A Clinical Study to Evaluate Ianalumab in Participants With Diffuse Cutaneous Systemic Sclerosis

NCT ID: NCT06470048

Last Updated: 2025-12-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

200 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-10-09

Study Completion Date

2030-07-15

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to evaluate efficacy, safety and tolerability of s.c. ianalumab administered in participants with diffuse cutaneous systemic sclerosis relative to placebo

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

The study consists of the following periods:

* Screening Period, with a duration of up to 6 weeks;
* Treatment Period 1, with a duration of 52 weeks;
* Treatment Period 2 (Open-label treatment), with a duration of 52 weeks;
* Post-treatment Follow-up Period, with a duration of at least 20 weeks post last dose and up to 2 years.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Diffuse Cutaneous Systemic Sclerosis

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

Diffuse Cutaneous Systemic Sclerosis (dcSSc) Diffuse Scleroderma Diffuse Systemic Sclerosis Scleroderma, Diffuse Scleroderma, Progressive Sclerosis, Progressive Systemic Sudden Onset Scleroderma B cell depletion Revised Composite Response Index in Systemic Sclerosis 25 (rCRISS25) modified Rodnan skin score forced vital capacity

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

VAY736 (Ianalumab)

Treatment Period 1:

Ianalumab subcutaneous (s.c.) injection as defined in the protocol

Treatment Period 2:

Open-label (OL) Ianalumab subcutaneous (s.c.) injection as defined in the protocol

Group Type EXPERIMENTAL

Ianalumab

Intervention Type DRUG

subcutaneous (s.c.) injection as defined in the protocol

Placebo

Treatment Period 1:

Placebo to Ianalumab subcutaneous (s.c.) injection as defined in the protocol

Treatment Period 2:

Open-label (OL) Ianalumab subcutaneous (s.c.) injection as defined in the protocol

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Ianalumab matching placebo subcutaneous (s.c.) injection as defined in the protocol

Ianalumab

Intervention Type DRUG

subcutaneous (s.c.) injection as defined in the protocol

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Placebo

Ianalumab matching placebo subcutaneous (s.c.) injection as defined in the protocol

Intervention Type DRUG

Ianalumab

subcutaneous (s.c.) injection as defined in the protocol

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

VAY736

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Male and female participants \>= 18 and =\< 70 years (at the time of the screening visit).
* Diagnosis of systemic sclerosis, as defined by the 2013 American College of Rheumatology/ European League Against Rheumatism (ACR/EULAR) classification criteria for SSc (van den Hoogen et al 2013) and meet the dcSSc subset classification according to LeRoy (LeRoy 1988)
* Disease duration of =\< 60 months (defined as time from the first non-Raynaud phenomenon manifestation, e.g., puffy hands, scleroderma, digital ulcers, arthralgia, dyspnea)
* mRSS units of \>= 15 and =\< 45 at the time of the screening visit
* Active disease that meets at least one of the following criteria at screening:

* Disease duration of =\< 18 months defined as time from the first non-Raynaud phenomenon manifestation
* Increase in mRSS of \>= 3 units compared with the most recent assessment performed within the previous 6 months
* Involvement of one new body area and an increase in mRSS of \>= 2 units compared with the most recent assessment performed within the previous 6 months
* Involvement of two new body areas within the previous 6 months
* Elevated acute phase reactants (ESR) \>= 30 mm/hr or high-sensitivity C-reactive protein (hsCRP) \>= 6 mg/L)
* Presence of SSc-interstitial lung disease (ILD) and ATA autoantibody positivity
* Modified EUSTAR disease activity index (mDAI) ≥ 2.5
* Participant must be positive for at least one of the following autoantibodies:

* anti-topoisomerase I (ATA) (also known as anti-SCL-70)
* anti-RNA polymerase III (anti-RNAP3)
* anti-nuclear antibody (ANA) (≥ 1:80) Participants who are positive only for ANA (while being negative for both ATA /anti-RNAP3) will be limited to 30% of the overall randomized study population.

* Treatment with any investigational agent within ≤ 4 weeks (or 5 half-lives of the investigational drug, whichever is longer) of the baseline visit.
* Use of anti-fibrotic agents including colchicine, D-penicillamine, pirfenidone, or tyrosine kinase inhibitors (e.g., nintedanib, nilotinib, imatinib, dasatinib) in the 4 weeks prior to baseline visit. Patients with SSc-ILD requiring antifibrotics for management of ILD during the study, as per investigator judgement, should be excluded.
* Previous treatment with chlorambucil, bone marrow transplantation or total lymphoid irradiation.
* Women of childbearing potential, defined as all women physiologically capable of becoming pregnant from menarche until becoming post-menopausal, unless they are using highly effective methods of contraception (failure rate \< 1% per year) while taking study treatment and for 6 months after stopping study treatment.

