A Study to Assess Efficacy and Safety of KarXT for the Treatment of Psychosis Associated With Alzheimer's Disease (ADEPT-1)

NCT ID: NCT05511363

Last Updated: 2026-01-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

380 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-08-23

Study Completion Date

2026-10-05

Brief Summary

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This is a Phase 3, 38-week, randomized, double-blind, placebo-controlled, multicenter, outpatient study in subjects with psychosis associated with Alzheimer's Disease.

The primary objective of the study is to evaluate relapse prevention in subjects with psychosis associated with Alzheimer's Disease treated with KarXT compared to placebo. The secondary objectives of the study are to evaluate the time from randomization to discontinuation for any reason and safety and tolerability in subjects with psychosis associated with Alzheimer's Disease treated with KarXT compared to placebo.

Detailed Description

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Conditions

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Psychosis Associated With Alzheimer's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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KarXT

Xanomeline and Trospium Chloride Capsules

Group Type EXPERIMENTAL

KarXT

Intervention Type DRUG

KarXT 20 mg/2 mg TID KarXT 30 mg/3 mg TID KarXT 40 mg/4 mg TID KarXT 50 mg/5 mg TID KarXT 66.7/6.67 mg TID

Placebo

Placebo Capsules

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo Capsules

Interventions

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KarXT

KarXT 20 mg/2 mg TID KarXT 30 mg/3 mg TID KarXT 40 mg/4 mg TID KarXT 50 mg/5 mg TID KarXT 66.7/6.67 mg TID

Intervention Type DRUG

Placebo

Placebo Capsules

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Is aged 55 to 90 years, inclusive, at Screening
2. Can understand the nature of the study and protocol requirements and provide a signed informed consent form before any study assessments are performed. If the subject is deemed not competent to provide consent, the following requirements for consent must be met.

1. The subject's legally acceptable representative or caregiver/study partner, if local regulations allow, must provide informed consent
2. The subject must provide informed assent
3. Meets clinical criteria for possible or probable Alzheimer's Disease
4. Has a Magnetic Resonance Imaging (MRI) or Computed Tomography (CT) scan of the brain (completed within the past 5 years) taken during or subsequent to the onset of dementia to rule out other central nervous system (CNS) disease that could account for the dementia syndrome. If not available, a non-contrast brain MRI or non-contrast head CT must be done during screening.
5. Living at the same home or residential assisted-living facility for a minimum of six weeks before Screening
6. Capable of self-locomotion (alone or with the aid of an assistive device) and have an identified or proxy caregiver (spends approximately 10 hours/week with the subject) that is willing to:

1. Attend all visits and report on subject's status
2. Oversee subject compliance with medication and study procedures
3. Participate in the study assessments and provide informed consent to participate in the study
7. History of psychotic symptoms (meeting International Psychogeriatric Association \[IPA\] criteria) for at least 2 months prior to Screening.
8. Clinical Global Impressions-Severity (CGI-S) scale with a score ≥4 (moderate) at Screening and Baseline. CGI-S requires the assessor to consider aspects of the psychosis prior to providing a global assessment of severity. These aspects include hallucinations and delusions.
9. Subjects are required to meet at least one of the following criteria at Screening and Baseline:

1. Moderate to severe delusions, defined as Neuropsychiatric Inventory-Clinician (NPI-C): Delusions domain score of ≥2 on two of the eight items OR
2. Moderate to severe hallucinations, defined as NPI-C: Hallucinations domain score of ≥ 2 on two of the seven items.
10. Mini-Mental State Examination (MMSE) score of 8 to 22, inclusive, at Screening
11. If the subject is taking a cholinesterase inhibitor and/or memantine, they must have been on a stable dose for 6 weeks prior to Screening and be willing to maintain a stable dose for the duration of the study.
12. Subject is willing and able to visit the clinic in an outpatient setting for the study duration, follow instructions, and comply with the protocol requirements
13. BMI must be within 18 to 40 kg/m2 inclusive
14. Female subjects must not be pregnant or breastfeeding. Women of childbearing potential (WOCBP), or men whose sexual partners are WOCBP, must be able and willing to use at least 1 highly effective method of contraception during the study and for at least 1 menstrual cycle (e.g., 30 days) after the last dose of IMP or matching placebo. Sperm donation is not allowed for 30 days after the final dose of the IMP or matching placebo.

