Phase 1/2 Study to Evaluate Vosilasarm (EP0062) as Monotherapy and in Combination in Patients With Advanced or Metastatic AR+/HER-2-/ER+ Breast Cancer

NCT ID: NCT05573126

Last Updated: 2025-10-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-01-11

Study Completion Date

2026-11-30

Brief Summary

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The aim of this study is to identify the optimal dose for Vosilasarm (EP0062) as monotherapy and in combination with standard-of-care therapies to assess its Safety, Tolerability, Pharmacokinetics, and Efficacy in Patients with Relapsed Locally Advanced or Metastatic AR+/HER-2-/ER+ Breast Cancer

Detailed Description

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Vosilasarm (EP0062) is being investigated in this modular, interventional, open label, Phase 1/2 dose finding, optimisation and expansion study to determine the optimal dose of Vosilasarm given as monotherapy and for evaluation in combination with standard-of-care therapies in patients with Relapsed Locally Advanced or Metastatic AR+/HER-2-/ER+ Breast Cancer. Module A (phase 1 dose finding) has completed and an optimal dose has been selected for module B (phase 2 expansion).

Conditions

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Hormone Receptor-positive Breast Cancer Hormone Receptor Positive HER-2 Negative Breast Cancer Metastatic Breast Cancer

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Module A - Vosilasarm Dose Finding

Patients are assigned to dose level cohorts to identify optimal dose and assess safety, tolerability and PK profile.

Group Type EXPERIMENTAL

Vosilasarm

Intervention Type DRUG

Vosilasarm is an orally administered investigational selective androgen receptor modulator (SARM)

Module B - Vosilasarm+ standard of care targeted therapy (elacestrant).

3-6 patients enrolled, with possible expansion up to 25 patients.

Group Type EXPERIMENTAL

Vosilasarm

Intervention Type DRUG

Vosilasarm is an orally administered investigational selective androgen receptor modulator (SARM)

Elacestrant

Intervention Type DRUG

Oral SERD

Module B - Vosilasarm+ standard of care targeted therapy (everolimus)

3-6 patients enrolled, with possible expansion up to 25 patients.

Group Type EXPERIMENTAL

Vosilasarm

Intervention Type DRUG

Vosilasarm is an orally administered investigational selective androgen receptor modulator (SARM)

Everolimus

Intervention Type DRUG

mTOR Inhibitor

Interventions

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Vosilasarm

Vosilasarm is an orally administered investigational selective androgen receptor modulator (SARM)

Intervention Type DRUG

Elacestrant

Oral SERD

Intervention Type DRUG

Everolimus

mTOR Inhibitor

Intervention Type DRUG

Other Intervention Names

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EP0062

Eligibility Criteria

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Inclusion Criteria

1. Women 18 years or older at the time of informed consent
2. Histologically proven diagnosis of breast cancer with evidence of metastatic or locally advanced breast adenocarcinoma as defined by the American Joint Committee on Cancer/Union for International Cancer Control/Tumour Node Metastases (AJCC/UICC TNM) staging classification (8th Ed, 2017) and where no conventional therapy is available or considered appropriate by the Investigator or is declined by the patient
3. Availability of archival tumour sample (formalin-fixed, paraffin-embedded block(s) or slides from a primary tumour or biopsy of a metastatic tumour lesion or lesions); in the absence of an archival tumour sample, or if only archival bone tissue is available, a fresh biopsy will need to be collected
4. Biopsy-proven AR+ and ER+ breast cancer

* For Module A, AR+ breast cancer is defined as ≥ 10% AR nuclei staining by central immunohistochemistry (IHC) using the Ventana assay
* For Modules B and C, AR+ breast cancer is defined as ≥ 30% AR nuclei staining by central IHC using the Ventana assay
5. HER2-negative breast cancer, defined as negative by fluorescence in situ hybridisation (FISH) or IHC score of 0 or 1+. If IHC is equivocal at 2+, a negative FISH test (HER2/Amplification of the centromeric region of chromosome 17)CEP17 ratio of \<2.0) is required
6. Postmenopausal, as defined by at least one of the following:

1. Age over 60 years
2. Amenorrhea \> 12 months at the time of informed consent and an intact uterus, with follicle-stimulating hormone (FSH) and oestradiol in the postmenopausal ranges (as per local practice)
3. FSH and oestradiol in the postmenopausal ranges (as per local practice) in women aged \<55 years who have undergone hysterectomy
4. Prior bilateral oophorectomy
7. Module B arm 1: patients who have progressed on ≤ 2 prior lines of endocrine therapy, including a prior CDK4/6 inhibitor.
8. Module B arm 2: patients who have progressed on ≤ 2 prior lines of endocrine therapy in advanced/metastatic setting, including prior CDK4/6 inhibitor

