Frespaciguat (MK-5475) INSIGNIA-PH-COPD: A Study of the Efficacy and Safety of Frespaciguat (an Inhaled sGC Stimulator) in Adults With PH-COPD

NCT ID: NCT05612035

Last Updated: 2025-10-07

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

120 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-03-16

Study Completion Date

2029-10-07

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Researchers are looking for ways to treat pulmonary hypertension (PH) caused by chronic obstructive pulmonary disease (COPD). The goal of the study is to learn if people who take frespaciguat can walk farther in 6 minutes at Week 24 compared to people who take placebo.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Pulmonary Hypertension Chronic Obstructive Pulmonary Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Double-blind

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Frespaciguat

Participants with PH-COPD will receive 380 µg of frespaciguat as an oral inhalation once daily for 24 weeks (base period) and thereafter for up to 42 months (optional extension period).

Group Type EXPERIMENTAL

Frespaciguat

Intervention Type DRUG

Frespaciguat 380 µg administered as dry powder inhalation once daily.

Placebo

Participants with PH-COPD will receive matching placebo as an oral inhalation once daily for 24 weeks (base period) and then 380 µg of frespaciguat as an oral inhalation once daily for up to 42 months (optional extension period).

Group Type PLACEBO_COMPARATOR

Frespaciguat

Intervention Type DRUG

Frespaciguat 380 µg administered as dry powder inhalation once daily.

Placebo

Intervention Type DRUG

Placebo administered as dry powder inhalation once daily.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Frespaciguat

Frespaciguat 380 µg administered as dry powder inhalation once daily.

Intervention Type DRUG

Placebo

Placebo administered as dry powder inhalation once daily.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

MK-5475

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Has Group 3.1 pulmonary hypertension chronic obstructive pulmonary disease (PH-COPD) as defined by the Clinical Classification of Pulmonary Hypertension.
* Has a right heart catheterization (RHC) at screening or historical RHC within 12 months before screening that meets hemodynamic criteria.
* Has a physician diagnosis of obstructive lung disease on pulmonary function testing (PFT) performed at screening.
* Has a WHO Functional Class assessment of Class II to IV.
* If on supplemental oxygen, the regimen must be stable.
* Has stable and optimized chronic, baseline COPD-specific therapy.
* If on PDE5 inhibitor, has stable concomitant use (initiated at least 3 months prior to randomization and no change in drug or dosage for at least 3 months prior to randomization) and changes to PDE5 inhibitor dosing is not anticipated during the 24 week Base Period.
* If on antihypertensives and/or a diuretic regimen has stable concomitant use.
* If on anticoagulants has stable concomitant use.
* Is of any sex/gender from 40 to 85 years of age inclusive.
* Female is not pregnant or breastfeeding, and is not of childbearing potential or uses acceptable contraceptive method or abstains from sexual intercourse, or has a negative highly sensitive pregnancy test within 24 hours before the first dose of study intervention, or whose history and sexual activity has been reviewed by the investigator.

Exclusion Criteria

* Has Group 1 pulmonary arterial hypertension (PAH), Groups 2, 4 or 5 pulmonary hypertension (PH).
* Has non-COPD related Group 3 PH.
* Has evidence of untreated more than mild obstructive sleep apnea.
* Has significant left heart disease.
* Expects to receive a lung and/or heart transplant from screening through the end of the 24 week Base Period.
* Has evidence of a resting oxygen saturation (SpO2) \< 88%.
* Has experienced a moderate or severe COPD exacerbation within 2 months before randomization.
* Has experienced right heart failure within 2 months before randomization.
* Has uncontrolled tachyarrhythmia.
* Has acute coronary syndrome, undergone coronary artery bypass graft, or percutaneous coronary intervention within 2 months before randomization.
* Has evidence of significant chronic renal insufficiency.
* Has evidence of chronic liver disease, portal hypertension, cirrhosis, or hepatic abnormalities.
* Initiated a pulmonary rehabilitation program within 2 months before randomization.
* Has impairments that limit the ability to perform 6MWT.
* Has history of cancer.
* Is a user of illicit drugs or has a recent history of drug/alcohol abuse or dependence.
* Has used PAH-specific therapies within 2 months of randomization.
Minimum Eligible Age

40 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

UCSF Helen Diller Medical Center at Parnassus Heights ( Site 0110)

San Francisco, California, United States

Site Status

University of Colorado Anschutz Medical Campus-University of Colorado Hospital Cardiac and Vascular ( Site 0101)

Aurora, Colorado, United States

Site Status

Clinovation Intl. Corp. ( Site 0108)

Sebring, Florida, United States

Site Status

Alexian Brothers Medical Center-Pulmonary ( Site 0109)

Elk Grove Village, Illinois, United States

Site Status

University of Iowa ( Site 0103)

Iowa City, Iowa, United States

Site Status

University of Kansas Medical Center-IM-Pulmonary and Critical Care Medicine ( Site 0102)

Kansas City, Kansas, United States

Site Status

Lexington VA Medical Center - Cooper Division ( Site 0137)