Exclusion Criteria

1. Psychotic symptoms that are primarily attributable to a condition other than the Alzheimer's Disease causing dementia
2. History of major depressive episode with psychotic features during the 12 months prior to Screening
3. History of a diagnosis of bipolar disorder, schizophrenia, or schizoaffective disorder
4. Significant or severe medical conditions including pulmonary, hepatic, renal, hematologic, gastrointestinal, endocrine, immunologic, dermatologic, neurologic, cardiovascular or oncologic disease, or any other condition that, in the opinion of the Investigator, could jeopardize the safety of the subject, ability to complete or comply with the study procedures or validity of the study results
5. Significant or severe renal impairment based on a screening cutoff for Estimated Glomerular Filtration Rate (eGFR) of \<60 mL/min/1.73 m2
6. History of ischemic stroke within 12 months prior to Screening or any evidence of hemorrhagic stroke
7. History of cerebral amyloid angiopathy, epilepsy, central nervous system neoplasm, unstable thyroid function, or unexplained syncope
8. Any of the following:

1. New York Heart Association Class 2 congestive heart failure
2. Grade 2 or greater angina pectoris
3. Sustained ventricular tachycardia
4. Ventricular fibrillation
5. Torsade de pointes
6. Implantable cardiac defibrillator
9. Myocardial infarction within the 6 months prior to Screening
10. Personal or family history of symptoms of long QT syndrome as evaluated by the investigator
11. Human immunodeficiency virus, cirrhosis, biliary duct abnormalities, hepatobiliary carcinoma, and/or active hepatic viral infections as indicated by medical history or liver function tests results
12. History or high risk of urinary retention, gastric retention, or narrow-angle glaucoma as evaluated by the investigator
13. For males only, any one of the following:

1. History of bladder stones
2. History of recurrent urinary tract infections
3. Serum prostate specific antigen (PSA) \> 10 ng/mL at Screening
4. An International Prostate Symptom Score (IPSS) of 5 (almost always) on items 1, 3, 5, or 6
5. A sum of scores on IPSS items 1, 3, 5, and 6 of ≥9
14. History of irritable bowel syndrome (with or without constipation) or serious constipation requiring treatment within the last 6 months
15. Risk of suicidal behavior during the study as determined by clinical assessment and/ or C-SSRS
16. Clinically significant abnormal finding on the physical examination, electrocardiogram, or clinical laboratory results at Screening
17. Urine toxicology screen is positive substances other than cannabis or benzodiazepines (both cannabis and short-or medium-acting benzodiazepines are allowed in limited quantities during the study) unless approval has been given by the Medical Monitor
18. Recent history of receiving monoamine oxidase inhibitors, anticonvulsants (e.g., lamotrigine, divalproex), lithium, tricyclic antidepressants (e.g., imipramine, desipramine), or any other psychoactive medications except for as-needed anxiolytics (e.g., lorazepam, chloral hydrate)

1. Selective serotonin reuptake inhibitors and serotonin norepinephrine reuptake inhibitors taken at a stable dose for at least 8 weeks prior to Screening may be permitted
2. Mirtazapine or trazodone may be used as a hypnotic if started at least 8 weeks prior to Screening. If needed, an extension (up to two weeks) of the Screening Period may be allowed with approval of the Sponsor/Medical Monitor.
19. If, in the opinion of the Investigator and/or Sponsor/Medical Monitor, subject is unsuitable for enrollment in the study or subject has any finding that, in the view of the Investigator and/or Sponsor/ Medical Monitor, may compromise the safety of the subject or affect his/her ability to adhere to the protocol visit schedule or fulfill visit requirements
20. Positive test for coronavirus (COVID-19) within 2 weeks before or at Screening; antigen or PCR local testing can be done at the discretion of the Investigator
21. Unable to taper and discontinue a concomitant medication that would preclude participation in the study
22. Prior exposure to KarXT
23. Experienced any significant adverse events due to trospium, including a known hypersensitivity to trospium
24. Participation in another clinical study in which the subject received an experimental or investigational drug within 3 months before Screening or has participated in more than 2 clinical studies in the past year
Minimum Eligible Age

55 Years

Maximum Eligible Age

90 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Karuna Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Local Institution - 1029

