Study of Nab-Paclitaxel and Gemcitabine With or Without SBP-101 in Pancreatic Cancer

NCT ID: NCT05254171

Last Updated: 2024-11-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2/PHASE3

Total Enrollment

600 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-08-08

Study Completion Date

2027-01-01

Brief Summary

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The study is a randomized, double-blind, placebo-controlled, multicenter study of standard treatment with nab-paclitaxel and gemcitabine with or without SBP-101 in subjects previously untreated for metastatic pancreatic ductal adenocarcinoma (PDA), including subjects who have received prior neoadjuvant or adjuvant treatment.

Detailed Description

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This trial will enroll approximately 600 patients to evaluate the effect of SBP-101 on Overall Survival when administered with gemcitabine and nab-paclitaxel compared to gemcitabine and nab-paclitaxel and a placebo. Secondary endpoints include Progression-free survival, radiologic responses to treatment, and Quality of Life measures. An independent, external Data Safety Monitoring Board (DSMB) will monitor safety and efficacy and a planned futility analysis.

Conditions

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Pancreatic Cancer Metastatic Pancreatic Ductal Adenocarcinoma Pancreatic Cancer Stage IV

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

1:1 randomization to Experimental Arm vs. Control Arm
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Experimental Arm

SBP-101 + Nab-paclitaxel and Gemcitabine

Group Type EXPERIMENTAL

SBP-101

Intervention Type DRUG

small molecule polyamine metabolic inhibitor for subcutaneous injection

Nab-paclitaxel

Intervention Type DRUG

paclitaxel protein-bound particles for injectable suspension

Gemcitabine

Intervention Type DRUG

gemcitabine for injection

Control Arm

Placebo + Nab-Paclitaxel and Gemcitabine

Group Type PLACEBO_COMPARATOR

Nab-paclitaxel

Intervention Type DRUG

paclitaxel protein-bound particles for injectable suspension

Gemcitabine

Intervention Type DRUG

gemcitabine for injection

Placebo

Intervention Type OTHER

Normal Saline

Interventions

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SBP-101

small molecule polyamine metabolic inhibitor for subcutaneous injection

Intervention Type DRUG

Nab-paclitaxel

paclitaxel protein-bound particles for injectable suspension

Intervention Type DRUG

Gemcitabine

gemcitabine for injection

Intervention Type DRUG

Placebo

Normal Saline

Intervention Type OTHER

Other Intervention Names

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ivospemin Abraxane Gemzar

Eligibility Criteria

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Inclusion Criteria

* Histologically or cytologically confirmed metastatic pancreatic ductal adenocarcinoma.
* Is previously untreated for metastatic pancreatic ductal adenocarcinoma; metastatic disease must have been diagnosed within the past 3 months; and subject is expected to receive standard treatment with gemcitabine and nab-paclitaxel. Subjects who have had planned or prior surgery, such as a Whipple procedure, with or without neo-adjuvant/or adjuvant chemotherapy may be included.
* Life expectancy ≥ 3 months.
* Measurable disease on computed tomography (CT) or magnetic resonance imaging (MRI) scan by RECIST v1.1 criteria.
* Eastern Cooperative Oncology Group (ECOG) Performance Status 0-1.
* Adult, age ≥ 18 years, male or female.
* Females of child-bearing potential must have a negative serum pregnancy test within 14 days prior to start of study treatment and must use an adequate method of contraception from 2 weeks before the first administration of SBP-101 until 6 months after the last administration of study drug (i.e., last dose of any of the three drugs in the regimen). Female subjects are considered to be of childbearing potential unless they are postmenopausal (at least 12 months of consecutive amenorrhea, without other known or suspected cause) and over 55 years old or have been sterilized surgically (i.e., bilateral tubal ligation, hysterectomy, or bilateral oophorectomy, all with surgery at least one month before dosing).
* Adequate bone marrow, hepatic and renal function as outlined in protocol.
* QTc interval ≤ 470 ms (for women) and ≤ 450 ms (for men) on the ECG at baseline calculated by either the Fridericia or Framingham formula.
* Willing and able to provide written informed consent: voluntary agreement to participate in the study following disclosure of risks and procedures required.

