 (Day 1), 1, 4, 8\*, 16, 24, 36, 48 and 52. \*The visit at Week 8 may be either by telephone or in person.
* Open Label Treatment Period: At Week 52, all participants will be given anifrolumab (subcutaneous) once weekly for 52 weeks (last dose at Week 103). Participation will involve in-clinic study visits at Weeks 52, 53\*, 56, 64, 76. 88 and 104. \*The visit at Week 53 may be either by telephone or in person.
* Safety Follow-up Period: All participants will return to the clinic for a 12-week post treatment visit. This will occur post Double Blind Treatment Period (Week 52 or Double Blind Period early discontinuation) or post Open Label Treatment Period (Week 104 or Open Label Period early discontinuation).

Conditions

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Systemic Sclerosis Scleroderma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Subjects will be randomized in a 1:1 ratio to either anifrolumab or matching placebo for 52 weeks (double blind treatment period). At Week 52, all patients will be treated with Anifrolumab for 52 weeks (open label treatment period).
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Double blind period- masking -everyone will be masked to the treatment allocation during the first 52 weeks Open label period - no masking- beginning at week 52, all participants will receive Anifrolumab for 52 weeks. During the open label period, there is no masking of study treatment, however, the treatment that participants received in the double blind period (first 52 weeks) will remain masked until the end of the study.

Study Groups

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Anifrolumab (subcutaneous weekly injection)

Anifrolumab subcutaneous injection once weekly

Group Type EXPERIMENTAL

Anifrolumab (blinded)

Intervention Type COMBINATION_PRODUCT

Anifrolumab treatment delivered subcutaneously, once weekly for 52 weeks

Anifrolumab (unblinded, open label)

Intervention Type COMBINATION_PRODUCT

At Week 52, all patients will receive Anifrolumab subcutaneously once weekly for 52 weeks

matched placebo control (subcutaneous weekly injection)

matched placebo control subcutaneous injection once weekly

Group Type PLACEBO_COMPARATOR

Placebo (blinded)

Intervention Type DRUG

matched placebo delivered subcutaneously, once weekly for 52 weeks

Interventions

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Anifrolumab (blinded)

Anifrolumab treatment delivered subcutaneously, once weekly for 52 weeks

Intervention Type COMBINATION_PRODUCT

Placebo (blinded)

matched placebo delivered subcutaneously, once weekly for 52 weeks

Intervention Type DRUG

Anifrolumab (unblinded, open label)

At Week 52, all patients will receive Anifrolumab subcutaneously once weekly for 52 weeks

Intervention Type COMBINATION_PRODUCT

Other Intervention Names

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Treatment arm (blinded) Placebo arm (blinded) Treatment arm (not blinded)

Eligibility Criteria

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Inclusion Criteria

1. Adult patients from 18 to 70 years of age inclusive
2. Systemic sclerosis according to 2013 ACR/EULAR classification criteria
3. Limited or diffuse cutaneous subsets
4. Systemic sclerosis disease duration within 6 years from first non-Raynaud's phenomenon manifestation at the time of signing the ICF
5. Either HAQ-DI score ≥ 0.25 points or PtGA score ≥ 3 points
6. mRSS \> 10 with early disease or rapid progression as defined by the protocol
7. mRSS ≥ 15 with disease duration ≥ 18 months and active disease as defined by the protocol
8. Stable background therapies can be used including hydroxychloroquine, methotrexate, azathioprine, mycophenolate mofetil, mycophenolate sodium, mycophenolic acid, oral glucocorticoids or tacrolimus
9. Women of childbearing potential with a negative urine pregnancy test
10. Uninvolved skin at injection sites

Exclusion Criteria

1. Anticentromere antibody seropositivity on central laboratory
2. Severe cardiopulmonary disease as defined by the protocol
3. History of systemic sclerosis renal crisis within past 12 months (estimated glomerular filtration rate(eGFR) \< 45 mL/min/1.73m2)
4. Overlap syndromes, systemic lupus erythematosus with anti-double-stranded deoxyribonucleic acid antibody seropositivity or anti-citrullinated protein antibodies-positive rheumatoid arthritis, or SSc mimics (eg, scleromyxedema, eosinophilic fasciitis)
5. History of, or current, any other inflammatory diseases, eg, inflammatory bowel disease, skin disease, that, in the opinion of the investigator, could interfere with efficacy and safety assessments or require immunomodulatory therapy
6. Evidence of moderately severe concurrent nervous system, renal, endocrine, hepatic (eg, underlying chronic liver disease \[Child Pugh A, B, C hepatic impairment\]), or gastrointestinal disease (eg, clinical signs of malabsorption or needing parenteral nutrition) not related to SSc, as determined by the investigator
7. Hematopoietic stem cell transplantation or solid organ/limb transplantation
8. Any severe case of Herpes Zoster infection as defined by the protocol
9. Known malignancy or a history of malignancy within 5 years, with exception of excised/cured local basal or squamous cell carcinoma of the skin or carcinoma in situ of the uterine cervix
10. Major surgery within 8 weeks prior to and/or during study enrollment
11. Known active current or history of recurrent infections
12. Any condition that, in the opinion of the investigator or AstraZeneca, would interfere with the efficacy or safety evaluation of the study intervention or put participant at safety risk
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Research Site

