A Study to Evaluate the Safety and Efficacy of Cotadutide Given by Subcutaneous Injection in Adult Participants With Non-cirrhotic Non-alcoholic Steatohepatitis With Fibrosis

NCT ID: NCT05364931

Last Updated: 2025-09-03

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

54 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-07-14

Study Completion Date

2024-04-19

Brief Summary

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The purpose of this study is to evaluate the safety and efficacy of cotadutide in participants with non-cirrhotic NASH with fibrosis.

Detailed Description

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A Phase 2, randomized, double-blind, placebo-controlled study to evaluate the safety and efficacy of two different doses of cotadutide at 300 and 600 μg in participants with non-cirrhotic non-alcoholic steatohepatitis with fibrosis.

Conditions

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Non-cirrhotic Non-alcoholic Steatohepatitis With Fibrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Cotadutide 300μg

Group Type EXPERIMENTAL

Cotadutide

Intervention Type DRUG

Cotadutide administered subcutaneously once daily

Placebo 300μg

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo administered subcutaneously once daily

Cotadutide 600μg

Group Type EXPERIMENTAL

Cotadutide

Intervention Type DRUG

Cotadutide administered subcutaneously once daily

Placebo 600μg

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo administered subcutaneously once daily

Interventions

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Cotadutide

Cotadutide administered subcutaneously once daily

Intervention Type DRUG

Placebo

Placebo administered subcutaneously once daily

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Provision of informed consent
2. Males and female participants ≥ 18 to ≤ 75 years of age (inclusive) at the time of signing the informed consent.
3. Histologically confirmed non-alcoholic steatohepatitis (NASH) per NASH Clinical Research Network (CRN) criteria as diagnosed by histology from a liver biopsy performed ≤ 180 days from randomization and fulfilling all of the following histological criteria:

1. NAS (Non-alcoholic Fatty Liver Disease Activity Score) ≥ 4 with a score of ≥ 1 for each component: steatosis, lobular inflammation, and ballooning
2. Presence of fibrosis stage F2 or F3
4. Women of childbearing potential, non-pregnant and nonbreastfeeding and using appropriate birth control to avoid pregnancy throughout the study and for up to 4 weeks after the last dose of study intervention.

Exclusion Criteria

1. Chronic liver disease of other etiologies.
2. History of cirrhosis and/or hepatic decompensation, including evidence of portal hypertension (e.g. low platelet count, splenomegaly, ascites, history of hepatic encephalopathy, esophageal varices, or variceal bleeding).
3. Clinically significant cardiovascular or cerebrovascular disease within 90 days prior to screening, including but not limited to, myocardial infarction, acute coronary syndrome, unstable angina pectoris, transient ischemic attack, or stroke, or participants who have undergone percutaneous coronary intervention or a coronary artery bypass graft within the past 90 days or who are due to undergo these procedures at the time of screening
4. History of malignant neoplasms within 5 years prior to screening, except for adequately treated basal cell, squamous cell skin cancer, or any in situ carcinoma.
5. Participation in another clinical study with an investigational product administered within the last 30 days or 5 half-lives of the therapy (whichever is longer) at the time of screening or the time of the historical biopsy or concurrent participation in another interventional study of any kind or prior randomization in this study.
6. Severe allergy/hypersensitivity to any of the proposed study treatments or excipients
7. Contraindication to liver biopsy (eg, bleeding diathesis, such as hemophilia, suspected hemangioma, or suspected echinococcal infection) or inability to safely obtain a liver biopsy as determined by the investigator
8. Severely uncontrolled hypertension defined as SBP ≥ 180 mmHg or DBP ≥ 110 mmHg on the average of 2 seated BP measurements after being at rest for at least 10 minutes at screening or randomization 9 Any positive results for human immunodeficiency virus infection, positive results for hepatitis B surface antigen or hepatitis C antibody test along with a positive HCV RNA test.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Research Site

Tucson, Arizona, United States

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Canoga Park, California, United States

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Gilroy, California, United States

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Sacramento, California, United States

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Englewood, Colorado, United States

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Bradenton, Florida, United States

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Homestead, Florida, United States

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Jacksonville, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Winter Park, Florida, United States

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Munster, Indiana, United States

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Houma, Louisiana, United States

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Marrero, Louisiana, United States

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Marrero, Louisiana, United States

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Shreveport, Louisiana, United States

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Ann Arbor, Michigan, United States

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Las Vegas, Nevada, United States

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Las Vegas, Nevada, United States

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Lawrence, New Jersey, United States

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Warren Township, New Jersey, United States

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Morehead City, North Carolina, United States

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Chattanooga, Tennessee, United States

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Arlington, Texas, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Lewisville, Texas, United States

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San Antonio, Texas, United States

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Ogden, Utah, United States

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CABA, , Argentina

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Heidelberg, , Australia

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Kogarah, , Australia

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Meadowbrook, , Australia

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Melbourne, , Australia

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Westmead, , Australia

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Vienna, , Austria

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Vienna, , Austria

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London, Ontario, Canada

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Terrebonne, Quebec, Canada

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Montpellier, , France

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Paris, , France

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Dresden, , Germany

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Konstanz, , Germany

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Athens, , Greece

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Ioannina, , Greece

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Haifa, , Israel

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Jerusalem, , Israel

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Nahariya, , Israel

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Petah Tikva, , Israel

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Tel Aviv, , Israel

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Tel Litwinsky, , Israel

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Catania, , Italy

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Foggia, , Italy

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Milan, , Italy

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Roma, , Italy

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Roma, , Italy

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Rozzano, , Italy

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San Giovanni Rotondo, , Italy

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Chiba, , Japan

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Fukui-shi, , Japan

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Gifu, , Japan

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Hiroshima, , Japan

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Kawasaki-shi, , Japan

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Kawasaki-shi, , Japan

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Kure-shi, , Japan

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Osaka, , Japan

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Saga, , Japan

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Sapporo, , Japan

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Sendai, , Japan

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Shinjuku-ku, , Japan

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Suita-shi, , Japan

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Takasaki-shi, , Japan

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Toon-shi, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Kuala Lumpur, , Malaysia

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Kuala Lumpur, , Malaysia

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Malacca, , Malaysia

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Seremban, , Malaysia

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Auckland, , New Zealand

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Christchurch, , New Zealand

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Grafton, , New Zealand

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Plumstead, , South Africa

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Busan, , South Korea

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Gangwon-do, , South Korea

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Junggu, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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A Coruña, , Spain

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Almería, , Spain

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Lleida, , Spain

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Madrid, , Spain

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Málaga, , Spain

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Seville, , Spain

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Kaohsiung City, , Taiwan

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Tainan City, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Hat Yai, , Thailand

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Khon Kaen, , Thailand

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Ankara, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Aberdeen, , United Kingdom

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Glasgow, , United Kingdom

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Ipswich, , United Kingdom

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Liverpool, , United Kingdom

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London, , United Kingdom

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Preston, , United Kingdom

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Rochdale, , United Kingdom

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Sheffield, , United Kingdom

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Countries

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United States Argentina Australia Austria Canada France Germany Greece Israel Italy Japan Malaysia New Zealand South Africa South Korea Spain Taiwan Thailand Turkey (Türkiye) United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2021-005484-53

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D5671C00006

Identifier Type: -

Identifier Source: org_study_id

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