Study of AVZO-021 in Patients With Advanced Solid Tumors

NCT ID: NCT05867251

Last Updated: 2025-11-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

430 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-08-30

Study Completion Date

2030-01-31

Brief Summary

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This study, the first clinical trial of AVZO-021, aims to determine the safety, tolerability, pharmacokinetics, pharmacodynamics, maximum tolerated dose, and anti-tumor effects of AVZO-021 in patients with advanced solid tumors. AVZO-021 is an oral medication that inhibits cyclin-dependent kinase 2 (CDK 2).

Detailed Description

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AVZO-021 is a compound being developed for the treatment of patients with advanced solid tumors, specifically, HR+/HER2- breast cancer and cyclin E1 (CCNE1) altered malignancies. AVZO-021 is a selective and potent cyclin-dependent kinase 2 (CDK2) inhibitor, which plays an important role in cell cycle regulation. This is a Phase 1/2 first-in-human, open-label, nonrandomized, multicenter study of AVZO-021. Phase 1 is a dose-escalation phase aimed at assessing the safety and tolerability of AVZO-021 and determining the recommended phase 2 dose (RP2D) as monotherapy and combination therapy. Phase 2 is a dose-expansion phase that will be conducted to assess the antitumor activity of AVZO-021 as monotherapy and combination therapy.

Conditions

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Advanced Solid Tumor HR+/HER2- Breast Cancer HR+, HER2-, Advanced Breast Cancer CCNE1 Amplification Epithelial Ovarian Cancer Primary Peritoneal Cancer Fallopian Tube Cancer Endometrial Cancer TNBC - Triple-Negative Breast Cancer

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Phase 1 dose-escalation Phase 2 dose-expansion
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Phase 1, monotherapy (Part 1A)

Escalating doses of once daily, oral AVZO-021 in 28-day cycles.

Group Type EXPERIMENTAL

AVZO-021

Intervention Type DRUG

AVZO-021 is a selective and potent oral inhibitor of CDK2 being developed for the treatment of patients with advanced solid tumors with CDK2 dependency (1A), CCNE1 amplified solid tumors (2A), HR+/HER2- BC (1B1-1B5, 2B1-2B5) and CCNE1 amplified EOC (1C, 2C)

Phase 1, combination (Parts 1B and 1C)

Escalating doses of once daily, oral AVZO-021 in 28-day cycles starting at least 1 DL below the monotherapy MTD/RP2D dose in combination with:

1B1) fulvestrant

1B2) palbociclib plus either fulvestrant or letrozole

1B3) ribociclib plus either fulvestrant or letrozole

1B4) abemaciclib plus either fulvestrant or letrozole

1B5) sacituzumab govitecan-hziy

1C) carboplatin

Group Type EXPERIMENTAL

AVZO-021

Intervention Type DRUG

AVZO-021 is a selective and potent oral inhibitor of CDK2 being developed for the treatment of patients with advanced solid tumors with CDK2 dependency (1A), CCNE1 amplified solid tumors (2A), HR+/HER2- BC (1B1-1B5, 2B1-2B5) and CCNE1 amplified EOC (1C, 2C)

Palbociclib

Intervention Type DRUG

Antineoplastic agent, cyclin-dependent kinase 4/6 inhibitor

Fulvestrant

Intervention Type DRUG

Antineoplastic agent, estrogen receptor antagonist

Letrozole

Intervention Type DRUG

Antineoplastic agent, aromatase inhibitor

Ribociclib

Intervention Type DRUG

Antineoplastic CDK4/6 inhibitor

Abemaciclib

Intervention Type DRUG

Antineoplastic CDK4/6 inhibitor

Carboplatin

Intervention Type DRUG

Alkylating agent

Sacituzumab Govitecan-hziy

Intervention Type DRUG

Trop-2 antibody and topoisomerase inhibitor

Phase 2, monotherapy (Part 2A)

Oral doses of AVZO-021 in 28-day cycles at the RP2D determined in Part 1A.

