Masitinib in the Treatment of Patients With Primary Progressive or Non-active Secondary Progressive Multiple Sclerosis

NCT ID: NCT05441488

Last Updated: 2025-09-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

800 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-06-28

Study Completion Date

2028-12-31

Brief Summary

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To evaluate the efficacy and safety of oral masitinib versus placebo in the treatment of patients with primary progressive or secondary progressive multiple sclerosis without relapse.

Detailed Description

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Masitinib is a selective tyrosine kinase inhibitor, targeting innate immune cells (mast cells and microglia) that are involved in the pathophysiology of progressive multiple sclerosis (MS). This is a multicenter, double-blind, randomized, placebo-controlled, comparative study of oral masitinib in the treatment of patients with progressive MS who were progressing but not clinically active.

Conditions

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Progressive Multiple Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Masitinib (4.5)

Participants receive masitinib (3.0 mg/kg/day), given orally twice daily, with a dose escalation to 4.5 mg/kg/day after 4 weeks of treatment. Each ascending dose titration is subjected to a safety control.

Group Type EXPERIMENTAL

Masitinib (4.5)

Intervention Type DRUG

Masitinib (titration to 4.5 mg/kg/day)

Placebo

Participants receive a matched dose placebo, given orally twice daily.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

treatment per os

Interventions

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Placebo

treatment per os

Intervention Type DRUG

Masitinib (4.5)

Masitinib (titration to 4.5 mg/kg/day)

Intervention Type DRUG

Other Intervention Names

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Placebo Oral Tablet AB1010

Eligibility Criteria

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Inclusion Criteria

* Patients with either primary progressive or secondary progressive multiple sclerosis with onset of symptoms at least five years before baseline and with no relapse diagnosed according to the 2017 revised McDonald's criteria at least two years before screening
* Patients with Expanded Disability Status Scale (EDSS) score between 3.0 to 6.0 (both inclusive) at screening and baseline
* Patients with an EDSS score progression ≥1 point with no improvement during 2 years
* Absence of T1 Gadolinium-enhancing brain lesions as measured by MRI at screening

Exclusion Criteria

* Patients suffering from a disease other than MS that would better explain the patient's neurological clinical signs and symptoms and/or MRI lesions observed at screening
* Inability to complete screening MRI (contraindications for MRI) and/or any known allergy or hypersensitivity or any contra-indication to gadolinium macrocyclic
* Patients treated with other disease modifying treatments in the time frames and conditions mentioned under previous treatment wash out period, assessed at baseline
* Patients with lymphocytes \<1.0 × 10\^9/L at screening and at baseline
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AB Science

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Patrick VERMERSCH, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

University of Lille, CHU of Lille, France

Locations

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Service de Neurologie Hôpital Henri-Mondor

Créteil, , France

Site Status

Hôpital Roger Salengro

Lille, , France

Site Status

Hôpital Pasteur - CHU de Nice

Nice, , France

Site Status

Centre Hospitalier Universitaire Nimes - Service de Neurologie

Nîmes, , France

Site Status

Centre hospitalier intercommunal de Poissy-Saint-Germain-en-Laye

Poissy, , France

Site Status

Le Centre hospitalier universitaire de Poitiers

Poitiers, , France

Site Status

Centre Hospitalier Universitaire de Rouen

Rouen, , France

Site Status

Centre Hospitalier Universitaire de Strasbourg

Strasbourg, , France

Site Status

Centre Hospitalier Universitaire Toulouse

Toulouse, , France

Site Status

Athens Naval Hospital

Athens, , Greece

Site Status

Eginition Hospital, Athens University Medical School

Athens, , Greece

Site Status

General University Hospital of Larissa

Larissa, , Greece

Site Status

AHEPA University Hospital, Aristotle University of Thessaloniki

Thessaloniki, , Greece

Site Status

Private Clinic ELPIS

Volos, , Greece

Site Status

Azienda Ospedaliero Universitaria Policlinico "G.Rodolico -San Marco"

Catania, , Italy

Site Status

Nzoz Neuro-Medic

Katowice, , Poland

Site Status

NOVI-MED

Ksawerów, , Poland

Site Status

Centrum Neurologii Krzysztof Selmaj

Lodz, , Poland

Site Status

NZOZ Neuro-Med

Lublin, , Poland

Site Status

Generała Jarosława Dąbrowskiego

Oświęcim, , Poland

Site Status

NZOZ Neuro-Kard

Poznan, , Poland

Site Status

Clinical Best Solutions

Warsaw, , Poland

Site Status

State Budgetary Institution of Health of the City of Moscow City Polyclinic #2

Moscow, , Russia

Site Status

Perm Regional Clinical Hospital

Perm, , Russia

Site Status

City Hospital No. 40 Kurortny District

Saint Petersburg, , Russia

Site Status

LLC "Center of socially significant diseases"

Saint Petersburg, , Russia

Site Status

Hospital del Mar

Barcelona, , Spain

Site Status

Hospital Universitario de Cruces

Bilbao, , Spain

Site Status

Gregorio Marañón General University Hospital

Madrid, , Spain

Site Status

Hospital Clínico San Carlos

Madrid, , Spain

Site Status

Hospital Universitario y Politécnico La Fe

Valencia, , Spain

Site Status

Sahlgrenska University Hospital

Gothenburg, , Sweden

Site Status

Centrum för neurologi

Stockholm, , Sweden

Site Status

Lviv Regional Clinical Hospital

Lviv, , Ukraine

Site Status

Rivne Regional Specialized Dispensary for Radiation Protection of the Population Municipal Enterprise

Rivne, , Ukraine

Site Status

Communal Non-Profit Enterprise "Ternopil Regional Clinical Psychoneurological Hospital" of Ternopil Regional Council, Department of Neurology #1

Ternopil, , Ukraine

Site Status

Salutem Medical Center

Vinnytsia, , Ukraine

Site Status

Countries

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France Greece Italy Poland Russia Spain Sweden Ukraine

References

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Vermersch P, Brieva-Ruiz L, Fox RJ, Paul F, Ramio-Torrenta L, Schwab M, Moussy A, Mansfield C, Hermine O, Maciejowski M; AB07002 Study Group. Efficacy and Safety of Masitinib in Progressive Forms of Multiple Sclerosis: A Randomized, Phase 3, Clinical Trial. Neurol Neuroimmunol Neuroinflamm. 2022 Feb 21;9(3):e1148. doi: 10.1212/NXI.0000000000001148. Print 2022 May.

Reference Type BACKGROUND
PMID: 35190477 (View on PubMed)

Vermersch P, Benrabah R, Schmidt N, Zephir H, Clavelou P, Vongsouthi C, Dubreuil P, Moussy A, Hermine O. Masitinib treatment in patients with progressive multiple sclerosis: a randomized pilot study. BMC Neurol. 2012 Jun 12;12:36. doi: 10.1186/1471-2377-12-36.

Reference Type BACKGROUND
PMID: 22691628 (View on PubMed)

Latham BD, Oskin DS, Crouch RD, Vergne MJ, Jackson KD. Cytochromes P450 2C8 and 3A Catalyze the Metabolic Activation of the Tyrosine Kinase Inhibitor Masitinib. Chem Res Toxicol. 2022 Sep 19;35(9):1467-1481. doi: 10.1021/acs.chemrestox.2c00057. Epub 2022 Sep 1.

Reference Type DERIVED
PMID: 36048877 (View on PubMed)

Other Identifiers

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AB20009; MAXIMS

Identifier Type: -

Identifier Source: org_study_id

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