Scottsdale, Arizona, United States

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Chula Vista, California, United States

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Los Angeles, California, United States

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Orange, California, United States

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Aurora, Colorado, United States

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New Haven, Connecticut, United States

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Washington D.C., District of Columbia, United States

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Boca Raton, Florida, United States

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Fort Lauderdale, Florida, United States

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Gainesville, Florida, United States

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Jacksonville, Florida, United States

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Margate, Florida, United States

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South Miami, Florida, United States

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Tamarac, Florida, United States

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Chicago, Illinois, United States

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Kansas City, Kansas, United States

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New Orleans, Louisiana, United States

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Baltimore, Maryland, United States

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Ann Arbor, Michigan, United States

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Rochester, Minnesota, United States

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Babylon, New York, United States

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New York, New York, United States

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Cincinnati, Ohio, United States

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Pittsburgh, Pennsylvania, United States

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Allen, Texas, United States

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Houston, Texas, United States

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Graz, , Austria

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Innsbruck, , Austria

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Vienna, , Austria

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Ghent, , Belgium

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Leuven, , Belgium

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Calgary, Alberta, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Montreal, Quebec, Canada

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Québec, , Canada

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Beijing, , China

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Beijing, , China

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Guangzhou, , China

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Guangzhou, , China

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Hangzhou, , China

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Lanzhou, , China

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Shanghai, , China

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Shanghai, , China

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Tianjin, , China

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Bordeaux, , France

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Brest, , France

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Paris, , France

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Paris, , France

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Rennes, , France

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Strasbourg, , France

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Toulouse, , France

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Freiburg im Breisgau, , Germany

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Mainz, , Germany

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Minden, , Germany

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Münster, , Germany

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Tübingen, , Germany

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Pécs, , Hungary

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Szeged, , Hungary

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Ahmedabad, , India

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Delhi, , India

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Gurugram, , India

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Hyderabad, , India

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Kolkata, , India

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Mumbai, , India

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Mysuru, , India

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New Delhi, , India

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Pune, , India

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Secunderabad, , India

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Afula, , Israel

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Haifa, , Israel

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Haifa, , Israel

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Jerusalem, , Israel

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Kfar Saba, , Israel

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Ramat Gan, , Israel

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Ancona, , Italy

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Brescia, , Italy

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Cona, , Italy

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Milan, , Italy

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Padua, , Italy

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Roma, , Italy

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Roma, , Italy

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Roma, , Italy

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Bunkyō City, , Japan

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Fukuoka, , Japan

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Iruma-Gun, , Japan

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Kanazawa, , Japan

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Maebashi, , Japan

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Nagasaki, , Japan

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Nagoya, , Japan

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Sapporo, , Japan

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Sendai, , Japan

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Shinjuku-ku, , Japan

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Shinjuku-ku, , Japan

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Suita-shi, , Japan

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Takatsuki-shi, , Japan

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Toyoake-shi, , Japan

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Yokohama, , Japan

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Kuala Lumpur, , Malaysia

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Kuching, , Malaysia

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Seremban, , Malaysia

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Chihuahua City, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Mexico City, , Mexico

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San Luis Potosí City, , Mexico

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San Luis Potosí City, , Mexico

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Groningen, , Netherlands

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Bydgoszcz, , Poland

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Krakow, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Sosnowiec, , Poland

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Warsaw, , Poland

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Bucharest, , Romania

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Bucharest, , Romania

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Cluj-Napoca, , Romania

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Iași, , Romania

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Parktown, , South Africa

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Pretoria, , South Africa

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Busan, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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A Coruña, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Madrid, , Spain

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Málaga, , Spain

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Valencia, , Spain

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Valencia, , Spain

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Ankara, , Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Antalya, , Turkey (Türkiye)

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Kazımkarabekir, , Turkey (Türkiye)

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Kocaeli, , Turkey (Türkiye)

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Merkez, , Turkey (Türkiye)

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Cannock, , United Kingdom

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Leeds, , United Kingdom

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London, , United Kingdom

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Sheffield, , United Kingdom

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Hanoi, , Vietnam

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Hà Nội, , Vietnam

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Ho Chi Minh City, , Vietnam

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Ho Chi Minh City, , Vietnam

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Hochiminh, , Vietnam

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Countries

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United States Austria Belgium Canada China France Germany Hungary India Israel Italy Japan Malaysia Mexico Netherlands Poland Romania South Africa South Korea Spain Turkey (Türkiye) United Kingdom Vietnam

Other Identifiers

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2023-505976-31

Identifier Type: OTHER

Identifier Source: secondary_id

D3460C00002

Identifier Type: -

Identifier Source: org_study_id

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