Masitinib in Combination With Gemcitabine for Treatment of Patients With Advanced/Metastatic Pancreatic Cancer

NCT ID: NCT00789633

Last Updated: 2018-12-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

353 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-11-25

Study Completion Date

2012-08-31

Brief Summary

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The objective of this study is to compare the efficacy and safety of masitinib in combination with gemcitabine to placebo in combination with gemcitabine in patients with advanced/metastatic pancreatic cancer.

Detailed Description

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Human pancreatic cancer overexpresses a number of important tyrosine kinase (TK) growth factors receptors and ligands, including expression of both PDGF and PDGF receptors. Drugs that can selectively inhibit TKs are likely to be of benefit in pancreatic cancer. Masitinib is a TK inhibitor, selectively and effectively inhibiting c-Kit (mast cell growth factor receptor), PDGF receptor, FGF receptor and to a lower extent the FAK kinases. Pre-clinical and clinical studies have shown that masitinib can reverse resistance of pancreatic tumor cell lines to gemcitabine. Based on pre-clinical and phase 2 clinical studies, masitinib can be considered as a good candidate to use in combination with gemcitabine in the treatment of pancreatic cancer.

Conditions

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Pancreatic Cancer

Keywords

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Pancreatic cancer Advanced pancreatic cancer Metastatic pancreatic cancer Gemcitabine Chemo-naive

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Masitinib & gemcitabine

Participants receive masitinib (9 mg/kg/day), given orally twice daily, plus gemcitabine at 1000mg/m2 by intravenous infusion during 30 minutes, once every 7 days, for up to 7 weeks, followed by a week of rest. Subsequent cycles should consist of an IV infusion, once every 7 days, for 3 consecutive weeks out of every 4 weeks, until disease progression, death, limiting toxicity or patient consent withdrawal.

Group Type EXPERIMENTAL

Masitinib

Intervention Type DRUG

Masitinib at 9 mg/kg/day given orally twice daily

Gemcitabine

Intervention Type DRUG

Gemcitabine at 1000 mg/m2 by intravenous infusion

Placebo & gemcitabine

Participants receive matching placebo, given orally twice daily, plus gemcitabine at 1000mg/m2 by intravenous infusion during 30 minutes, once every 7 days, for up to 7 weeks, followed by a week of rest. Subsequent cycles should consist of an IV infusion, once every 7 days, for 3 consecutive weeks out of every 4 weeks, until disease progression, death, limiting toxicity or patient consent withdrawal.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo given orally twice daily

Gemcitabine

Intervention Type DRUG

Gemcitabine at 1000 mg/m2 by intravenous infusion

Interventions

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Masitinib

Masitinib at 9 mg/kg/day given orally twice daily

Intervention Type DRUG

Placebo

Matching placebo given orally twice daily

Intervention Type DRUG

Gemcitabine

Gemcitabine at 1000 mg/m2 by intravenous infusion

Intervention Type DRUG

Other Intervention Names

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AB1010 Gemzar

Eligibility Criteria

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Inclusion Criteria

1. Histologically or cytologically confirmed adenocarcinoma of the pancreas
2. Chemo naïve patients with advanced/metastatic disease
3. Documented decision justifying non eligibility for surgical resection. The documentation of the non eligibility for surgical resection will be reviewed by an independent committee.
4. Men and women, age \>18 years
5. Men and women of childbearing potential (entering the study after a confirmed menstrual period and who have a negative pregnancy test), must agree to use two methods (one for the patient and one for the partner) of medically acceptable forms of contraception during the study and for 3 months after the last treatment intake.
6. Patient should be able and willing to comply with study visits and procedures as per protocol.
7. Patient should understand, sign, and date the written voluntary informed consent form at the screening visit prior to any protocol-specific procedures performed.

Exclusion Criteria

1. Patient treated for a cancer other than pancreatic cancer within 5 years before enrollment, with the exception of basal cell carcinoma or in situ cervical cancer
2. Any condition that the physician judges could be detrimental to subjects participating in this study; including any clinically important deviations from normal clinical laboratory values or concurrent medical events Previous treatment
3. Any anti-tumor therapy (any chemotherapy, radiotherapy, immunotherapy, biologic or hormonal therapy) within 6 months prior to baseline
4. Treatment with any investigational agent within 4 weeks prior to baseline
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AB Science

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gaël Deplanque, MD

Role: PRINCIPAL_INVESTIGATOR

Hôpital Saint Joseph, Paris, France

Locations

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Eastern Connecticut Hematology and Oncology (ECHO)

