FOG-001 in Locally Advanced or Metastatic Solid Tumors

NCT ID: NCT05919264

Last Updated: 2026-01-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

575 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-05-23

Study Completion Date

2027-08-31

Brief Summary

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The goal of this clinical trial is to determine if FOG-001 is safe and effective in participants with locally advanced or metastatic cancer.

Detailed Description

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This is a FIH, Phase 1/2, multicenter, open-label, non-randomized, dose escalation and dose expansion study to evaluate the safety, tolerability, PK, pharmacodynamics, and antitumor activity of FOG-001 as monotherapy and in combination with other anticancer agents in participants with advanced or metastatic solid tumors likely or known to have a Wnt pathway activating mutation (WPAM).

Conditions

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Cancer Colorectal Cancer Solid Tumor Locally Advanced Solid Tumor Metastatic Cancer WNT Pathway β-catenin Beta-catenin Adenomatous Polyposis Coli APC HCC Desmoid Microsatellite Stable Colorectal Cancer Metastatic Castration-resistant Prostate Cancer FAP Endometrial Carcinoma Prostate Cancer Microsatellite Instability-High Colorectal Cancer CTNNB1 Adamantinomatous Craniopharyngioma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Part 1a

Solid Tumors with any WNT-Pathway Activating Mutation (WPAM) or Microsatellite Stable (MSS) Colorectal Cancer (CRC), irrespective of WPAM status

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 1b

MSS CRC (known WPAM negative participants are not eligible)

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 1c

Hepatocellular Carcinoma (documented WPAM in APC or CTNNB1 required)

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 1d-1

Desmoid Tumors

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 1d-2

Desmoid Tumors

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 1e-1

Solid Tumors with documented WPAM or MSS CRC, irrespective of WPAM status

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 1e-2

Solid Tumors with documented WPAM or MSS CRC, irrespective of WPAM status

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 1f-1

MSS CRC (known WPAM negative participants are not eligible)

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

mFOLFOX-6

Intervention Type DRUG

mFOLFOX-6 will be administered per the prescribing information in combination with FOG-001

Bevacizumab

Intervention Type DRUG

Bevacizumab will be administered per the prescribing information in combination with FOG-001

Part 1f-2

Solid Tumors with documented WPAM or MSS CRC (known WPAM negative participants are not eligible)

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Nivolumab

Intervention Type DRUG

Nivolumab will be administered per the prescribing information in combination with FOG-001

Part 1f-3

MSS CRC (known WPAM negative participants are not eligible)

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Trifluridine/tipiracil

Intervention Type DRUG

Trifluridine/tipiracil will be administered per the prescribing information in combination with FOG-001

Bevacizumab

Intervention Type DRUG

Bevacizumab will be administered per the prescribing information in combination with FOG-001

Part 2a

MSS CRC, irrespective of WPAM status

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 2b

Solid Tumors with documented WPAM

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 2c

Hepatocellular Carcinoma (documented WPAM in APC or CTNNB1 required)

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 2d

Desmoid Tumors

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 2e

Metastatic Castration-Resistant Prostate Cancer (documented WPAM in APC or CTNNB1 required)

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Part 2f-1

MSS CRC (known WPAM negative participants are not eligible)

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

mFOLFOX-6

Intervention Type DRUG

mFOLFOX-6 will be administered per the prescribing information in combination with FOG-001

Bevacizumab

Intervention Type DRUG

Bevacizumab will be administered per the prescribing information in combination with FOG-001

Part 2f-2

Solid Tumors with documented WPAM or MSS CRC (known WPAM negative participants are not eligible)

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Nivolumab

Intervention Type DRUG

Nivolumab will be administered per the prescribing information in combination with FOG-001

Part 2f-3

MSS CRC (known WPAM negative participants are not eligible)

Group Type EXPERIMENTAL

FOG-001

Intervention Type DRUG

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Trifluridine/tipiracil

Intervention Type DRUG

Trifluridine/tipiracil will be administered per the prescribing information in combination with FOG-001

Bevacizumab

Intervention Type DRUG

Bevacizumab will be administered per the prescribing information in combination with FOG-001

Interventions

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FOG-001

FOG-001 will be administered IV at assigned doses in continuous cycles of 28 days

Intervention Type DRUG

mFOLFOX-6

mFOLFOX-6 will be administered per the prescribing information in combination with FOG-001

Intervention Type DRUG

Nivolumab

Nivolumab will be administered per the prescribing information in combination with FOG-001

Intervention Type DRUG

Trifluridine/tipiracil

Trifluridine/tipiracil will be administered per the prescribing information in combination with FOG-001

Intervention Type DRUG

Bevacizumab

Bevacizumab will be administered per the prescribing information in combination with FOG-001

Intervention Type DRUG

Other Intervention Names

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Leucovorin, 5-fluorouracil, Oxaliplatin Opdivo Lonsurf Avastin

Eligibility Criteria

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Inclusion Criteria

* Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
* Adequate organ and marrow function.


* Diagnosis of treatment-refractory advanced/metastatic solid tumor that is non-MSI-H or non-dMMR colorectal cancer (CRC) or any other solid tumor with documented WNT- pathway activating mutations (WPAMs).


* Diagnosis of treatment-refractory advanced/metastatic non-MSI-H or non-dMMR CRC.
* At least one lesion that is suitable for a core needle biopsy.


* Diagnosis of HCC with a documented WPAM (by local testing) in APC or CTNNB1. HCC that is radiographically confirmed without tissue biopsy may be enrolled with a documented CTNNB1 mutation (e.g., by ctDNA).


