Efficacy and Safety of Tozorakimab in Symptomatic Chronic Obstructive Pulmonary Disease With a History of Exacerbations

NCT ID: NCT05166889

Last Updated: 2026-01-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

1132 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-01-03

Study Completion Date

2026-03-23

Brief Summary

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The purpose of this Phase III study is to evaluate the efficacy and safety of tozorakimab Dose 1 and Dose 2 administered subcutaneously (SC) in adult participants with symptomatic COPD and history of ≥ 2 moderate or ≥ 1 severe exacerbation of COPD in the previous 12 months. Participants should be receiving optimised treatment with maintenance inhaled therapy (ICS/LABA/LAMA triple therapy, or dual therapy if triple is not considered appropriate) in stable doses throughout at least 3 months prior to enrolment.

Detailed Description

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Conditions

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Chronic Obstructive Pulmonary Disease (COPD)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
unblinded administrator/pharmacist

Study Groups

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Tozorakimab Dose 1

Dosing subcutaneously tozorakimab Dose 1 and placebo

Group Type EXPERIMENTAL

Tozorakimab

Intervention Type DRUG

Administered subcutaneously tozorakimab Dose 1 and placebo through Week 52.

Tozorakimab Dose 2

Dosing subcutaneously tozorakimab Dose 2

Group Type EXPERIMENTAL

Tozorakimab

Intervention Type DRUG

Administered subcutaneously tozorakimab Dose 2 through Week 52.

Placebo

Dosing subcutaneously with equivalent volume to tozorakimab

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo administered subcutaneously, equivalent volume to tozorakimab through week 52.

Interventions

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Tozorakimab

Administered subcutaneously tozorakimab Dose 1 and placebo through Week 52.

Intervention Type DRUG

Tozorakimab

Administered subcutaneously tozorakimab Dose 2 through Week 52.

Intervention Type DRUG

Placebo

Placebo administered subcutaneously, equivalent volume to tozorakimab through week 52.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Participant must be ≥ 40 years of age and capable of giving signed informed consent.
2. Documented diagnosis of COPD for at least one year prior to enrolment.
3. Post BD FEV1/FVC \< 0.70 and post-BD FEV1 \>20% of predicted normal value.
4. Documented history of ≥ 2 moderate or ≥ 1 severe COPD exacerbations within 12 months prior to enrolment.
5. Documented optimized inhaled dual or triple therapy at a stable dose for at least 3 months prior to enrolment.
6. Smoking history of ≥ 10 pack-years.
7. CAT total score ≥10, with each of the phlegm (sputum) and cough items with a score ≥ 2.

Exclusion Criteria

1. Clinically important pulmonary disease other than COPD.
2. Radiological findings suggestive of a respiratory disease other than COPD that is significantly contributing to the participant's respiratory symptoms.
3. Current diagnosis of asthma, prior history of asthma, or asthma-COPD overlap. Childhood history of asthma is allowed and defined as asthma diagnosed and resolved before the age of 18.
4. Any unstable disorder, including, but not limited to, cardiovascular, gastrointestinal, hepatic, renal, neurological, musculoskeletal, infectious, endocrine, metabolic, haematological, psychiatric disorder, major physical and/or cognitive impairment that could affect safety, study findings or participants ability to complete the study.
5. COPD exacerbation, within 2 weeks prior to randomization, that was treated with systemic corticosteroids and/or antibiotics, and/or led to hospitalization.
6. Active significant infection within the 4 weeks prior to randomization, pneumonia within 6 weeks prior to randomization, or medical condition that predisposes the participant to infection.
7. Suspicion of, or confirmed, ongoing SARS-CoV-2 infection.
8. Significant COVID-19 illness within the 6 months prior to enrolment.
9. Unstable cardiovascular disorder.
10. Diagnosis of cor pulmonale, pulmonary arterial hypertension and/or right ventricular failure.
11. History of known immunodeficiency disorder, including a positive test for HIV-1 or HIV 2.
12. History of positive test or treatment for hepatitis B or hepatitis C (except for cured hepatitis C)
13. Evidence of active liver disease, including jaundice during screening.
14. Malignancy, current or within the past 5 years, except for adequately treated non-invasive basal cell and squamous cell carcinoma of the skin and cervical carcinoma-in-situ treated with apparent success more than one year prior to enrolment. Suspected malignancy or undefined neoplasms.
15. Participants who have evidence of active TB.
16. Participants that have previously received tozorakimab.
17. Any clinically significant abnormal findings in physical examination, vital signs, ECG, or laboratory testing during the screening period, which in the opinion of the investigator may put the participant at risk because of their participation in the study, or may influence the results of the study, or the participant's ability to complete the entire duration of the study.
18. Active vaping of any products or using smoked marijuana within the 6 months prior to randomization and during the study.
Minimum Eligible Age

