Study Results
The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.
Basic Information
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ENROLLING_BY_INVITATION
10 participants
OBSERVATIONAL
2022-11-08
2024-12-31
Brief Summary
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Detailed Description
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Conditions
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Study Groups
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Rehabilitation Arm
Participants will participate in outpatient physical and/or occupational therapies while participating in the tofersen early access program (EAP)
Rehabilitation
Particapants currently receiving tofersen treatment will be referred to outpatient physical and/or occupational therapy.
Interventions
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Rehabilitation
Particapants currently receiving tofersen treatment will be referred to outpatient physical and/or occupational therapy.
Other Intervention Names
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Eligibility Criteria
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Inclusion Criteria
* Current enrollment in the tofersen expanded access program
* Age greater than 18 years
* Medically able to participate in outpatient physical therapy and/or home-based rehabilitation, as determined by the treating health care provider
Exclusion Criteria
18 Years
ALL
No
Sponsors
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Washington University School of Medicine
OTHER
Responsible Party
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Sean E Smith
Instructor in Neurology
Locations
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Washington University School of Medicine
St Louis, Missouri, United States
Countries
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Related Links
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Washington University ALS Center website
Other Identifiers
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202208170
Identifier Type: -
Identifier Source: org_study_id
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