A Phase 2 Study of ONO-2808 in Patients With Multiple System Atrophy

NCT ID: NCT05923866

Last Updated: 2025-06-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

92 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-09-22

Study Completion Date

2025-08-31

Brief Summary

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This is a Phase 2, double-blind, parallel-group, placebo-controlled study to assess the safety, tolerability, pharmacokinetics, pharmacodynamics, and efficacy of multiple doses of ONO-2808 in patients with MSA. This is the first study of ONO-2808 in patients with MSA.

Detailed Description

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The purpose of the study is to evaluate 3 doses of ONO-2808 compared to placebo in MSA patients, including: 1) safety and tolerability, 2) pharmacokinetics, and 3) changes in clinical outcome assessments (COA) and biomarkers considered to be related to the pharmacodynamics and potential efficacy of ONO-2808.

Conditions

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Multiple System Atrophy (MSA)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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ONO-2808 Arm

Group Type EXPERIMENTAL

ONO-2808

Intervention Type DRUG

Oral administration of ONO-2808 at low, middle or high doses once a daily for 24 weeks

Placebo Arm

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Oral administration of placebo once a daily for 24 weeks

Interventions

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ONO-2808

Oral administration of ONO-2808 at low, middle or high doses once a daily for 24 weeks

Intervention Type DRUG

Placebo

Oral administration of placebo once a daily for 24 weeks

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Female or male patients with a diagnosis of clinically-established or clinically-probable MSA according to the novel Movement Disorder Society (MDS) criteria for MSA diagnosis (2022), including patients with MSA of either subtype (MSA-P or MSA-C).
2. Patients at the early stages of the disease, defined as a maximum of 5 years since the onset of one of the following symptoms associated with MSA:

* Parkinsonism
* Ataxia
* Orthostatic hypotension and/or urinary dysfunction
3. Patients with an anticipated survival of at least 3 years in the opinion of the Investigator.
4. Patients who are able to ambulate without the assistance of another person, defined as the ability to take at least 10 steps and then to turn around and walk at least another 10 steps. Use of assistive devices (e.g., walker or cane) is allowed.
5. Ability to swallow oral medication and be willing to adhere to the study intervention regimen.

Exclusion Criteria

1. Pregnant or lactating females.
2. Patients with a clinically-significant or unstable medical or surgical condition other than MSA that, in the opinion of the Investigator, might preclude safe completion of the study or might affect the results of the study (e.g., pulmonary, cardiovascular \[including bradyarrhythmia\], macular edema, and significant renal or hepatic dysfunction).
3. Neurological diseases/disorders other than MSA, such as Parkinson's disease, dementia with Lewy bodies, essential tremor, progressive supranuclear palsy, spinocerebellar ataxia, spastic paraparesis, corticobasal degeneration, or vascular, normal pressure hydrocephalus, pharmacological, or post-encephalitic parkinsonism.
4. Patients with documented liver diseases or cirrhosis.
5. Positive results at Screening for active viral infections that include positive human immunodeficiency virus (HIV), hepatitis B surface antigen (HBsAg) and hepatitis B core antibody, and hepatitis C virus (HCV).
6. Patients with suicide ideation according to the Investigator's clinical judgment per the Columbia Suicide Severity Rating Scale (C-SSRS) at Screening or who have made a suicide attempt in the 6 months before Screening.
Minimum Eligible Age

30 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ono Pharmaceutical Co. Ltd

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Project Leader

Role: STUDY_DIRECTOR

Ono Pharmaceutical Co. Ltd

Locations

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The Parkinson's Movement and Disorder Institute

Fountain Valley, California, United States

Site Status

University of Southern California

Los Angeles, California, United States

Site Status

David Geffen School of Medicine at UCLA

Los Angeles, California, United States

Site Status

Stanford University School of Medicine

Palo Alto, California, United States

Site Status

CenExel Rocky Mountain Clinical Research

Englewood, Colorado, United States

Site Status

Yale School of Medicine - Yale Church Street Research Unit (CRSU)

New Haven, Connecticut, United States

Site Status

Parkinson's Disease and Movement Disorders Center of Boca Raton

Boca Raton, Florida, United States

Site Status

Norman Fixel Institute for Neurological Diseases - University of Florida

Gainesville, Florida, United States

Site Status

Mayo Clinic in Florida

Jacksonville, Florida, United States

Site Status

University of Miami Miller School of Medicine

Miami, Florida, United States

Site Status

Emory University School of Medicine

Atlanta, Georgia, United States

Site Status

University of Kansas Medical Center Research Institute

Kansas City, Kansas, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

University of Michigan School of Medicine

Ann Arbor, Michigan, United States

Site Status

Quest Research Institute

Farmington Hills, Michigan, United States

Site Status

Mayo Clinic - Rochester

Rochester, Minnesota, United States

Site Status

University of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status

NYU Langone Health - NYU Dysautonomia Center

New York, New York, United States

Site Status

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status

Columbia University

New York, New York, United States

Site Status

University of Cincinnati College of Medicine

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

Penn State University - Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

The University of Pennsylvania - Pennsylvania Hospital

Philadelphia, Pennsylvania, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

Virginia Commonwealth University Medical Center

Richmond, Virginia, United States

Site Status

Evergreen Health

Kirkland, Washington, United States

Site Status

Swedish Neuroscience Institute, Movement Disorders Clinic

Seattle, Washington, United States

Site Status

Fujita Health University Hospital

Toyoake, Aichi-ken, Japan

Site Status

National Hospital Organization Sendai Nishitaga Hospital

Sendai, Miyagi, Japan

Site Status

National Hospital Organization Osaka Toneyama Medical Center

Toyonaka, Osaka, Japan

Site Status

Tokyo Metropolitan Neurological Hospital

Fuchū, Tokyo, Japan

Site Status

National Hospital Organization Utano National Hospital

Kyoto, , Japan

Site Status

Countries

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United States Japan

Other Identifiers

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jRCT2041230153

Identifier Type: REGISTRY

Identifier Source: secondary_id

ONO-2808-03

Identifier Type: -

Identifier Source: org_study_id

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