Exclusion Criteria

* When results of germline or somatic testing done prior to screening are known, subjects known to have mutations of the BRCA 1/2 (Breast Cancer gene) are excluded.
* Concomitant metformin administration. Diabetic subjects on treatment with metformin, or any other derivative thereof, must discontinue it at least 5 days prior to C1D1 and not take metformin while on study (other diabetic medications are allowed).
* Any history of retinopathy or at risk for retinal detachment (personal or family history of retinal detachment, extreme myopia \[-6.0 diopters or approximately 20/500\], eye surgery \<6 months prior to C1D1, or history of a severe eye injury. Subjects with findings of retinopathy on baseline ophthalmology exams will be excluded.
* Evidence of severe or uncontrolled systemic disease or any concurrent condition that, in the opinion of the Investigator or Medical Monitor, makes it undesirable for the subject to participate in the study or that would jeopardize compliance with the protocol. Subjects with pre-existing well-controlled diabetes are not excluded.
* Medical or psychiatric conditions that compromise the subject's ability to give informed consent or to complete the protocol or a history of non-compliance.
* Presence of islet-cell or pancreatic neuroendocrine tumor or mixed adenocarcinoma-neuroendocrine carcinoma.
* Symptomatic central nervous system (CNS) malignancy or metastasis. Screening of asymptomatic subjects without history of CNS metastases is not required.
* Serum albumin \< 30 g/L (3.0 g/dL).
* Deep vein thrombosis (DVT) or portal vein occlusion, pulmonary embolism (PE), or other thromboembolic event that occurs during screening.
* Presence of known active bacterial, fungal, or viral infection requiring systemic therapy.
* Known active infection with human immunodeficiency virus (HIV), hepatitis B or C.
* Presence of interstitial lung disease, pulmonary fibrosis, or pulmonary hypersensitivity reaction.
* Myocardial infarction within the last 12 months, severe/unstable angina, symptomatic congestive heart failure New York Heart Association (NYHA) class III or IV.
* Pregnant or lactating.
* Major surgery within 4 weeks prior to the start of study drug treatment, without complete recovery.
* Known hypersensitivity to any component of study treatments.
* Participation in any other clinical investigation within 4 weeks of receiving the first dose of study drug.
* Any history of hydroxychloroquine use (Plaquenil® and other brand names).
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Panbela Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Michael J Walker, MD

Role: STUDY_DIRECTOR

Panbela Therapeutics, Inc.

Locations

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Genesis Cancer and Blood Institute (SCRI)

Hot Springs, Arkansas, United States

Site Status WITHDRAWN

Providence Medical Foundation

Fullerton, California, United States

Site Status RECRUITING

Yale Cancer Center

New Haven, Connecticut, United States

Site Status RECRUITING

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status ACTIVE_NOT_RECRUITING

Henry Ford Health System

Detroit, Michigan, United States

Site Status RECRUITING

CentraCare Health

Saint Cloud, Minnesota, United States

Site Status WITHDRAWN

Columbia University Medical Center

New York, New York, United States

Site Status RECRUITING

University of Rochester

Rochester, New York, United States

Site Status RECRUITING

Mark H Zangmeister Center - SCRI - PPDS

Columbus, Ohio, United States

Site Status TERMINATED

Tennessee Oncology NASH - SCRI - PPDS

Nashville, Tennessee, United States

Site Status ACTIVE_NOT_RECRUITING

HOPE Cancer Center of East Texas

Tyler, Texas, United States

Site Status RECRUITING

Medical Oncology Associates - Spokane

Spokane, Washington, United States

Site Status RECRUITING

MultiCare Regional Cancer Center - Tacoma

Tacoma, Washington, United States

Site Status RECRUITING

Froedtert Hospital & the Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status RECRUITING

Canberra Region Cancer Centre

Garran, Australia Capital Territory, Australia

Site Status RECRUITING

The Tweed Hospital

Tweed Heads, New South Wales, Australia

Site Status WITHDRAWN

Ashford Cancer Centre Research

Kurralta Park, South Australia, Australia

Site Status RECRUITING

Austin Hospital

Heidelberg, Victoria, Australia

Site Status RECRUITING

St John of God Murdoch Hospital

Murdoch, Western Australia, Australia

Site Status RECRUITING

Klinikum Klagenfurt Am Woerthersee

Klagenfurt, Carinthia, Austria

Site Status RECRUITING

Universitätsklinikum St. Pölten

Sankt Pölten, Lower Austria, Austria

Site Status RECRUITING

Ordensklinikum Linz, Krankenhaus der Barmherzigen Schwestern Linz Betriebsgesellschaft m.b.H

