Standardizing Treatments for Pulmonary Exacerbations - Aminoglycoside Study

NCT ID: NCT05548283

Last Updated: 2024-08-26

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE4

Total Enrollment

730 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-04-23

Study Completion Date

2026-11-15

Brief Summary

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The purpose of this study is to look at pulmonary exacerbations in people with cystic fibrosis (CF) that need to be treated with antibiotics given through a tube inserted into a vein (intravenous or IV). A pulmonary exacerbation is a worsening of respiratory symptoms in people with CF that needs medical intervention. Both doctors and CF patients are trying to understand the best way to treat pulmonary exacerbations. This study is trying to answer the following questions about treating a pulmonary exacerbation:

* Do participants have the same improvement in lung function and symptoms if they are treated with one type of antibiotic (called beta-lactams or β-lactams) versus taking two different types of antibiotics (tobramycin and β-lactams)?
* Is taking one type of antibiotic just as good as taking two types?

Detailed Description

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Cystic Fibrosis Foundation (CFF) treatment guidelines for the management of pulmonary exacerbations (PEx) identified evidence gaps in current clinical best practices. The STOP program offers a platform for the conduct of controlled trials to develop the evidence base in order to define clinical best practices. The interventional Aminoglycoside Study (AG Study) will be a prospective, multi-center, parallel group, randomized (1:1 ratio), open-label, superiority study of intravenous aminoglycoside and β-lactams versus intravenous β-lactams only. Randomization will occur at Visit 1. The primary objective of this platform trial is to evaluate the efficacy and safety of differing treatments in CF PEx during a planned 14 day course of IV antimicrobials. Primary efficacy will be evaluated as the difference in mean Percent Predicted Forced Expiratory Volume in 1 Second (ppFEV1) changes from Visit 1 to Visit 2 (Day 28 ± 2 days) between intervention arms.

Conditions

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Cystic Fibrosis Cystic Fibrosis Pulmonary Exacerbation

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

The aminoglycoside study will compare treatment of an IV β-lactam and aminoglycoside (AG) versus an IV β-lactam only (non-AG). Individuals will be randomly assigned in a 1:1 fashion to receive either the AG or non-AG intervention for a planned 14 day course of IV antibiotics. IV antibiotic treatments for each intervention arm will be selected by the treating physician following standard of care.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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β-lactam Only (Non-AG)

Participants randomized to this arm will be prescribed a standard of care intravenous (IV) β-lactam as selected by their treating physician. Treatment must not include an IV aminoglycoside.

Group Type OTHER

Beta-lactam antibiotic

Intervention Type DRUG

Intravenous (IV) β-lactam will be selected by the treating physician following standard of care. Treatment will last for 14 days (± 2 days).

β-lactam and Aminoglycoside (AG)

Participants randomized to this arm will be prescribed a standard of care intravenous (IV) β-lactam and aminoglycoside selected by their treating physician.

Group Type OTHER

Beta-lactam antibiotic

Intervention Type DRUG

Intravenous (IV) β-lactam will be selected by the treating physician following standard of care. Treatment will last for 14 days (± 2 days).

Aminoglycoside

Intervention Type DRUG

Intravenous (IV) aminoglycoside will be selected by the treating physician following standard of care. Treatment will last for 14 days (± 2 days).

Interventions

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Beta-lactam antibiotic

Intravenous (IV) β-lactam will be selected by the treating physician following standard of care. Treatment will last for 14 days (± 2 days).

Intervention Type DRUG

Aminoglycoside

Intravenous (IV) aminoglycoside will be selected by the treating physician following standard of care. Treatment will last for 14 days (± 2 days).