Norwich, Connecticut, United States

Site Status

MD Anderson

Orlando, Florida, United States

Site Status

The Emory Clinic

Atlanta, Georgia, United States

Site Status

Decatur Memorial Hospital

Decatur, Illinois, United States

Site Status

Medical & Surgical Specialists

Galesburg, Illinois, United States

Site Status

Berkshire Hematology Oncology

Pittsfield, Massachusetts, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

Metro MN CCOP

Saint Louis Park, Minnesota, United States

Site Status

Saint Luke's Cancer Institute

Kansas City, Missouri, United States

Site Status

The Valley Hospital

Paramus, New Jersey, United States

Site Status

Southeastern Medical Oncology Center

Goldsboro, North Carolina, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

Teaching Hospital Brno-Bohunice

Brno, , Czechia

Site Status

Hospital Chomutov

Chomutov, , Czechia

Site Status

Oncology Surgery

Kutná Hora, , Czechia

Site Status

Department of Oncology Teaching Hospital Olomouc

Olomouc, , Czechia

Site Status

Teaching Hospital Královské

Prague, , Czechia

Site Status

Teaching Hospital Na Bulovce

Prague, , Czechia

Site Status

Hospital na Homolce

Prague, , Czechia

Site Status

CHU Amiens

Amiens, , France

Site Status

Hôpital Privé d'Antony

Antony, , France

Site Status

Institut Sainte-Catherine

Avignon, , France

Site Status

Hôpital Jean Minjoz

Besançon, , France

Site Status

Hôpital Saint-André

Bordeaux, , France

Site Status

CHU de la Cavale Blanche

Brest, , France

Site Status

CHU de Caen

Caen, , France

Site Status

CHU Hôtel Dieu

Clermont-Ferrand, , France

Site Status

Groupement Hospitalier Universitaire Nord - Beaujon

Clichy, , France

Site Status

CHU Henri Mondor

Créteil, , France

Site Status

CHU Henri Mondor

Créteil, , France

Site Status

Hôpital Victor Jousselin

Dreux, , France

Site Status

Centre Gastro-Loire

Gien, , France

Site Status

Institut Daniel Hollard

Grenoble, , France

Site Status

CHD Les Oudairies

La Roche-sur-Yon, , France

Site Status

Hôpital André Mignot

Le Chesnay, , France

Site Status

Hôpital Robert Boulin

Libourne, , France

Site Status

Hôpital Claude Huriez

Lille, , France

Site Status

Centre Hospitalier de Longjumeau

Longjumeau, , France

Site Status

Hôpital Privé Jean Mermoz

Lyon, , France

Site Status

Hôpital Edouard Herriot

Lyon, , France

Site Status

Centre Léon Bérard

Lyon, , France

Site Status

Assistance Publique des Hôpitaux de Marseille

Marseille, , France

Site Status

Hôpital Saint Joseph

Marseille, , France

Site Status

Centre Hospitalier Belfort - Montbéliard

Montbéliard, , France

Site Status

CHU Hôtel Dieu

Nantes, , France

Site Status

Centre Catherine de Sienne

Nantes, , France

Site Status

Hôpital de la Source

Orléans, , France

Site Status

Groupe Hospitalier Diaconesse Croix Saint Simon

Paris, , France

Site Status

Hôpital Tenon

Paris, , France

Site Status

Hôpital Hôtel Dieu

Paris, , France

Site Status

Hôpital Saint-Joseph

Paris, , France

Site Status

Hôpital Haut-Lévêque

Pessac, , France

Site Status

Polyclinique Francheville

Périgueux, , France

Site Status

Hôpital Hautepierre

Strasbourg, , France

Site Status

CHU Brabois

Vandœuvre-lès-Nancy, , France

Site Status

Hôpital Paul Brousse

Villejuif, , France

Site Status

Hotel Dieu de France

Beirut, , Lebanon

Site Status

Makassed General Hospital Tarik Jadide

Beirut, , Lebanon

Site Status

Rafik Hariri University Hospital

Beirut, , Lebanon

Site Status

Saint Georges Hospital UMC

Beirut, , Lebanon

Site Status

Middle East Institute of Health- Bsaleem

Metn, , Lebanon

Site Status

Saint Joseph Hospital Baouchrieh

Metn, , Lebanon

Site Status

Hammoud Hospital University Medical Center

Saida, , Lebanon

Site Status

Municipal Clinical Hospital

Arad, , Romania

Site Status

County Hospital

Baia Mare, , Romania

Site Status

Emergency Clinical Hospital

Constanța, , Romania

Site Status

Pelica Impex SRL Hospital

Pelica Impex, , Romania

Site Status

County Hospital

Satu Mare, , Romania

Site Status

Countries

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United States Czechia France Lebanon Romania

References

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Deplanque G, Demarchi M, Hebbar M, Flynn P, Melichar B, Atkins J, Nowara E, Moye L, Piquemal D, Ritter D, Dubreuil P, Mansfield CD, Acin Y, Moussy A, Hermine O, Hammel P. A randomized, placebo-controlled phase III trial of masitinib plus gemcitabine in the treatment of advanced pancreatic cancer. Ann Oncol. 2015 Jun;26(6):1194-1200. doi: 10.1093/annonc/mdv133. Epub 2015 Apr 9.

Reference Type RESULT
PMID: 25858497 (View on PubMed)

Related Links

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Other Identifiers

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AB07012

Identifier Type: -

Identifier Source: org_study_id