A Study of GEn-1124 in Subjects With Acute Respiratory Distress Syndrome (ARDS)

NCT ID: NCT05795465

Last Updated: 2025-10-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

52 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-04-04

Study Completion Date

2026-12-31

Brief Summary

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GEn1E-1124-002 is a two-part Phase 2 study to evaluate the safety and tolerability of GEn-1124 in subjects with ARDS. Treatment with IV infusion dosing as early as possible after ARDS diagnosis. Subjects will be given a second dose approximately 8 hours after the first dose and will continue with twice daily dosing (BID regimen) for 5 days.

Detailed Description

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Randomized , double-blind, placebo controlled, dose escalation study to evaluate the pharmacokinetics (PK), pharmacodynamics (PD), safety, and tolerability of GEn1124.

GEn-1124 or placebo will be administered as a 2-hour IV infusion as early as possible after ARDS diagnosis. Participants will receive a second dose approximately 8 hours after the first and will continue BID for the remaining schedule (Days 2-5). Follow-up will be for a total of 60 days after the first dose or death (whichever comes first).

An independent Safety Review Committee (SRC) will be responsible for reviewing data throughout the study.

Conditions

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Respiratory Distress Syndrome, Acute

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Part 1 - Randomized, double-blind, dose escalation. Part 2 - Randomized, double-blind, placebo controlled, parallel group.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
All subjects, investigators, and study personnel involved in the conduct of the study, including data management, will be blinded to treatment assignment with the exception of some designated personnel. The unblinded study personnel will not participate in study procedures or data analysis prior to unblinding of the study data to all study-related personnel.

Study Groups

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Part 1 Cohort 1: GEn-1124

Subjects in cohort 1 will receive low dose GEn-1124 BID intravenous 5 days.

Group Type EXPERIMENTAL

GEn-1124

Intervention Type DRUG

Intravenous infusion

Part 1 Cohort 2: GEn-1124

Subjects in cohort 2 will receive high dose GEn-1124 BID intravenous for 5 days.

Group Type EXPERIMENTAL

GEn-1124

Intervention Type DRUG

Intravenous infusion

Placebo

Subjects randomized to placebo will receive a placebo in a matching dosing regimen (Placebo BID intravenous for 5 days).

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Intravenous infusion

Part 2: GEn-1124

Depending on the analysis of part 1, subjects in part 2 will receive GEn-1124 BID intravenous for 5 days.

Group Type EXPERIMENTAL

GEn-1124

Intervention Type DRUG

Intravenous infusion

Interventions

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GEn-1124

Intravenous infusion

Intervention Type DRUG

Placebo

Intravenous infusion

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Male or female subject between the ages of 18 and 85 years old, inclusive.
2. Written informed consent .
3. Dosing as early as possible after first meeting ARDS 2023 Global definition.
4. Acceptable method of birth control.

Exclusion Criteria

1. Subject, surrogate, or physician not committed, or eligible, to receive full supportive care measures.
2. Pregnant or breastfeeding
3. Currently incarcerated in a correctional institution or involuntarily committed to an inpatient mental health facility.
4. Active malignancy (other than non-melanoma skin cancer) requiring treatment with immunosuppressant drugs within the last 3 months or within the last 6 months if an anti-B cell antibody was received.
5. Any other irreversible disease or condition for which 6-month mortality is estimated to be \>50%.
6. Moderate to severe liver failure.
7. Estimated glomerular filtration rate (eGFR) \<10 mL/min/1.73 m2 or requiring dialysis at screening.
8. Subjects with known:

1. New York Heart Association Class IV heart disease; or
2. Acute Coronary Syndrome within the past 30 days (e.g., myocardial infarction, unstable angina) or dosing; or
3. Cardiac arrest within 30 days of dosing with sequelae likely to increase mortality.
9. Severe chronic respiratory disease with continuous home oxygen \>2 liters per minute (LPM) or \>28% (adjusted for altitude); and/or home noninvasive ventilation (except for the treatment of obstructive sleep apnea).
10. Poly-traumatic injury resulting in significant blood loss and/or likely to require major surgery within the study period, or subject condition that would interfere with study procedures.
11. History of any type of solid organ or cellular transplant.
12. Receiving immunosuppressive therapy for solid organ or hematopoietic cancer, transplant anti-rejection medication, and/or other chronic conditions.
13. Moribund subject not expected to survive 24 hours.
14. Do not resuscitate (DNR) status.
15. World Health Organization (WHO) functional class III or IV pulmonary hypertension.
16. Subject has been on mechanical ventilation for more than 7 days at time of dosing.
17. Burn victims currently undergoing treatment for \>40% total body surface area (TBSA) involvement or for known airway inhalation injury.
18. Neuromuscular disease that could impact ability to wean from mechanical ventilation.
19. History of tuberculosis (TB); undergoing treatment for latent TB infection (LTBI); untreated LTBI (as determined by documented results within 3 months of Screening of a positive TB test).
20. Active Hepatitis B, positive Hepatitis C (and has not completed antiviral treatment), or positive human immunodeficiency (HIV) screen.
21. Use of any investigational drug or device within last 30 days of dosing or 5 half-lives, whichever is longer.
22. Any other medical, psychiatric, or social condition that, in the opinion of the investigator, is likely to unfavorably alter the risk-benefit of subject participation, to interfere with protocol compliance, or to confound safety.
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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GEn1E Lifesciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Ritu Lal, PhD, MS

Role: STUDY_DIRECTOR

GEn1E Lifesciences

Locations

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Medstar Washington Hospital Center

Washington D.C., District of Columbia, United States

Site Status WITHDRAWN

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status RECRUITING

University of Maryland Medical Center

Baltimore, Maryland, United States

Site Status RECRUITING

University of Maryland - Baltimore Washington Medical Center

Glen Burnie, Maryland, United States

Site Status RECRUITING

Ocean Springs Hospital

Ocean Springs, Mississippi, United States

Site Status COMPLETED

Washington University School of Medicine

St Louis, Missouri, United States

Site Status RECRUITING

Cooper University Hospital

Camden, New Jersey, United States

Site Status RECRUITING

The Mount Sinai Hospital

New York, New York, United States

Site Status RECRUITING

Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

Houston Methodist Hospital

Houston, Texas, United States

Site Status WITHDRAWN

Intermountain Medical Center

Murray, Utah, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Ritu Lal, PhD, MS

Role: CONTACT

(650) 248-2429

Related Links

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https://www.gen1e.com/

GEn1E Lifesciences

Other Identifiers

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GEn-1124-002

Identifier Type: -

Identifier Source: org_study_id

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