Safety and Efficacy of ADVM-022 in Treatment-Experienced Patients With Neovascular Age-related Macular Degeneration [LUNA]

NCT ID: NCT05536973

Last Updated: 2025-08-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

69 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-08-23

Study Completion Date

2028-08-31

Brief Summary

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Neovascular or wet age-related macular degeneration (nAMD) is a degenerative ocular disease associated with the infiltration of abnormal blood vessels in the retina from the underlying choroid layer and is a leading cause of blindness in patients over 65 years of age. The abnormal angiogenic process in nAMD is stimulated and modulated by vascular endothelial growth factor (VEGF). Treatment of nAMD requires frequent intravitreal (IVT) injections of VEGF inhibitors (anti-VEGF) administered every 4-16 weeks. ADVM-022 (AAV.7m8-aflibercept) is a gene therapy product being developed for the treatment of nAMD and offers the potential for sustained intraocular expression of aflibercept following a single IVT injection. ADVM-022 is designed to reduce the current treatment burden which often results in undertreatment and vision loss in patients with nAMD receiving anti-VEGF therapy in clinical practice.

Detailed Description

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This Phase 2, multi-center, randomized, double-masked, parallel group study is designed to evaluate the safety, tolerability, and efficacy of a single IVT injection of ADVM-022 at one of two doses (2 × 10\^11 vg/eye \[2E11\] or 6 × 10\^10 vg/eye \[6E10\]) accompanied by one of four prophylactic corticosteroid treatment regimens.

Anti-VEGF treatment-experienced study participants meeting the eligibility criteria that will be randomized between the 2E11 vg/eye and 6E10 vg/eye ADVM-022 doses each with 4 prophylaxis arms for a total of 8 treatment arms, and only one eye per study participant will be selected as the study eye.

Safety, tolerability, and efficacy will be evaluated for a period of approximately 5 years from baseline.

Conditions

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Neovascular Age-related Macular Degeneration

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Dose 1

A single intravitreal injection of ADVM-022 2E11 vg/eye

Group Type EXPERIMENTAL

ADVM-022

Intervention Type GENETIC

A single IVT injection of 2E11 vg/eye ADVM-022 dose in combination with one (1) of four (4) corticosteroid treatment regimens

Dose 2

A single intravitreal injection of ADVM-022 6E10 vg/eye

Group Type EXPERIMENTAL

ADVM-022

Intervention Type GENETIC

A single IVT injection of 6E10 vg/eye ADVM-022 dose in combination with one (1) of four (4) corticosteroid treatment regimens

Interventions

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ADVM-022

A single IVT injection of 2E11 vg/eye ADVM-022 dose in combination with one (1) of four (4) corticosteroid treatment regimens

Intervention Type GENETIC

ADVM-022

A single IVT injection of 6E10 vg/eye ADVM-022 dose in combination with one (1) of four (4) corticosteroid treatment regimens

Intervention Type GENETIC

Eligibility Criteria

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Inclusion Criteria

* Male or female participants, ≥ 50 years of age
* Willing and able to provide written, signed informed consent for this study
* Demonstrated a meaningful response to anti-VEGF therapy
* Participants must be under active anti-VEGF treatment for wet AMD and received a minimum of 2 injections within 4 months prior to screening for the treatment of choroidal neovascularization secondary to nAMD in the study eye
* Vision of the study eye at Baseline: BCVA in the range of 25 - 83 ETDRS letters, inclusive (approximate Snellen equivalent visual acuity range of 20/25 - 20/320)
* Vision of the non-study eye at Baseline: BCVA ≥ 35 ETDRS letters (approximate Snellen equivalent of 20/200 or better)

