Outcomes of Autologous Bone Marrow Mononuclear Cell Administration in the Treatment of Neurologic Sequelea in Children With Spina Bifida

NCT ID: NCT05472428

Last Updated: 2022-07-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

11 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-07-01

Study Completion Date

2021-08-31

Brief Summary

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The aim of this study was to evaluate the safety and efficacy of autologous bone marrow mononuclear cell infusion in the management of neurological sequelae in children with spina bifida

Detailed Description

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The aim of this study was to evaluate the safety and effectiveness of autologous bone marrow mononuclear cells in 11 patients with spina bifida at Vinmec Research Institute of Stem Cell and Gene Technology in Hanoi, Vietnam from 2016 to 2020

Conditions

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Stem Cell Infusion

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Open Label

Study Groups

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Autologous BMMNC transplantation

\- Autologous bone marrow mononuclear cell transplantation 2 intrathecal administrations of autologous bone marrow mononuclear cells at baseline and 6 months afterward

Group Type EXPERIMENTAL

Autologous bone marrow mononuclear cell transplantation

Intervention Type COMBINATION_PRODUCT

Transplantation of Autologous Bone Marrow Mononuclear cells

Interventions

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Autologous bone marrow mononuclear cell transplantation

Transplantation of Autologous Bone Marrow Mononuclear cells

Intervention Type COMBINATION_PRODUCT

Eligibility Criteria

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Inclusion Criteria

* The patient who was diagnosed with lumbar spina bifida underwent spinal cord close-up surgery.
* Both genders.
* Aged between 6 months and 15 years old.
* Exhibited bowel disorders (constipation, fecal incontinence) and urinary dysfunction (urinary retention or leakage).

Exclusion Criteria

* Vertebrae clefts in the chest, neck, and other spinal locations.
* Coagulopathy.
* Acute and chronic infection.
* Kidney function disorder, liver failure
* Patients with complex cardiovascular diseases (including valvular heart disease, cardiomyopathy, arrhythmia, congenital heart disease, hypertrophy syndrome).
* Distress
Minimum Eligible Age

6 Months

Maximum Eligible Age

15 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Vinmec Health Care System (Vingroup Joint Stock Company)

UNKNOWN

Sponsor Role collaborator

Vinmec Research Institute of Stem Cell and Gene Technology

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Liem T Nguyen, MD., PhD

Role: PRINCIPAL_INVESTIGATOR

Vinmec Research Institute of Stem Cell and Gene Technology

Locations

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Vinmec Research Institute of Stem Cell and Gene Technology

Hanoi, , Vietnam

Site Status

Countries

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Vietnam

References

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Liem NT, Chinh VD, Thinh NT, Minh ND, Duc HM. Improved Bowel Function in Patients with Spina Bifida After Bone Marrow-Derived Mononuclear Cell Transplantation: A Report of 2 Cases. Am J Case Rep. 2018 Aug 25;19:1010-1018. doi: 10.12659/AJCR.909801.

Reference Type RESULT
PMID: 30143601 (View on PubMed)

Aghayan HR, Arjmand B, Yaghoubi M, Moradi-Lakeh M, Kashani H, Shokraneh F. Clinical outcome of autologous mononuclear cells transplantation for spinal cord injury: a systematic review and meta-analysis. Med J Islam Repub Iran. 2014 Oct 14;28:112. eCollection 2014.

Reference Type RESULT
PMID: 25678991 (View on PubMed)

Than UTT, Nguyen LT, Nguyen PH, Nguyen XH, Trinh DP, Hoang DH, Nguyen PAT, Dang VD. Inflammatory mediators drive neuroinflammation in autism spectrum disorder and cerebral palsy. Sci Rep. 2023 Dec 18;13(1):22587. doi: 10.1038/s41598-023-49902-8.

Reference Type DERIVED
PMID: 38114596 (View on PubMed)

Nguyen LT, Le HT, Nguyen KT, Bui HT, Nguyen APT, Ngo DV, Hoang DM, Ngo MD. Outcomes of autologous bone marrow mononuclear cell administration in the treatment of neurologic sequelae in children with spina bifida. Stem Cell Res Ther. 2023 Apr 28;14(1):115. doi: 10.1186/s13287-023-03349-w.

Reference Type DERIVED
PMID: 37118832 (View on PubMed)

Other Identifiers

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CS. ĐT.19H1

Identifier Type: -

Identifier Source: org_study_id

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