Exclusion Criteria

* Rheumatic disease other than dcSSc, including limited cutaneous disease (lcSSc) or sine scleroderma at the screening visit. Secondary Sjogren's disease and scleroderma myopathy are not exclusionary.
* Positive anti-centromere antibody (ACA+) without positive ATA or anti-RNAP3 autoantibody result at the screening visit
* Previous improvement (decrease) in mRSS \> 10 units
* Pulmonary disease with FVC ≤ 50% of predicted or diffusing capacity of the lung for carbon monoxide (DLCO, corrected for hemoglobin) ≤ 40% of predicted at the screening visit
* WHO Functional Class 3 or higher assessment for pulmonary arterial hypertension (PAH, as defined on right heart catheterization), receiving IV therapy for PAH or evidence of other moderately severe pulmonary disease
* Participants treated with cyclophosphamide within 12 weeks prior to Baseline.
* Prior use of a B-cell depleting therapy other than ianalumab (e.g., rituximab, other anti-CD20 mAb, anti-CD22 mAb, or anti-CD52 mAb) administered within 36 weeks prior to randomization, or as long as B cell count is less than the lower limit of normal or baseline value prior to receipt of B cell-depleting therapy (whichever is lower).
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Arizona Arthritis and Rheumatology Research PLLC

Mesa, Arizona, United States

Site Status RECRUITING

UCLA

Los Angeles, California, United States

Site Status RECRUITING

Hoag Hospital

Newport Beach, California, United States

Site Status RECRUITING

Clinical Res Of W Florida

Clearwater, Florida, United States

Site Status RECRUITING

GNP Research

Cooper City, Florida, United States

Site Status RECRUITING

IRIS Research and Development

Plantation, Florida, United States

Site Status RECRUITING

Sarasota Arthritis Res Ctr

Sarasota, Florida, United States

Site Status RECRUITING

University of Chicago Hospitals

Chicago, Illinois, United States

Site Status RECRUITING

UMC New Orleans

New Orleans, Louisiana, United States

Site Status RECRUITING

Uni Of Michigan Health System

Ann Arbor, Michigan, United States

Site Status RECRUITING

Clinical Research Inst of MI

Saint Clair Shores, Michigan, United States

Site Status RECRUITING

West Tennessee Research Institute

Jackson, Tennessee, United States

Site Status RECRUITING

Arthritis and Rheumatology Ins

Allen, Texas, United States

Site Status RECRUITING

Novel Research LLC

Bellaire, Texas, United States

Site Status RECRUITING

Prolato Clinical Research Center

Houston, Texas, United States

Site Status RECRUITING

Novartis Investigative Site

CABA, Buenos Aires, Argentina

Site Status RECRUITING

Novartis Investigative Site

CABA, Buenos Aires, Argentina

Site Status RECRUITING

Novartis Investigative Site

Caba, , Argentina

Site Status RECRUITING

Novartis Investigative Site

Caba, , Argentina

Site Status RECRUITING

Novartis Investigative Site

San Miguel de Tucumán, , Argentina

Site Status RECRUITING

Novartis Investigative Site

Graz, , Austria

Site Status RECRUITING

Novartis Investigative Site

Leuven, , Belgium

Site Status RECRUITING

Novartis Investigative Site

Salvador, Estado de Bahia, Brazil

Site Status RECRUITING

Novartis Investigative Site

Curitiba, Paraná, Brazil

Site Status RECRUITING

Novartis Investigative Site

Porto Alegre, Rio Grande do Sul, Brazil

Site Status RECRUITING

Novartis Investigative Site

Sao Jose Rio Preto, São Paulo, Brazil

Site Status RECRUITING

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Site Status RECRUITING

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Site Status RECRUITING

Novartis Investigative Site

Nanning, Guangxi, China

Site Status RECRUITING

Novartis Investigative Site

Zhengzhou, Henan, China

Site Status RECRUITING

Novartis Investigative Site

Changchun, Jilin, China

Site Status RECRUITING

Novartis Investigative Site

Chengdu, Sichuan, China

Site Status RECRUITING

Novartis Investigative Site

Ningbo, Zhejiang, China

