HTD1801 in Adults With Nonalcoholic Steatohepatitis and Liver Fibrosis Who Have Type 2 Diabetes or Pre-Diabetes

NCT ID: NCT05623189

Last Updated: 2025-05-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

218 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-12-27

Study Completion Date

2025-04-30

Brief Summary

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A phase 2b, multicenter, randomized, double-blind, placebo-controlled study of HTD1801 in adult subjects with non-alcoholic steatohepatitis and liver fibrosis who have type 2 diabetes mellitus or pre-diabetes.

Detailed Description

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This phase 2b, double-blind, randomized, placebo-controlled, multicenter study will evaluate the effect of HTD1801, 1250 mg twice daily (BID) compared to placebo BID on histologic improvements in adult subjects with non-alcoholic steatohepatitis and liver fibrosis who have type 2 diabetes mellitus or pre-diabetes.

The study will enroll approximately 210 subjects with biopsy-confirmed non-alcoholic steatohepatitis and evidence of stage 2 or stage 3 liver fibrosis. Subjects will receive investigational product for up to 60 weeks.

Conditions

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Nonalcoholic Steatohepatitis (NASH) Type 2 Diabetes

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

This phase 2b, double-blind, placebo-controlled, multicenter study will evaluate the effect of HTD1801 on histologic improvements in adult subjects with non-alcoholic steatohepatitis (NASH) and liver fibrosis who have type 2 diabetes mellitus or pre-diabetes. Approximately 210 subjects with biopsy-confirmed NASH and evidence of stage 2 or stage 3 liver fibrosis will be randomized 2:1 to receive HTD1801 1250 mg twice daily (BID) or placebo BID. Subjects will receive investigational product for up to 60 weeks.
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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HTD1801

HTD1801,1250 mg, BID

Group Type EXPERIMENTAL

HTD1801

Intervention Type DRUG

HTD1801,1250 mg, BID

placebo

placebo, BID

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo, BID

Interventions

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HTD1801

HTD1801,1250 mg, BID

Intervention Type DRUG

Placebo

Placebo, BID

Intervention Type DRUG

Other Intervention Names

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HTD1801 capsules placebo capsules

Eligibility Criteria

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Inclusion Criteria

* Clinical diagnosis of non-alcoholic steatohepatitis (NASH) upon central read of a liver biopsy obtained no more than 6 months before Day 0.
* Histologic evidence of fibrosis stage 2 or stage 3 as defined by the non-alcoholic steatohepatitis (NASH) clinical research network (CRN) scoring of fibrosis.
* Clinically documented diagnosis of type 2 diabetes mellitus for at least 6 months prior to screening or prediabetes at screening.
* BMI \>25 kilograms/meters squared (\>23 kilograms/meters squared if Asian).

Exclusion Criteria

* Fibrosis stage 4.
* History of alcohol or substance abuse or dependence.
* Liver disease unrelated to non-alcoholic steatohepatitis.
* History of significant cardiovascular disease.
* History of type 1 diabetes.
* Inability or unwillingness to undergo 2 planned liver biopsies OR 1 planned biopsy if historical liver biopsy was used to confirm eligibility at entry.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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HighTide Biopharma Pty Ltd

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Adrian Di Bisceglie, MD, FACP, FAASLD

Role: STUDY_DIRECTOR

Hightide Therapeutics USA, LLC

Locations

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The Institute for Liver Health (Arizona Liver Health)

Chandler, Arizona, United States

Site Status

Arizona Liver Health - Glendae

Peoria, Arizona, United States

Site Status

Adobe Clinical Research LLC

Tucson, Arizona, United States

Site Status

Aizona Liver Health

Tucson, Arizona, United States

Site Status

San Fernando Valley Health Institute

Canoga Park, California, United States

Site Status

Clinnova Research Solutions

Garden Grove, California, United States

Site Status

Catalina Research Institute

Montclair, California, United States

Site Status

California Liver Institute

Pasadena, California, United States

Site Status

Inland Empire Liver Foundation

Rialto, California, United States

Site Status

Excel Medical Clinical Trials, LLC

Boca Raton, Florida, United States

Site Status

Tampa Bay Medical Research, Inc.

Clearwater, Florida, United States

Site Status

Covenant Metabolic Specialists - Fort Meyers

Fort Myers, Florida, United States

Site Status

Evolution Clinical Trials, Inc.

Hialeah Gardens, Florida, United States

Site Status

ClinCloud LLC Maitland

Maitland, Florida, United States

Site Status

Clinical Pharmacology of Miami, LLC

Miami, Florida, United States

Site Status

Panax Clinical Research

Miami Lakes, Florida, United States

Site Status

Floridain Clinical Research

Miami Lakes, Florida, United States

Site Status

Covenant Metabolic Specialists - Sarasota

Sarasota, Florida, United States

Site Status

Theia Clinical Research LLC

Temple Terrace, Florida, United States

Site Status

ClinCloud LLC Melbourn

Viera, Florida, United States

Site Status

Metabolic Research Institute, Inc.

West Palm Beach, Florida, United States

Site Status

Conquest Research

Winter Park, Florida, United States

Site Status

Louisvill Metabolic and Atherosclerosis Research Center (L-MARC)

Louisville, Kentucky, United States

Site Status

Tandem Clinical Research

Marrero, Louisiana, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

Jubilee Clinical Research, Inc.

Las Vegas, Nevada, United States

Site Status

Tandem Clinical Research GI - New York

New York, New York, United States

Site Status

Lucas Research - Diabetes and Endocrinology

Morehead City, North Carolina, United States

Site Status

Clinical Research Institute of Ohio

Westlake, Ohio, United States

Site Status

Palmetto Clinical Research

Summerville, South Carolina, United States

Site Status

ClinSearch LLC

Chattanooga, Tennessee, United States

Site Status

Premier Research

Clarksville, Tennessee, United States

Site Status

Texas Clinical Research Institute

Arlington, Texas, United States

Site Status

Pinnacle Clinical Research

Austin, Texas, United States

Site Status

South Texas Research Institute

Brownsville, Texas, United States

Site Status

EPIC Medical Research

DeSoto, Texas, United States

Site Status

Pinnacle Research, Georgetown TX

Georgetown, Texas, United States

Site Status

Quality Research, Inc.

San Antonio, Texas, United States

Site Status

Sun Research Institute

San Antonio, Texas, United States

Site Status

Pinnacle Clinical Research San Antonio

San Antonio, Texas, United States

Site Status

Impact Research Institute

Waco, Texas, United States

Site Status

Manassas Clinical Research Center

Manassas, Virginia, United States

Site Status

Liver Institute NW

Seattle, Washington, United States

Site Status

Chinese University of Hong Kong Prince of Wales Hospital

Shatin, , Hong Kong

Site Status

FDI Clinical Research

San Juan, Munoz Rivera San Juan, Puerto Rico

Site Status

Countries

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United States Hong Kong Puerto Rico

Other Identifiers

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The CENTRICITY Study

Identifier Type: OTHER

Identifier Source: secondary_id

HTD1801.PCT014

Identifier Type: -

Identifier Source: org_study_id

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