Linz, Upper Austria, Austria

Site Status NOT_YET_RECRUITING

Pyhrn-Eisenwurzen Klinikum Steyr

Steyr, Upper Austria, Austria

Site Status WITHDRAWN

Klinikum Wels-Grieskirchen GmbH

Wels, Upper Austria, Austria

Site Status RECRUITING

Landeskrankenhaus Feldkirch

Rankweil, Vorarlberg, Austria

Site Status RECRUITING

Kepler Universitätsklinikum Linz

Linz, , Austria

Site Status RECRUITING

Salzburg Cancer Research Institute

Salzburg, , Austria

Site Status ACTIVE_NOT_RECRUITING

A.ö. Krankenhaus der Barmherzigen Brüder

Wein, , Austria

Site Status RECRUITING

Landesklinikum Wiener Neustadt

Wiener Neustadt, , Austria

Site Status RECRUITING

Imelda VZW

Bonheiden, Antwerpen, Belgium

Site Status RECRUITING

Cliniques Universitaires Saint-Luc

Brussels, Belgique, Belgium

Site Status NOT_YET_RECRUITING

Hôpital de Jolimont

La Louvière, Hainaut, Belgium

Site Status RECRUITING

Centre Hospitalier de l'Ardenne

Libramont, Luxembourg, Belgium

Site Status RECRUITING

CHU UCL Namur asbl - Site Godinne

Yvoir, Namur, Belgium

Site Status RECRUITING

Onze-Lieve-Vrouwziekenhuis

Aalst, Oost-Vlaanderen, Belgium

Site Status RECRUITING

UZ Gent

Ghent, Oost-Vlaanderen, Belgium

Site Status RECRUITING

AZ Groeninge

Kortrijk, West-Vlaanderen, Belgium

Site Status RECRUITING

Grand Hopital de Charleroi asbl

Charleroi, , Belgium

Site Status RECRUITING

UZ Leuven

Leuven, , Belgium

Site Status RECRUITING

CHU de Liège

Liège, , Belgium

Site Status RECRUITING

Hopitaux de La Timone

Marseille, Bouches-du-Rhône, France

Site Status RECRUITING

Centre François Baclesse

Caen, Calvados, France

Site Status RECRUITING

Hopital Jean Minjoz

Besançon, Doubs, France

Site Status RECRUITING

Hôpital de Rangueil

Toulouse, Haute-Garonne, France

Site Status RECRUITING

EDOG - Centre Eugene Marquis Centre Regional de Lutte Contre Le Cancer - PPDS

Rennes, Ille-et-Vilaine, France

Site Status RECRUITING

Universitätsklinikum Carl Gustav Carus an der TU Dresden

Dresden, Saxony, Germany

Site Status NOT_YET_RECRUITING

Charité - Universitätsmedizin Berlin

Berlin, , Germany

Site Status RECRUITING

Asklepios Klinik Altona

Hamburg, , Germany

Site Status ACTIVE_NOT_RECRUITING

Universitätsklinikum Tübingen

Tübingen, , Germany

Site Status RECRUITING

Klinikum Weiden

Weiden, , Germany

Site Status ACTIVE_NOT_RECRUITING

Ospedale Casa Sollievo Della Sofferenza IRCCS

San Giovanni Rotondo, Apulia, Italy

Site Status RECRUITING

Istituto Romagnolo per lo Studio dei Tumori "Dino Amadori" - IRST S.r.l - PPDS

Meldola, Emilia-Romagna, Italy

Site Status RECRUITING

Azienda Unita Sanita Locale di Reggio Emilia IRCCS

Reggio Emilia, Emilia-Romagna, Italy

Site Status RECRUITING

Ospedale San Raffaele S.r.l. - PPDS

Milan, Lombardy, Italy

Site Status RECRUITING

Instituto Europeo Di Oncologia

Milan, Lombardy, Italy

Site Status RECRUITING

Ospedale degli Infermi

Candiolo, Piedmont, Italy

Site Status COMPLETED

Azienda Ospedaliero Universitaria Pisana