40 Years

Maximum Eligible Age

130 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Research Site

Huntsville, Alabama, United States

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Mobile, Alabama, United States

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Montgomery, Alabama, United States

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Tempe, Arizona, United States

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Bakersfield, California, United States

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Sacramento, California, United States

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Boynton Beach, Florida, United States

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Ormond Beach, Florida, United States

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Plantation, Florida, United States

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Meridian, Idaho, United States

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Evergreen Park, Illinois, United States

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Normal, Illinois, United States

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Iowa City, Iowa, United States

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Kansas City, Kansas, United States

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Baton Rouge, Louisiana, United States

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Zachary, Louisiana, United States

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Baltimore, Maryland, United States

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Rochester, Minnesota, United States

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St Louis, Missouri, United States

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Missoula, Montana, United States

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Brick, New Jersey, United States

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New York, New York, United States

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The Bronx, New York, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Gastonia, North Carolina, United States

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Fargo, North Dakota, United States

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DuBois, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Sayre, Pennsylvania, United States

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Rapid City, South Dakota, United States

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Franklin, Tennessee, United States

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Houston, Texas, United States

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Kingwood, Texas, United States

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Salt Lake City, Utah, United States

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Burlington, Vermont, United States

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Buenos Aires, , Argentina

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CABA, , Argentina

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Ciudad de Buenos Aires, , Argentina

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Córdoba, , Argentina

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Mar del Plata, , Argentina

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Mar del Plata, , Argentina

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Mendoza, , Argentina

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Quilmes, , Argentina

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San Fernando, , Argentina

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San Juan Bautista, , Argentina

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San Miguel de Tucumán, , Argentina

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Brussels, , Belgium

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Ghent, , Belgium

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Leuven, , Belgium

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Liège, , Belgium

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Namur, , Belgium

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Dupnitsa, , Bulgaria

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Haskovo, , Bulgaria

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Kozloduy, , Bulgaria

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Lovech, , Bulgaria

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Petrich, , Bulgaria

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Pleven, , Bulgaria

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Rousse, , Bulgaria

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Sliven, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Troyan Municipality, , Bulgaria

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Vratsa, , Bulgaria

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Calgary, Alberta, Canada

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Edmonton, Alberta, Canada

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Sherwood Park, Alberta, Canada

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Kamloops, British Columbia, Canada

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Kelowna, British Columbia, Canada

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Ajax, Ontario, Canada

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Guelph, Ontario, Canada

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Markham, Ontario, Canada

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Stouffville, Ontario, Canada

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Winchester, Ontario, Canada

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Montreal, PQ, Canada

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Québec, Quebec, Canada

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Québec, Quebec, Canada

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Terrebonne, Quebec, Canada

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Brno, , Czechia

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Broumov, , Czechia

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Jindřichův Hradec, , Czechia

