A Study of NST-6179 in Subjects With Intestinal Failure-Associated Liver Disease (IFALD).

NCT ID: NCT05919680

Last Updated: 2025-01-07

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

36 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-01-15

Study Completion Date

2025-06-30

Brief Summary

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This is a phase 2a, multicenter, randomized, double-blind, placebo-controlled study to evaluate the safety, tolerability, pharmacokinetics (PK), and pharmacodynamics (PD) of NST-6179 in subjects with intestinal failure-associated liver disease (IFALD) receiving parenteral nutrition (PN).

The study will be conducted in 2 sequential parts. Up to 36 subjects diagnosed with IFALD will be enrolled in the study, of which up to 18 subjects will be enrolled in each of the 2 parts and randomized (2:1) to receive NST-6179 (N=12/part) or matched placebo (N=6/part). Subjects in Part A will receive once daily (QD) oral administration of 800 mg (32 mL solution) NST-6179 or placebo for 4 weeks. The NST-6179 dose for Part B is planned to be 1200 mg QD for 12 weeks. Actual dose, however, will be determined during the safety review meeting.

Detailed Description

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Conditions

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Intestinal Failure Associated Liver Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Part A-800 mg NST-6179

up to 12 subjects

Group Type EXPERIMENTAL

NST-6179 Part A

Intervention Type DRUG

Once daily (QD) oral administration of 800mg (32 mL solution) of NST-6179 for 4 weeks

Part A matched NST-6179 placebo

up to 6 subjects

Group Type EXPERIMENTAL

Matched Placebo

Intervention Type OTHER

Matched placebo for administration in Part A or Part B

Part B- 1200mg NST-6179

up to 12 subjects

Group Type EXPERIMENTAL

NST-6179 Part B

Intervention Type DRUG

Once daily (QD) oral administration of 1200mg of NST-6179 for 12 weeks

Part B matched NST-6179 placebo

up to 6 subjects

Group Type EXPERIMENTAL

Matched Placebo

Intervention Type OTHER

Matched placebo for administration in Part A or Part B

Interventions

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NST-6179 Part A

Once daily (QD) oral administration of 800mg (32 mL solution) of NST-6179 for 4 weeks

Intervention Type DRUG

NST-6179 Part B

Once daily (QD) oral administration of 1200mg of NST-6179 for 12 weeks

Intervention Type DRUG

Matched Placebo

Matched placebo for administration in Part A or Part B

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Adult persons aged 16 years or older at the time of informed consent.
* Minimum of 6 months on Parenteral supplementation.
* Established clinical diagnosis of IFALD based on a persistent elevation of

1. liver enzymes (ALP, AST, ALT, or GGT ≥1.5 × upper limit of normal \[ULN\]) for ≥6 months and/or
2. total bilirubin \> ULN for ≥6 months.
* Laboratory parameters consistent with stable liver disease without cirrhosis as defined by:

1. ALT and AST \<5 × ULN;
2. Total bilirubin ≤2.5 mg/dL in the absence of Gilbert's Syndrome.
3. Serum albumin ≥2.5 g/dL;
4. International normalized ratio (INR) ≤1.3 in the absence of anticoagulant therapy;
5. Platelet count ≥120,000/mm3.

Exclusion Criteria

* Clinical, laboratory, imaging, or histopathologic evidence of other causes of acute or chronic liver disease, including autoimmune, viral, metabolic, or alcoholic liver disease.
* Clinical evidence of compensated or decompensated hepatic cirrhosis as assessed by historical liver histology, ultrasound-based and/or signs and symptoms of hepatic decompensation (including, but not limited to, jaundice, ascites, variceal hemorrhage, and/or hepatic encephalopathy).
* Presence of hepatic impairment, end-stage liver disease, and/or a model for end-stage liver disease (MELD) score \>12.
* Transient elastography read \>20.0 kPA within 3 months prior to or during the Screening Period.
* Estimated glomerular filtration rate \<45 mL/min based on the 2021 CKD-EPI creatinine equation.
* Poor nutritional status defined as body mass index (BMI) \<17 kg/m2.
Minimum Eligible Age

16 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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NorthSea Therapeutics B.V.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Mayo Clinic Scottsdale Campus

Scottsdale, Arizona, United States

Site Status RECRUITING

University of California San Francisco Medical Center

San Francisco, California, United States

Site Status RECRUITING

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status NOT_YET_RECRUITING

Emory University School of Medicine

Atlanta, Georgia, United States

Site Status RECRUITING

The University of Chicago Medical Center

Chicago, Illinois, United States

Site Status RECRUITING

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Henry Ford Hospital

Detroit, Michigan, United States

Site Status RECRUITING

Mayo Clinic Rochester Campus

Rochester, Minnesota, United States

Site Status RECRUITING

Mount Sinai Medical Center

New York, New York, United States

Site Status RECRUITING

Duke University Medical Center

Durham, North Carolina, United States

Site Status RECRUITING

The Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

Vanderbilt University School of Medicine

Nashville, Tennessee, United States

Site Status RECRUITING

University of Washington

Seattle, Washington, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Michelle Yokley

Role: CONTACT

+31 (0) 35 760 65 05

Facility Contacts

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John DiBaise, MD

Role: primary

Kendall Beck, MD

Role: primary

Sukanya Subramanian

Role: primary

Thomas Ziegler, MD

Role: primary

Carol Semrad, MD

Role: primary

Mark Puder, MD

Role: primary

Syed-Mohammed Jafri, MD

Role: primary

Manpreet Mundi, MD

Role: primary

Kishore Iyer, MD

Role: primary

Maria Segovia, MD

Role: primary

Don Kirby, MD

Role: primary

Dawn Adams

Role: primary

Lei Yu, MD

Role: primary

Other Identifiers

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NST-6179-02

Identifier Type: -

Identifier Source: org_study_id

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