Site Status RECRUITING

Novartis Investigative Site

Beijing, , China

Site Status RECRUITING

Novartis Investigative Site

Beijing, , China

Site Status RECRUITING

Novartis Investigative Site

Tianjin, , China

Site Status RECRUITING

Novartis Investigative Site

Medellín, Antioquia, Colombia

Site Status RECRUITING

Novartis Investigative Site

Bogota, Cundinamarca, Colombia

Site Status RECRUITING

Novartis Investigative Site

Bogota, Cundinamarca, Colombia

Site Status RECRUITING

Novartis Investigative Site

Cali, Valle del Cauca Department, Colombia

Site Status RECRUITING

Novartis Investigative Site

Bogotá, , Colombia

Site Status RECRUITING

Novartis Investigative Site

Medellín, , Colombia

Site Status RECRUITING

Novartis Investigative Site

Dijon, , France

Site Status RECRUITING

Novartis Investigative Site

Le Mans, , France

Site Status RECRUITING

Novartis Investigative Site

Lille, , France

Site Status RECRUITING

Novartis Investigative Site

Montpellier, , France

Site Status RECRUITING

Novartis Investigative Site

Paris, , France

Site Status RECRUITING

Novartis Investigative Site

Rennes, , France

Site Status RECRUITING

Novartis Investigative Site

Strasbourg, , France

Site Status RECRUITING

Novartis Investigative Site

Toulouse, , France

Site Status RECRUITING

Novartis Investigative Site

Würzburg, Bavaria, Germany

Site Status RECRUITING

Novartis Investigative Site

Jena, Thuringia, Germany

Site Status RECRUITING

Novartis Investigative Site

Berlin, , Germany

Site Status RECRUITING

Novartis Investigative Site

Alexandroupoli, , Greece

Site Status RECRUITING

Novartis Investigative Site

Athens, , Greece

Site Status RECRUITING

Novartis Investigative Site

Athens, , Greece

Site Status RECRUITING

Novartis Investigative Site

Pécs, Baranya, Hungary

Site Status RECRUITING

Novartis Investigative Site

Debrecen, Hajdu Bihar Megye, Hungary

Site Status RECRUITING

Novartis Investigative Site

Kochi, Kerala, India

Site Status RECRUITING

Novartis Investigative Site

Mumbai, Maharashtra, India

Site Status RECRUITING

Novartis Investigative Site

Mumbai, Maharashtra, India

Site Status RECRUITING

Novartis Investigative Site

New Delhi, National Capital Territory of Delhi, India

Site Status RECRUITING

Novartis Investigative Site

Jaipur, Rajasthan, India

Site Status RECRUITING

Novartis Investigative Site

New Delhi, , India

Site Status RECRUITING

Novartis Investigative Site

Ancona, AN, Italy

Site Status RECRUITING

Novartis Investigative Site

Milan, MI, Italy

Site Status RECRUITING

Novartis Investigative Site

Rozzano, MI, Italy

Site Status RECRUITING

Novartis Investigative Site

Modena, MO, Italy

Site Status RECRUITING

Novartis Investigative Site

Palermo, PA, Italy

Site Status RECRUITING

Novartis Investigative Site

Pavia, PV, Italy

Site Status RECRUITING

Novartis Investigative Site

Roma, RM, Italy

Site Status RECRUITING

Novartis Investigative Site

Verona, VR, Italy

Site Status RECRUITING

Novartis Investigative Site

Nagoya, Aichi-ken, Japan

Site Status RECRUITING

Novartis Investigative Site

Kitakyushu, Fukuoka, Japan

Site Status RECRUITING

Novartis Investigative Site

Maebashi, Gunma, Japan

Site Status RECRUITING

Novartis Investigative Site

Sapporo, Hokkaido, Japan

Site Status RECRUITING

Novartis Investigative Site

Sapporo, Hokkaido, Japan

Site Status RECRUITING

Novartis Investigative Site

Kanazawa, Ishikawa-ken, Japan

Site Status RECRUITING

Novartis Investigative Site

Yokohama, Kanagawa-ku, Japan

Site Status RECRUITING

Novartis Investigative Site

Iruma-gun, Saitama, Japan

Site Status RECRUITING

Novartis Investigative Site

Bunkyo-ku, Tokyo, Japan

Site Status RECRUITING

Novartis Investigative Site

Chuo Ku, Tokyo, Japan

Site Status RECRUITING

Novartis Investigative Site

Shinjuku Ku, Tokyo, Japan

Site Status RECRUITING

Novartis Investigative Site

Fukuoka, , Japan

Site Status RECRUITING

Novartis Investigative Site