Pisa, Tuscany, Italy

Site Status RECRUITING

Ospedale Santa Maria Della Misericordia Di Perugia

Terni, Umbria, Italy

Site Status RECRUITING

Azienda Ospedaliera Universitaria Integrata Di Verona

Verona, Venito, Italy

Site Status RECRUITING

Fondazione IRCCS Policlinico San Matteo di Pavia-Vialle Camillo Golgi 19

Pavia, , Italy

Site Status RECRUITING

National Cancer Center

Seoul, Gyeonggido, South Korea

Site Status RECRUITING

CHA Bundang Medical Center, CHA University

Seoul, Gyeonggido, South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Severance Hospital Yonsei University Health System - PPDS

Seoul, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Chonnam National University Hwasun Hospital

Hwasun, , South Korea

Site Status RECRUITING

Asan Medical Center - PPDS

Seoul, , South Korea

Site Status RECRUITING

Hospital Universitario Germans Trias i Pujol

Badalona, Barcelona, Spain

Site Status RECRUITING

Hospital Universitario Marques de Valdecilla

Santander, Cantabria, Spain

Site Status RECRUITING

Hospital Universitario de Jaen

Jaén, Jaen, Spain

Site Status RECRUITING

Hospital de La Santa Creu i Sant Pau

Barcelona, Madrid, Spain

Site Status RECRUITING

Hospital Universitario HM Sanchinarro - CIOCC

Madrid, Madrid, Communidad Delaware, Spain

Site Status RECRUITING

Hospital Universitario Virgen de La Arrixaca

El Palmar, Murcia, Spain

Site Status RECRUITING

Clinica Universidad Navarra

Pamplona, Navarre, Spain

Site Status RECRUITING

Hospital Universitario de Navarra

Pamplona, Navarre, Spain

Site Status RECRUITING

Hospital Universitario Cruces

Barakaldo, Vizcaya, Spain

Site Status RECRUITING

Hospital Universitario A Coruña

A Coruña, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario de Badajoz

Badajoz, , Spain

Site Status RECRUITING

Hospital Universitario Vall d'Hebron - PPDS

Barcelona, , Spain

Site Status RECRUITING

ICO l'Hospitalet - Hospital Duran i Reynals

Barcelona, , Spain

Site Status RECRUITING

Institut Catala d'Oncologia Girona

Girona, , Spain

Site Status RECRUITING

Hospital General Universitario Gregorio Marañon

Madrid, , Spain

Site Status RECRUITING

MD Anderson Cancer Center Madrid - España

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz - PPDS

Madrid, , Spain

Site Status RECRUITING

Hospital Regional Universitario de Malaga - Hospital General

Málaga, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocio - PPDS

Seville, , Spain

Site Status RECRUITING

Hospital Universitario Virgen Macarena

Seville, , Spain

Site Status RECRUITING

Aberdeen Royal Infirmary - PPDS

Aberdeen, Aberdeen City, United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Hammersmith Hospital

London, City of London, United Kingdom

Site Status RECRUITING

Derriford Hospital

Plympton, Devon, United Kingdom

Site Status RECRUITING

Countries

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United States Australia Austria Belgium France Germany Italy South Korea Spain United Kingdom