Lexington, Kentucky, United States

Site Status

Corewell Health ( Site 0133)

Grand Rapids, Michigan, United States

Site Status

Mayo Clinic in Rochester, Minnesota ( Site 0131)

Rochester, Minnesota, United States

Site Status

Creighton University Clinical Research Office ( Site 0123)

Omaha, Nebraska, United States

Site Status

University of New Mexico Hospital ( Site 0146)

Albuquerque, New Mexico, United States

Site Status

UNC Health - Eastowne Medical Office-Clinical Trials Unit ( Site 0147)

Chapel Hill, North Carolina, United States

Site Status

Temple University Hospital ( Site 0104)

Philadelphia, Pennsylvania, United States

Site Status

UPMC Montefiore University Hospital-Department of Medicine ( Site 0149)

Pittsburgh, Pennsylvania, United States

Site Status

UT Southwestern Medical Center ( Site 0114)

Dallas, Texas, United States

Site Status

The University of Texas Health Science Center at Houston ( Site 0105)

Houston, Texas, United States

Site Status

Intermountain Medical Center-Division of Pulmonary & Critical Care Medicine ( Site 0140)

Murray, Utah, United States

Site Status

University of Virginia Health System-Division of Pulmonary and Critical Care Medicine ( Site 0111)

Charlottesville, Virginia, United States

Site Status

Fundación Respirar ( Site 0305)

CABA, Buenos Aires, Argentina

Site Status

Centro Medico Capital ( Site 0301)

La Plata, Buenos Aires, Argentina

Site Status

Instituto de Cardiologia de Tucuman-Area de Investigacion Clinica ( Site 0303)

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Hospital Britanico de Buenos Aires ( Site 0307)

CABA, , Argentina

Site Status

Hospital Privado Universitario de Córdoba-Clinical Cardiology Department ( Site 0302)

Córdoba, , Argentina

Site Status

Royal Prince Alfred Hospital-Department of Respiratory Medicine ( Site 0903)

Camperdown, New South Wales, Australia

Site Status

Westmead Hospital ( Site 0902)

Westmead, New South Wales, Australia

Site Status

WESLEY RESEARCH INSTITUTE Limited ( Site 0906)

Auchenflower, Queensland, Australia

Site Status

The Prince Charles Hospital ( Site 0904)

Brisbane, Queensland, Australia

Site Status

Mater Misericordiae Limited ( Site 0905)

South Brisbane, Queensland, Australia

Site Status

Medizinische Universität Graz-Klinische Abteilung für Pulmonologie ( Site 1201)

Graz, Styria, Austria

Site Status

Medizinische Universitaet Innsbruck ( Site 1202)

Innsbruck, Tyrol, Austria

Site Status

Université Libre de Bruxelles - Hôpital Erasme ( Site 1302)

Brussels, Bruxelles-Capitale, Region de, Belgium

Site Status

UZ Leuven ( Site 1301)

Leuven, Vlaams-Brabant, Belgium

Site Status

Clinica Cardio VID ( Site 0504)

Medellín, Antioquia, Colombia

Site Status

Ciensalud Ips S A S ( Site 0508)

Barranquilla, Atlántico, Colombia

Site Status

Fundación Valle del Lili ( Site 0509)

Cali, Valle del Cauca Department, Colombia

Site Status

Centro de Investigaciones Clinicas SAS ( Site 0505)

Cali, Valle del Cauca Department, Colombia

Site Status

C.H.U Hôpital Nord ( Site 1503)

Marseille, Bouches-du-Rhone, France

Site Status

Centre Hospitalier Régional Universitaire de Nancy - Hôpitaux de Brabois ( Site 1502)

Vandœuvre-lès-Nancy, Lorraine, France

Site Status

CHU Angers ( Site 1506)

Angers, Maine-et-Loire, France

Site Status

Hôpitaux Universitaires Paris Sud - Hôpital Bicêtre-Pneumologie ( Site 1501)

Le Kremlin-Bicêtre, Paris, France

Site Status

Centre Hospitalier Universitaire de Poitiers ( Site 1505)

Poitiers, Vienne, France

Site Status

Thoraxklinik-Heidelberg gGmbH-Zentrum für Pulmonale Hypertonie ( Site 1603)

Heidelberg, Baden-Wurttemberg, Germany

Site Status

UKGM Gießen/Marburg ( Site 1604)

Giessen, Hesse, Germany

Site Status

Medizinische Hochschule Hannover ( Site 1602)

Hanover, Lower Saxony, Germany

Site Status

Universitaetsklinikum Carl Gustav Carus Dresden ( Site 1601)

Dresden, Saxony, Germany

Site Status

Universitätsklinikum Schleswig-Holstein-Pneumologie ( Site 1605)

Lübeck, Schleswig-Holstein, Germany

Site Status

Unidad De Diagnostico Cardiologico-Unidad de Diagnostico Cardiologico ( Site 0605)