Group Type EXPERIMENTAL

AVZO-021

Intervention Type DRUG

AVZO-021 is a selective and potent oral inhibitor of CDK2 being developed for the treatment of patients with advanced solid tumors with CDK2 dependency (1A), CCNE1 amplified solid tumors (2A), HR+/HER2- BC (1B1-1B5, 2B1-2B5) and CCNE1 amplified EOC (1C, 2C)

Phase 2, combination (Parts 2B and 2C)

Oral doses of AVZO-021 in 28-day cycles at the RP2D determined in Parts 1B/1C, in combination with:

2B1) fulvestrant

2B2) palbociclib plus either fulvestrant or letrozole

2B3) ribociclib plus either fulvestrant or letrozole

2B4) abemaciclib plus either fulvestrant or letrozole

2B5) sacituzumab govitecan-hziy

2C) carboplatin

Group Type EXPERIMENTAL

AVZO-021

Intervention Type DRUG

AVZO-021 is a selective and potent oral inhibitor of CDK2 being developed for the treatment of patients with advanced solid tumors with CDK2 dependency (1A), CCNE1 amplified solid tumors (2A), HR+/HER2- BC (1B1-1B5, 2B1-2B5) and CCNE1 amplified EOC (1C, 2C)

Palbociclib

Intervention Type DRUG

Antineoplastic agent, cyclin-dependent kinase 4/6 inhibitor

Fulvestrant

Intervention Type DRUG

Antineoplastic agent, estrogen receptor antagonist

Letrozole

Intervention Type DRUG

Antineoplastic agent, aromatase inhibitor

Ribociclib

Intervention Type DRUG

Antineoplastic CDK4/6 inhibitor

Abemaciclib

Intervention Type DRUG

Antineoplastic CDK4/6 inhibitor

Carboplatin

Intervention Type DRUG

Alkylating agent

Sacituzumab Govitecan-hziy

Intervention Type DRUG

Trop-2 antibody and topoisomerase inhibitor

Interventions

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AVZO-021

AVZO-021 is a selective and potent oral inhibitor of CDK2 being developed for the treatment of patients with advanced solid tumors with CDK2 dependency (1A), CCNE1 amplified solid tumors (2A), HR+/HER2- BC (1B1-1B5, 2B1-2B5) and CCNE1 amplified EOC (1C, 2C)

Intervention Type DRUG

Palbociclib

Antineoplastic agent, cyclin-dependent kinase 4/6 inhibitor

Intervention Type DRUG

Fulvestrant

Antineoplastic agent, estrogen receptor antagonist

Intervention Type DRUG

Letrozole

Antineoplastic agent, aromatase inhibitor

Intervention Type DRUG

Ribociclib

Antineoplastic CDK4/6 inhibitor

Intervention Type DRUG

Abemaciclib

Antineoplastic CDK4/6 inhibitor

Intervention Type DRUG

Carboplatin

Alkylating agent

Intervention Type DRUG

Sacituzumab Govitecan-hziy

Trop-2 antibody and topoisomerase inhibitor

Intervention Type DRUG

Other Intervention Names

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Ibrance Faslodex Femara Kisqali Verzenio Trodelvy

Eligibility Criteria

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Inclusion Criteria

1. Male or female aged ≥18 years old at screening with Eastern Cooperative Oncology Group (ECOG) 0-1.

i) Phase 1a Monotherapy Dose Escalation: Patients with locally advanced or metastatic HR+/HER2- breast cancer, CCNE1-amplified tumors that are either epithelial ovarian cancer, primary peritoneal cancer, fallopian tube cancer, endometrial cancer or TNBC, with no other oncogenic driver mutations that are treatable and standard therapies are no longer effective, appropriate, or safe in the opinion of the investigator and medical monitor. Patients with any additional tumor type with CCNE1 amplification can be enrolled only if clinical data is supportive and approved by medical monitor (Cohort 1A).

ii) Phase 1b Combination Dose Escalation: histologically or cytologically confirmed diagnosis of locally advanced or metastatic HR+ HER2- (HER2-low may be allowed if failed standard of care therapy) breast cancer, who have been previously treated with inhibitor of CDK4/6 and endocrine therapy(Cohorts 1B1, 1B2, 1B3, 1B4, and 1B5); or histologically or cytologically confirmed diagnosis of CCNE1- amplified, locally advanced or metastatic, platinum-refractory or platinum-resistant EOC, primary peritoneal, or fallopian tube cancer (Cohort 1C).

iii) Phase 2a Monotherapy dose expansion: Histologically or cytologically confirmed diagnosis of locally advanced or metastatic CCNE1 amplified epithelial ovarian cancer, primary peritoneal cancer, fallopian tube cancer, endometrial cancer or TNBC, with no other oncogenic driver mutations that are treatable and standard therapies are no longer effective, appropriate, or safe in the opinion of the investigator and medical monitor (Cohort 2A).

