A Safety, Tolerability and Efficacy Study of Veligrotug (VRDN 001) in Healthy Volunteers and Participants With Thyroid Eye Disease (TED) ( THRIVE )

NCT ID: NCT05176639

Last Updated: 2025-07-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

113 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-12-03

Study Completion Date

2025-03-27

Brief Summary

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The investigational drug, veligrotug (VRDN-001), is a monoclonal antibody that inhibits the activity of a cell surface receptor called insulin-like growth factor-1 receptor (IGF-1R). Inhibition of IGF-1R may help to reduce the inflammation and associated tissue swelling that occurs in patients with thyroid eye disease (TED). The primary objective of this clinical trial is to establish the safety, tolerability, and efficacy of veligrotug, and the pharmacokinetic (PK) and pharmacodynamic (PD) profiles of veligrotug in active TED patients who received 10 mg/kg.

Detailed Description

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Conditions

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Thyroid Eye Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Phase 3 Cohort (THRIVE) veligrotug (VRDN-001)

Participants with TED will be randomized to either veligrotug (VRDN-001) 10mg/kg or placebo.

Group Type EXPERIMENTAL

VRDN-001 Phase 3 Cohort (THRIVE)

Intervention Type DRUG

5 IV Infusions of veligrotug (VRDN-001) 10mg/kg

Phase 3 Cohort (THRIVE) VRDN-001 Placebo

Participants with TED will be randomized to either veligrotug (VRDN-001) 10mg/kg or placebo.

Group Type PLACEBO_COMPARATOR

VRDN-001 Placebo

Intervention Type DRUG

5 IV Infusions of veligrotug (VRDN-001) placebo

Interventions

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VRDN-001 Phase 3 Cohort (THRIVE)

5 IV Infusions of veligrotug (VRDN-001) 10mg/kg

Intervention Type DRUG

VRDN-001 Placebo

5 IV Infusions of veligrotug (VRDN-001) placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Must have moderate to severe active TED with documented evidence of ocular symptoms or signs that began within 15 months prior to screening
* Must have Clinical Activity Score (CAS) of ≥ 3 on the 7-item scale for the study eye
* Must agree to use highly effective contraception as specified in the protocol
* Female TED participants must have a negative serum pregnancy test at screening

Exclusion Criteria

* Must not have received prior treatment with another anti-IGF-1R therapy or any investigational agent for TED
* Must not have used systemic corticosteroids or selenium within 2 weeks prior to Day 1
* Must not have received rituximab, tocilizumab or other immunosuppressive agents or any other therapy for TED within 8 weeks prior to Day 1
* Must not have received an investigational agent for any condition with 8 weeks prior to Day 1
* Must not have a pre-existing ophthalmic condition in the study eye that in the opinion of the Investigator would confound interpretation of the study results
* Must not have had previous orbital irradiation or surgery for TED in the study eye
* Must not have a history of inflammatory bowel disease
* Must not have a history of or screening audiometry assessment of clinically significant (as determined by investigator) ear pathology, relevant ear surgery, or hearing loss
* Female TED participants must not be pregnant or lactating

Note: Prior thyroidectomy, radioactive iodine (RAI) treatment, or orbital decompression surgery limited to bone only are NOT exclusions.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Viridian Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Colorado - Department of Ophthalmology

Aurora, California, United States

Site Status

The Private Office of Raymond Douglas

Beverly Hills, California, United States

Site Status

USC Roski Eye Institute

Los Angeles, California, United States

Site Status

MACRO Trials, Inc.

Los Angeles, California, United States

Site Status

Amy Patel Jain, MD

Newport Beach, California, United States

Site Status

Byers Eye Institute/Stanford University

Palo Alto, California, United States

Site Status

Senta Clinic

San Diego, California, United States

Site Status

University of California, San Francisco

San Francisco, California, United States

Site Status

University of Colorado

Aurora, Colorado, United States

Site Status

Sina Medical Center

Homestead, Florida, United States

Site Status

Med-Care Research Inc.

