Open-Label Extension Study of DCCR in Patients With Prader-Willi Syndrome

NCT ID: NCT05701774

Last Updated: 2025-04-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

83 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-01-31

Study Completion Date

2028-06-30

Brief Summary

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The purpose of this is study is to evaluate the long-term safety of DCCR (diazoxide choline) extended-release tablets) in patients with Prader-Willi syndrome.

Detailed Description

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Conditions

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Prader-Willi Syndrome

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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DCCR

75 - 525 mg DCCR

Group Type EXPERIMENTAL

DCCR

Intervention Type DRUG

Once daily oral administration

Interventions

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DCCR

Once daily oral administration

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Provide voluntary, written informed consent (parent(s) / legal guardian(s) of patient); provide voluntary, written assent (subjects, as appropriate)
2. Participant must:

1. Have participated in and completed the Study C602 Randomized Withdrawal (RW) Period;
2. Have participated in but discontinued from the Study C602 RW Period and at least 16 weeks have elapsed since the date of their randomization into the C602 RW Period; or
3. Have participated in Study C602 OLE period, did not consent to participate in the RW Period, and at least 16 weeks have elapsed since the date of their C602 Open-Label Extension End of Treatment Visit.

Exclusion Criteria

1. Positive urine pregnancy test (in females of child-bearing potential)
2. Females who are pregnant or breastfeeding, and/or plan to become pregnant or to breast-feed during or within 30 days after study participation.
3. Participation in a clinical study of an investigational drug (including approved drugs for unapproved uses), investigational device, or therapeutic intervention subsequent to the C602 Open-Label Extension End of Treatment Visit.
Minimum Eligible Age

4 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Soleno Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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UC Irvine

Orange, California, United States

Site Status

Stanford University

Palo Alto, California, United States

Site Status

Rady Children's Hospital of San Diego

San Diego, California, United States

Site Status

U of Florida Gainesville

Gainesville, Florida, United States

Site Status

Emory Children's Center

Atlanta, Georgia, United States

Site Status

Indiana University School of Medicine

Indianapolis, Indiana, United States

Site Status

National Institutes of Health

Bethesda, Maryland, United States

Site Status

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status

Sparrow Clinical Research Institute

Lansing, Michigan, United States

Site Status

Children's Hospital and Clinic Minnesota

Saint Paul, Minnesota, United States

Site Status

St. Joseph's University Medical Center

Paterson, New Jersey, United States

Site Status

NYU Winthrop Hospital

Mineola, New York, United States

Site Status

The Research Institute at Nationwide Children's Hospital

Columbus, Ohio, United States

Site Status

Vanderbilt University

Nashville, Tennessee, United States

Site Status

Research Institute of Dallas

Dallas, Texas, United States

Site Status

University of Utah

Salt Lake City, Utah, United States

Site Status

Seattle Children's

Seattle, Washington, United States

Site Status

Fulbourn Hospital

Cambridge, , United Kingdom

Site Status

The Queen Elizabeth University

Glasgow, , United Kingdom

Site Status

Hull and East Yorkshire Hospitals NHS Trust

Hull, , United Kingdom

Site Status

Royal London Hospital

London, , United Kingdom

Site Status

Chelsea and Westminster Hospital

London, , United Kingdom

Site Status

Countries

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United States United Kingdom

Other Identifiers

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C614

Identifier Type: -

Identifier Source: org_study_id

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