Study of ATH434 in Participants with Multiple System Atrophy

NCT ID: NCT05109091

Last Updated: 2024-12-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

77 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-07-01

Study Completion Date

2024-11-28

Brief Summary

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This study will assess the safety and efficacy of ATH434 in participants with Multiple System Atrophy

Detailed Description

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Conditions

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Multiple System Atrophy

Keywords

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Multiple System Atrophy ATH434 Neurodegenerative disease Shy-Drager Syndrome Movement disorders Autonomic dysfunction Synucleinopathies Atypical parkinsonism

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ATH434 Arm 1

Group Type EXPERIMENTAL

ATH434 dose level 1

Intervention Type DRUG

ATH434 taken BID

ATH434 Arm 2

Group Type EXPERIMENTAL

ATH434 dose level 2

Intervention Type DRUG

ATH434 taken BID

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo taken BID

Interventions

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ATH434 dose level 1

ATH434 taken BID

Intervention Type DRUG

ATH434 dose level 2

ATH434 taken BID

Intervention Type DRUG

Placebo

Placebo taken BID

Intervention Type DRUG

Other Intervention Names

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PBT434 PBT434

Eligibility Criteria

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Inclusion Criteria

1. Participant has clinical features of parkinsonism.
2. Participant has evidence of orthostatic hypotension and/or bladder dysfunction.
3. Participant has ataxia and/or pyramidal signs on neurological examination.
4. Participant is ambulatory.
5. Participant has biomarker evidence of MSA in biologic fluid and on MRI.

Exclusion Criteria

1. Participant has motor symptoms for \> 4 years.
2. Participant has advanced disease, as indicated by frequent falls or choking.
3. Participant has structural brain abnormality on MRI.
4. Participant has any significant neurological disorder other than MSA.
5. Participant has an unstable medical or psychiatric illness.
6. Participant has a contraindication to, or is unable to tolerate, MRI or lumbar puncture.
Minimum Eligible Age

30 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Alterity Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of California San Diego

La Jolla, California, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Johns Hopkins University

Baltimore, Maryland, United States

Site Status

Columbia University Irving Medical Center

New York, New York, United States

Site Status

The Movement Disorder Clinic of Oklahoma

Tulsa, Oklahoma, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

St Vincent's Hospital (Sydney)

Darlinghurst, New South Wales, Australia

Site Status

Westmead Hospital

Westmead, New South Wales, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

CHU de Toulouse/Hôpital Pierre-Paul Riquet

Toulouse, Haute-Garonne, France

Site Status

CHU de Bordeaux/Groupe Hospitalier Pellegrin

Bordeaux, , France

Site Status

CHU de Marseille/Hôpital de la Timone

Marseille, , France

Site Status

CHU/HU Pitié Salpêtrière

Paris, Île-de-France Region, France

Site Status

IRCCS Istituto Delle Scienze Neurologiche di Bologna

Bologna, Bologna, Italy

Site Status

Policlinico di Milano

Milan, , Italy

Site Status

Azienda Ospedaliero-Universitaria Pisana

Pisa, , Italy

Site Status

AOU San Giovanni di Dio Ruggi d'Aragona

Salerno, , Italy

Site Status

New Zealand Brain Research Institute

Christchurch, , New Zealand

Site Status

Auckland City Hospital

Grafton, , New Zealand

Site Status

University College London

London, England, United Kingdom

Site Status

Newcastle University

Newcastle upon Tyne, England, United Kingdom

Site Status

Salford Royal Hospital

Salford, England, United Kingdom

Site Status

Queen Elizabeth University Hospital

Glasgow, Scotland, United Kingdom

Site Status

Countries

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Austria United States Australia France Italy New Zealand United Kingdom

Other Identifiers

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ATH434-201

Identifier Type: -

Identifier Source: org_study_id