Exclusion Criteria

* Any condition that could affect the interpretation of results or render the participant at high risk of treatment complications in the opinion of the Investigator
* Ocular or periocular infection or intraocular inflammation in either eye within 1 month prior to or at the Randomization Visit (Day -7)
* Uncontrolled diabetes or HbA1c ≥ 7.0 %
* History or evidence of significant uncontrolled concomitant disease within 6 months of the Screening visit
* Any history of ongoing bleeding disorders or INR \>3.0
* History or evidence of macular or retinal disease other than nAMD
* History or evidence of retinal detachment or retinal pigment epithelium rip/tear
* Uncontrolled ocular hypertension or glaucoma
* Prior treatment with photodynamic therapy or retinal laser for the treatment of nAMD
* Any history of vitrectomy or any other vitreoretinal surgery
* Prior treatment with gene therapy at any time or any non-gene therapy investigational treatment or medical device in the study eye within 3 months of the Screening Visit or 5 half-lives of the investigational medicinal product
Minimum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Adverum Biotechnologies, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Adam Turpcu, PhD

Role: STUDY_DIRECTOR

Adverum Biotechnologies, Inc.

Locations

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Adverum Clinical Site 178

Phoenix, Arizona, United States

Site Status

Adverum Clinical Site 126

Phoenix, Arizona, United States

Site Status

Adverum Clinical Site 159

Tucson, Arizona, United States

Site Status

Adverum Clinical Site 100

Beverly Hills, California, United States

Site Status

Adverum Clinical Site 172

Encino, California, United States

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Adverum Clinical Site 169

Fullerton, California, United States

Site Status

Adverum Clinical Site 170

Pasadena, California, United States

Site Status

Adverum Clinical Site 174

Poway, California, United States

Site Status

Adverum Clinical Site 164

Riverside, California, United States

Site Status

Adverum Clinical Site 166

Sacramento, California, United States

Site Status

Adverum Clinical Site 175

Santa Barbara, California, United States

Site Status

Adverum Clinical Site 116

Lakewood, Colorado, United States

Site Status

Adverum Clinical Site 165

Waterford, Connecticut, United States

Site Status

Adverum Clinical Site 124

Deerfield Beach, Florida, United States

Site Status

Adverum Clinical Site 176

Fort Lauderdale, Florida, United States

Site Status

Adverum Clinical Site 168

Jacksonville, Florida, United States

Site Status

Adverum Clinical Site 149

‘Aiea, Hawaii, United States

Site Status

Adverum Clinical Site 167

Detroit, Michigan, United States

Site Status

Adverum Clinical Site 161

Royal Oak, Michigan, United States

Site Status

Adverum Clinical Site 163

Southaven, Mississippi, United States

Site Status

Adverum Clinical Site 177

Omaha, Nebraska, United States

Site Status

Adverum Clinical Site 119

Reno, Nevada, United States

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Adverum Clinical Site 146

Cherry Hill, New Jersey, United States

Site Status

Adverum Clinical Site 171

Teaneck, New Jersey, United States

Site Status

Adverum Clinical Site 122

West Columbia, South Carolina, United States

Site Status

Adverum Clinical Site 144

Rapid City, South Dakota, United States

Site Status

Adverum Clinical Site 101

Nashville, Tennessee, United States

Site Status

Adverum Clinical Site 123

Abilene, Texas, United States

Site Status

Adverum Clinical Site 154

Austin, Texas, United States

Site Status

Adverum Clinical Site 108

Bellaire, Texas, United States

Site Status

Adverum Clinical Site 162

McAllen, Texas, United States

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Adverum Clinical Site 151

San Antonio, Texas, United States

Site Status

Adverum Clinical Site 107

The Woodlands, Texas, United States

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Adverum Clinical Site 152

Morgantown, West Virginia, United States

Site Status

Adverum Clinical Site 502

Nantes, Loire-Atlantique, France

Site Status

Adverum Clinical Site 501

Lyon, Rhône, France

Site Status

Adverum Clinical Site 500

Créteil, Val-de-Marne, France

Site Status

Adverum Clinical Site 600

London, , United Kingdom

Site Status

Adverum Clinical Site 601

Oxford, , United Kingdom

Site Status

Countries

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United States France United Kingdom

Other Identifiers

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ADVM-022-11

Identifier Type: -

Identifier Source: org_study_id

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