Homewood, Alabama, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1044

Phoenix, Arizona, United States

Site Status COMPLETED

Local Institution - 1033

Encino, California, United States

Site Status COMPLETED

Local Institution - 1031

Irvine, California, United States

Site Status WITHDRAWN

ATP Clinical Research-302 W La Veta Ave

Orange, California, United States

Site Status RECRUITING

Local Institution - 1043

Pasadena, California, United States

Site Status COMPLETED

Local Institution - 1047

San Marcos, California, United States

Site Status ACTIVE_NOT_RECRUITING

Sunwise Clinical Research, LLC - Walnut Creek - IVY - PPDS

Walnut Creek, California, United States

Site Status RECRUITING

Local Institution - 1014

Colorado Springs, Colorado, United States

Site Status COMPLETED

Local Institution - 1013

Stamford, Connecticut, United States

Site Status COMPLETED

Local Institution - 1011

Boca Raton, Florida, United States

Site Status COMPLETED

Envision Trials LLC

Bonita Springs, Florida, United States

Site Status RECRUITING

Local Institution - 1015

Bradenton, Florida, United States

Site Status COMPLETED

Local Institution - 1048

Clermont, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Arrow Clinical Trials

Daytona Beach, Florida, United States

Site Status RECRUITING

Local Institution - 1045

Doral, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1046

Hialeah, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1024

Hialeah, Florida, United States

Site Status WITHDRAWN

Local Institution - 1052

Hialeah, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1049

Homestead, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

K2 Medical Research - Maitland

Maitland, Florida, United States

Site Status RECRUITING

Premier Clinical Research Institute

Miami, Florida, United States

Site Status RECRUITING

Local Institution - 1005

Miami, Florida, United States

Site Status COMPLETED

Floridian Neuroscience Institute-1901 SW 1 St

Miami, Florida, United States

Site Status RECRUITING

Local Institution - 1010

Miami, Florida, United States

Site Status COMPLETED

Local Institution - 1143

Miami, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1009

Miami, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Future Care Solution LLC

Miami, Florida, United States

Site Status RECRUITING

South Florida Research Phase I-IV, Inc. - Miami

Miami, Florida, United States

Site Status RECRUITING

Novel Clinical Research Center, LLC.

Miami, Florida, United States

Site Status RECRUITING

Local Institution - 1111

Miami, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Coral Research Clinic & Coral Diagnostic Center

Miami, Florida, United States

Site Status RECRUITING

Local Institution - 1042

Miami, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1032

Miami Lakes, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1026

Miami Springs, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1027

Ocala, Florida, United States

Site Status WITHDRAWN

Local Institution - 1012

Pensacola, Florida, United States

Site Status COMPLETED

Local Institution - 1008

St. Petersburg, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1050

Tampa, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

K2 Medical Research - Tampa

Tampa, Florida, United States

Site Status RECRUITING

Local Institution - 1040

The Villages, Florida, United States

Site Status WITHDRAWN

Local Institution - 1037

Chicago, Illinois, United States

Site Status COMPLETED

Local Institution - 1018

Manhasset, New York, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1030

New York, New York, United States

Site Status WITHDRAWN

Local Institution - 1051

New York, New York, United States

Site Status COMPLETED

Local Institution - 1017

New York, New York, United States

Site Status COMPLETED

Local Institution - 1002

Staten Island, New York, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1034

Stony Brook, New York, United States

Site Status COMPLETED

Five Towns Neurology, PC

Woodmere, New York, United States

Site Status RECRUITING

Local Institution - 1003

Canton, Ohio, United States

Site Status WITHDRAWN

Local Institution - 1028

Oklahoma City, Oklahoma, United States

Site Status WITHDRAWN

Local Institution - 1016

Oklahoma City, Oklahoma, United States

Site Status COMPLETED

Local Institution - 1019

Allentown, Pennsylvania, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1035