Intervention Type DRUG

Other Intervention Names

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β-lactam AG

Eligibility Criteria

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Inclusion Criteria

* All genders ≥ 6 years of age at Visit 1
* Documentation of a CF diagnosis
* Clinician intent to treat index CF PEx with a planned 14-day course of IV antimicrobials
* At least one documented Pa positive culture within two years prior to Visit 1

Exclusion Criteria

* Participant is not pregnant
* No known renal impairment or history of solid organ transplantation
* No IV antimicrobial treatment, ICU admission, pneumothorax, or hemoptysis within 6 weeks prior to Visit 1
* No use of investigational therapies, new CF transmembrane conductance regulator (CFTR) modulators, or treatment for Nontuberculous mycobacteria (NTM) within 4 weeks prior to Visit 1
* No history of hypersensitivity, vestibular, or auditory toxicity with aminoglycosides
* No more than one day of IV aminoglycosides administered for the current PEx treatment prior to Visit 1
Minimum Eligible Age

6 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University of Washington

OTHER

Sponsor Role collaborator

Medical University of South Carolina

OTHER

Sponsor Role collaborator

Cystic Fibrosis Foundation

OTHER

Sponsor Role collaborator

Chris Goss

OTHER

Sponsor Role lead

Responsible Party

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Chris Goss

Associate Director, UW Adult CF Center

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

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Patrick Flume, MD

Role: PRINCIPAL_INVESTIGATOR

Medical University of South Carolina

Locations

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The Children's Hospital Alabama, University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status RECRUITING

Tucson Cystic Fibrosis Center

Tucson, Arizona, United States

Site Status RECRUITING

University of California San Diego

La Jolla, California, United States

Site Status RECRUITING

Long Beach Memorial Medical Center

Long Beach, California, United States

Site Status RECRUITING

CHOC Children's Hospital

Orange, California, United States

Site Status RECRUITING

University of California at Davis Medical Center

Sacramento, California, United States

Site Status RECRUITING

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status NOT_YET_RECRUITING

University of Florida

Gainesville, Florida, United States

Site Status RECRUITING

Joe DiMaggio Children's Hospital

Hollywood, Florida, United States

Site Status RECRUITING

Nemours Children's Clinic

Jacksonville, Florida, United States

Site Status RECRUITING

University of Miami

Miami, Florida, United States

Site Status RECRUITING

All Children's Hospital

St. Petersburg, Florida, United States

Site Status RECRUITING

Emory University

Atlanta, Georgia, United States

Site Status RECRUITING

Saint Luke's Cystic Fibrosis Center of Idaho

Boise, Idaho, United States

Site Status RECRUITING

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

Site Status RECRUITING

Northwestern University

Chicago, Illinois, United States

Site Status RECRUITING

OSF Saint Francis Medical Center

Peoria, Illinois, United States

Site Status RECRUITING

Indiana University Medical Center

Indianapolis, Indiana, United States

Site Status RECRUITING

Riley Hospital for Children

Indianapolis, Indiana, United States

Site Status RECRUITING

University of Iowa

Iowa City, Iowa, United States

Site Status RECRUITING

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status RECRUITING

University of Louisville

Louisville, Kentucky, United States

Site Status RECRUITING

Maine Medical Center

Portland, Maine, United States

Site Status RECRUITING

John Hopkins Hospital

Baltimore, Maryland, United States

Site Status RECRUITING

Boston Children's Hospital, Brigham & Women's Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

University of Massachusetts Memorial Health Care

Worcester, Massachusetts, United States

Site Status RECRUITING

University of Michigan, Michigan Medicine

Ann Arbor, Michigan, United States

Site Status RECRUITING

Helen DeVos Children's Hospital

Grand Rapids, Michigan, United States

Site Status RECRUITING

SSM Health Cardinal Glennon Children's Hospital

St Louis, Missouri, United States

Site Status RECRUITING

Washington University School of Medicine

St Louis, Missouri, United States

Site Status RECRUITING

Billings Clinic

Billings, Montana, United States

Site Status RECRUITING

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status RECRUITING

Morristown Medical Center

Morristown, New Jersey, United States

Site Status RECRUITING

Rutgers - Robert Wood Johnson Medical School

New Brunswick, New Jersey, United States

Site Status RECRUITING

Lenox Hill Hospital Cystic Fibrosis Center

New York, New York, United States

Site Status RECRUITING

Children's Hospital of New York

New York, New York, United States

Site Status RECRUITING

New York Medical College at Westchester Medical Center

Valhalla, New York, United States

Site Status RECRUITING

Children's Hospital Medical Center of Akron

Akron, Ohio, United States

Site Status RECRUITING

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status RECRUITING

University of Cincinnati Medical Center

Cincinnati, Ohio, United States

Site Status RECRUITING

Rainbow Babies and Children's Hospital/University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status RECRUITING