Central Contacts

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Rachel Bragg, MPH

Role: CONTACT

952-479-1196

Tammy Groene

Role: CONTACT

952-479-1196

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Jagruti Khandhadia

Role: primary

714-446-5900 ext. 2277

Jill Lacy, MD

Role: primary

203-737-1600

Philip Philip, MD

Role: primary

313-576-8728

Navigator Office Nurse

Role: primary

212-342-5162

Chris LeFeber

Role: primary

585-275-0407

Grace Loredo

Role: primary

903-592-6152 ext. 286

Monika Chaudhry, PhD

Role: primary

509-462-2273 ext. 418

Samantha Blake

Role: primary

253-572-7320

Medical College of Wisconsin Cancer Center Clinical Trials Office

Role: primary

414-805-8900

Mandana Kamgar, Study Principle Investigator

Role: backup

Ankit Jain, MBBS

Role: primary

+61266565733

Sue Yeend

Role: primary

+61882922204

Niall Tebbutt

Role: primary

+61394965763

Rebecca Weselman

Role: primary

+61894389599

Wolfgang Eisterer, MD

Role: primary

+4346353834603

Petra Pichler, MD

Role: primary

+43274290042142

Angela Plasser

Role: primary

+4373276774319

Birgit Reisinger-Eisenrauch

Role: primary

+4372424153452

Thomas Winder, PhD

Role: primary

+4355223032300

Isabella Rauscher

Role: primary

+4357680836204

Johannes Meran, MD

Role: primary

+431211212105

Klaus Loidolt

Role: primary

+432622900423511

Doreen Iwens

Role: primary

+3215504710

Tuon Le

Role: primary

+3227644213

Alexandre Dermine

Role: primary

+3264231804

Celine Lewis

Role: primary

+3263552197

Géraldine Mineur

Role: primary

+3281423853

Esther Dujardin

Role: primary

+3253728716

Tine Derre

Role: primary

+3293325125

Fien Verplancke

Role: primary

+3256633338

Matthias Papier

Role: primary

+3271104767

Ramy Slimane

Role: primary

+3216338670

Joelle Collignon, MD

Role: primary

+3243667801

Laetitia Dahan, MD

Role: primary

+33491386023

Natacha Duval

Role: primary

+33231455050

Angélique Vienot, MD

Role: primary

+33381479999

Rosine Guimbaud, MD, PhD

Role: primary

+33561322142

Samuel Le Sourd, MD

Role: primary

+33299253089

Gunnar Folprecht, MD

Role: primary

+493514584794

Uwe Pelzer, MD, PhD

Role: primary

+4930450553844

Pavlos Missios, MD

Role: primary

+4970712984457

Evaristo Maiello, MD

Role: primary

+390882410640

Giovanni Luca Frassineti, MD

Role: primary

+390543739100

Michele Panebianco, MD

Role: primary

+390522296858

Michele Reni, MD

Role: primary

+390226437644

Chiara Alessandra Cella, MD

Role: primary

+390257489258

Caterina Vivaldi, MD

Role: primary

+39050992455

Fausto Riola, MD

Role: primary

+390755784211

Davide Melisi, MD, PhD

Role: primary

+390458128120

Anna Pagani

Role: primary

+390382501671

Woo Jin Lee, MD

Role: primary

+82319201612

Hong Jae Chon, MD

Role: primary

+82317803453

Do-Youn Oh, MD

Role: primary

+82220720701

Hye Jin Choi, MD, PhD

Role: primary

+82222288133

Jun Eul Hwang, MD

Role: primary

+82613797622

Baek-yeol Ryoo, MD, PhD

Role: primary

+82230103211

Laura Layos, MD

Role: primary

+34934978925

Fernando Rivera Herrero Sr., MD, PhD

Role: primary

+34942202525

Natalia Luque Caro, MD

Role: primary

+34953220306

Paula Cerda Serda, MD

Role: primary

+34935565638

Antonio Cubillo Gracián, MD

Role: primary

+34917567850

Miguel Marin Vera, MD

Role: primary

+34968369516

Mariano Ponz-Sarvisé, MD, PhD

Role: primary

+34948255400

Ruth Vera Garcia, MD

Role: primary

+34848422576

Alberto Muñoz Llarena, MD

Role: primary

+34946006399

Veronica Serrano Pecos, MD

Role: primary

+34924218040

Teresa Macarulla Mercade, MD

Role: primary

+34934894301

Berta Laquente Sáez, MD

Role: primary

+34932607744

Adelaida García-Velasco, MD, PhD

Role: primary

+34972225828

Andres Muñoz Martin, MD, PhD

Role: primary

+34914269394

Jose Ignacio Martin Valades

Role: primary

+348888888888

Carmen Guillen Ponce, MD

Role: primary

+34913368835

Angela Lamarca

Role: primary

+34915504800 ext. 2299

Angela Lamarca Lete, MD

Role: primary

+34915504800 ext. 2299

Rocio Garcia Carbonero, PhD

Role: primary

+34913908923

Jaime Feliu, MD

Role: primary

+34917277516

Sabrina López

Role: primary

+34951308129

Esperanza Muñoz

Role: primary

Rosario Carrillo, MD

Role: primary

+34955926578

Rowan Dulson

Role: primary

Derriford Hospital University Hospitals Plymouth

Role: primary

Other Identifiers

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CL-SBP-101-04

Identifier Type: -

Identifier Source: org_study_id

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