Charleston, South Carolina, United States

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 1038

Franklin, Tennessee, United States

Site Status COMPLETED

Local Institution - 1022

Flower Mound, Texas, United States

Site Status COMPLETED

Local Institution - 1036

Frisco, Texas, United States

Site Status COMPLETED

Clinical Trial Network - 7080 Southwest Fwy

Houston, Texas, United States

Site Status RECRUITING

Medical Center Sveti Naum EOOD

Sofia, Sofia-Grad, Bulgaria

Site Status RECRUITING

Local Institution - 4505

Sofia, Sofia-Grad, Bulgaria

Site Status COMPLETED

Local Institution - 4502

Sofia, Sofia-Grad, Bulgaria

Site Status COMPLETED

Medical Center Medconsult Pleven OOD

Pleven, , Bulgaria

Site Status RECRUITING

Local Institution - 4504

Vratsa, , Bulgaria

Site Status COMPLETED

Local Institution - 4102

Zagreb, City of Zagreb, Croatia

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 4103

Zagreb, City of Zagreb, Croatia

Site Status COMPLETED

Local Institution - 4105

Zagreb, City of Zagreb, Croatia

Site Status ACTIVE_NOT_RECRUITING

Klinika za psihijatriju Vrapce

Zagreb, City of Zagreb, Croatia

Site Status RECRUITING

Psychiatric Clinic Sveti Ivan

Zagreb, City of Zagreb, Croatia

Site Status RECRUITING

CLINTRIAL s.r.o.

Prague, Praha, Hlavní Mesto, Czechia

Site Status RECRUITING

Local Institution - 4003

Brno, South Moravian, Czechia

Site Status WITHDRAWN

Neuroterapie KH, s.r.o

Kutná Hora, , Czechia

Site Status RECRUITING

A-SHINE s.r.o.

Pilsen, , Czechia

Site Status RECRUITING

Clinoxus s.r.o.

Prague, , Czechia

Site Status RECRUITING

Vestra Clinics s.r.o.

Rychnov nad Kněžnou, , Czechia

Site Status RECRUITING

Local Institution - 2501

Reims, Marne, France

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 2502

Dijon, , France

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 2503

Rouen, , France

Site Status COMPLETED

Local Institution - 2401

Böblingen, Baden-Wurttemberg, Germany

Site Status COMPLETED

Local Institution - 2403

Bayreuth, Bavaria, Germany

Site Status WITHDRAWN

Local Institution - 2402

Homburg, Saarland, Germany

Site Status WITHDRAWN

Local Institution - 2301

Rome, Lazio, Italy

Site Status COMPLETED

Local Institution - 2306

Baggiovara, Modena, Italy

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 2307

Ponderano (Biella), Piedmont, Italy

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 2308

Florence, Tuscany, Italy

Site Status COMPLETED

Local Institution - 2304

Milan, , Italy

Site Status COMPLETED

Local Institution - 2305

Monza, , Italy

Site Status COMPLETED

Local Institution - 2302

Pisa, , Italy

Site Status COMPLETED

Local Institution - 2303

Roma, , Italy

Site Status ACTIVE_NOT_RECRUITING

Local Institution - 2309

Roma, , Italy

Site Status COMPLETED

University Clinical Center of Serbia - Pasterova 2 - PPDS

Belgrade, Belgrade, Serbia

Site Status RECRUITING

Clinical Hospital Center Dragisa Misovic Dedinje

Belgrade, , Serbia

Site Status RECRUITING

Local Institution - 4307

Belgrade, , Serbia

Site Status COMPLETED

Military Medical Academy

Belgrade, , Serbia

Site Status RECRUITING

Military Medical Academy

Belgrade, , Serbia

Site Status RECRUITING

Special Hospital for Psychiatric Diseases Kovin

Kovin, , Serbia

Site Status RECRUITING

University Clinical Center Kragujevac

Kragujevac, , Serbia

Site Status RECRUITING

University Clinical Center Kragujevac

Kragujevac, , Serbia

Site Status RECRUITING

University Clinical Center Kragujevac

Kragujevac, , Serbia

Site Status RECRUITING

Clinical Centre of Vojvodina

Novi Sad, , Serbia

Site Status RECRUITING

Local Institution - 4311

Vršac, , Serbia

Site Status COMPLETED

Univerzitna nemocnica L Pasteura Kosice-Rastislavova 43

Košice, Košice Region, Slovakia

Site Status RECRUITING

MUDr. Beata Dupejova, Neurologicka ambulancia, s.r.o.

Banská Bystrica, , Slovakia

Site Status RECRUITING

KONZILIUM s.r.o

Dubnica nad Váhom, , Slovakia

Site Status RECRUITING

EPAMED s.r.o

Košice, , Slovakia

Site Status RECRUITING

Crystal Comfort, s.r.o.