Guatemala City, , Guatemala

Site Status

MEDI-K ( Site 0607)

Guatemala City, , Guatemala

Site Status

Clinica Medica ( Site 0601)

Guatemala City, , Guatemala

Site Status

Private Practice - Dr. Jeremias Guerra Mejia ( Site 0603)

Guatemala City, , Guatemala

Site Status

Rambam Health Care Campus ( Site 1701)

Haifa, , Israel

Site Status

Rabin Medical Center ( Site 1702)

Petah Tikva, , Israel

Site Status

Cattinara Hospital ( Site 1801)

Trieste, Friuli Venezia Giulia, Italy

Site Status

Ospedale San Gerardo-ASST Monza-Cardio Vasolare- Clinica pneumologica ( Site 1802)

Monza, Lombardy, Italy

Site Status

ISMETT Istituto Mediterraneo per i Trapianti e Terapie ad Alta Specializzazione ( Site 1804)

Palermo, , Italy

Site Status

Centro Médico Nacional Siglo XXI ( Site 0708)

Mexico City, Mexico City, Mexico

Site Status

Instituto Nacional de Ciencias Medicas y Nutricion Salvador Zubiran ( Site 0704)

Mexico City, Mexico City, Mexico

Site Status

INVECORDIS S.C. ( Site 0703)

Hacienda de Las Palmas, State of Mexico, Mexico

Site Status

Instituto Nacional de Cardiologia Ignacio Chavez ( Site 0701)

México, , Mexico

Site Status

Unidad de Investigacon de la Clinica Internacional ( Site 0804)

Lima Cercado, Lima region, Peru

Site Status

Clinica Ricardo Palma-Centro de Investigacion de Enfermedades Respiratorias Thorax ( Site 0806)

San Isidro, Lima region, Peru

Site Status

Clínica Providencia ( Site 0803)

San Miguel, Lima region, Peru

Site Status

Charlotte Maxeke Johannesburg Academic Hospital ( Site 2108)

Johannesburg, Gauteng, South Africa

Site Status

Netcare Milpark Hospital ( Site 2103)

Johannesburg, Gauteng, South Africa

Site Status

Netcare St Augustine's Hospital ( Site 2105)

Durban, KwaZulu-Natal, South Africa

Site Status

TREAD Research ( Site 2101)

Cape Town, Western Cape, South Africa

Site Status

Gachon University Gil Medical Center ( Site 1101)

Namdong-gu, Incheon, South Korea

Site Status

Seoul National University Hospital ( Site 1103)

Seoul, , South Korea

Site Status

Asan Medical Center ( Site 1102)

Seoul, , South Korea

Site Status

Samsung Medical Center ( Site 1104)

Seoul, , South Korea

Site Status

Hospital Universitario Marqués de Valdecilla-Pneumology ( Site 2003)

Santander, Cantabria, Spain

Site Status

HOSPITAL CLÍNIC DE BARCELONA ( Site 2001)

Barcelona, Catalonia, Spain

Site Status

Parc de Salut Mar - Hospital del Mar ( Site 2006)

Barcelona, , Spain

Site Status

Hospital Universitari Vall d'Hebron ( Site 2002)

Barcelona, , Spain

Site Status

HOSPITAL UNIVERSITARIO VIRGEN DEL ROCIO ( Site 2005)

Seville, , Spain

Site Status

University Hospital Basel ( Site 2205)

Basel, Canton of Basel-City, Switzerland

Site Status

UniversitätsSpital Zürich ( Site 2201)

Zurich, Canton of Zurich, Switzerland

Site Status

Cantonal Hospital St.Gallen ( Site 2203)

Sankt Gallen, , Switzerland

Site Status

Hacettepe Universite Hastaneleri ( Site 2301)

Ankara, , Turkey (Türkiye)

Site Status

Ankara Bilkent Şehir Hastanesi. ( Site 2307)

Ankara, , Turkey (Türkiye)

Site Status

Eskisehir Osmangazi University-Cardiology ( Site 2304)

Eskişehir, , Turkey (Türkiye)

Site Status

Istanbul Universitesi Istanbul Tıp Fakultesi Hastanesi-Chest Disease ( Site 2302)

Istanbul, , Turkey (Türkiye)

Site Status

Hammersmith Hospital-Department of Cardiology ( Site 2401)

London, London, City of, United Kingdom

Site Status

Sheffield Teaching Hospitals NHS Foundation Trust-Clinical Research Facility ( Site 2405)

Sheffield, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Australia Austria Belgium Colombia France Germany Guatemala Israel Italy Mexico Peru South Africa South Korea Spain Switzerland Turkey (Türkiye) United Kingdom

Related Links

Access external resources that provide additional context or updates about the study.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

MK-5475-013

Identifier Type: OTHER

Identifier Source: secondary_id

2022-501201-13-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

U1111-1279-8512

Identifier Type: REGISTRY

Identifier Source: secondary_id

5475-013

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

A Study of Mosliciguat in PH-ILD
NCT06635850 RECRUITING PHASE2