Exclusion Criteria

Patients with any of the following will not be included in the study:

1. Prior anti-cancer or investigational drug treatment within the following time windows:

* Any chemotherapy within 21 days prior to the first dose of study drug
* Any non-chemotherapy investigational anti-cancer drug \< 5 half-lives (28 days for biologics) or \< 14 days for small-molecule therapeutics or if half-life is not known
* Tamoxifen and aromatase inhibitors within 14 days prior to the first dose of study drug
* Fulvestrant or other investigational Selective Estrogen Receptor Degraders (SERDs) within 21 days prior to first dose of study drug
2. Currently taking testosterone, methyltestosterone, oxandrolone, oxymetholone, danazol, fluoxymesterone, testosterone-like agents (e.g., dehydroepiandrosterone, androstenedione, and other androgenic compounds, including herbals), or antiandrogens
3. Radiation therapy within 14 days prior to the first dose of study drug and scheduled to have radiation therapy during participation in this study. Short courses of palliative radiation therapy during the study might be allowed following discussion with and approval by the Medical Monitor. Palliative radiotherapy within 6 weeks prior to first dose of study drug is permitted
4. Unresolved or unstable serious toxic side effects of prior chemotherapy or radiotherapy, i.e., ≥ Grade 2 per Common Terminology Criteria for Adverse Events (CTCAE) v5.0, except fatigue, alopecia, and Grade 2 chemotherapy-induced neuropathy
5. Confirmed Corrected QT Interval by Fridericia (QTcF) \> 470 ms on screening ECG, or history of torsades de pointes (TdP), or history of congenital long QT syndrome, or immediate family history of long QT syndrome, unexplained sudden death at a young age, or sudden cardiac death
6. Any other clinically important abnormalities in rhythm, conduction, or morphology on resting ECG (e.g., complete left bundle branch block, third-degree heart block); rate-controlled atrial fibrillation is permitted
7. Concomitant medications that prolong the corrected QT interval and/or increase the risk for TdP that cannot be discontinued or substituted with another drug within 5 half-lives or 14 days before the first dose of study drug, whichever is longer
8. Congestive heart failure Grades II-IV according to the New York Heart Association at the time of screening
9. Myocardial infarction or unstable angina within the previous 6 months
10. Patients receiving medications that are known to be strong inhibitors or inducers of CYP3A4 within 5 half-lives or 14 days, whichever is longer, before the first dose of study drug
11. Prior treatment with selected combination agent
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Ellipses Pharma

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Yale School of Medicine

New Haven, Connecticut, United States

Site Status RECRUITING

Moffitt Cancer Center

Tampa, Florida, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Henry Ford Hospital

Detroit, Michigan, United States

Site Status RECRUITING

Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status RECRUITING

Texas Oncology Baylor University Medical Center

Dallas, Texas, United States

Site Status RECRUITING

Virginia Cancer Specialists

Fairfax, Virginia, United States

Site Status RECRUITING

Hospital 12 de Octubre

Usera, Madrid, Spain

Site Status RECRUITING

Hospital Universitari Vall d'Hebron (VHIO)

Barcelona, , Spain

Site Status RECRUITING

Hospital Universitario Ramón y Cajal

Madrid, , Spain

Site Status RECRUITING

NEXT Oncology Hospital Quironsalud

Madrid, , Spain

Site Status RECRUITING

Sarah Cannon Research Institute UK

London, Harley Saint, United Kingdom

Site Status RECRUITING

The Christie NHS Foundation Trust

Manchester, Wilmslow Rd, United Kingdom

Site Status RECRUITING

The Clatterbridge Cancer Centre

Liverpool, , United Kingdom

Site Status RECRUITING

Countries

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United States Spain United Kingdom

Central Contacts

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Clinical Trials Team

Role: CONTACT

+44 (0)20 3743 0992

Facility Contacts

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Neveen Abdo

Role: primary

0000000000

Role: primary

617-726-6500

Bethany Adams

Role: primary

0000000000

M Girgis

Role: backup

Role: primary

0000000000

Joyce O'Shaughnessy

Role: primary

0000000000

Christine Terraciano

Role: backup

Carrie Friedman

Role: primary

703-636-1473

Rodrigo Sanchez

Role: primary

0000000000

Role: primary

0000000000

Role: primary

0000000000

C Palmieri

Role: primary

0000000000

Other Identifiers

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EP0062-101

Identifier Type: -

Identifier Source: org_study_id

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