iv) Phase 2b Combination dose expansion: Histologically or cytologically confirmed diagnosis of locally advanced or metastatic HR+/HER2- (HER2-low may be allowed if failed standard of care therapy) breast cancer who have been previously treated with no more than 1 prior CDK4/6 inhibitor and endocrine therapy (Cohorts 2B1, 2B2, 2B3, 2B4, and 2B5); or Histologically or cytologically confirmed diagnosis of locally advanced or metastatic, CCNE1-amplified, platinum-refractory or platinum-resistant EOC, primary peritoneal cancer, or fallopian tube cancer (Cohort 2C).
3. No more than 2 prior cytotoxic chemotherapy regimens for locally advanced/metastatic disease (excepting patients treated with an antibody-drug conjugate, with ovarian cancer if there disease is platinum resistant or refractory, having progressed beyond all SOC care; and patients who have received prior chemotherapy in the adjuvant or neoadjuvant setting \>12 months prior to starting AVZO-021 treatment).
4. Measurable disease as determined by RECIST version 1.1.
5. Adequate bone marrow and organ function.
6. Ability to swallow capsules or tablets.

Exclusion Criteria

1. Received an investigational agent or anticancer therapy within 2 weeks, or 5 half-lives of the drug, whichever is shorter, prior to planned start of AVZO-021.
2. Received any CDK2 inhibitor, protein kinase membrane associated tyrosine/threonine 1 (PKMYT1) inhibitor, or WEE1 inhibitor anticancer therapy. For cohort B5, prior therapy with topoisomerase inhibitors is not permitted.
3. Undergone major surgery within 4 weeks prior to planned start of AVZO-021.
4. Received radiotherapy for palliation within 7 days of the first dose of study treatment, unless specified otherwise in the protocol.
5. Active CNS metastases or confirmed leptomeningeal disease are not eligible.
6. Unresolved toxicities from prior therapy greater than Common Terminology Criteria for Adverse Events (CTCAE) version 5.0 Grade \>1 at the time of starting study treatment.
7. Clinically unstable cardiac function as described in the protocol.
8. Any active or chronic infection/disease that compromises the immune system.
9. Current treatment with strong or moderate cytochrome P450 (CYP)3A4 inhibitors or inducers.
10. Active second malignancy unless in remission with life expectancy \> 2 years and with documented sponsor approval.
11. Pregnancy, lactation, or plans to breastfeed during the study or within 6 months of the last dose of study intervention.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Avenzo Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Yale Cancer Center

New Haven, Connecticut, United States

Site Status RECRUITING

Florida Cancer Specialists

Sarasota, Florida, United States

Site Status RECRUITING

Moffitt Cancer Center

Tampa, Florida, United States

Site Status RECRUITING

Perlmutter Cancer Center at NYU Langone Hospital - Long Island

Mineola, New York, United States

Site Status RECRUITING

NYU Langone Medical Center (Tisch Hospital)

New York, New York, United States

Site Status RECRUITING

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status RECRUITING

Oklahoma University

Oklahoma City, Oklahoma, United States

Site Status RECRUITING

Providence Cancer Institute

Portland, Oregon, United States

Site Status RECRUITING

Sidney Kimmel Cancer Center (SKCC) at Jefferson Health

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Texas Oncology - DFW

Dallas, Texas, United States

Site Status RECRUITING

NEXT Virginia

Fairfax, Virginia, United States

Site Status RECRUITING

Macquarie University Hospital

Macquarie University, New South Wales, Australia

Site Status RECRUITING

Cancer Care Wollongong

Wollongong, New South Wales, Australia

Site Status RECRUITING

Countries

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United States Australia

Central Contacts

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Medical Information

Role: CONTACT

(858) 239-2944

Facility Contacts

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Yale Cancer Center

Role: primary

Florida Cancer Specialists

Role: primary

Moffitt Cancer Center

Role: primary

Perlmutter Cancer Center at NYU Langone Hospital - Long Island

Role: primary

NYU Langone Medical Center (Tisch Hospital)

Role: primary

University Hospitals Cleveland Medical Center

Role: primary

Oklahoma University

Role: primary

Providence Cancer Institute

Role: primary

Sidney Kimmel Cancer Center (SKCC)

Role: primary

Texas Oncology - DFW

Role: primary

NEXT Virginia

Role: primary

Macquarie University Hospital

Role: primary

Cancer Care Wollongong

Role: primary

Other Identifiers

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AVZO-021-1001

Identifier Type: -

Identifier Source: org_study_id

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