Miami, Florida, United States

Site Status

Edward Jenner Research Group Center LLC

Plantation, Florida, United States

Site Status

Sarasota Retina Institue

Sarasota, Florida, United States

Site Status

Vision Medical Research Inc.

Orland Park, Illinois, United States

Site Status

University Health Diabetes, Endocrinology & Nephrology Center

Kansas City, Kansas, United States

Site Status

KU Medical Center, University of Kansas

Kansas City, Kansas, United States

Site Status

Massachusetts Eye and Ear

Boston, Massachusetts, United States

Site Status

Ophthalmic Consultants of Boston

Weymouth, Massachusetts, United States

Site Status

Fraser Eye Care Center

Fraser, Michigan, United States

Site Status

Kahana Oculoplastic & Orbital Surgery

Livonia, Michigan, United States

Site Status

University of Minnesota, Department of Ophthalmology and Visual Neurosciences

Minneapolis, Minnesota, United States

Site Status

Advanced Research International, LLC

Las Vegas, Nevada, United States

Site Status

Rutgers-New Jersey Medical School-Newark

Newark, New Jersey, United States

Site Status

New York Eye Ear Infirmary of Mount Sinai

New York, New York, United States

Site Status

Baylor College of Medicine (BCM)-Opthalmology

Houston, Texas, United States

Site Status

Neuro-Eye Clinical Trials

Houston, Texas, United States

Site Status

Neuro-Ophthalmology of Texas PLLC

Houston, Texas, United States

Site Status

University of Vermont Medical Center

Burlington, Vermont, United States

Site Status

West Virgina University Eye Insitute

Morgantown, West Virginia, United States

Site Status

Sydney Eye Hospital

Sydney, , Australia

Site Status

North Shore Eye Surgery

Sydney, , Australia

Site Status

CHU d'Angers

Angers, , France

Site Status

CH Nice

Nice, , France

Site Status

Centre Hospitalier National D'ophtalmologie

Paris, , France

Site Status

AP-HP- Hopital de la Pitie Salpetriere

Paris, , France

Site Status

Universitatsmedizin Gottingen

Göttingen, , Germany

Site Status

Johannes Gutenberg-University Medical Center

Mainz, , Germany

Site Status

NZOZ E-Vita

Bialystok, , Poland

Site Status

Specjakistyczny Osrodek Okulistyczny Oculomedica

Bydgoszcz, , Poland

Site Status

Santa Familia PTG Lodz

Lodz, , Poland

Site Status

Panstwowy Instytut Medycsny MSWiA

Warsaw, , Poland

Site Status

4 Wojskowy Szpital Kliniczny z Polikinika SP ZOZ

Wroclaw, , Poland

Site Status

Clinica Bonanova de Cirugia Ocular

Barcelona, , Spain

Site Status

Hospital Arruzafa

Córdoba, , Spain

Site Status

Clinica Universidad de Navarra

Madrid, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Clinica Universidad de Navarra

Pamplona, , Spain

Site Status

Complexo Hospiralario Universitario de Santiago-Hospital Medico-Ciruxico de Conxo

Santiago, , Spain

Site Status

Hospital Universitatio Virgen De La Macarena, Servicio de Oftalmologia

Seville, , Spain

Site Status

Hospital Universitario Miguel Servet, Servicio de Paseo Isabel La Catdlica1

Zaragoza, , Spain

Site Status

Northwick Park Hospital

London, United Kingdon, United Kingdom

Site Status

Western Eye Hospital Imperial College NHS trust

London, United Kingdon, United Kingdom

Site Status

Guy's and St. Thomas NHS Trust

London, United Kingdon, United Kingdom

Site Status

Countries

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United States Australia France Germany Poland Spain United Kingdom

Other Identifiers

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VRDN-001-101

Identifier Type: -

Identifier Source: org_study_id

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