Vranov nad Topľou, , Slovakia

Site Status RECRUITING

Local Institution - 4404

Žilina, , Slovakia

Site Status WITHDRAWN

Local Institution - 2205

Barcelona, , Spain

Site Status COMPLETED

Local Institution - 2207

Madrid, , Spain

Site Status ACTIVE_NOT_RECRUITING

Complejo Asistencial Universitario de Salamanca - H. Clinico

Salamanca, , Spain

Site Status RECRUITING

Hospital Victoria Eugenia

Seville, , Spain

Site Status RECRUITING

Hospital Universitario Rio Hortega

Valladolid, , Spain

Site Status RECRUITING

Hospital Provincial de Zamora

Zamora, , Spain

Site Status RECRUITING

Hospital Viamed Montecanal

Zaragoza, , Spain

Site Status RECRUITING

Local Institution - 2103

Swindon, Wiltshire, United Kingdom

Site Status WITHDRAWN

Local Institution - 2105

Aberdeen, , United Kingdom

Site Status WITHDRAWN

Local Institution - 2104

Motherwell, , United Kingdom

Site Status WITHDRAWN

Countries

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United States Bulgaria Croatia Czechia France Germany Italy Serbia Slovakia Spain United Kingdom

Central Contacts

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BMS Clinical Trials Contact Center www.BMSClinicalTrials.com

Role: CONTACT

855-907-3286

First line of the email MUST contain the NCT# and Site #.

Role: CONTACT

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Gustavo Alva, Site 1001

Role: primary

949-354-5353

Ira Glick, Site 1007

Role: primary

925-298-5147

Daniel Mandri, Site 1020

Role: primary

305-819-2909

David Billmeier, Site 1023

Role: primary

386-278-8000

Brandon Lenox, Site 1039

Role: primary

407-670-5833

Emelina Arocha, Site 1021

Role: primary

305-445-5994

Emilio Mantero-Atienza, Site 1115

Role: primary

305-326-0776

Pilar Trueba, Site 1129

Role: primary

305-888-0410

Silvia Silva Duluc, Site 1053

Role: primary

305-669-6166

Heber Varela, Site 1006

Role: primary

786-773-2737

Jorge Paoli Bruno, Site 1054

Role: primary

000-000-0000

Kelley Yokum, Site 1041

Role: primary

813-800-5252

David Steiner, Site 1025

Role: primary

516-239-1800

Nelson Berrios, Site 1004

Role: primary

Assen Karadaliev, Site 4501

Role: primary

+359888220704

Maria Aleksandrova, Site 4503

Role: primary

+35964910999

Ninoslav Mimica, Site 4101

Role: primary

+38513780678

Igor Filipcic, Site 4104

Role: primary

38513430020

Zdenek Solle, Site 4002

Role: primary

+420222510607

Slavomír Pietrucha, Site 4001

Role: primary

420777551077

Lubos Janu, Site 4005

Role: primary

420777242101

Michaela Klementova, Site 4004

Role: primary

+420724773546

Ladislav Pazdera, Site 4006

Role: primary

420604236033

Tanja Stojkovic, Site 4302

Role: primary

381607545958

Vladimir Diligenski, Site 4306

Role: primary

+381637708765

Ranko Raicevic, Site 4304

Role: primary

381113609206

Aleksandar Eror, Site 4308

Role: primary

381113609206

Jovanka Petrovic, Site 4305

Role: primary

+38163529054

Mirjana Jovanovic, Site 4310

Role: primary

+381698776622

Dragana Ignjatovic Ristic, Site 4303

Role: primary

+38163685994

Vladimir Janjic, Site 4301

Role: primary

+38134370208

Marija Semnic, Site 4309

Role: primary

381184601111

Slavka Dubinska, Site 4405

Role: primary

+421903625643

Beata Dupejova, Site 4401

Role: primary

+421484124549

Magdalena Perichtova, Site 4402

Role: primary

+421424426231

Eva Palova, Site 4406

Role: primary

+421556402727

Dagmar Breznoscakova, Site 4403

Role: primary

+421574880251

Angel Montejo Gonzalez, Site 2204

Role: primary

+34923126580

Felix Viñuela Fernandez, Site 2201

Role: primary

+34654566812

Juan Muñoz Sanchez, Site 2203

Role: primary

+34679279973

Manuel Angel Franco Martin, Site 2202

Role: primary

34980520200

Antonio Oliveros-Cid, Site 2206

Role: primary

+34670492099

Related Links

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Other Identifiers

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CN012-0026

Identifier Type: OTHER

Identifier Source: secondary_id

KAR-031

Identifier Type: OTHER

Identifier Source: secondary_id

CN012-0026

Identifier Type: -

Identifier Source: org_study_id

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