* Desmoid tumor (aggressive fibromatosis)


* Diagnosis of locally advanced or metastatic non-MSI-H or non-dMMR CRC
* Participants with tumors known to be negative for APC LoF mutations or CTNNB1 GoF mutations (per NGS tests) are not eligible.
* One dose of mFOLFOX6 in the unresectable or metastatic setting prior to enrollment is allowed.


* Non-MSI-H or non-dMMR (by local testing) CRC with or without liver metastases.
* MSI-H CRC or solid tumors that are WPAM and resistant to a-PD-1/PD-L1
* Participants with tumors known to be negative for APC LoF mutations or CTNNB1 GoF mutations (per NGS tests) are not eligible


* Diagnosis of locally advanced or metastatic non-MSI-H or non-dMMR (by local testing) CRC
* Participants with tumors known to be negative for APC LoF mutations or CTNNB1 GoF mutations (per NGS tests) are not eligible.


* Diagnosis of locally advanced or metastatic non-MSI-H or non-dMMR (by local testing) CRC


* Diagnosis of advanced or metastatic solid tumors with a documented WPAM (by local testing) or equivalent evidence

Exclusion Criteria

* Known history of bone metastasis. Bone metastasis are allowed for patients with mCRPC.
* Evidence of vertebral compression fracture or non-traumatic bone fracture within the past 12 months and who are not receiving antiresorptive therapy.
* Osteoporosis, which is defined as a T-score of ≤-2.5 at the lumbar spine (L1 - L4), left (or right) femoral neck or left (or right) total hip as determined by DXA scan.
* Uncontrolled inflammatory bowel disease (i.e., ulcerative colitis or Crohn's disease)
* Unstable/inadequate cardiac function.
* Has known meningeal carcinomatosis, leptomeningeal carcinomatosis, spinal cord compression, or symptomatic or unstable brain metastases.
* Pregnant, lactating, or planning to become pregnant.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Parabilis Medicines, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Jorge Ramos, DO

Role: STUDY_CHAIR

Parabilis Medicines, Inc.

Locations

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Honor Health

Scottsdale, Arizona, United States

Site Status RECRUITING

Stanford Cancer Institute, Stanford University

Palo Alto, California, United States

Site Status RECRUITING

University of California San Francisco, Helen Diller Family Comprehensive Cancer Center

San Francisco, California, United States

Site Status RECRUITING

Sarcoma Oncology Center

Santa Monica, California, United States

Site Status RECRUITING

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status RECRUITING

Johns Hopkins University, Sibley Memorial Hospital

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Florida Cancer Specialists

Lake Mary, Florida, United States

Site Status RECRUITING

Johns Hopkins University, The Sidney Kimmel Comprehensive Cancer Center

Baltimore, Maryland, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status RECRUITING

M Health Fairview University of Minnesota Medical Center

Minneapolis, Minnesota, United States

Site Status RECRUITING

Washington University School of Medicine

St Louis, Missouri, United States

Site Status RECRUITING

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status RECRUITING

University Hospitals Cleveland Medical Center, Seidman Cancer Center

Cleveland, Ohio, United States

Site Status RECRUITING

Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

Oregon Health and Science University

Portland, Oregon, United States

Site Status RECRUITING

University of Pittsburgh Medical Center, Hillman Cancer Center

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status RECRUITING

The University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

South Texas Accelerated Research Therapeutics, LLC

San Antonio, Texas, United States

Site Status RECRUITING

University of Virginia

Charlottesville, Virginia, United States

Site Status RECRUITING

University of Wisconsin, Carbone Cancer Center

Madison, Wisconsin, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Clinical Trial Inquiries

Role: CONTACT

(857) 259-6305

Facility Contacts

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Sunil Sharma, MD

Role: primary

480-323-1350

Nam Bui

Role: primary

650-498-6000

Varun Monga, MD

Role: primary

888-689-8273

Sant Chawla, MD

Role: primary

301-552-9999

Michael Cecchini, MD

Role: primary

415-302-7807

Mike J Pishvaian, MD/PhD

Role: primary

202-804-3343

Alexander Philipovskiy, MD/PhD

Role: primary

407-804-6133

Mike J Pishvaian, MD/PhD

Role: primary

410-955-8964

Eric Christenson, MD

Role: backup

410-955-8964

Samuel Klempner, MD

Role: primary

617-724-4000

Candace Haddox, MD

Role: primary

617-632-3000

Ajay Prakash, MD/PhD

Role: primary

612-273-8383

Moh'd Khushman, MD

Role: primary

314-362-9115

Rona Yaeger, MD

Role: primary

646-888-5109

David Bajor, MD

Role: primary

216-765-9033

Wen Wee Ma, MBBS

Role: primary

216-444-2200

Dale Shepard, MD, PhD

Role: backup

(216) 444-2200

Shivaani Kummar, MD

Role: primary

503-494-8534

Dennis J Hsu, MD

Role: primary

412-623-1722

Meredith S Pelster, MD

Role: primary

615-329-6862

Jordi Rodon Ahnert, MD/PhD

Role: primary

713-792-5603

Kyriakos Papadopoulos, MD

Role: primary

210-593-5255

Ludimila Cavalcante, MD

Role: primary

434-358-8780

Jeremy Kratz, MD

Role: primary

608-263-1300

Other Identifiers

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FOG-001-101

Identifier Type: -

Identifier Source: org_study_id

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