Nationwide Children's Hospital

Columbus, Ohio, United States

Site Status RECRUITING

Dayton Children's Hospital

Dayton, Ohio, United States

Site Status RECRUITING

Toledo Children's Hospital

Toledo, Ohio, United States

Site Status RECRUITING

Oklahoma Cystic Fibrosis Center

Oklahoma City, Oklahoma, United States

Site Status RECRUITING

Oregon Health Sciences University

Portland, Oregon, United States

Site Status RECRUITING

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status RECRUITING

Vanderbilt Children's Hospital

Nashville, Tennessee, United States

Site Status RECRUITING

University of Texas Southwestern / Children's Health

Dallas, Texas, United States

Site Status RECRUITING

University of Texas Southwestern

Dallas, Texas, United States

Site Status RECRUITING

Cook Children's Medical Center

Fort Worth, Texas, United States

Site Status RECRUITING

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status RECRUITING

Seattle Children's Hospital

Seattle, Washington, United States

Site Status RECRUITING

University of Washington Medical Center

Seattle, Washington, United States

Site Status RECRUITING

Providence Medical Group, Cystic Fibrosis Clinic

Spokane, Washington, United States

Site Status RECRUITING

West Virginia University - Morgantown

Morgantown, West Virginia, United States

Site Status RECRUITING

University of Wisconsin

Madison, Wisconsin, United States

Site Status RECRUITING

University of Calgary Adult Cystic Fibrosis Clinic (Calgary, AB)

Calgary, Alberta, Canada

Site Status RECRUITING

Countries

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United States Canada

Central Contacts

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Rachael Buckingham, BS

Role: CONTACT

206-884-7517

Barbra Fogarty

Role: CONTACT

206-884-7592

Facility Contacts

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Heather Hathorne

Role: primary

Elizabeth Ryan

Role: primary

Jenna Mielke,

Role: primary

Marylee Melendrez

Role: primary

Lila Klein

Role: primary

Daniel Diaz-Vigil

Role: primary

Jack Serio

Role: primary

Melissa Lingis

Role: primary

Norma (Jean) Barton

Role: primary

Jennifer (Jenn) Gafford

Role: primary

Ylber Whitaker

Role: primary

Diana Hodge

Role: primary

Ashleigh Streby

Role: primary

Lejla Godusevic

Role: primary

Yung Hsuan (Irene) Wu

Role: primary

Rachel Nelson

Role: primary

Ashley Scott

Role: primary

Lisa Bendy

Role: primary

Lisa Bendy

Role: primary

Mary Teresi

Role: primary

Lawrence Scott

Role: primary

Melissa Thomas

Role: primary

Harmony Renna

Role: primary

Jeanne Pinto

Role: primary

Robert Fowler

Role: primary

Jaclyn Longtine

Role: primary

Dawn Kruse

Role: primary

Andrew James

Role: primary

Freda Branch

Role: primary

Irma Bauer

Role: primary

Jerimiah Lysinger

Role: primary

Barbara A Rodgers

Role: primary

Debra Connolly

Role: primary

Sheila Redding, Sheila

Role: primary

Teresa Demarco

Role: primary

Hossein Sadeghi

Role: primary

Zachary Messer

Role: primary

Michelle Parrish

Role: primary

Kelly Thornton

Role: primary

Nicole Hummel

Role: primary

Primary RC & Participant Contact General Contact

Role: primary

Diana Gilmore

Role: primary

Amy Jones

Role: primary

Kelly Hoot

Role: primary

CF Center Participant Contact

Role: primary

Jenna Bucher

Role: primary

Melissa Molter

Role: primary

Elizabeth Hartigan

Role: primary

Ashley Warden

Role: primary

Brijesh Patel

Role: primary

Mary Klosterman

Role: primary

Ashley Keller

Role: primary

Jill Finto

Role: primary

Akilah Pierre-Louis

Role: primary

Sharon McNamara

Role: primary

Lauren Bartlett

Role: primary

Joan Milton

Role: primary

Tammy Clark

Role: primary

Melanie Nelson

Role: primary

Clare Smith

Role: primary

Other Identifiers

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STOP360-IP-22 AG

Identifier Type: -

Identifier Source: org_study_id

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