Hiroshima, , Japan

Site Status RECRUITING

Novartis Investigative Site

Toyama, , Japan

Site Status RECRUITING

Novartis Investigative Site

Cheras, Kuala Lumpur, Malaysia

Site Status RECRUITING

Novartis Investigative Site

Kuala Lumpur, , Malaysia

Site Status RECRUITING

Novartis Investigative Site

Guadalajara, Jalisco, Mexico

Site Status RECRUITING

Novartis Investigative Site

Mexico City, Mexico City, Mexico

Site Status RECRUITING

Novartis Investigative Site

Mexico City, Mexico City, Mexico

Site Status RECRUITING

Novartis Investigative Site

Chihuahua City, , Mexico

Site Status RECRUITING

Novartis Investigative Site

Bydgoszcz, , Poland

Site Status RECRUITING

Novartis Investigative Site

Warsaw, , Poland

Site Status RECRUITING

Novartis Investigative Site

Coimbra, , Portugal

Site Status RECRUITING

Novartis Investigative Site

Lisbon, , Portugal

Site Status RECRUITING

Novartis Investigative Site

Vila Nova de Gaia, , Portugal

Site Status RECRUITING

Novartis Investigative Site

Seoul, Korea, South Korea

Site Status ACTIVE_NOT_RECRUITING

Novartis Investigative Site

Busan, , South Korea

Site Status RECRUITING

Novartis Investigative Site

Seoul, , South Korea

Site Status RECRUITING

Novartis Investigative Site

Seoul, , South Korea

Site Status RECRUITING

Novartis Investigative Site

Valencia, Valencia, Spain

Site Status RECRUITING

Novartis Investigative Site

Barcelona, , Spain

Site Status RECRUITING

Novartis Investigative Site

Madrid, , Spain

Site Status RECRUITING

Novartis Investigative Site

Málaga, , Spain

Site Status RECRUITING

Novartis Investigative Site

Salamanca, , Spain

Site Status RECRUITING

Novartis Investigative Site

Changhua, , Taiwan

Site Status RECRUITING

Novartis Investigative Site

Kaohsiung City, , Taiwan

Site Status RECRUITING

Novartis Investigative Site

Taichung, , Taiwan

Site Status RECRUITING

Novartis Investigative Site

Taoyuan District, , Taiwan

Site Status RECRUITING

Novartis Investigative Site

Khon Kaen, THA, Thailand

Site Status RECRUITING

Novartis Investigative Site

Bangkok, , Thailand

Site Status RECRUITING

Novartis Investigative Site

Istanbul, Fatih, Turkey (Türkiye)

Site Status RECRUITING

Novartis Investigative Site

Ankara, Sihhiye-Altindag, Turkey (Türkiye)

Site Status RECRUITING

Novartis Investigative Site

Ankara, Yenimahalle, Turkey (Türkiye)

Site Status RECRUITING

Novartis Investigative Site

Basingstoke, Hampshire, United Kingdom

Site Status RECRUITING

Novartis Investigative Site

Bristol, , United Kingdom

Site Status RECRUITING

Novartis Investigative Site

London, , United Kingdom

Site Status RECRUITING

Novartis Investigative Site

Ho Chi Minh City, VNM, Vietnam

Site Status RECRUITING

Novartis Investigative Site

Ho Chi Minh City, , Vietnam

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Austria Belgium Brazil China Colombia France Germany Greece Hungary India Italy Japan Malaysia Mexico Poland Portugal South Korea Spain Taiwan Thailand Turkey (Türkiye) United Kingdom Vietnam

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Novartis Pharmaceuticals

Role: CONTACT

Phone: 1-888-669-6682

Email: [email protected]

Novartis Pharmaceuticals

Role: CONTACT

Phone: +41613241111

Email: [email protected]

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Debra Mc Dermed

Role: primary

Lauren Nam

Role: primary

Vicki Tan

Role: primary

Carrie Rycort

Role: primary

Melissa Pierce

Role: primary

Jhon Galindo

Role: primary

Carole Kringel

Role: primary

J Heannhehbelle Rosier

Role: primary

Cathryn Leggio

Role: primary

Marco Santella

Role: primary

Amelia Paliewicz

Role: primary

Sherry Wiggins

Role: primary

Samina Shehzad

Role: primary

Hassan Khan

Role: primary

Mohammad Alsayed

Role: primary

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2024-511933-36-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

CVAY736S12201

Identifier Type: -

Identifier Source: org_study_id