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Liberec, , Czechia

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Olomouc, , Czechia

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Rokycany, , Czechia

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Aalborg, , Denmark

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Hvidovre, , Denmark

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København NV, , Denmark

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Næstved, , Denmark

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Roskilde, , Denmark

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Vejle, , Denmark

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Hämeenlinna, , Finland

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Helsinki, , Finland

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Kuopio, , Finland

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Tampere, , Finland

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Turku, , Finland

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Turku, , Finland

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Budapest, , Hungary

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Debrecen, , Hungary

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Edelény, , Hungary

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Encs, , Hungary

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Mosonmagyaróvár, , Hungary

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Nyíregyháza-Sóstóhegy, , Hungary

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Százhalombatta, , Hungary

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Ahmedabad, , India

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Belagavi, , India

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Coimbatore, , India

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Dehradun, , India

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Hyderabad, , India

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Jaipur, , India

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Mohali, , India

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Nagpur, , India

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Nashik, , India

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New Delhi, , India

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Surat, , India

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Thane, , India

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Asahikawa-shi, , Japan

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Chikushino-shi, , Japan

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Chūōku, , Japan

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Fujieda-shi, , Japan

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Fukuoka, , Japan

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Hamamatsu, , Japan

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Hamamatsu, , Japan

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Hiroshima, , Japan

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Iizuka-shi, , Japan

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Itabashi-ku, , Japan

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Iwata-shi, , Japan

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Joyo-shi, , Japan

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Kagoshima, , Japan

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Kanazawa, , Japan

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Kawachinagano-shi, , Japan

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Kitakyusyu-shi, , Japan

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Kobe, , Japan

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Koga-shi, , Japan

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Kokubunji-shi, , Japan

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Matsusaka-shi, , Japan

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Mizunami-shi, , Japan

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Nagaoka-shi, , Japan

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Nagoya, , Japan

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Obihiro, , Japan

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Okayama, , Japan

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Osaka, , Japan

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Osaka, , Japan

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Osaka, , Japan

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Sakaishi, , Japan

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Shinjuku-ku, , Japan

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Shizuoka, , Japan

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Toshima-ku, , Japan

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Toyonaka-shi, , Japan

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Yanagawa-shi, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Yokohama, , Japan

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Benito Juárez, , Mexico

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Chihuahua City, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Mexico City, , Mexico

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Mérida, , Mexico

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Monterrey, , Mexico

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Morelia, , Mexico

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Oaxaca City, , Mexico

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Veracruz, , Mexico

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Alkmaar, , Netherlands

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Eindhoven, , Netherlands

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Groningen, , Netherlands

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Harderwijk, , Netherlands

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Heerlen, , Netherlands

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Zutphen, , Netherlands

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Zwolle, , Netherlands

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Ålesund, , Norway

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Bergen, , Norway

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Bodø, , Norway

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Levanger, , Norway

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Lørenskog, , Norway

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Oslo, , Norway

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Tønsberg, , Norway

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Guimarães, , Portugal

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Lisbon, , Portugal

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Lisbon, , Portugal

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Matosinhos Municipality, , Portugal

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Vila Franca de Xira, , Portugal

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Vila Nova de Gaia, , Portugal

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Guaynabo, , Puerto Rico

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Daegu, , South Korea

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Incheon, , South Korea

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Jeonju, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Galdakao, , Spain

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Madrid, , Spain

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Málaga, , Spain

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Mérida, , Spain

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Pozuelo de Alarcón, , Spain

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Santander, , Spain

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Valencia, , Spain

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Zaragoza, , Spain

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Gothenburg, , Sweden

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Gothenburg, , Sweden

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Lund, , Sweden

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Malmo, , Sweden

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Stockholm, , Sweden

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Ankara, , Turkey (Türkiye)

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Aydin, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Mersin, , Turkey (Türkiye)

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Hanoi, , Vietnam

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Ho Chi Minh City, , Vietnam

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Countries

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United States Argentina Belgium Bulgaria Canada Czechia Denmark Finland Hungary India Japan Mexico Netherlands Norway Portugal Puerto Rico South Korea Spain Sweden Turkey (Türkiye) Vietnam

Other Identifiers

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2023-503571-19-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

2021-003797-30

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D9180C00003

Identifier Type: -

Identifier Source: org_study_id

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