A Study to Evaluate the Efficacy, Safety, Tolerability, and Pharmacokinetics of SPR720 as Compared With Placebo for the Treatment of Participants With Mycobacterium Avium Complex (MAC) Pulmonary Disease

NCT ID: NCT05496374

Last Updated: 2025-10-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

25 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-12-14

Study Completion Date

2024-12-02

Brief Summary

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The purpose of the study is to evaluate

1. The microbiological response and clinical efficacy of SPR720 compared with placebo in participants with nontuberculous mycobacteria pulmonary disease (NTM-PD).
2. The safety and tolerability of SPR720 in participants with NTM- PD
3. The pharmacokinetic (PK) of SPR719, active moiety, following orally (po) administered prodrug SPR720 in participants with NTM-PD.

Detailed Description

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Conditions

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Nontuberculous Mycobacterial Pulmonary Disease (NTM-PD)

Keywords

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Mycobacterium avium Complex MAC Pulmonary disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Investigator Blind: Placebo

Participants received SPR720 matching-placebo capsules, orally, once daily (QD) for 56 days.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo-matching capsules was administered orally.

Investigator Blind: SPR720 500 mg

Participants received SPR720 500 mg (250 mg × 2) capsules along with 2 SPR720 matching- placebo capsules, orally, QD for 56 days.

Group Type EXPERIMENTAL

SPR720 500 mg

Intervention Type DRUG

SPR720 500 mg (250 mg × 2 capsules) was administered orally.

Investigator Blind: SPR720 1000 mg

Participants received SPR720 1000 mg (250 mg × 4) capsules, orally, QD for 56 days.

Group Type EXPERIMENTAL

SPR720 1000 mg

Intervention Type DRUG

SPR720 500 mg (250 mg × 4 capsules) was administered orally.

Open-label: SPR720 1000 mg

Participants received SPR720 1000 mg (250 mg × 4) capsules, orally, QD for 56 days.

Group Type EXPERIMENTAL

SPR720 1000 mg

Intervention Type DRUG

SPR720 500 mg (250 mg × 4 capsules) was administered orally.

Open-label: SPR720 500 mg

Participants received SPR720 500 mg (250 mg × 2) capsules, orally, twice daily (BID) for 56 days.

Group Type EXPERIMENTAL

SPR720 500 mg

Intervention Type DRUG

SPR720 500 mg (250 mg × 2 capsules) was administered orally.

Interventions

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Placebo

Placebo-matching capsules was administered orally.

Intervention Type DRUG

SPR720 500 mg

SPR720 500 mg (250 mg × 2 capsules) was administered orally.

Intervention Type DRUG

SPR720 1000 mg

SPR720 500 mg (250 mg × 4 capsules) was administered orally.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Has a prior diagnosis of NTM-PD due to MAC according to American Thoracic Society (ATS) criteria
2. Has at least one prior lower respiratory culture (sputum or bronchoalveolar lavage \[BAL\]) positive for MAC in the 12 months prior to consent
3. Has an induced sputum culture at Screening positive for MAC by quantitative culture on solid agar
4. Is either treatment naïve and has not received any prior treatment for MAC, OR if previously treated for MAC and meets all of the following criteria:

1. Has a history of successful treatment with sputum culture conversion to negative
2. Has recent sputum or BAL culture evidence of recurrent or relapsed disease and
3. Has been off therapy for at least 3 months prior to consent
5. Has clinical signs and symptoms within the 6 weeks prior to consent that are consistent with NTM-PD with ≥2 of the following:

1. chronic cough
2. fatigue
3. frequent throat clearing
4. shortness of breath (dyspnea)
5. coughing up of blood (hemoptysis)
6. excessive mucus (sputum) production
7. fever (temperature \>38ºC or \>100.4ºF)
8. night sweats
9. loss of appetite
10. unintended weight loss
11. wheezing
12. chest pain
6. Has a measured forced expiratory volume in the first second following maximal inhalation (FEV1) % predicted ≥30% within 3 months prior to consent. If prior FEV1% predicted test result is not available, obtain FEV1% predicted at Screening to confirm eligibility

Exclusion Criteria

1. In the opinion of the Investigator, is not a candidate for a 5-month delay in initiation of standard multidrug therapy to participate in a placebo-controlled clinical trial (e.g., participant has severe symptoms or, extensive disease burden)
2. Has disseminated or extrapulmonary NTM disease
3. Has end-stage NTM-PD or treatment-refractory NTM-PD
4. Has isolation on lower respiratory (sputum or BAL) cultures of any Mycobacterium species other than those included in MAC within the 6 months prior to consent
5. Has any other condition or prior therapy, which, in the opinion of the Investigator, would make the participant unsuitable for this study, including compliance with all study assessments and adherence to the protocol schedule of assessment
6. Prior exposure to SPR720. Participants who are unable to comply with the requirements of the study or who in the opinion of the Investigator should not participate in the study are not eligible
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Spero Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Xilla Ussrey, MD

Role: STUDY_DIRECTOR

Spero Therapeutics Inc

Locations

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Medical Facility

Birmingham, Alabama, United States

Site Status

Medical Facility

Fresno, California, United States

Site Status

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Los Angeles, California, United States

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Newport Beach, California, United States

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Northridge, California, United States

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Santa Clarita, California, United States

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Washington D.C., District of Columbia, United States

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Kissimmee, Florida, United States

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Loxahatchee Groves, Florida, United States

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Miami, Florida, United States

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Sebring, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Iowa City, Iowa, United States

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Kansas City, Kansas, United States

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New Bedford, Massachusetts, United States

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Rochester, Minnesota, United States

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Lebanon, New Hampshire, United States

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New Hyde Park, New York, United States

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Chapel Hill, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Cleveland, Ohio, United States

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Portland, Oregon, United States

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Pittsburgh, Pennsylvania, United States

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Charleston, South Carolina, United States

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Denison, Texas, United States

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Sherman, Texas, United States

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Medical Facility

Tyler, Texas, United States

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Countries

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United States

Other Identifiers

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SPR720-202

Identifier Type: -

Identifier Source: org_study_id